{"id":16804,"date":"2025-02-07T22:30:12","date_gmt":"2025-02-07T22:30:12","guid":{"rendered":"https:\/\/www.globalresearchdata.kr\/?p=5455"},"modified":"2026-09-13T14:10:06","modified_gmt":"2026-09-13T05:10:06","slug":"morquio-syndrome-therapy-market-datam","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/morquio-syndrome-therapy-market-datam\/","title":{"rendered":"\uc138\uacc4\uc758 \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 (2024-2031) : \uc720\ud615\ubcc4 (\ud6a8\uc18c \ub300\uccb4 \uc694\ubc95, \uc9c0\uc6d0\/\uc99d\uc0c1 \uce58\ub8cc, \uae30\ud0c0), \uce58\ub8cc\ubc95\ubcc4 (MPS IV \uc720\ud615 A, MPS IV \uc720\ud615 B)"},"content":{"rendered":"<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-5456\" src=\"https:\/\/www.globalresearchdata.kr\/wp-content\/uploads\/2025\/02\/1-148.png\" alt=\"\" width=\"1350\" height=\"672\" \/><\/p>\n<p>&nbsp;<\/p>\n<ol>\n<li><b>\ubc29\ubc95\ub860 \ubc0f \ubc94\uc704<\/b>\n<ol>\n<li>\uc5f0\uad6c \ubc29\ubc95\ub860<\/li>\n<li>\ubcf4\uace0\uc11c\uc758 \uc5f0\uad6c \ubaa9\uc801 \ubc0f \ubc94\uc704<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc815\uc758 \ubc0f \uac1c\uc694<\/b><\/li>\n<li><b>\uc784\uc6d0 \uc694\uc57d<\/b>\n<ol>\n<li>\uc720\ud615\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uce58\ub8cc\ubc95\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc5ed\ud559<\/b>\n<ol>\n<li>\uc601\ud5a5 \uc694\uc778\n<ol>\n<li>\ub4dc\ub77c\uc774\ubc84\n<ol>\n<li>\uaddc\uc81c \uae30\uad00\uc758 \uc2b9\uc778<\/li>\n<li>XX<\/li>\n<\/ol>\n<\/li>\n<li>\uc81c\uc57d\n<ol>\n<li>\ub192\uc740 \uce58\ub8cc \ube44\uc6a9<\/li>\n<li>XX<\/li>\n<\/ol>\n<\/li>\n<li>\uae30\ud68c<\/li>\n<li>\uc601\ud5a5 \ubd84\uc11d<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc0b0\uc5c5 \ubd84\uc11d<\/b>\n<ol>\n<li>\ud3ec\ud130\uc758 \ub2e4\uc12f \uac00\uc9c0 \ud798 \ubd84\uc11d<\/li>\n<li>\uacf5\uae09\ub9dd \ubd84\uc11d<\/li>\n<li>\uac00\uaca9 \ubd84\uc11d<\/li>\n<li>\uaddc\uc81c \ubd84\uc11d<\/li>\n<li>\ud658\uae09 \ubd84\uc11d<\/li>\n<li>\ud2b9\ud5c8 \ubd84\uc11d<\/li>\n<li>\ud30c\uc774\ud504\ub77c\uc778 \ubd84\uc11d<\/li>\n<li>\uc5ed\ud559<\/li>\n<li>SWOT \ubd84\uc11d<\/li>\n<li>DMI \uc758\uacac<\/li>\n<\/ol>\n<\/li>\n<li><b>\ucf54\ub85c\ub09819 \ubd84\uc11d<\/b>\n<ol>\n<li>\ucf54\ub85c\ub09819 \ubd84\uc11d\n<ol>\n<li>\ucf54\ub85c\ub098 \uc774\uc804 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ucf54\ub85c\ub09819 \uc911 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ucf54\ub85c\ub098 \uc774\ud6c4 \uc2dc\ub098\ub9ac\uc624<\/li>\n<\/ol>\n<\/li>\n<li>\ucf54\ub85c\ub09819\uc5d0 \ub530\ub978 \uac00\uaca9 \uc5ed\ud559<\/li>\n<li>\uc218\uc694-\uacf5\uae09 \uc2a4\ud399\ud2b8\ub7fc<\/li>\n<li>\ud32c\ub370\ubbf9 \uae30\uac04 \uc911 \uc2dc\uc7a5\uacfc \uad00\ub828\ub41c \uc815\ubd80 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uc81c\uc870\uc5c5\uccb4\uc758 \uc804\ub7b5\uc801 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uacb0\ub860<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc720\ud615\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ud6a8\uc18c \ub300\uccb4 \uc694\ubc95*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\ube44\ubbf8\uc9d0(\uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c)<\/li>\n<\/ol>\n<\/li>\n<li>\uc9c0\uc9c0\/\uc99d\uc0c1 \uce58\ub8cc\n<ol>\n<li>\uc9c4\ud1b5\uc81c<\/li>\n<li>\ubcf4\ucda9\uc81c<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li><b>\uce58\ub8cc\ubc95\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uce58\ub8cc\ubc95\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218, \uce58\ub8cc\ubc95\ubcc4<\/li>\n<\/ol>\n<\/li>\n<li>MPS IV A\ud615*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<\/ol>\n<\/li>\n<li>MPS IV \uc720\ud615 B<\/li>\n<\/ol>\n<\/li>\n<li><b>\ud22c\uc5ec \uacbd\ub85c\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\ud22c\uc5ec \uacbd\ub85c\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144\ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\uc8fc\uc0ac\uc81c*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144\ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<\/ol>\n<\/li>\n<li>\uacbd\uad6c\uc6a9<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc720\ud1b5 \ucc44\ub110\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc720\ud1b5 \ucc44\ub110\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144\ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubcd1\uc6d0 \uc57d\uad6d*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144\ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d (%)<\/li>\n<\/ol>\n<\/li>\n<li>\uc18c\ub9e4 \uc57d\uad6d<\/li>\n<li>\uc628\ub77c\uc778 \uc57d\uad6d<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc9c0\uc5ed\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubd81\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%), \uc720\ud615\ubcc4<\/li>\n<li>\uce58\ub8cc\ubc95 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ubbf8\uad6d<\/li>\n<li>Canada<\/li>\n<li>\uba55\uc2dc\ucf54<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\ub7fd\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc\ubc95 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ub3c5\uc77c<\/li>\n<li>\uc601\uad6d<\/li>\n<li>\ud504\ub791\uc2a4<\/li>\n<li>\uc774\ud0c8\ub9ac\uc544<\/li>\n<li>\uc2a4\ud398\uc778<\/li>\n<li>\uae30\ud0c0 \uc720\ub7fd<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\ub0a8\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc\ubc95 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ube0c\ub77c\uc9c8<\/li>\n<li>\uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li>\uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc\ubc95 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\uc911\uad6d<\/li>\n<li>\uc778\ub3c4<\/li>\n<li>\uc77c\ubcf8<\/li>\n<li>\ud638\uc8fc<\/li>\n<li>\uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc\ubc95 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ud22c\uc5ec \uacbd\ub85c \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uc720\ud1b5 \ucc44\ub110 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li><b>\uacbd\uc7c1 \ud658\uacbd<\/b>\n<ol>\n<li>\uacbd\uc7c1 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\uc2dc\uc7a5 \ud3ec\uc9c0\uc154\ub2dd\/\uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li>\uc778\uc218\ud569\ubcd1 \ubd84\uc11d<\/li>\n<\/ol>\n<\/li>\n<li><b>\uae30\uc5c5 \ud504\ub85c\ud544<\/b><\/li>\n<\/ol>\n<p>&nbsp;<\/p>\n<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-5457\" src=\"https:\/\/www.globalresearchdata.kr\/wp-content\/uploads\/2025\/02\/2-111.png\" alt=\"\" width=\"1378\" height=\"396\" \/><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\uae00\ub85c\ubc8c \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5\uc740 2023-2030\ub144 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 CAGR\uc5d0 \ub3c4\ub2ec\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70\uc740 \uc5b4\ub9b0\uc774\uc758 \ubf08\uc640 \ucc99\ucd94, \uc7a5\uae30 \ubc0f \uc2e0\uccb4 \uae30\ub2a5\uc5d0 \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 \ub4dc\ubb38 \uc720\uc804 \uc9c8\ud658\uc785\ub2c8\ub2e4. \uc774 \uc7a5\uc560\ub97c \uac00\uc9c4 \uc5b4\ub9b0\uc774\ub294 \uccb4\ub0b4\uc5d0\uc11c \ubcf8\uc9c8\uc801\uc73c\ub85c \uc0dd\uc131\ub418\ub294 \ub2f9\uc1c4\ub97c \ub300\uc0ac\ud558\ub294 \ud6a8\uc18c\uac00 \uacb0\ud54d\ub418\uac70\ub098 \ucda9\ubd84\ud55c \uc591\uc744 \uc0dd\uc0b0\ud558\uc9c0 \ubabb\ud569\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uc0ac\uc2ac\uc740 \uc138\ud3ec, \ud608\uc561, \ud798\uc904 \ubc0f \uc778\ub300\uc5d0 \ube44\ucd95\ub418\uc5b4 \uc2dc\uac04\uc774 \uc9c0\ub0a8\uc5d0 \ub530\ub77c \ub9c8\ubaa8\ub97c \uc720\ubc1c\ud569\ub2c8\ub2e4. 2014\ub144\uc5d0 FDA\ub294 MPS IVA \uce58\ub8cc\ub97c \uc704\ud574 \uc7ac\uc870\ud569 \uc778\uac04 GALNS \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(\uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c \ub610\ub294 \ube44\ubbf8\uc9d0)\uc744 \uc2b9\uc778\ud588\uc73c\uba70, \ub2e4\ub978 MPS IV \uce58\ub8cc\ubc95\uc740 \uc99d\uc0c1 \uc644\ud654 \ubc0f \ubcf4\uc870 \uc694\ubc95\uc785\ub2c8\ub2e4.<\/p>\n<p>\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 \uc5ed\ud559<br \/>\n\uaddc\uc81c \uae30\uad00\uc758 \uc2b9\uc778<br \/>\n\uae30\uc874 \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \uc0c8\ub85c\uc6b4 \uc2b9\uc778\uacfc \uac1c\ubcc4 \uaddc\uc81c \ub2f9\uad6d\uc758 \uc9c0\uc6d0 \uc99d\uac00\ub294 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ucd09\uc9c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2019\ub144 6\uc6d4, \ubc14\uc774\uc624\ub9c8\ub9b0 \ud30c\ub9c8\uc288\ud2f0\uceec\uc740 \ubaa8\ud0a4\uc624 A \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4 \ubba4\ucf54\ub2e4\ub2f9\uc99d IVA(MPS IVA) \ud658\uc790 \uce58\ub8cc\uc5d0 \ub300\ud55c \ube44\ubbf8\uc9d0(\uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c)\uc758 \ubbf8\uad6d \uad6d\ub9bd\uc758\ub8cc\uc81c\ud488\uccad(NMPA) \uc2b9\uc778\uc744 \ud68d\ub4dd\ud588\uc2b5\ub2c8\ub2e4. \ube44\ubbf8\uc9d0\uc740 \uc911\uad6d\uc5d0\uc11c \uc774 \uc9c8\ud658\uc5d0 \ub300\ud574 \uc2b9\uc778\ub41c \ucd5c\ucd08\uc758 \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4.<br \/>\n\ub610\ud55c 2022\ub144 3\uc6d4 \uc601\uad6d \uad6d\ub9bd\ubcf4\uac74\uc784\uc0c1\uc5f0\uad6c\uc6d0(NICE)\uc740 \uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c(\ube44\ubbf8\uc9d0\uc774\ub77c\uace0\ub3c4 \ud558\uba70 \ubc14\uc774\uc624\ub9c8\ub9b0\uc5d0\uc11c \uc81c\uc870)\ub97c \uc810\uc561\ub2e4\ub2f9\uc99d 4A\ud615(MPS 4A \ubc0f \ubaa8\ud0a4\uc624 A \uc99d\ud6c4\uad70\uc774\ub77c\uace0\ub3c4 \ud568) \uce58\ub8cc\ub97c \uc704\ud574 NHS\uc5d0\uc11c \ubc18\ubcf5\uc801\uc73c\ub85c \uc0ac\uc6a9\ud558\ub3c4\ub85d \uc81c\uc548\ud558\ub294 \ucd5c\uc885 \uc9c0\uce68 \ucd08\uc548\uc744 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. \ub610\ud55c \uc5f0\uad6c \ud65c\ub3d9\uc758 \uc99d\uac00, \uc778\uc2dd \ubc0f \uc720\ubcd1\ub960 \uc99d\uac00\ub3c4 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ucd09\uc9c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ub192\uc740 \uce58\ub8cc \ube44\uc6a9<br \/>\n\ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ubc29\ud574 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, \uc77c\ubd80 \uad6d\uac00\uc758 \uc5d8\ub85c \uc124\ud30c \uc81c \uc54c\ud30c \ube44\uc6a9\uc740 \uc5f0\uac04 2,080,000 \ub2ec\ub7ec\uc5d0\uc11c 6,240,000 \ub2ec\ub7ec \uc0ac\uc774\uc774\ubbc0\ub85c \uc77c\ubd80 \uac74\uac15 \ubcf4\ud5d8\uc5d0\uc11c \uac10\ub2f9\ud558\uae30 \uc5b4\ub835\uc2b5\ub2c8\ub2e4. \ub610\ud55c \ub0ae\uc740 \uce58\ub8cc \uc120\ud0dd, \ub0ae\uc740 \uc720\ubcd1\ub960 \ubc0f \ub192\uc740 \uc57d\ubb3c \uac1c\ubc1c \ube44\uc6a9\ub3c4 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ubc29\ud574 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 \uc138\ubd84 \ubd84\uc11d<br \/>\n\uae00\ub85c\ubc8c \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5\uc740 \uc720\ud615, \uce58\ub8cc\ubc95, \ud22c\uc5ec \uacbd\ub85c, \uc720\ud1b5 \ucc44\ub110 \ubc0f \uc9c0\uc5ed\uc5d0 \ub530\ub77c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4.<br \/>\nMPS IV \uc720\ud615 A\uac00 \uc2dc\uc7a5\uc744 \uc9c0\ubc30 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uae0d\uc815\uc801 \uc778 \uc5f0\uad6c \uc870\uc0ac \uacb0\uacfc\uc758 \uc99d\uac00\uc640 MPS IV \uc720\ud615 B\ubcf4\ub2e4 MPS IV \uc720\ud615 A\uc758 \ub192\uc740 \uc720\ubcd1\ub960\ub85c \uc778\ud574 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc744 \uc9c0\ubc30 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, \uc2a4\ud398\uc778 \ubc14\ub974\uc140\ub85c\ub098 \ub300\ud559(UAB)\uc758 \uc5f0\uad6c\ud300\uc740 \ubaa8\ud0a4\uc624 A\ud615 \uc9c8\ud658\uc774\ub77c\uace0\ub3c4 \ubd88\ub9ac\ub294 \ubba4\ucf54\ub2e4\ub2f9\uc99d IVA\ud615 \ud658\uc790\uac00 \uacaa\ub294 \ubaa8\ub4e0 \uc7a5\uc560\uc801 \ubcc0\ud654\ub97c \uc694\uc57d\ud55c \ucd5c\ucd08\uc758 \uc950 \ubaa8\ub378\uc744 \uac1c\ubc1c\ud588\uc2b5\ub2c8\ub2e4. \uc5f0\uad6c\ud300\uc740 \ub2e8 \ud55c \ubc88\uc758 \uc815\ub9e5 \ub0b4 \ubc14\uc774\ub7ec\uc2a4 \ubca1\ud130 \ud22c\uc5ec \ud6c4 \uc950 \ubaa8\ub378\uc758 \uadf9\uc2ec\ud55c \uc804\uc2e0 \ubcc0\ud654\ub97c \uc644\uc804\ud788 \ud68c\ubcf5\uc2dc\ud0a4\ub294 \uc720\uc804\uc790 \uce58\ub8cc\ubc95\uc744 \uac1c\ubc1c\ud558\uc5ec \uc774 \ud76c\uadc0 \uc9c8\ud658\uc744 \uc553\uace0 \uc788\ub294 \ud658\uc790\uc5d0\uac8c \uc5b4\ub9b0 \ub098\uc774\uc5d0 \ud22c\uc5ec\ud558\uc5ec \ubf08 \uae30\ud615, \uace8\uad00\uc808\uc5fc \ubc0f \uae30\ud0c0 \uc0dd\uba85\uc744 \uc704\ud611\ud558\ub294 \ubcc0\ud654\ub97c \ud53c\ud560 \uc218 \uc788\ub294 \uc7a0\uc7ac\uc801 \uce58\ub8cc\uc758 \ubb38\uc744 \uc5f4\uc5c8\uc2b5\ub2c8\ub2e4.<br \/>\n\ub610\ud55c, \ubbf8\uad6d \ud76c\uadc0\uc9c8\ud658\ud611\ud68c(National Organization for Rare Disorders, Inc.)\uc5d0 \ub530\ub974\uba74 MPS IVA\ub294 \ub2e4\uc74c\uacfc \uac19\uc740 \ud76c\uadc0 \uc9c8\ud658\uc5d0\uc11c \ubc1c\uacac\ub429\ub2c8\ub2e4. \uc5d0 \ub530\ub974\uba74 MPS IVA\ub294 MPS IV\uc5d0 \uc601\ud5a5\uc744 \ubc1b\ub294 \uac1c\uc778\uc758 95%\uc5d0\uc11c \ubc1c\uacac\ub418\ub294 \ubc18\uba74, MPS IVB\ub294 \uc57d 5%\uc5d0\uc11c \ubc1c\uacac\ub429\ub2c8\ub2e4.<br \/>\n\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 \uc9c0\ub9ac\uc801 \uc810\uc720\uc728<br \/>\n\ubd81\ubbf8\uac00 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc744 \uc9c0\ubc30 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uc5f0\uad6c \uc774\ub2c8\uc154\ud2f0\ube0c\uc640 \uc790\uae08 \uc9c0\uc6d0\uc758 \uc99d\uac00\ub85c \uc778\ud574 \ubd81\ubbf8 \uc2dc\uc7a5\uc774 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc744 \uc9c0\ubc30\ud558\uba74\uc11c \ubd81\ubbf8 \uc2dc\uc7a5\uc774 \ud65c\uc131\ud654 \ub420 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023 \ub144 5 \uc6d4, \uad6d\ub9bd \ubcf4\uac74\uc6d0 (FNIH) \uac00\uc18d\ud654 \uc758\uc57d\ud488 \ud30c\ud2b8\ub108\uc2ed \ub9de\ucda4\ud615 \uc720\uc804\uc790 \uce58\ub8cc \ucee8\uc18c\uc2dc\uc5c4 (AMP BGTC)\uc758 \uad6c\uc131 \uc694\uc18c\ub85c\uc11c Nemours Children &#8216;s Health\ub294 Morquio A \uc99d\ud6c4\uad70\uc5d0 \ub300\ud55c \ucd5c\ucd08\uc758 \uc720\uc804\uc790 \uce58\ub8cc \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uc218\ud589\ud558\ub3c4\ub85d \uc120\uc815\ub418\uc5c8\uc2b5\ub2c8\ub2e4.<br \/>\n\ub610\ud55c, 2023\ub144 8\uc6d4\uc5d0\ub294 \uc774\ub974\uba74 \ub0b4\ub144\ubd80\ud130 \ubaa8\ud0a4\uc624 \ubc0f \uae30\ud0c0 7\uac00\uc9c0 \ucd08\ud76c\uadc0 \uc9c8\ud658\uc744 \uc553\uace0 \uc788\ub294 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \uc720\uc804\uc790 \uce58\ub8cc\ubc95\uc744 \uc2dc\ud5d8\ud558\ub294 \uc5f0\uad6c\uc790\ub4e4\uc744 \uc9c0\uc6d0\ud558\uae30 \uc704\ud574 9,700\ub9cc \ub2ec\ub7ec\uc758 \uc790\uae08\uacfc \uc804\ubb38 \uc9c0\uc2dd\uc744 \uc81c\uacf5\ud558\ub294 \ub3c5\ud2b9\ud55c \uc774\ub2c8\uc154\ud2f0\ube0c\uac00 \ucd94\uc9c4\ub429\ub2c8\ub2e4. \ube44\uc601\ub9ac\ub2e8\uccb4, \uc815\ubd80, \uc0b0\uc5c5\uacc4\uac00 \uc5f0\ud569\ud55c \uc774 \ud504\ub85c\uadf8\ub7a8\uc740 \ube44\uc601\ub9ac\ub2e8\uccb4\uc778 \uad6d\ub9bd\ubcf4\uac74\uc6d0 \uc7ac\ub2e8\uc774 \uc8fc\uad00\ud569\ub2c8\ub2e4. \ub610\ud55c, \uc774 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd\uacfc \uc720\ubcd1\ub960\uc758 \uc99d\uac00\ub294 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc9c0\uc5ed \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \uae30\uc5ec\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\nCOVID-19 \uc601\ud5a5 \ubd84\uc11d<br \/>\n\ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT)\uc740 \ud2b9\uc815 \uc720\ud615\uc758 \ub9ac\uc18c\uc880 \uc800\uc7a5 \uc9c8\ud658(LSD)\uc5d0 \ub300\ud55c \uc77c\ubc18\uc801\uc778 \uce58\ub8cc\ubc95\uc73c\ub85c, \ub9e4\uc8fc \ub610\ub294 \uaca9\uc8fc\ub85c \uc815\ub9e5 \ud22c\uc5ec\ud558\ub294 \uac83\uc744 \ud3ec\ud568\ud569\ub2c8\ub2e4. ERT\ub294 \ud638\ud761\uae30 \ubc0f \uc2ec\uc7a5 \uae30\ub2a5\uc744 \uac1c\uc120\ud558\uace0, \uc7a5\uae30 \ube44\ub300\uc99d\uc744 \uc644\ud654\ud558\uba70, \uc6b4\ub3d9 \ubc94\uc704\ub97c \uac1c\uc120\ud558\uace0, \uc77c\ubd80 \uc720\ud615\uc758 \ubba4\ucf54\ub2e4\ub2f9\uc99d(MPS)\uc758 \uc804\ubc18\uc801\uc778 \uac74\uac15 \uad00\ub828 \uc0b6\uc758 \uc9c8\uc744 \ud5a5\uc0c1\uc2dc\ud0a4\ub294 \uac83\uc73c\ub85c \ubc1d\ud600\uc84c\uc2b5\ub2c8\ub2e4.<br \/>\n\uadf8\ub7ec\ub098 \ucf54\ub85c\ub09819\ub85c \uc778\ud574 \uc608\uc815\ub41c ERT\uc758 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc7a5\uc740 \ubd80\uc815\uc801\uc778 \uc601\ud5a5\uc744 \ubc1b\uc558\uc2b5\ub2c8\ub2e4. \ub9ac\uc18c\uc880 \ucd95\uc801 \uc9c8\ud658\uc740 \ud638\ud761\uae30, \uc2e0\uc7a5, \uc2ec\uc7a5 \uae30\ub2a5\uc5d0 \uad00\uc5ec\ud558\uae30 \ub54c\ubb38\uc5d0 \uace0\uc704\ud5d8\uad70 \uc9c8\ud658\uc785\ub2c8\ub2e4. \ucf54\ub85c\ub09819 \ud32c\ub370\ubbf9\uc73c\ub85c \uc778\ud574 ERT\uc758 \uacf5\uae09\uc5d0\ub3c4 \ucc28\uc9c8\uc774 \uc0dd\uaca8 \uc804 \uc138\uacc4 \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \ud070 \uc601\ud5a5\uc744 \ubbf8\ucce4\uc2b5\ub2c8\ub2e4.<br \/>\n\uc8fc\uc694 \uac1c\ubc1c \ub3d9\ud5a5<br \/>\n2022\ub144 3\uc6d4, \uc601\uad6d \uad6d\ub9bd\ubcf4\uac74\uc784\uc0c1\uc5f0\uad6c\uc6d0(NICE)\uc740 NHS\uc5d0\uc11c \uc810\uc561\ub2e4\ub2f9\uc99d 4A\ud615(MPS 4A) \ub610\ub294 \ubaa8\ud0a4\uc624 A\ud615 \uc99d\ud6c4\uad70 \uce58\ub8cc\ub97c \uc704\ud574 \ubc14\uc774\uc624\ub9c8\ub9b0\uc774 \uc0dd\uc0b0\ud558\ub294 \uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c\ub97c \ubc18\ubcf5\uc801\uc73c\ub85c \uc0ac\uc6a9\ud560 \uac83\uc744 \uad8c\uace0\ud558\ub294 \uacb0\uc815\uc801\uc778 \uc9c0\uce68 \ucd08\uc548\uc744 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n\ubc14\uc774\uc624\ub9c8\ub9b0 \ud30c\ub9c8\uc288\ud2f0\uceec\uc758 \ube44\ubbf8\uc9d0(\uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c)\uc774 2019\ub144 \uc601\uad6d \uad6d\ub9bd\uc758\ub8cc\uc81c\ud488\uccad(NMPA)\uc73c\ub85c\ubd80\ud130 \ubba4\ucf54\ub2e4\ub2f9\uc99d 4A\ud615(MPS 4A) \ub610\ub294 \ubaa8\ud0a4\uc624 A \uc99d\ud6c4\uad70 \ud658\uc790 \uce58\ub8cc\uc81c\ub85c \uc2b9\uc778\ubc1b\uc558\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uc911\uad6d\uc5d0\uc11c \uc774 \ud76c\uadc0 \uc9c8\ud658\uc5d0 \ub300\ud55c \ucd5c\ucd08\uc758 \uc2b9\uc778\ub41c \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4.<\/p>\n<p>\ubcf4\uace0\uc11c\ub97c \uad6c\ub9e4\ud558\ub294 \uc774\uc720\ub294?<br \/>\n\uc720\ud615, \uce58\ub8cc\ubc95, \ud22c\uc5ec \uacbd\ub85c, \uc720\ud1b5 \ucc44\ub110 \ubc0f \uc9c0\uc5ed\uc5d0 \ub530\ub77c \uae00\ub85c\ubc8c \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 \uc138\ubd84\ud654\ub97c \uc2dc\uac01\ud654\ud558\uace0 \uc8fc\uc694 \uc0c1\uc5c5 \uc790\uc0b0 \ubc0f \ud50c\ub808\uc774\uc5b4\ub97c \uc774\ud574\ud569\ub2c8\ub2e4.<br \/>\n\ub3d9\ud5a5\uacfc \uacf5\ub3d9 \uac1c\ubc1c\uc744 \ubd84\uc11d\ud558\uc5ec \uc0c1\uc5c5\uc801 \uae30\ud68c\ub97c \ud30c\uc545\ud569\ub2c8\ub2e4.<br \/>\n\ubaa8\ub4e0 \uc138\uadf8\uba3c\ud2b8\uc5d0 \ub300\ud55c \ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70 \uce58\ub8cc \uc2dc\uc7a5 \uc218\uc900\uc758 \uc218\ub9ce\uc740 \ub370\uc774\ud130 \ud3ec\uc778\ud2b8\uac00 \ud3ec\ud568 \ub41c Excel \ub370\uc774\ud130 \uc2dc\ud2b8.<br \/>\nPDF \ubcf4\uace0\uc11c\ub294 \ucca0\uc800\ud55c \uc815\uc131\uc801 \uc778\ud130\ubdf0\uc640 \uc2ec\uce35 \uc5f0\uad6c\ub97c \uac70\uce5c \uc885\ud569\uc801\uc778 \ubd84\uc11d\uc73c\ub85c \uad6c\uc131\ub418\uc5b4 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n\ubaa8\ub4e0 \uc8fc\uc694 \uc5c5\uccb4\uc758 \uc8fc\uc694 \uc81c\ud488\uc73c\ub85c \uad6c\uc131\ub41c \uc81c\ud488 \ub9e4\ud551\uc744 \uc5d1\uc140\ub85c 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