{"id":17108,"date":"2025-02-25T14:46:36","date_gmt":"2025-02-25T14:46:36","guid":{"rendered":"https:\/\/www.globalresearchdata.kr\/?p=6444"},"modified":"2026-09-13T04:31:06","modified_gmt":"2026-09-12T19:31:06","slug":"metachromatic-leukodystrophy-treatment-market-datam","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/metachromatic-leukodystrophy-treatment-market-datam\/","title":{"rendered":"\uc138\uacc4\uc758 \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 (2024-2031) : \uc720\ud615\ubcc4 (\ud6c4\uae30 \uc601\uc544 MLD, \uccad\uc18c\ub144 MLD, \uc131\uc778 MLD), \uc9c4\ub2e8\ubcc4 (\ud608\uc561 \uac80\uc0ac, \uc720\uc804\uc790 \uac80\uc0ac, \uc2e0\uacbd \uc804\ub3c4 \uc5f0\uad6c, \uc790\uae30 \uacf5\uba85 \uc601\uc0c1 (MRI), \uc2ec\ub9ac\/\uc778\uc9c0 \uac80\uc0ac, \uae30\ud0c0)"},"content":{"rendered":"<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-6445\" src=\"https:\/\/www.globalresearchdata.kr\/wp-content\/uploads\/2025\/02\/1-465.png\" alt=\"\" width=\"1350\" height=\"281\" \/><\/p>\n<p>&nbsp;<\/p>\n<ol>\n<li>\ubc29\ubc95\ub860 \ubc0f \ubc94\uc704\n<ol>\n<li>\uc5f0\uad6c \ubc29\ubc95\ub860<\/li>\n<li>\ubcf4\uace0\uc11c\uc758 \uc5f0\uad6c \ubaa9\uc801 \ubc0f \ubc94\uc704<\/li>\n<\/ol>\n<\/li>\n<li>\uc2dc\uc7a5 \uc815\uc758 \ubc0f \uac1c\uc694<\/li>\n<li>\uc784\uc6d0 \uc694\uc57d\n<ol>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uc2a4 \ub2c8\ud3ab<\/li>\n<li>\uc9c4\ub2e8\ubcc4 \uc2dc\uc7a5 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uc2a4 \ub2c8\ud3ab<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4 \ub9c8\ucf13 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \ub9c8\ucf13 \uc2a4 \ub2c8\ud3ab<\/li>\n<\/ol>\n<\/li>\n<li>\uc2dc\uc7a5 \uc5ed\ud559\n<ol>\n<li>\uc2dc\uc7a5 \uc601\ud5a5 \uc694\uc778\n<ol>\n<li>\ub3d9\uc778\n<ol>\n<li>\ud0c8\uc218 \ucd08\uc131 \uc9c8\ud658 \uce58\ub8cc\ub97c\uc704\ud55c \uc81c\ud488\uc758 \ud601\uc2e0\uc774 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc8fc\ub3c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/li>\n<\/ol>\n<\/li>\n<li>\uc81c\uc57d:\n<ol>\n<li>\ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc\ub97c \uc704\ud55c \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/li>\n<\/ol>\n<\/li>\n<li>\uae30\ud68c<\/li>\n<li>\uc601\ud5a5 \ubd84\uc11d<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc0b0\uc5c5 \ubd84\uc11d\n<ol>\n<li>\uacf5\uae09\ub9dd \ubd84\uc11d<\/li>\n<li>\uac00\uaca9 \ubd84\uc11d<\/li>\n<li>\ucda9\uc871\ub418\uc9c0 \uc54a\uc740 \uc694\uad6c \uc0ac\ud56d<\/li>\n<\/ol>\n<\/li>\n<li>\ucf54\ub85c\ub09819 \ubd84\uc11d\n<ol>\n<li>\uc2dc\uc7a5\uc5d0\uc11c\uc758 \ucf54\ub85c\ub09819 \ubd84\uc11d\n<ol>\n<li>\ucf54\ub85c\ub09819 \uc774\uc804 \uc2dc\uc7a5 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ud604\uc7ac \ucf54\ub85c\ub09819 \uc2dc\uc7a5 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ucf54\ub85c\ub09819 \uc774\ud6c4 \ub610\ub294 \ubbf8\ub798 \uc2dc\ub098\ub9ac\uc624<\/li>\n<\/ol>\n<\/li>\n<li>\ucf54\ub85c\ub09819\uc5d0 \ub530\ub978 \uac00\uaca9 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc218\uc694-\uacf5\uae09 \uc2a4\ud399\ud2b8\ub7fc<\/li>\n<li>\ud32c\ub370\ubbf9 \uae30\uac04 \uc911 \uc2dc\uc7a5\uacfc \uad00\ub828\ub41c \uc815\ubd80 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uc81c\uc870\uc5c5\uccb4\uc758 \uc804\ub7b5\uc801 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uacb0\ub860<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\ud615\ubcc4\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218, \uc720\ud615\ubcc4 \uc138\uadf8\uba3c\ud2b8<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\uc544\uae30 \ud6c4\uae30 MLD*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d, \ubbf8\ud654 \ubc31\ub9cc \ub2ec\ub7ec, 2020-2029\ub144 \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<\/ol>\n<\/li>\n<li>\uccad\uc18c\ub144 MLD<\/li>\n<li>\uc131\uc778 MLD<\/li>\n<\/ol>\n<\/li>\n<li>\uc9c4\ub2e8\ubcc4\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc9c4\ub2e8\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<li>\uc9c4\ub2e8 \ubd80\ubb38\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ud608\uc561 \uac80\uc0ac*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d, \ubbf8\ud654 \ubc31\ub9cc \ub2ec\ub7ec, 2020-2029\ub144 \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\uc804\uc790 \uac80\uc0ac<\/li>\n<li>\uc2e0\uacbd \uc804\ub3c4 \uc5f0\uad6c<\/li>\n<li>\uc790\uae30 \uacf5\uba85 \uc601\uc0c1(MRI)<\/li>\n<li>\uc2ec\ub9ac \ubc0f \uc778\uc9c0 \ud14c\uc2a4\ud2b8<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615 \uc138\uadf8\uba3c\ud2b8\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\uc57d\ubb3c \uc694\ubc95*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d, \ubbf8\ud654 \ubc31\ub9cc \ub2ec\ub7ec, 2020-2029\ub144 \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\uc804\uc790 \uce58\ub8cc\n<ol>\n<li>AGT-183<\/li>\n<li>GSK-2696274<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li>\ud6a8\uc18c \ub300\uccb4 \ub610\ub294 \uac15\ud654 \uc694\ubc95<\/li>\n<li>\uae30\uc9c8 \uac10\uc18c \uc694\ubc95<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \uc138\uadf8\uba3c\ud2b8\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubcd1\uc6d0*\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d, \ubbf8\ud654 \ubc31\ub9cc \ub2ec\ub7ec, 2020-2029\ub144 \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<\/ol>\n<\/li>\n<li>\ud074\ub9ac\ub2c9<\/li>\n<li>\uc9c4\ub2e8 \uc13c\ud130<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li>\uc9c0\uc5ed\ubcc4\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d, \ubbf8\ud654 \ubc31\ub9cc \ub2ec\ub7ec, 2020-2029\ub144 \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%), 2021-2029\ub144<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubd81\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%), \uc720\ud615\ubcc4<\/li>\n<li>\uc9c4\ub2e8 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ubbf8\uad6d<\/li>\n<li>\uce90\ub098\ub2e4<\/li>\n<li>\uba55\uc2dc\ucf54<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\ub7fd\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d (%)<\/li>\n<li>\uc9c4\ub2e8 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ub3c5\uc77c<\/li>\n<li>\uc601\uad6d<\/li>\n<li>\ud504\ub791\uc2a4<\/li>\n<li>\uc774\ud0c8\ub9ac\uc544<\/li>\n<li>\uc2a4\ud398\uc778<\/li>\n<li>\uae30\ud0c0 \uc720\ub7fd<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\ub0a8\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d (%)<\/li>\n<li>\uc9c4\ub2e8 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ube0c\ub77c\uc9c8<\/li>\n<li>\uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li>\ub098\uba38\uc9c0 \ub0a8\ubbf8<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc9c4\ub2e8 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\uc911\uad6d<\/li>\n<li>\uc778\ub3c4<\/li>\n<li>\uc77c\ubcf8<\/li>\n<li>\ud638\uc8fc<\/li>\n<li>\uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc9c4\ub2e8\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%), \uc9c4\ub2e8\ubcc4<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uacbd\uc7c1 \ud658\uacbd\n<ol>\n<li>\uc8fc\uc694 \uac1c\ubc1c \ubc0f \uc804\ub7b5<\/li>\n<li>\uae30\uc5c5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li>\uc81c\ud488 \ubca4\uce58\ub9c8\ud0b9<\/li>\n<li>\uc8fc\ubaa9\ud574\uc57c \ud560 \uc8fc\uc694 \uae30\uc5c5 \ubaa9\ub85d<\/li>\n<\/ol>\n<\/li>\n<li>\ud68c\uc0ac \ud504\ub85c\ud544<\/li>\n<\/ol>\n<p>&nbsp;<\/p>\n<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-6446\" src=\"https:\/\/www.globalresearchdata.kr\/wp-content\/uploads\/2025\/02\/2-364.png\" alt=\"\" width=\"1298\" height=\"164\" \/><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc740 \uc608\uce21 \uae30\uac04 (2023-2030 \ub144) \ub3d9\uc548 6.3 %\uc758 CAGR\ub85c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n\ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d\uc740 \uc8fc\ub85c \ub1cc, \ucc99\uc218 \ubc0f \ub9d0\ucd08 \uc2e0\uacbd\uc758 \uc138\ud3ec\uc5d0 \uc9c0\ubc29 \ubb3c\uc9c8(\uc9c0\uc9c8)\uc774 \ucd95\uc801\ub418\ub294 \ud76c\uadc0 \uc720\uc804\uc131(\uc720\uc804\uc801) \uc9c8\ud658\uc785\ub2c8\ub2e4. \uc124\ud30c\ud2f0\ub4dc\ub77c\uace0 \ud558\ub294 \uc9c0\uc9c8\uc744 \ubd84\ud574\ud558\ub294 \ud6a8\uc18c\uac00 \ubd80\uc871\ud558\uba74 \uc774\ub7ec\ud55c \ucd95\uc801\uc774 \ubc1c\uc0dd\ud569\ub2c8\ub2e4. \uc2e0\uacbd \uc138\ud3ec\ub97c \ub36e\uace0 \ubcf4\ud638\ud558\ub294 \ubb3c\uc9c8(\ubbf8\uc5d8\ub9b0)\uc774 \ud30c\uad34\ub418\uc5b4 \ub1cc\uc640 \uc2e0\uacbd\uacc4\uac00 \uc11c\uc11c\ud788 \uae30\ub2a5\uc744 \uc783\uac8c \ub429\ub2c8\ub2e4. \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d\uc740 \ud604\uc7ac \uce58\ub8cc\uac00 \ubd88\uac00\ub2a5\ud569\ub2c8\ub2e4. \uc870\uae30\uc5d0 \ubc1c\uacac\ud558\uace0 \uce58\ub8cc\ud558\uba74 \ubc1c\ubcd1 \ud615\ud0dc\uc640 \uc5f0\ub839\uc5d0 \ub530\ub77c \uc77c\ubd80 \uc9d5\ud6c4\uc640 \uc99d\uc0c1\uc744 \uad00\ub9ac\ud558\uace0 \uc9c8\ubcd1\uc758 \uc9c4\ud589\uc744 \uc9c0\uc5f0\uc2dc\ud0a4\ub294 \ub370 \ub3c4\uc6c0\uc774 \ub420 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\nDataM Intelligence\uc5d0 \ub530\ub974\uba74 \ubcc0\uc0c9 \uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc5f0\uad6c \ubd84\uc11d\uc740 \uc591\uc801 \ubc0f \uc9c8\uc801 \ub370\uc774\ud130\uac00 \ud3ec\ud568 \ub41c \uc2dc\uc7a5\uc5d0 \ub300\ud55c \uc2ec\uce35\uc801 \uc778 \uc804\ub9dd\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \uc2dc\uc7a5 \uc138\ubd84\ud654\ub97c \uae30\ubc18\uc73c\ub85c \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc5d0 \ub300\ud55c \uc804\ub9dd\uacfc \uc608\uce21\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ub610\ud55c \ubbf8\uad6d, \uce90\ub098\ub2e4, \ube0c\ub77c\uc9c8, \ub3c5\uc77c, \uc774\ud0c8\ub9ac\uc544, \uc2a4\ud398\uc778, \uc601\uad6d, \ub7ec\uc2dc\uc544, \uc720\ub7fd \uad6d\uac00, \uc544\ub78d \uc5d0\ubbf8\ub9ac\ud2b8, \uc0ac\uc6b0\ub514 \uc544\ub77c\ube44\uc544, \ub0a8\uc544\ud504\ub9ac\uce74 \uacf5\ud654\uad6d, \uc77c\ubcf8, \uc911\uad6d, \uc778\ub3c4, \ud55c\uad6d, \ud638\uc8fc \ubc0f \uc804 \uc138\uacc4 \ub098\uba38\uc9c0 \uad6d\uac00\uc640 \uac19\uc740 \uc8fc\uc694 \uad6d\uac00\uc5d0 \ub300\ud55c \uc874\uc911\uacfc \ud568\uaed8 \uae00\ub85c\ubc8c \ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5, \ucd5c\uc2e0 \ub3d9\ud5a5, \uae30\ud68c \ubc0f 2029 \ub144\uae4c\uc9c0 \uc608\uce21\uacfc \ud568\uaed8 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4.<br \/>\n\ubaa8\ub4e0 \uc9c0\uc5ed \uc911\uc5d0\uc11c \ubd81\ubbf8 \uc9c0\uc5ed\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc5d0\uc11c \uac00\uc7a5 \ud070 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ubbf8\uad6d\uacfc \uce90\ub098\ub2e4\uc758 \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc740 \uac00\uc7a5 \ud070 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ubc18\uba74 \uc720\ub7fd \ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc740 2022-2029 \ub144 \ub3d9\uc548 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uadf8 \uc874\uc7ac\ub97c \uacc4\uc18d\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc5ed\ud559<br \/>\n\ud0c8\uc218 \ucd08\uc131 \uc9c8\ud658\uc744 \uce58\ub8cc\ud558\uae30\uc704\ud55c \uc81c\ud488\uc758 \ud601\uc2e0\uc774 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc8fc\ub3c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubbf8\uad6d \ub4c0\ud06c \ub300\ud559\uc758 \uc18c\uc544\uacfc \ubc0f \ubcd1\ub9ac\ud559 \uad50\uc218\uc778 \uc870\uc564 \ucee4\uce20\ubc84\uadf8\ub294 \uc81c\ub300\ud608\uc5d0\uc11c \uc0dd\uc131\ub41c \uc138\ud3ec\ub85c \ud0c8\uc218\ucd08\uc131 \uc9c8\ud658 \ud658\uc790\uc5d0\uac8c \ub3c4\uc6c0\uc774 \ub418\ub294 \uac83\uc73c\ub85c \uc785\uc99d\ub41c \ub4c0\ud06c \uc624 \uc140 \ub610\ub294 DUOC-01\uc774\ub77c\ub294 \uc81c\ud488\uc744 \uac1c\ubc1c\ud588\uc2b5\ub2c8\ub2e4. \uc774 \uc81c\ud488\uc740 \uc720\uc804\uc131 \ub300\uc0ac \ubb38\uc81c\uac00 \uc788\ub294 \uccad\uc18c\ub144\uc758 \ube60\ub978 \uc0dd\ucc29\uc744 \ub3d5\uae30 \uc704\ud55c \uac00\uad50 \uc694\ubc95\uc73c\ub85c \uc0ac\uc6a9\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \ub610\ud55c \uc544\ud2f0\ub2e4\uc0ac\uc9c4 \uc624\ud1a0\ud15c\uc140(ARSA-CEL)\uc740 \uc790\uac00 \uc870\ud608\ubaa8\uc138\ud3ec \ubc0f \uc804\uad6c\uc138\ud3ec(HSPC)\ub97c \uc0dd\uccb4 \uc678\uc5d0\uc11c ARSA cDNA\ub97c \ucf54\ub529\ud558\ub294 \ub80c\ud2f0\ubc14\uc774\ub7ec\uc2a4 \ubca1\ud130\ub85c \uc804\uc774\uc2dc\ud0a8 \uc720\uc804\uc790 \uce58\ub8cc \uc758\uc57d\ud488\uc73c\ub85c, HSPC\uc640 \uadf8 \uc790\uc190\uc5d0\uc11c \ucd08\uc815\uc0c1 ARSA \ubc1c\ud604\uc744 \uc720\ub3c4\ud558\uba70 \ucd08\uae30 \ubc1c\ubcd1 MLD \ud658\uc790\uc5d0\uc11c \uc548\uc804\uc131 \ubc0f \ud6a8\ub2a5\uc5d0 \ub300\ud55c \uc608\ube44 \uc99d\uac70\ub97c \ubcf4\uc720\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub530\ub77c\uc11c \uc704\uc758 \uc9c4\uc220\uc5d0\uc11c \uc2dc\uc7a5\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc8fc\ub3c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uad6c\uc18d:<br \/>\n\ubcc0\uc0c9\uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc\ub97c\uc704\ud55c \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uacfc \ubcc0\uc0c9\uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d\uc744 \uc644\uc804\ud788 \uce58\ub8cc\ud560 \uc218\uc788\ub294 FDA \uc2b9\uc778 \uc57d\ub9ac\ud559 \uc81c\ud488\uc774 \uc2dc\uc7a5\uc5d0 \ub098\uc640 \uc788\uc9c0 \uc54a\ub2e4\ub294 \uac83\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5\uc744 \ubc29\ud574 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\ub294 \uc694\uc778\uc785\ub2c8\ub2e4.<br \/>\nCOVID-19 \uc601\ud5a5 \ubd84\uc11d<br \/>\nCOVID-19 \ud32c\ub370\ubbf9\uc740 \uc758\ub8cc \uc2dc\uc2a4\ud15c\uacfc \uc2dc\uc7a5\uc5d0 \uc801\ub2f9\ud55c \uc601\ud5a5\uc744 \ubbf8\ucce4\uc2b5\ub2c8\ub2e4. \ud32c\ub370\ubbf9 \uae30\uac04 \ub3d9\uc548 \uac00\uc815 \uac04\ud638\uc0ac\ub97c \uc704\ud55c \uac1c\uc778 \ubcf4\ud638 \uc7a5\ube44(PPE)\uc5d0 \ub300\ud55c \ud45c\uc900 \uc6b4\uc601 \uc808\ucc28\uac00 \ubd88\ubd84\uba85\ud588\uc2b5\ub2c8\ub2e4. \uc758\uc0ac\ub4e4\uc740 \ubaa8\ub4e0 \ud658\uc790\uc5d0\uac8c \uc774\uba54\uc77c\uc774\ub098 \uc804\ud654\ub85c \uc5f0\ub77d\ud558\uace0, \uc774\uba54\uc77c\uc774\ub098 \uc778\ud130\ub137\uc5d0 \uc811\uc18d\ud560 \uc218 \uc5c6\ub294 \ud658\uc790\uc5d0\uac8c\ub294 \ud3b8\uc9c0\ub97c \ubcf4\ub0c8\uc2b5\ub2c8\ub2e4. \ud32c\ub370\ubbf9 \ucd08\uae30\uc5d0\ub294 SARS-CoV-2 \uac10\uc5fc\uc774 \ud76c\uadc0\uc9c8\ud658\uc5d0 \ubbf8\uce58\ub294 \uc601\ud5a5\uc5d0 \ub300\ud55c \uc99d\uac70\uac00 \uac70\uc758 \uc5c6\uc5c8\uae30 \ub54c\ubb38\uc5d0, \uc6b0\ub9ac\ub294 SARS-CoV-2 \ubc1c\ubcd1 \uc704\ud5d8\uc774 \uce58\ub8cc \uc911\ub2e8\uc758 \uc704\ud5d8\ubcf4\ub2e4 \ub354 \ud06c\ub2e4\uace0 \ud310\ub2e8\ud588\uc2b5\ub2c8\ub2e4. \ub610\ud55c, \uacc4\ud68d\uc801\uc774\ub4e0 \ubd88\uac00\ud53c\ud55c \uac83\uc774\ub4e0 \uce58\ub8cc\uac00 \uc911\ub2e8\ub418\uba74 \uc784\uc0c1 \uc9c0\ud45c\uc640 \uc0b6\uc758 \uc9c8\uc774 \uc545\ud654\ub420 \ubfd0\ub9cc \uc544\ub2c8\ub77c \uc2ec\uc7a5 \uc9c8\ud658\uc774\ub098 \uc2e0\uc7a5 \uae30\ub2a5 \uc800\ud558\uc640 \uac19\uc740 \ubd80\uc815\uc801\uc778 \uacb0\uacfc\uac00 \ubc1c\uc0dd\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n\ub610\ud55c \ucf54\ub85c\ub09819 \ud32c\ub370\ubbf9\uc774 \uc804\uc784\uc0c1 \ubc0f \uc784\uc0c1 \uac1c\ubc1c, \uacf5\uae09\ub9dd, \uc0c1\uc5c5 \ud504\ub85c\uadf8\ub7a8 \ub4f1 \ube44\uc988\ub2c8\uc2a4\uc5d0 \ubbf8\uce58\ub294 \uc601\ud5a5\uc758 \uc2ec\uac01\uc131\ub3c4 \uc601\ud5a5\uc744 \ubc1b\uc558\uc2b5\ub2c8\ub2e4. \ub530\ub77c\uc11c \uc704\uc640 \uac19\uc774 \uc2dc\uc7a5\uc774 \uc601\ud5a5\uc744 \ubc1b\uc558\uc73c\uba70, \uacbd\uc81c \ud65c\ub3d9\uc774 \uc7ac\uac1c\ub418\uba74 \ube60\ub974\uac8c \ud68c\ubcf5\ub420 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubcc0\uc0c9 \uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc138\ubd84 \ubd84\uc11d<br \/>\n\uc720\uc804\uc790 \uce58\ub8cc \ubd80\ubb38\uc740 \ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc5d0\uc11c \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uc720\uc804\uc790 \uce58\ub8cc \ubd80\ubb38\uc740 2021 \ub144\uc5d0 \uc9c0\ubc30\uc801 \uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774 \ubd80\ubb38\uc758 \uc131\uc7a5\uc740 \uc720\uc804\uc790 \uce58\ub8cc\uac00 \uc870\uae30 \ubc1c\ubcd1 \ubcc0\uc0c9\uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d(MLD)\uc744 \uc553\ub294 \uc18c\uc544 \ud658\uc790\uc5d0\uc11c \uc774\uc810\uc744 \ubcf4\uc600\uae30 \ub54c\ubb38\uc5d0 \uc720\uc775\ud569\ub2c8\ub2e4. \ud604\uc7ac MLD\uc5d0 \ub300\ud55c \uce58\ub8cc\ubc95\uc740 \uc5c6\uc2b5\ub2c8\ub2e4. \uc774\uc5d0 \uc720\ub7fd\uc758\uc57d\ud488\uccad(EMA)\uc740 \uc544\ub9b4\uc124\ud30c\ud0c0\uc81c-A \uc720\uc804\uc790\ub97c \ucf54\ub529\ud558\ub294 \ub0c9\ub3d9 \ubcf4\uc874\ub41c \uc790\uac00 CD34+ \uc138\ud3ec\ub85c \uad6c\uc131\ub41c \uc720\uc804\uc790 \uce58\ub8cc\uc81c Libmeldy\ub97c \uc2e0\uacbd\uacc4\uc5d0 \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 \ud76c\uadc0 \uc720\uc804\uc131 \ub300\uc0ac \uc9c8\ud658\uc778 \ubcc0\uc0c9\uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d(MLD) \uce58\ub8cc\uc81c\ub85c \uc720\ub7fd\uc5f0\ud569\uc5d0\uc11c \ud310\ub9e4 \ud5c8\uac00\ub97c \uc2b9\uc778\ud560 \uac83\uc744 \uad8c\uace0\ud588\uc2b5\ub2c8\ub2e4. \ub9ac\uba5c\ub514\ub294 \uacb0\ud568 \uc720\uc804\uc790 \ubcf4\uc720\uc790\ub85c \uc9c4\ub2e8\ub418\uc5c8\uc9c0\ub9cc \uc544\uc9c1 \uc99d\uc0c1\uc774 \ub098\ud0c0\ub098\uc9c0 \uc54a\uc558\uace0 &#8216;\uc601\uc544\uae30 \ud6c4\uae30&#8217; \ub610\ub294 &#8216;\uccad\uc18c\ub144\uae30 \ucd08\uae30&#8217; \ubcc0\uc885 MLD\ub97c \uc553\uace0 \uc788\ub294 \uc5b4\ub9b0\uc774\ub97c \uc704\ud55c \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4. \uc774 \uce58\ub8cc\ubc95\uc740 \ucd08\uae30 \uccad\uc18c\ub144 \ud615\ud0dc\uc758 \uc9c8\ubcd1 \uc9c4\ub2e8\uc744 \ubc1b\uc558\uc73c\uba70 \uc544\uc9c1 \ub3c5\ub9bd\uc801\uc73c\ub85c \uac78\uc744 \uc218 \uc788\uace0 \uc778\uc9c0 \uc7a5\uc560\uac00 \ub098\ud0c0\ub098\uae30 \uc804\uc5d0 \uc99d\uc0c1\uc774 \ub098\ud0c0\ub098\uae30 \uc2dc\uc791\ud55c \uc5b4\ub9b0\uc774\uc5d0\uac8c \uc0ac\uc6a9\ub429\ub2c8\ub2e4. \ub530\ub77c\uc11c \uc704\uc758 \uc9c4\uc220\uc5d0\uc11c \uc2dc\uc7a5 \ubd80\ubb38\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcc0\uc0c9 \uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc9c0\ub9ac\uc801 \ubd84\uc11d<br \/>\n\ubd81\ubbf8 \uc9c0\uc5ed\uc740 \uae00\ub85c\ubc8c \ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc5d0\uc11c \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n2021 \ub144 \ubd81\ubbf8\ub294 \uac00\uc7a5 \ub192\uc740 \ub9e4\ucd9c \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \ubcc0\uc0c9 \uc131 \ubc31\ud608\uad6c \uac10\uc18c\uc99d\uc758 \uc720\ubcd1\ub960 \uc99d\uac00, \uc9c4\ub2e8 \ud658\uc790 \uc218 \uc99d\uac00, \uc9c4\ud589\uc911\uc778 \uc784\uc0c1 \uc2dc\ud5d8, \uce58\ub8cc\ub97c\uc704\ud55c \uc5f0\uad6c \uac1c\ubc1c\uc744\uc704\ud55c \uc815\ubd80 \uc790\uae08 \uc99d\uac00, \uc9c0\uc5ed \ub0b4 \uc870\uc9c1\uc758 \uc5f0\ub77d\ucc98 \ub4f1\ub85d \uc2dc\uc791\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5\uc774 \uc99d\uac00 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\ub294 \uba87 \uac00\uc9c0 \uc694\uc778\uc785\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d\uc740 \ubbf8\uad6d\uc5d0\uc11c \ucd9c\uc0dd\uc544 40,000\uba85 \uc911 1\uba85\uaf34\ub85c \ubc1c\uc0dd\ud569\ub2c8\ub2e4. \ub610\ud55c, \ubbf8\uad6d \ud76c\uadc0\uc9c8\ud658\uae30\uad6c\ub294 \ub3cc\uc774\ud0ac \uc218 \uc5c6\ub294 \ubc31\uc9c8 \ud30c\uad34\ub97c \uc77c\uc73c\ud0a4\ub294 \ub1cc \uc9c8\ud658\uc778 \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d(MLD)\uc744 \uc870\uc0ac\ud558\uae30 \uc704\ud55c \ub300\uaddc\ubaa8 \uc5f0\uad6c\uc5d0 \ucc29\uc218\ud588\uc2b5\ub2c8\ub2e4. \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \ucee4\ubba4\ub2c8\ud2f0 \uc5f0\ud569 \uc5f0\uad6c \ubc0f \ucc38\uc5ec \uc870\uc0ac(MLDCures)\ub294 \uc804 \uc138\uacc4 \ubcc0\uc0c9\uc131 \ubc31\uc9c8\uc774\uc601\uc591\uc99d \ud658\uc790\ub4e4\uc774 \uc774 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc815\ubcf4\ub97c \uc81c\uacf5\ud560 \uc218 \uc788\ub294 \ud50c\ub7ab\ud3fc\uc744 \uc81c\uacf5\ud558\ub294 \uc0c8\ub85c\uc6b4 \ud504\ub85c\uc81d\ud2b8\uc785\ub2c8\ub2e4. \uc774 \ud504\ub85c\uc81d\ud2b8\uc758 \ubaa9\ud45c\ub294 \uacfc\ud559\uc790\ub4e4\uc774 \ud5a5\ud6c4 \uc5f0\uad6c\uc5d0 \ud65c\uc6a9\ud560 \uc218 \uc788\ub294 \uad6d\uc81c\uc801\uc778 \ub9ac\uc18c\uc2a4\ub97c \ub9cc\ub4dc\ub294 \uac83\uc785\ub2c8\ub2e4. \ub610\ud55c Cure MLD\ub294 7,000\uac1c \ud76c\uadc0\uc9c8\ud658\uc758 \uc2dd\ubcc4 \ubc0f \uce58\ub8cc\ub97c \uc9c0\uc6d0\ud558\uae30 \uc704\ud574 IAMRARE \ud50c\ub7ab\ud3fc\uc744 \uac1c\ubc1c\ud55c \ub3c5\ub9bd \uae30\uad00\uc778 \uad6d\ub9bd \ud76c\uadc0\uc9c8\ud658\uae30\uad6c(NORD)\uc640 \uc774 \uc5f0\uad6c\uc5d0 \ud611\ub825\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub530\ub77c\uc11c \uc704\uc758 \uc9c4\uc220\uc5d0 \ub530\ub974\uba74 \ubd81\ubbf8 \uc9c0\uc5ed\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c 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