{"id":19392,"date":"2025-02-04T16:09:50","date_gmt":"2025-02-04T16:09:50","guid":{"rendered":"https:\/\/www.mizuho.kr\/?p=5111"},"modified":"2026-09-06T18:40:01","modified_gmt":"2026-09-06T09:40:01","slug":"mucopolysaccharidosis-treatment-market-datam","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/mucopolysaccharidosis-treatment-market-datam\/","title":{"rendered":"\uae00\ub85c\ubc8c \uc810\uc561 \ub2e4\ub2f9\ub958\uc99d \uce58\ub8cc \uc2dc\uc7a5 : \uc9c8\ubcd1 \uc720\ud615\ubcc4 (MPS \uc720\ud615 1, MPS \uc720\ud615 2, MPS \uc720\ud615 3, MPS \uc720\ud615 4, \uae30\ud0c0)"},"content":{"rendered":"<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-5112\" src=\"https:\/\/www.mizuho.kr\/wp-content\/uploads\/2025\/02\/1-59.png\" alt=\"\" width=\"1353\" height=\"532\" \/><\/p>\n<p>&nbsp;<\/p>\n<ol>\n<li><b>\ubc29\ubc95\ub860 \ubc0f \ubc94\uc704<\/b>\n<ol>\n<li>\uc5f0\uad6c \ubc29\ubc95\ub860<\/li>\n<li>\ubcf4\uace0\uc11c\uc758 \uc5f0\uad6c \ubaa9\uc801 \ubc0f \ubc94\uc704<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc815\uc758 \ubc0f \uac1c\uc694<\/b><\/li>\n<li><b>\uc784\uc6d0 \uc694\uc57d<\/b>\n<ol>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \uc2a4\ub2c8\ud3ab<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc5ed\ud559<\/b>\n<ol>\n<li>\uc601\ud5a5 \uc694\uc778\n<ol>\n<li>\ub3d9\uc778\n<ol>\n<li>\ub354 \ub098\uc740 \uce58\ub8cc \uacb0\uacfc\ub97c \uc704\ud55c \uaddc\uc81c \ub2f9\uad6d\uc758 \uc9c8\ubcd1 \uc2b9\uc778 \uc99d\uac00<\/li>\n<li>\uae30\uc220 \ubc1c\uc804\uc758 \uc99d\uac00<\/li>\n<\/ol>\n<\/li>\n<li>\uc81c\uc57d \uc694\uc778\n<ol>\n<li>\ub192\uc740 \uce58\ub8cc \ube44\uc6a9<\/li>\n<\/ol>\n<\/li>\n<li>\uae30\ud68c<\/li>\n<li>\uc601\ud5a5 \ubd84\uc11d<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc0b0\uc5c5 \ubd84\uc11d<\/b>\n<ol>\n<li>\ud3ec\ud130\uc758 \ub2e4\uc12f \uac00\uc9c0 \ud798 \ubd84\uc11d<\/li>\n<li>\uacf5\uae09\ub9dd \ubd84\uc11d<\/li>\n<li>\uac00\uaca9 \ubd84\uc11d<\/li>\n<li>\uaddc\uc81c \ubd84\uc11d<\/li>\n<li>\ub7ec\uc2dc\uc544-\uc6b0\ud06c\ub77c\uc774\ub098 \uc804\uc7c1 \uc601\ud5a5 \ubd84\uc11d<\/li>\n<li>DMI \uc758\uacac<\/li>\n<\/ol>\n<\/li>\n<li><b>\ucf54\ub85c\ub09819 \ubd84\uc11d<\/b>\n<ol>\n<li>\ucf54\ub85c\ub09819 \ubd84\uc11d\n<ol>\n<li>\ucf54\ub85c\ub098 \uc774\uc804 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ucf54\ub85c\ub09819 \uc911 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\ucf54\ub85c\ub098 \uc774\ud6c4 \uc2dc\ub098\ub9ac\uc624<\/li>\n<\/ol>\n<\/li>\n<li>\ucf54\ub85c\ub09819\uc5d0 \ub530\ub978 \uac00\uaca9 \uc5ed\ud559<\/li>\n<li>\uc218\uc694-\uacf5\uae09 \uc2a4\ud399\ud2b8\ub7fc<\/li>\n<li>\ud32c\ub370\ubbf9 \uae30\uac04 \uc911 \uc2dc\uc7a5\uacfc \uad00\ub828\ub41c \uc815\ubd80 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uc81c\uc870\uc5c5\uccb4\uc758 \uc804\ub7b5\uc801 \uc774\ub2c8\uc154\ud2f0\ube0c<\/li>\n<li>\uacb0\ub860<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc9c8\ubcd1 \uc720\ud615\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li><b>MPS 1\ud615((\ud5d0\ub7ec \uc99d\ud6c4\uad70)* *<\/b>\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<\/ol>\n<\/li>\n<li>MPS 2\ud615(\ud5cc\ud130\uc99d\ud6c4\uad70)<\/li>\n<li>MPS 3\ud615(\uc0b0\ud544\ub9ac\ud3ec \uc99d\ud6c4\uad70)<\/li>\n<li>MPS 4\ud615(\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70)<\/li>\n<li>MPS 6\ud615(\ub9c8\ub85c\ud1a0-\ub77c\ubbf8 \uc99d\ud6c4\uad70)<\/li>\n<li>MPS 7\ud615(\uc2ac\ub77c\uc774 \uc99d\ud6c4\uad70)<\/li>\n<li>MPS 9\ud615(\ub098\ud1a0\ube44\uce20 \uc99d\ud6c4\uad70)<\/li>\n<\/ol>\n<\/li>\n<li><b>\uce58\ub8cc \uc720\ud615\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ud6a8\uc18c \ub300\uccb4 \uc694\ubc95 *\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<\/ol>\n<\/li>\n<li>\uc870\ud608 \uc904\uae30 \uc138\ud3ec \uc774\uc2dd (HSCT)<\/li>\n<li>\uc720\uc804\uc790 \uce58\ub8cc<\/li>\n<li>\uae30\ud0c0<\/li>\n<\/ol>\n<\/li>\n<li><b>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubcd1\uc6d0 *\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<\/ol>\n<\/li>\n<li><b>\uc778\ud4e8\uc804 \uc13c\ud130<\/b><\/li>\n<li><b>\uc678\ub798 \uc218\uc220 \uc13c\ud130<\/b><\/li>\n<\/ol>\n<\/li>\n<li><b>\uc9c0\uc5ed\ubcc4<\/b>\n<ol>\n<li>\uc18c\uac1c\n<ol>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \ub9e4\ub825\ub3c4 \uc9c0\uc218<\/li>\n<\/ol>\n<\/li>\n<li>\ubd81\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ubbf8\uad6d<\/li>\n<li>\uce90\ub098\ub2e4<\/li>\n<li>\uba55\uc2dc\ucf54<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc720\ub7fd\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ub3c5\uc77c<\/li>\n<li>\uc601\uad6d<\/li>\n<li>\ud504\ub791\uc2a4<\/li>\n<li>\uc774\ud0c8\ub9ac\uc544<\/li>\n<li>\uc2a4\ud398\uc778<\/li>\n<li>\uae30\ud0c0 \uc720\ub7fd<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\ub0a8\ubbf8\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\ube0c\ub77c\uc9c8<\/li>\n<li>\uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li>\ub098\uba38\uc9c0 \ub0a8\ubbf8<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<li>\uad6d\uac00 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)\n<ol>\n<li>\uc911\uad6d<\/li>\n<li>\uc778\ub3c4<\/li>\n<li>\uc77c\ubcf8<\/li>\n<li>\ud638\uc8fc<\/li>\n<li>\uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74\n<ol>\n<li>\uc18c\uac1c<\/li>\n<li>\uc8fc\uc694 \uc9c0\uc5ed\ubcc4 \uc5ed\ud559 \uad00\uacc4<\/li>\n<li>\uc9c8\ubcd1 \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d(%)<\/li>\n<li>\uce58\ub8cc \uc720\ud615\ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5\ub960 \ubd84\uc11d (%)<\/li>\n<li>\ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubcc4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubd84\uc11d \ubc0f \uc804\ub144 \ub300\ube44 \uc131\uc7a5 \ubd84\uc11d (%)<\/li>\n<\/ol>\n<\/li>\n<\/ol>\n<\/li>\n<li>\uacbd\uc7c1 \ud658\uacbd\n<ol>\n<li>\uacbd\uc7c1 \uc2dc\ub098\ub9ac\uc624<\/li>\n<li>\uc2dc\uc7a5 \ud3ec\uc9c0\uc154\ub2dd\/\uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li>\uc778\uc218\ud569\ubcd1 \ubd84\uc11d<\/li>\n<\/ol>\n<\/li>\n<li>\uae30\uc5c5 \ud504\ub85c\ud544<\/li>\n<\/ol>\n<p>&nbsp;<\/p>\n<p><img loading=\"lazy\" decoding=\"async\" class=\"alignnone size-full wp-image-5113\" src=\"https:\/\/www.mizuho.kr\/wp-content\/uploads\/2025\/02\/2-47.png\" alt=\"\" width=\"1371\" height=\"235\" \/><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\uae00\ub85c\ubc8c \uc810\uc561 \ub2e4\ub2f9\ub958\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc740 2023 \ub144\uc5d0 \ubbf8\ud654 YY \uc5b5 \ub2ec\ub7ec\uc5d0 \ub3c4\ub2ec\ud588\uc73c\uba70 2024-2031 \ub144 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \ubbf8\ud654 YY %\uc758 CAGR\ub85c \uc131\uc7a5\ud558\uc5ec 2031 \ub144\uae4c\uc9c0 \ubbf8\ud654 YY \ubc31\ub9cc \ub2ec\ub7ec\uc5d0\uc774\ub97c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\ubba4\ucf54\ub2e4\ub2f9\uc99d(MPS)\uc740 \ub2e4\ubc1c\uc131 \ubc0f \uc911\uc99d \uc99d\uc0c1\uc744 \ub3d9\ubc18\ud558\ub294 \ud76c\uadc0 \ub9ac\uc18c\uc880 \uc800\uc7a5 \uc9c8\ud658(LSD)\uc758 \ud55c \uadf8\ub8f9\uc785\ub2c8\ub2e4. MPS\ub294 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \ub2e4\uc591\ud55c \ud615\ud0dc\ub85c \ubc1c\uc0dd\ud558\uc9c0\ub9cc \ubc1c\ubcd1\ub960\uc740 \ub0ae\uc2b5\ub2c8\ub2e4. MPS\uc758 \uc720\ud589 \uc720\ud615\uc740 \ub300\ub959\ub9c8\ub2e4 \ub2e4\ub974\uba70, \uc774\ub294 \uc9c0\uc5ed \ubc0f \uc778\uc885\uc801 \ubc30\uacbd\uacfc \uad00\ub828\uc774 \uc788\uc744 \uc218 \uc788\uc74c\uc744 \ub098\ud0c0\ub0c5\ub2c8\ub2e4. \ud6a8\uc18c \uacb0\ud54d\uc73c\ub85c \uc778\ud55c \ubbf8\ubd84\ud574 \uae00\ub9ac\ucf54\uc0ac\ubbf8\ub178\uae00\ub9ac\uce78(GAG)\uc774 MPS\uc758 \uc8fc\uc694 \uc6d0\uc778\uc785\ub2c8\ub2e4. \uc784\uc0c1\uc801 \ud2b9\uc9d5\uc740 \uac70\uce5c \uc5bc\uad74 \ud2b9\uc9d5, \uc778\uc9c0 \uc9c0\uccb4, \uac04 \ube44\ub300, \ud0c8\uc7a5, \ud6c4\ub9cc\uc99d, \uac01\ub9c9 \ud63c\ud0c1 \ub4f1\uc744 \ud3ec\ud568\ud558\uc5ec \ud2b9\uc815 \ud6a8\uc18c \uacb0\ud54d\uc5d0 \ub530\ub77c \ub2e4\ub985\ub2c8\ub2e4.<br \/>\n\ubba4\ucf54\ub2e4\ub2f9\uc99d\uc740 \uad00\ub828 \ud6a8\uc18c \uacb0\ud54d\uc5d0 \uc758\ud574 \uc0dd\ud654\ud559\uc801\uc73c\ub85c \ubd84\ud654\ub418\uba70, MPS I\uc5d0\uc11c MPS IX\uae4c\uc9c0 7\uac00\uc9c0 \uc720\ud615\uc73c\ub85c \ubd84\ub958\ud560 \uc218 \uc788\uc73c\uba70(MPS V \ubc0f MPS VIII \uc81c\uc678), \uc77c\ubd80 \uc720\ud615\uc740 \ud558\uc704 \uc720\ud615\uc73c\ub85c \ub354 \ubd84\ub958\ub418\uae30\ub3c4 \ud569\ub2c8\ub2e4. \ucd1d 11\uac00\uc9c0 \uc720\ud615\uacfc \ud558\uc704 \uc720\ud615\uc73c\ub85c \ubd84\ub958\ub429\ub2c8\ub2e4. MPS\uc758 \uc784\uc0c1 \uc99d\uc0c1\uc740 \ud2b9\uc815 \ud6a8\uc18c \uacb0\ud54d\uc5d0 \ub530\ub77c \ub2e4\ub974\uc9c0\ub9cc \uc8fc\uc694 \uc784\uc0c1 \ud2b9\uc9d5\uc740 \uc2e0\uacbd\ud559\uc801 \uc99d\uc0c1, \uc548\uba74 \uae30\ud615, \uc2ec\uc7a5 \ubc0f \ud310\ub9c9 \uc9c8\ud658, \uace8\uaca9 \uae30\ub2a5 \uc7a5\uc560, \ud638\ud761\uae30 \ubb38\uc81c, \uc548\uad6c \uc7a5\uc560\uc785\ub2c8\ub2e4. <\/p>\n<p>\uc2dc\uc7a5 \uc5ed\ud559: \ub3d9\uc778 \ubc0f \uc81c\uc57d<br \/>\n\ub354 \ub098\uc740 \uce58\ub8cc \uacb0\uacfc\ub97c \uc704\ud55c \uaddc\uc81c \ub2f9\uad6d\uc758 \uc9c8\ubcd1 \uc2b9\uc778 \uc99d\uac00<br \/>\n\ub354 \ub098\uc740 \uce58\ub8cc \uacb0\uacfc\ub97c \uc704\ud574 \uaddc\uc81c \ub2f9\uad6d\uc758 \uc9c8\ubcd1 \uc2b9\uc778\uc744 \ub298\ub9ac\ub294 \uac83\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5\uc774 \uc131\uc7a5\ud558\ub294 \ub370 \ub3c4\uc6c0\uc774\ub418\ub294 \uc911\uc694\ud55c \uc694\uc18c \uc911 \ud558\ub098\uc785\ub2c8\ub2e4. \uc2dc\uc7a5\uc5d0\uc11c \ud65c\ub3d9\ud558\ub294 \uc8fc\uc694 \uc5c5\uccb4\ub4e4\uc740 \uace0\uae09 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc2b9\uc778\uc744 \uc5bb\ub294 \ub370 \uc8fc\ub825\ud558\uace0 \uc788\uc73c\uba70, \uc774\ub294 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc8fc\ub3c4 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uc608\ub97c \ub4e4\uc5b4, 2022 \ub144 8 \uc6d4 Regenxbio Inc.\ub294 \ud5cc\ud130 \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4 \ubba4\ucf54 \ub2e4\ub2f9\ub958 \uc99d II \ud615 (MPS II) \uce58\ub8cc\ub97c \uc704\ud574 FDA\uc758 \uac00\uc18d \uc2b9\uc778 \uacbd\ub85c\ub97c \uc0ac\uc6a9\ud558\uc5ec 2024 \ub144\uc5d0 \uc0dd\ubb3c \uc81c\uc81c \ud5c8\uac00 \uc2e0\uccad (BLA)\uc744 \uc81c\ucd9c\ud560 \uc758\uc0ac\ub97c \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4 (\ud5cc\ud130 \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4 RGX-121\uc5d0 \ub300\ud55c \uc2b9\uc778 \uacbd\ub85c). \ub610\ud55c \ud68c\uc0ac\ub294 RGX-121\uc5d0 \ub300\ud55c \uc911\ucd94\uc801\uc778 \ud504\ub85c\uadf8\ub7a8\uc774 \ud65c\uc131\ud654\ub418\uc5b4 \ud658\uc790\ub97c \ub4f1\ub85d\ud558\uace0 \uc788\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. RGX-121\uc740 \uc774\ub450\ub85c \ub124\uc774\ud2b8 -2- \uc124\ud30c \ud0c0\uc81c (I2S) \ud6a8\uc18c\ub97c \uc554\ud638\ud654\ud558\ub294 \uc720\uc804\uc790\ub97c \uc804\ub2ec\ud558\uae30 \uc704\ud574 NAV AAV9 \ubca1\ud130\ub97c \uc0ac\uc6a9\ud558\ub294 \uc5f0\uad6c\uc6a9 \uc77c\ud68c\uc131 AAV \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4.<br \/>\n\ub610\ud55c, 2021\ub144 6\uc6d4\uc5d0\ub294 \uae00\ub85c\ubc8c \uc0dd\uba85\uacf5\ud559 \uae30\uc5c5 \ubc14\uc774\uc624\ub9c8\ub9b0 \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4 \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4\uac00 \uc720\uc804\uc801 \uc6d0\uc778\uc5d0 \uc758\ud55c \ud76c\uadc0\uc9c8\ud658\uc744 \uc704\ud55c \ud601\uc2e0\uc801\uc778 \ubc14\uc774\uc624\uc758\uc57d\ud488 \uac1c\ubc1c \ubc0f \uc0c1\uc6a9\ud654\ub97c \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. \uc774 \ud68c\uc0ac\ub294 \ubaa8\ud0a4\uc624 A \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4 \ubba4\ucf54\ub2e4\ub2f9\uc99d IVA(MPS IVA) \ud658\uc790 \uce58\ub8cc\ub97c \uc704\ud574 \ubbf8\uad6d \uad6d\ub9bd\uc758\ub8cc\uc9c8\ubcd1\uad00\ub9ac\uad6d(NMPA)\uc73c\ub85c\ubd80\ud130 \ube44\ubbf8\uc9d0(\uc5d8\ub85c\uc124\ud30c\uc81c \uc54c\ud30c)\uc758 \uc2b9\uc778\uc744 \ubc1b\uc558\uc2b5\ub2c8\ub2e4. \ube44\ubbf8\uc9d0\uc740 \uc911\uad6d\uc5d0\uc11c \uc774 \uc9c8\ud658\uc5d0 \ub300\ud574 \uc2b9\uc778\ub41c \ucd5c\ucd08\uc758 \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4.<br \/>\n\ub610\ud55c \uc2dc\uc7a5\uc740 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc758 \ubc1c\uc804, \uc778\uc2dd \uc99d\uac00 \ubc0f \uc870\uae30 \uc9c4\ub2e8, \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95 \ub4f1\uc7a5, \uc8fc\uc694 \uc5c5\uccb4\uc758 \uc0c8\ub85c\uc6b4 \uc804\ub7b5 \ucc44\ud0dd \ub4f1\uacfc \uac19\uc740 \ub2e4\uc591\ud55c \uc694\uc778\uc5d0 \uc758\ud574 \uc8fc\ub3c4\ub418\uba70 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5\uc744 \ub354\uc6b1 \uc8fc\ub3c4 \ud560 \uac83\uc785\ub2c8\ub2e4.<br \/>\n\uc81c\uc57d<br \/>\n\uc9c4\ub2e8 \ubd88\ub7c9\uacfc \uacb0\ud569 \ub41c \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uae00\ub85c\ubc8c \uc810\uc561 \ub2e4\ub2f9\ub958 \uc99d (MPS) \uce58\ub8cc \uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \ubc29\ud574 \ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ube44\ubbf8\uc9c4(\uc5d8\ub85c\uc124\ud30c\uc81c-\uc54c\ud30c)\uc740 MPS IV(\ubaa8\ud0a4\uc624 \uc99d\ud6c4\uad70) \uce58\ub8cc\uc81c\uc785\ub2c8\ub2e4. \uc774 \uce58\ub8cc\uc81c\ub294 \uc5f0\uac04 38\ub9cc \ub2ec\ub7ec\uc758 \ube44\uc6a9\uc73c\ub85c \uc2dc\uc7a5\uc5d0 \ucd9c\uc2dc\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \uc778\ub3c4\uc640 \uac19\uc740 \uc2e0\ud765 \uacbd\uc81c\uad6d\uc758 \ud658\uc790\ub4e4\uc740 \ub192\uc740 \uac00\uaca9 \ub54c\ubb38\uc5d0 \uc774 \uce58\ub8cc\uc81c\ub97c \uac10\ub2f9\ud560 \uc218 \uc5c6\uc2b5\ub2c8\ub2e4. \ub610\ud55c \uc9c8\ubcd1\uc5d0 \ub300\ud55c \uc778\uc2dd \ubd80\uc871, \uc9c8\ubcd1\uacfc \uad00\ub828\ub41c \ud569\ubcd1\uc99d, \uaddc\uc81c \ubb38\uc81c \ub4f1\ub3c4 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc2dc\uc7a5 \uc131\uc7a5\ub960\uc744 \uc800\ud574\ud569\ub2c8\ub2e4.<br \/>\n\uc2dc\uc7a5 \uc138\ubd84 \ubd84\uc11d<br \/>\n\uae00\ub85c\ubc8c \uc810\uc561 \ub2e4\ub2f9\ub958\uc99d \uce58\ub8cc\ub294 \uc9c8\ubcd1 \uc720\ud615, \uce58\ub8cc \uc720\ud615, \ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubc0f \uc9c0\uc5ed\uc5d0 \ub530\ub77c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4.<br \/>\n\uce58\ub8cc \uc720\ud615 \ubd80\ubb38\uc758 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc740 \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 \uc57d 42.2 %\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n\uce58\ub8cc \uc720\ud615 \ubd80\ubb38\uc758 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc740 \uc57d 42.2 %\ub97c \ucc28\uc9c0\ud588\uc73c\uba70 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc9c0\ubc30\uc801 \uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc774\ub780 \uc815\uc81c\ub41c \uc778\uac04, \ub3d9\ubb3c \ub610\ub294 \uc7ac\uc870\ud569 \ud6a8\uc18c \uc81c\uc81c\ub97c \uc0ac\uc6a9\ud558\uc5ec \uc120\ucc9c\uc131 \ud6a8\uc18c \uacb0\ud54d\uc744 \uce58\ub8cc\ud558\ub294 \uac83\uc744 \ub9d0\ud569\ub2c8\ub2e4.<br \/>\n\ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT)\uc740 \uc2e4\ud604 \uac00\ub2a5\uc131\uacfc \uc548\uc804\uc131\uc73c\ub85c \uc989\uc2dc \uce58\ub8cc\ub97c \uc2dc\uc791\ud558\uace0 \uc608\ud6c4\ub97c \uac1c\uc120\ud560 \uc218 \uc788\uae30 \ub54c\ubb38\uc5d0 \uc77c\ubd80 \uc720\ud615\uc758 MPS\uc5d0 \ub300\ud55c \ud45c\uc900 \uce58\ub8cc \uc635\uc158\uc73c\ub85c \uc0ac\uc6a9\ub418\uc5b4 \uc654\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2021\ub144 11\uc6d4 GC\ub179\uc2ed\uc790\ub294 \uc138\uacc4 \ucd5c\ucd08\ub85c ICV \uc8fc\uc0ac\ub85c \ud22c\uc5ec\ud558\ub294 \ubba4\ucf54\ub2e4\ub2f9\uc99d 2\ud615 \ud6a8\uc18c \ub300\uccb4 \uce58\ub8cc\uc81c\uc778 \ud5cc\ud130\ub77c\uc81c ICV\uc5d0 \ub300\ud574 EMA\uac00 \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815\uc744 \ubd80\uc5ec\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n\ub610\ud55c 2021\ub144 1\uc6d4, \ud55c\uad6d\uc758 \ubc14\uc774\uc624 \uc81c\uc57d\ud68c\uc0ac\uc778 GC\ub179\uc2ed\uc790\uc640 \ub3c4\ucfc4\uc5d0 \ubcf8\uc0ac\ub97c \ub454 \ud074\ub9ac\ub2c8\uc820 K.K.(\uc774\ud558 &#8216;\ud074\ub9ac\ub2c8\uc820&#8217;)\ub294 \ubba4\ucf54\ub2e4\ub2f9\uc99d II\ud615(\ud5cc\ud130\uc99d\ud6c4\uad70) \uce58\ub8cc\uc81c\ub85c\uc11c \ud5cc\ud130\ub77c\uc81c ICV(\ub1cc\uc2e4 \ub0b4) \uc8fc\uc0ac 15mg(\uc77c\ubc18\uba85: idursulfase-beta(\uc7ac\uc870\ud569))\uc758 \uc77c\ubcf8 \uc81c\uc870 \ubc0f \ud310\ub9e4 \uc2b9\uc778\uc744 \ud68d\ub4dd\ud588\uc2b5\ub2c8\ub2e4. \uc815\ub9e5 \uc8fc\uc0ac\uc6a9 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc81c\ub294 \uc774\ubbf8 \uc77c\ubcf8 \ubc0f \uae30\ud0c0 \uad6d\uac00\uc5d0\uc11c \ubba4\ucf54\ub2e4\ub2f9\uc99d I\ud615\uc758 \uc804\uc2e0 \uc99d\uc0c1\uc5d0 \ub300\ud55c \uce58\ub8cc\uc81c\ub85c \uc0ac\uc6a9\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n\uc2dc\uc7a5 \uc9c0\ub9ac\uc801 \uc810\uc720\uc728<br \/>\n\ubd81\ubbf8\ub294 2022 \ub144 \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 \uc57d 38.4 %\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n\ubd81\ubbf8\ub294 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc804\uccb4 \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 \uc57d 38.4 %\ub97c \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc774\ub294 \uace0\uae09 \uce58\ub8cc \uc635\uc158\uc5d0 \ub300\ud55c \ud658\uc790 \uc778\uad6c\uc758 \ub192\uc740 \uc778\uc2dd, FDA \uc2b9\uc778, \uc9c4\ub2e8 \uc815\uad50\uc131 \uc99d\uac00, \uc911\uc694\ud55c \uc784\uc0c1 \uc2dc\ud5d8\uc758 \uc874\uc7ac, \uc8fc\uc694 \uc784\uc0c1 \ub2e8\uacc4 \ubc14\uc774\uc624 \uc81c\uc57d \ud68c\uc0ac\uc758 \uc874\uc7ac\uc640 \uacb0\ud569 \ub41c \uc694\uc778\uc73c\ub85c \uc778\ud574 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc5d0\uc11c\uc774 \uc9c0\uc5ed\uc5d0\uc11c \uac00\uc7a5 \ub192\uc740 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n\uc608\ub97c \ub4e4\uc5b4, 2023\ub144 6\uc6d4 \ub370\ub0a0\ub9ac \ud14c\ub77c\ud4e8\ud2f1\uc2a4\ub294 \ucd5c\uadfc MPS II(\ud5cc\ud130 \uc99d\ud6c4\uad70) \uc18c\uc544\ub97c \ub300\uc0c1\uc73c\ub85c \uc9c4\ud589 \uc911\uc778 DNL310\uc758 \uc624\ud508 \ub77c\ubca8, \ub2e8\uc77c\uad70 1\/2\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc758 \uc0c8\ub85c\uc6b4 \uc911\uac04 \ub370\uc774\ud130\ub97c \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. DNL310\uc740 \uc5f0\uad6c\uc6a9 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc73c\ub85c, BBB\ub97c \ud1b5\uacfc\ud558\uc5ec MPS II\uc758 \ud589\ub3d9, \uc778\uc9c0 \ubc0f \uc2e0\uccb4 \uc99d\uc0c1\uc744 \ud574\uacb0\ud558\uae30 \uc704\ud574 \uace0\uc548\ub418\uc5c8\uc2b5\ub2c8\ub2e4.<br \/>\n\ub610\ud55c 2023\ub144 1\uc6d4, \uae00\ub85c\ubc8c \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc120\ub3c4\uae30\uc5c5\uc778 \uc624\ucc28\ub4dc \ud14c\ub77c\ud4e8\ud2f1\uc2a4(Orchard Therapeutics)\ub294 \ubbf8\uad6d \uc2dd\ud488\uc758\uc57d\uad6d(FDA)\uc774 \ud5d0\ub7ec \uc544\ud615 \ubba4\ucf54\ub2e4\ub2f9\uc99d 1\ud615(MPS-IH) \uce58\ub8cc\ub97c \uc704\ud574 \uac1c\ubc1c \uc911\uc778 \uc870\ud608 \uc904\uae30\uc138\ud3ec(HSC) \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc778 OTL-203\uc5d0 \ub300\ud55c \uc784\uc0c1\uc2dc\ud5d8\uc2e0\uc57d(IND) \uc2e0\uccad\uc744 \uc2b9\uc778\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. \uc774 \ud68c\uc0ac\ub294 2023\ub144 \ud558\ubc18\uae30\uc5d0 \ud45c\uc900 \uce58\ub8cc\uc640 \ube44\uad50\ud558\uc5ec OTL-203\uc758 \ud6a8\ub2a5\uacfc \uc548\uc804\uc131\uc744 \ud3c9\uac00\ud558\ub294 \uae00\ub85c\ubc8c \ub4f1\ub85d \uc784\uc0c1\uc2dc\ud5d8\uc744 \uac1c\uc2dc\ud560 \uc608\uc815\uc785\ub2c8\ub2e4.<br \/>\n\ucf54\ub85c\ub09819 \uc601\ud5a5 \ubd84\uc11d<br \/>\n\ucf54\ub85c\ub09819 \ud32c\ub370\ubbf9\uc740 \ubba4\ucf54\ub2e4\ub2f9\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \ud070 \uc601\ud5a5\uc744 \ubbf8\uccd0 \uc5f0\uad6c \ubc0f \uc784\uc0c1\uc2dc\ud5d8\uc774 \uc9c0\uc5f0\ub418\uace0 \uc758\ub8cc \uc11c\ube44\uc2a4 \uc811\uadfc\uc131, \uacf5\uae09\ub9dd \uc911\ub2e8, \uacbd\uc81c\uc801 \uc5b4\ub824\uc6c0\uc5d0 \uc601\ud5a5\uc744 \ubbf8\ucce4\uc2b5\ub2c8\ub2e4. \uc548\uc804\uc131 \uc6b0\ub824\uc640 \uc81c\ud55c\uc73c\ub85c \uc778\ud574 \ubba4\ucf54\ub2e4\ub2f9\uc99d \uce58\ub8cc\uc81c\uc758 \uac1c\ubc1c\uacfc \uc2b9\uc778\uc774 \uc9c0\uc5f0\ub420 \uac00\ub2a5\uc131\uc774 \uc788\uc2b5\ub2c8\ub2e4. \ud32c\ub370\ubbf9\uc740 \uc758\ub8cc\ube44 \uc9c0\ucd9c\uacfc \ubcf4\ud5d8 \uc801\uc6a9 \ubc94\uc704\uc5d0\ub3c4 \uc601\ud5a5\uc744 \ubbf8\ucce4\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uac1c\ubc1c<br \/>\n2023\ub144 9\uc6d4 JCR \uc81c\uc57d\uc740 \ubba4\ucf54\ub2e4\ub2f9\uc99d 1\ud615(MPS 1\ud615, \ud5d0\ub7ec, \ud5d0\ub7ec-\uc0e4\uc774 \ubc0f \uc0e4\uc774 \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4) \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud55c JR-171\uc758 \uae00\ub85c\ubc8c 1\uc0c1\/2\uc0c1 \uc5f0\uad6c\uc758 52\uc8fc \uc911\uac04 \ub370\uc774\ud130\uc758 \uc8fc\uc694 \uacb0\uacfc\ub97c \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. JR-171\uc740 \ud608\uc561\ub1cc\uc7a5\ubcbd(\u201cBBB\u201d)\uc744 \ud22c\uacfc\ud558\ub294 \ud615\ud0dc\uc758 \uc7ac\uc870\ud569 \u03b1-L- \uc774\ub450\ub85c\ub2c8\ub2e4\uc81c\uc774\uba70, JCR\uc758 \ub3c5\uc810\uc801\uc778 J-Brain Cargo \uae30\uc220\uc744 \uc0ac\uc6a9\ud558\uc5ec \uac1c\ubc1c\ub418\uc5c8\uc2b5\ub2c8\ub2e4.<br \/>\n2021\ub144 3\uc6d4, JCR \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4\ub294 \uc77c\ubcf8 \ud6c4\uc0dd\ub178\ub3d9\uc131(MHLW)\uc73c\ub85c\ubd80\ud130 \uc810\uc561\ub2e4\ub2f9\uc99d II\ud615(MPS II, \ub610\ub294 \ud5cc\ud130\uc99d\ud6c4\uad70) \uce58\ub8cc\uc81c\ub85c &#8216;\uc544\uc774\uc988\uce74\ub974\uace0'(\ud30c\ube44\ub098\ud504\uc2a4 \uc54c\ud30c 10mL, \uc815\ub9e5 \uc810\uc801 \uc8fc\uc785\uc81c)\ub97c \uc2b9\uc778\ubc1b\uc558\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n2020\ub144 9\uc6d4, \ub3c5\uc790\uc801\uc778 NAV \uae30\uc220 \ud50c\ub7ab\ud3fc\uc744 \uae30\ubc18\uc73c\ub85c \uc720\uc804\uc790 \uce58\ub8cc\uc758 \uce58\ub8cc \uc7a0\uc7ac\ub825\uc744 \ud1b5\ud574 \uc0b6\uc744 \uac1c\uc120\ud558\uace0\uc790 \ud558\ub294 \uc120\ub3c4\uc801\uc778 \uc784\uc0c1 \ub2e8\uacc4 \uc0dd\uba85\uacf5\ud559 \uae30\uc5c5\uc778 \ub9ac\uc820\uc2a4\ubc14\uc774\uc624(REGENXBIO Inc.)\ub294 \ud5cc\ud130 \uc99d\ud6c4\uad70\uc73c\ub85c\ub3c4 \uc54c\ub824\uc9c4 \ubba4\ucf54\ub2e4\ub2f9\uc99d II\ud615(MPS II) \uce58\ub8cc\ub97c \uc704\ud55c RGX-121 \ud504\ub85c\uadf8\ub7a8\uc744 \ud655\uc7a5\ud558\uc5ec \uc9c8\ubcd1\uc758 \uc2e0\uacbd \ud1f4\ud589\uc131 \uc99d\uc0c1\uc5d0 \ub300\ud55c \ucd94\uac00\uc801\uc778 \ud1b5\ucc30\ub825\uc744 \uc5bb\uace0 \ub354 \uad11\ubc94\uc704\ud55c \ud658\uc790 \uc9d1\ub2e8\uc5d0\uc11c RGX-121\uc744 \ud3c9\uac00\ud55c\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n\ubcf4\uace0\uc11c\ub97c \uad6c\ub9e4\ud558\ub294 \uc774\uc720\ub294?<br \/>\n\uc9c8\ubcd1 \uc720\ud615, \uce58\ub8cc \uc720\ud615, \ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubc0f \uc9c0\uc5ed\uc744 \uae30\ubc18\uc73c\ub85c \uae00\ub85c\ubc8c \ubba4\ucf54\ub2e4\ub2f9\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc138\ubd84\ud654\ub97c \uc2dc\uac01\ud654\ud558\uace0 \uc8fc\uc694 \uc0c1\uc5c5 \uc790\uc0b0 \ubc0f \ud50c\ub808\uc774\uc5b4\ub97c \uc774\ud574\ud569\ub2c8\ub2e4.<br \/>\n\ud2b8\ub80c\ub4dc \ubd84\uc11d \ubc0f \uacf5\ub3d9 \uac1c\ubc1c\uc744 \ud1b5\ud55c \uc0c1\uc5c5\uc801 \uae30\ud68c \ud30c\uc545<br \/>\n\ubaa8\ub4e0 \uc138\uadf8\uba3c\ud2b8\uc5d0 \ub300\ud55c \uc218\ub9ce\uc740 \uc810\uc561 \ub2e4\ub2f9\ub958\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uc218\uc900\uc758 \ub370\uc774\ud130 \ud3ec\uc778\ud2b8\uac00 \ud3ec\ud568\ub41c Excel \ub370\uc774\ud130 \uc2dc\ud2b8.<br \/>\nPDF \ubcf4\uace0\uc11c\ub294 \ucca0\uc800\ud55c \uc815\uc131\uc801 \uc778\ud130\ubdf0\uc640 \uc2ec\uce35 \uc5f0\uad6c\ub97c \uac70\uce5c \uc885\ud569\uc801\uc778 \ubd84\uc11d\uc73c\ub85c \uad6c\uc131\ub418\uc5b4 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n\ubaa8\ub4e0 \uc8fc\uc694 \uc5c5\uccb4\uc758 \uc8fc\uc694 \uc9c8\ubcd1\uc73c\ub85c \uad6c\uc131\ub41c \uc5d1\uc140\ub85c \uc81c\uacf5\ub418\ub294 \uc9c8\ubcd1 \ub9e4\ud551.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[5],"tags":[],"class_list":["post-19392","post","type-post","status-publish","format-standard","hentry","category-industry-research-report"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/19392"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=19392"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/19392\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=19392"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=19392"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=19392"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}