{"id":28203,"date":"2026-02-07T10:21:00","date_gmt":"2026-02-07T10:21:00","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/alpha-mannosidosis-market-mordor\/"},"modified":"2026-09-18T05:21:09","modified_gmt":"2026-09-17T20:21:09","slug":"alpha-mannosidosis-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/alpha-mannosidosis-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \uc54c\ud30c \ub9cc\ub178\uc2dc\ub3c4\uc2dc\uc2a4 \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d \u2013 \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2025 &#8211; 2030)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/alpha-mannosidosis-market-1753555075527-major-players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/alpha-mannosidosis-market-size-image-1753472263894.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 Lamzede (Velmanase Alfa) ERT\uc758 \uc2b9\uc778 \ud6c4 \ucc44\ud0dd \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 \ub9ac\uc18c\uc880 \ucd95\uc801 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac \uc2dc\ubc94 \uc0ac\uc5c5 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.3 \ub3d9\uc815\uc801 \uc0ac\uc6a9 \ubc0f \uc870\uae30 \uc811\uadfc \ud504\ub85c\uadf8\ub7a8 \ud655\ub300<\/li>\n<li class=\"toc-level-3\">4.2.4 \uc720\uc804\uc790 \uce58\ub8cc \ud30c\uc774\ud504\ub77c\uc778 \ud601\uc2e0 (AAV \ubc0f LNP \ud50c\ub7ab\ud3fc)<\/li>\n<li class=\"toc-level-3\">4.2.5 EU \ub0b4 \ub2e4\uad6d\uac00 \ud76c\uadc0\uc758\uc57d\ud488 \uc0c1\ud658 \uc870\ud654<\/li>\n<li class=\"toc-level-3\">4.2.6 AI \uae30\ubc18 \ucd08\ud76c\uadc0 \uc9c8\ud658 \ud658\uc790 \ubc1c\uad74 \uc54c\uace0\ub9ac\uc998<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ub192\uc740 \uc5f0\uac04 \uce58\ub8cc \ube44\uc6a9 \ubc0f \uac00\uaca9 \uc800\ud56d<\/li>\n<li class=\"toc-level-3\">4.3.2 \ud604\uc7ac ERT\uc758 \ud608\ub1cc\uc7a5\ubcbd \uce68\ud22c \uc81c\ud55c<\/li>\n<li class=\"toc-level-3\">4.3.3 \ubd80\uc871\ud55c \uc7a5\uae30 \uc2e4\uc81c \uc548\uc804\uc131 \ub370\uc774\ud130<\/li>\n<li class=\"toc-level-3\">4.3.4 \uace8\uc218 \uae30\uc99d\uc790 \uc77c\uce58 \uacbd\uc7c1\uc73c\ub85c \uc778\ud55c HSCT \ucc44\ud0dd \uc81c\ud55c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \uacf5\uae09\ub9dd \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">4.5 \uaddc\uc81c \ud658\uacbd<\/li>\n<li class=\"toc-level-2\">4.6 \uae30\uc220 \uc804\ub9dd<\/li>\n<li class=\"toc-level-2\">4.7 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.7.1 \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.7.2 \uad6c\ub9e4\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.7.3 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.7.4 \ub300\uccb4\uc7ac\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.7.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc608\uce21 (\uac00\uce58, USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uce58\ub8cc \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc870\ud608\ubaa8\uc138\ud3ec \uc774\uc2dd<\/li>\n<li class=\"toc-level-3\">5.1.3 \uc720\uc804\uc790 \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.1.4 \ubcf4\uc870 \ubc0f \ubcf4\uc644 \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.1.5 \uc784\uc0c1 \uc5f0\uad6c \uc911\uc778 \uc57d\ub9ac\ud559\uc801 \uc0e4\ud398\ub860<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \ud22c\uc5ec \uacbd\ub85c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc815\ub9e5 \uc8fc\uc785<\/li>\n<li class=\"toc-level-3\">5.2.2 \uc678\uacfc\uc801 \uc774\uc2dd \ud22c\uc5ec<\/li>\n<li class=\"toc-level-3\">5.2.3 \uc218\ub9c9\uac15\ub0b4 \/ \uc911\ucd94\uc2e0\uacbd\uacc4 \uc9c1\uc811 \uc804\ub2ec<\/li>\n<li class=\"toc-level-3\">5.2.4 \uc804\uc2e0 \ubc14\uc774\ub7ec\uc2a4 \ubca1\ud130 \uc804\ub2ec<\/li>\n<li class=\"toc-level-3\">5.2.5 \uae30\ud0c0 \uacbd\ub85c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.3.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.3.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.3.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.3.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.3.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.3.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.3.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.3.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.3.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.3.2.6 \uc720\ub7fd \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.3.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.3.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.3.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.3.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.3.3.4 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.3.3.5 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.3.3.6 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.3.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.3.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.3.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.3.4.3 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.3.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.3.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.3.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.3.5.3 \ub0a8\ubbf8 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uac1c\uc694, \uc2dc\uc7a5 \uac1c\uc694, \ud575\uc2ec \ubd80\ubb38, \uac00\uc6a9 \uc7ac\ubb34 \uc815\ubcf4, \uc804\ub7b5 \uc815\ubcf4, \uc8fc\uc694 \uae30\uc5c5 \uc2dc\uc7a5 \uc21c\uc704\/\uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 Chiesi Farmaceutici S.p.A.<\/li>\n<li class=\"toc-level-3\">6.3.2 Sobi (Swedish Orphan Biovitrum)<\/li>\n<li class=\"toc-level-3\">6.3.3 Orchard Therapeutics plc<\/li>\n<li class=\"toc-level-3\">6.3.4 Avrobio Inc.<\/li>\n<li class=\"toc-level-3\">6.3.5 Ultragenyx Pharmaceutical Inc.<\/li>\n<li class=\"toc-level-3\">6.3.6 Regenxbio Inc.<\/li>\n<li class=\"toc-level-3\">6.3.7 Rocket Pharmaceuticals Inc.<\/li>\n<li class=\"toc-level-3\">6.3.8 M6P Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.9 SmartPharm Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.10 CSL Behring LLC<\/li>\n<li class=\"toc-level-3\">6.3.11 Takeda Pharmaceutical Company Ltd.<\/li>\n<li class=\"toc-level-3\">6.3.12 JCR Pharmaceuticals Co., Ltd.<\/li>\n<li class=\"toc-level-3\">6.3.13 Leadiant Biosciences Inc.<\/li>\n<li class=\"toc-level-3\">6.3.14 ArmaGen Inc.<\/li>\n<li class=\"toc-level-3\">6.3.15 Sangamo Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.16 Astellas Gene Therapies<\/li>\n<li class=\"toc-level-3\">6.3.17 Bluebird Bio Inc.<\/li>\n<li class=\"toc-level-3\">6.3.18 Genethon<\/li>\n<li class=\"toc-level-3\">6.3.19 Passage Bio<\/li>\n<li class=\"toc-level-3\">6.3.20 Denali Therapeutics<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\uc54c\ud30c \ub9cc\ub178\uc2dc\ub3c4\uc2dc\uc2a4(Alpha-Mannosidosis) \uc2dc\uc7a5\uc740 2025\ub144 4\uc5b5 3,310\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\uc5d0\uc11c 2030\ub144 9\uc5b5 3,850\ub9cc \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub418\uba70, \uc608\uce21 \uae30\uac04(2025-2030) \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 16.40%\uc758 \ub192\uc740 \uc131\uc7a5\uc138\ub97c \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ub450 \uc790\ub9bf\uc218 \uc131\uc7a5\uc740 \ubca8\ub9c8\ub098\uc81c \uc54c\ud30c(velmanase alfa)\uc758 \uc2dc\ud310 \ud6c4 \uc218\uc694 \uc99d\uac00, \uc720\uc804\uc790 \uce58\ub8cc\uc81c \ud30c\uc774\ud504\ub77c\uc778\uc758 \ubc1c\uc804, \uadf8\ub9ac\uace0 \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac \ud504\ub85c\uadf8\ub7a8\uc758 \ud655\ub300\uc5d0 \ud798\uc785\uc740 \ubc14\uac00 \ud07d\ub2c8\ub2e4. \uc9c4\ub2e8 \ub178\ub825\uc758 \uac15\ud654\ub294 \uc99d\uc0c1 \ubc1c\ud604 \ud6c4 \uc9c4\ub2e8\uc5d0\uc11c \uc99d\uc0c1 \uc804 \ub2e8\uacc4 \uc9c4\ub2e8\uc73c\ub85c \uc804\ud658\uc744 \uc720\ub3c4\ud558\uc5ec, \ud604\uc7ac \uc57d 5,000\uba85\uc73c\ub85c \uc9c4\ub2e8\ub41c \ud658\uc790 \ud480\uc744 \ub354\uc6b1 \ub113\ud788\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub2e8\uc77c \uce58\ub8cc \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uac00 \ud604\uc7ac \uc218\uc775\uc744 \uc9c0\ubc30\ud558\ub294 \ub9cc\uc131 \uc8fc\uc785 \ubaa8\ub378\uc744 \uc704\ud611\ud558\uba74\uc11c \uacbd\uc7c1 \uac15\ub3c4\uac00 \uc2ec\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc720\ub7fd\uc740 \uc870\uae30 \uc0c1\ud658\uc744 \ud1b5\ud574 \uc120\uc810 \ud6a8\uacfc\ub97c \uc720\uc9c0\ud558\uace0 \uc788\uc73c\ub098, 2024\ub144 FDA\uc758 Lamzede \uc2b9\uc778 \uc774\ud6c4 \ubd81\ubbf8\uac00 \uc804\ubc18\uc801\uc778 \uc131\uc7a5\uc744 \uc8fc\ub3c4\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \uc9c0\uc18d\uc801\uc73c\ub85c \ub192\uc740 \uc5f0\uac04 \uce58\ub8cc \ube44\uc6a9\uc740 \uac00\uaca9\uc5d0 \ubbfc\uac10\ud55c \uc9c0\uc5ed\uc5d0\uc11c\uc758 \ub2e8\uae30\uc801\uc778 \uc2dc\uc7a5 \uce68\ud22c\ub97c \uc81c\ud55c\ud558\uba70, \uc81c\uc870\uc5c5\uccb4\ub4e4\uc740 \uac00\uce58 \uae30\ubc18 \uacc4\uc57d \ubc0f \ud658\uc790 \uc9c0\uc6d0 \uae30\uae08 \ub9c8\ub828\uc744 \ubaa8\uc0c9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ub178\ub825\uc740 \ud2b9\ud788 \uac00\uaca9 \ubbfc\uac10\ub3c4\uac00 \ub192\uc740 \uc2e0\ud765 \uc2dc\uc7a5\uc5d0\uc11c \uc2dc\uc7a5 \uce68\ud22c\uc728\uc744 \ub192\uc774\ub294 \ub370 \uc911\uc694\ud55c \uc5ed\ud560\uc744 \ud560 \uac83\uc73c\ub85c \ubcf4\uc785\ub2c8\ub2e4. \ub610\ud55c, \ud76c\uadc0 \uc9c8\ud658 \uce58\ub8cc\uc81c \uac1c\ubc1c\uc5d0 \ub300\ud55c \uc815\ubd80 \uc9c0\uc6d0 \ubc0f \uc778\uc2dd \uc99d\uac00\ub294 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ub354\uc6b1 \uac00\uc18d\ud654\ud560 \uc7a0\uc7ac\ub825\uc744 \uac00\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ubcf5\uc7a1\ud55c \uaddc\uc81c \ud658\uacbd\uacfc \uc784\uc0c1 \uc2dc\ud5d8\uc758 \uc5b4\ub824\uc6c0\uc740 \uc5ec\uc804\ud788 \uc2dc\uc7a5 \uc9c4\uc785\uc758 \uc8fc\uc694 \uc7a5\ubcbd\uc73c\ub85c \uc791\uc6a9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud5a5\ud6c4 \uc2dc\uc7a5\uc740 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc\ubc95\uc758 \ub4f1\uc7a5\uacfc \uc9c4\ub2e8 \uae30\uc220\uc758 \ubc1c\uc804\uc774 \ub9de\ubb3c\ub824 \ub354\uc6b1 \uc5ed\ub3d9\uc801\uc778 \ubcc0\ud654\ub97c \uacaa\uc744 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \uae00\ub85c\ubc8c \uc54c\ud30c \ub9cc\ub178\uc2dc\ub3c4\uc2dc\uc2a4(Alpha Mannosidosis) \uc2dc\uc7a5\uc5d0 \ub300\ud55c \uc2ec\uce35 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \uc774 \ud76c\uadc0 \uc9c8\ud658\uc740 \uc804 \uc138\uacc4\uc801\uc73c\ub85c 50\ub9cc~100\ub9cc \uba85\uc758 \uc2e0\uc0dd\uc544 \uc911 1\uba85\uaf34\ub85c \ubc1c\uc0dd\ud558\uba70, \ud604\uc7ac \uc9c4\ub2e8\ub41c \ud658\uc790 \uc218\ub294 5,000\uba85 \ubbf8\ub9cc\uc785\ub2c8\ub2e4. \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2025\ub144 4\uc5b5 3,300\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2030\ub144 9\uc5b5 3,800\ub9cc \ub2ec\ub7ec\ub85c \uc5f0\ud3c9\uade0 16.4%\uc758 \ub192\uc740 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \uc694\uc778\uc73c\ub85c\ub294 Lamzede(Velmanase Alfa) \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT)\uc758 \uc2b9\uc778 \ud6c4 \ucc44\ud0dd \uc99d\uac00, \ub9ac\uc18c\uc880 \ucd95\uc801 \uc9c8\ud658(LSD)\uc5d0 \ub300\ud55c \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac \ud30c\uc77c\ub7ff \ud504\ub85c\uadf8\ub7a8 \ud655\ub300, \ub3d9\uc815\uc801 \uc0ac\uc6a9 \ubc0f \uc870\uae30 \uc811\uadfc \ud504\ub85c\uadf8\ub7a8\uc758 \ud655\uc7a5, AAV \ubc0f LNP \ud50c\ub7ab\ud3fc \uae30\ubc18 \uc720\uc804\uc790 \uce58\ub8cc\uc81c \ud30c\uc774\ud504\ub77c\uc778\uc758 \ud601\uc2e0\uc801\uc778 \ubc1c\uc804, \uc720\ub7fd \uc5f0\ud569(EU) \ub0b4 \ud76c\uadc0 \uc758\uc57d\ud488 \uc0c1\ud658 \uc815\ucc45\uc758 \ub2e4\uad6d\uc801 \uc870\ud654, \uadf8\ub9ac\uace0 AI \uae30\ubc18 \ucd08\ud76c\uadc0 \uc9c8\ud658 \ud658\uc790 \ubc1c\uad74 \uc54c\uace0\ub9ac\uc998\uc758 \ub3c4\uc785 \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubc18\uba74, \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c\ub294 \uc5f0\uac04 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uacfc \uc774\uc5d0 \ub530\ub978 \uac00\uaca9 \uc800\ud56d(\uc5f0\uac04 65\ub9cc \ub2ec\ub7ec \uc774\uc0c1\uc758 \uac00\uaca9\uc740 \uc131\uacfc \uae30\ubc18 \uacc4\uc57d \ubc0f \ud658\uc790 \uc9c0\uc6d0 \uc81c\ub3c4\ub97c \uc720\ubc1c), \ud604\uc7ac ERT\uc758 \uc81c\ud55c\uc801\uc778 \ud608\uc561-\ub1cc \uc7a5\ubcbd(BBB) \ud22c\uacfc\uc131, \uc7a5\uae30\uc801\uc778 \uc2e4\uc81c \uc548\uc804\uc131 \ub370\uc774\ud130 \ubd80\uc871, \uc870\ud608\ubaa8\uc138\ud3ec \uc774\uc2dd(HSCT) \ucc44\ud0dd\uc744 \uc81c\ud55c\ud558\ub294 \uace8\uc218 \uae30\uc99d\uc790 \ub9e4\uce6d \uacbd\uc7c1 \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubcf4\uace0\uc11c\ub294 \uc2dc\uc7a5\uc744 \uce58\ub8cc \uc720\ud615, \ud22c\uc5ec \uacbd\ub85c, \uc9c0\uc5ed\ubcc4\ub85c \uc138\ubd84\ud654\ud558\uc5ec \ubd84\uc11d\ud569\ub2c8\ub2e4. \uce58\ub8cc \uc720\ud615\ubcc4\ub85c\ub294 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95, \uc870\ud608\ubaa8\uc138\ud3ec \uc774\uc2dd, \uc720\uc804\uc790 \uce58\ub8cc, \ubcf4\uc870 \ubc0f \ubcf4\uc644 \uce58\ub8cc, \uc784\uc0c1 \uc2dc\ud5d8 \uc911\uc778 \uc57d\ub9ac\ud559\uc801 \uc0e4\ud398\ub860 \ub4f1\uc774 \ud3ec\ud568\ub429\ub2c8\ub2e4. \ud2b9\ud788 \uc720\uc804\uc790 \uce58\ub8cc\ub294 2030\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 18.4%\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \ud6c4\uae30 \uc784\uc0c1 \ub2e8\uacc4\ub85c \uc9c4\uc785\ud568\uc5d0 \ub530\ub77c \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc744 \ub2a5\uac00\ud560 \uac83\uc73c\ub85c \ubcf4\uc785\ub2c8\ub2e4. \ud22c\uc5ec \uacbd\ub85c\ubcc4\ub85c\ub294 \uc815\ub9e5 \uc8fc\uc785, \uc218\uc220\uc801 \uc774\uc2dd, \ub1cc\ucc99\uc218\uc561\/\uc911\ucd94\uc2e0\uacbd\uacc4 \uc9c1\uc811 \uc804\ub2ec, \uc804\uc2e0 \ubc14\uc774\ub7ec\uc2a4 \ubca1\ud130 \uc804\ub2ec \ub4f1\uc774 \ud3ec\ud568\ub429\ub2c8\ub2e4. \uc9c0\uc5ed\ubcc4\ub85c\ub294 \ubd81\ubbf8\uac00 Velmanase Alfa\uc758 FDA \uc2b9\uc778 \ubc0f \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac \ud655\ub300\uc5d0 \ud798\uc785\uc5b4 \uc5f0\ud3c9\uade0 15.7%\ub85c \uac00\uc7a5 \ub192\uc740 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc720\ub7fd, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8 \uc2dc\uc7a5 \ub610\ud55c \uc0c1\uc138\ud788 \ubd84\uc11d\ub429\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd \ubd84\uc11d\uc5d0\uc11c\ub294 Chiesi Farmaceutici, Sobi, Orchard Therapeutics, Takeda Pharmaceutical \ub4f1 \uc8fc\uc694 20\uac1c \uae30\uc5c5\uc758 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4, \uc2dc\uc7a5 \uc810\uc720\uc728, \uae30\uc5c5 \ud504\ub85c\ud544 \ubc0f \ucd5c\uadfc \uac1c\ubc1c \ub3d9\ud5a5\uc744 \uc2ec\uce35\uc801\uc73c\ub85c \ub2e4\ub8f9\ub2c8\ub2e4.<\/p>\n<p>\ud604\uc7ac \uce58\ub8cc\ubc95\uc758 \uc8fc\uc694 \ubbf8\ucda9\uc871 \uc218\uc694\ub294 \uc911\ucd94\uc2e0\uacbd\uacc4(CNS) \uce68\ud22c \ub2a5\ub825\uc785\ub2c8\ub2e4. \uae30\uc874 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95\uc740 \ud608\uc561-\ub1cc \uc7a5\ubcbd\uc744 \ud1b5\uacfc\ud558\uc9c0 \ubabb\ud558\uc5ec \uc778\uc9c0 \uae30\ub2a5 \uc800\ud558\ub97c \uad00\ub9ac\ud558\uc9c0 \ubabb\ud558\ubbc0\ub85c, CNS \ud45c\uc801 \uc194\ub8e8\uc158\uc758 \ud544\uc694\uc131\uc774 \uac15\uc870\ub429\ub2c8\ub2e4. \uc774\ub294 \ud5a5\ud6c4 \uc2dc\uc7a5\uc758 \uc911\uc694\ud55c \uae30\ud68c \uc601\uc5ed\uc73c\ub85c \uc791\uc6a9\ud560 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \uc54c\ud30c \ub9cc\ub178\uc2dc\ub3c4\uc2dc\uc2a4 \uc2dc\uc7a5\uc758 \uc804\ubc18\uc801\uc778 \ub3d9\ud5a5, \uc131\uc7a5 \ub3d9\ub825, \uc81c\uc57d \uc694\uc778, \uc138\ubd84\ud654\ub41c \ubd84\uc11d \ubc0f \uacbd\uc7c1 \uad6c\ub3c4\ub97c \ud3ec\uad04\uc801\uc73c\ub85c \uc81c\uc2dc\ud558\uc5ec \uc774\ud574\uad00\uacc4\uc790\ub4e4\uc5d0\uac8c \uadc0\uc911\ud55c \ud1b5\ucc30\ub825\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-28203","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/28203"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=28203"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/28203\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=28203"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=28203"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=28203"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}