{"id":31070,"date":"2026-02-08T15:30:20","date_gmt":"2026-02-08T15:30:20","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/monogenetic-disease-therapy-market-mordor\/"},"modified":"2026-10-09T10:07:22","modified_gmt":"2026-10-09T01:07:22","slug":"monogenetic-disease-therapy-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/monogenetic-disease-therapy-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2025-2030)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/monogenetic-disease-therapy-market-1735631022963-123.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/1737026863389-monogenetic-disease-therapy-market-Market-Summary.png\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \uc5ed\ud559<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 \ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658 \ubc1c\ubcd1\ub960 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.3 \ud65c\ubc1c\ud55c \uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \uc81c\ud55c\ub41c \uc131\uacf5\ub960<\/li>\n<li class=\"toc-level-3\">4.3.2 \uaddc\uc81c \ubb38\uc81c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.4.1 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.2 \uad6c\ub9e4\uc790\/\uc18c\ube44\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.3 \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.4 \ub300\uccb4 \uc81c\ud488\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uc138\ubd84\ud654 (\uac00\uce58 \uae30\uc900 \uc2dc\uc7a5 \uaddc\ubaa8 &#8211; USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uc720\uc804 \ud328\ud134\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \uc0c1\uc5fc\uc0c9\uccb4<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc5fc\uc0c9\uccb4<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \uce58\ub8cc \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.2.2 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95 (ERT)<\/li>\n<li class=\"toc-level-3\">5.2.3 RNA \uae30\ubc18 \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.2.4 \uc904\uae30\uc138\ud3ec \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.2.5 CRISPR \uae30\ubc18 \uc720\uc804\uc790 \ud3b8\uc9d1<\/li>\n<li class=\"toc-level-3\">5.2.6 \uae30\ud0c0<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc9c8\ubcd1 \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d<\/li>\n<li class=\"toc-level-3\">5.3.2 \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d<\/li>\n<li class=\"toc-level-3\">5.3.3 \ud5cc\ud305\ud134\ubcd1<\/li>\n<li class=\"toc-level-3\">5.3.4 \uae30\ud0c0<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.4.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.4.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.4.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.4.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.4.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.4.2.6 \uae30\ud0c0 \uc720\ub7fd<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.4.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.4.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.4.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.4.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.6 \uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-3\">5.4.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.4.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.3 \uae30\ud0c0 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-3\">5.4.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.4.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.4.5.3 \uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \ud68c\uc0ac \ud504\ub85c\ud544\n<ul>\n<li class=\"toc-level-3\">6.1.1 \ubc14\uc774\uc5d8 AG<\/li>\n<li class=\"toc-level-3\">6.1.2 \uc720\ub2c8\ud050\uc5b4<\/li>\n<li class=\"toc-level-3\">6.1.3 \ube0c\ub9ac\uc2a4\ud1a8-\ub9c8\uc774\uc5b4\uc2a4 \uc2a4\ud045<\/li>\n<li class=\"toc-level-3\">6.1.4 \uc560\ubcf4\ud2b8 \uc5f0\uad6c\uc18c<\/li>\n<li class=\"toc-level-3\">6.1.5 \ub178\ubc14\ud2f0\uc2a4<\/li>\n<li class=\"toc-level-3\">6.1.6 \ubc84\ud14d\uc2a4 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">6.1.7 \ud654\uc774\uc790 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.8 \uc0ac\ub819\ud0c0 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.1.9 \ube14\ub8e8\ubc84\ub4dc \ubc14\uc774\uc624<\/li>\n<li class=\"toc-level-3\">6.1.10 \uadf8\ub9ac\ud3f4\uc2a4 S.A.<\/li>\n<li class=\"toc-level-3\">6.1.11 \uc0ac\ub178\ud53c S.A.<\/li>\n<\/ul>\n<\/li>\n<li><strong>*\ubaa9\ub85d\uc740 \uc804\uccb4\uac00 \uc544\ub2d8<\/strong><\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \ub3d9\ud5a5<\/p>\n<div style=\"font-family:regular_semibold\">\uc774\uc6a9 \uac00\ub2a5 \uc5ec\ubd80\uc5d0 \ub530\ub77c \ub2ec\ub77c\uc9c8 \uc218 \uc788\uc74c<\/div>\n<div style=\"font-family:regular_semibold\">\uacbd\uc7c1 \ud658\uacbd \ud3ec\ud568 &#8211; \uc0ac\uc5c5 \uac1c\uc694, \uc7ac\ubb34, \uc81c\ud488 \ubc0f \uc804\ub7b5, \ucd5c\uadfc \uac1c\ubc1c \uc0ac\ud56d<\/div><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uac1c\uc694 (2025-2030)<\/p>\n<p># 1. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc804\ub9dd<\/p>\n<p>\ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 2025\ub144 362.8\uc5b5 \ub2ec\ub7ec \uaddc\ubaa8\ub85c \ucd94\uc815\ub418\uba70, 2030\ub144\uc5d0\ub294 605.8\uc5b5 \ub2ec\ub7ec\uc5d0 \ub2ec\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\uce21 \uae30\uac04(2025-2030\ub144) \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR)\uc740 10.80%\ub97c \uae30\ub85d\ud560 \uc804\ub9dd\uc785\ub2c8\ub2e4. \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc774 \ub420 \uac83\uc73c\ub85c \ubcf4\uc774\uba70, \ubd81\ubbf8 \uc9c0\uc5ed\uc740 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \uc720\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4. \ud604\uc7ac \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\ub294 \ub192\uc740 \uc218\uc900\uc785\ub2c8\ub2e4.<\/p>\n<p># 2. \uc2dc\uc7a5 \uc138\ubd84\ud654<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc744 \ub2e4\uc74c\uacfc \uac19\uc774 \uc138\ubd84\ud654\ud558\uc5ec \ubd84\uc11d\ud569\ub2c8\ub2e4.<\/p>\n<p>*   \uc720\uc804 \ud328\ud134\ubcc4: \uc0c1\uc5fc\uc0c9\uccb4\uc131(Autosomal), \uc5fc\uc0c9\uccb4\uc131(Chromosomal)<br \/>\n*   \uce58\ub8cc \uc720\ud615\ubcc4: \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc(Gene and Cell Therapy), \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(Enzyme Replacement Therapy, ERT), RNA \uae30\ubc18 \uce58\ub8cc, \uc904\uae30\uc138\ud3ec \uce58\ub8cc, CRISPR \uae30\ubc18 \uc720\uc804\uc790 \ud3b8\uc9d1, \uae30\ud0c0<br \/>\n*   \uc9c8\ubcd1 \uc720\ud615\ubcc4: \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d(Cystic Fibrosis), \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d(Sickle Cell Anemia), \ud5cc\ud305\ud134\ubcd1(Huntington&#8217;s Disease), \uae30\ud0c0<br \/>\n*   \uc9c0\uc5ed\ubcc4: \ubd81\ubbf8, \uc720\ub7fd, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \ub4f1<\/p>\n<p># 3. \uc8fc\uc694 \uc2dc\uc7a5 \ub3d9\uc778<\/p>\n<p>\ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc758 \uc131\uc7a5\uc740 \uc5ec\ub7ec \uc694\uc778\uc5d0 \uc758\ud574 \ud06c\uac8c \uc88c\uc6b0\ub429\ub2c8\ub2e4.<\/p>\n<p>*   \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \ubc1c\uc0dd\ub960 \uc99d\uac00: \uc720\uc804\uc801 \uc18c\uc778\uacfc \ud658\uacbd\uc801 \uc694\uc778\uc758 \ubcf5\ud569\uc801\uc778 \uc791\uc6a9\uc73c\ub85c \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc758 \ubc1c\uc0dd\ub960\uc774 \uc99d\uac00\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \ubc0f \uadfc\uc774\uc601\uc591\uc99d\uacfc \uac19\uc740 \uc9c8\ud658\uc758 \uc9c4\ub2e8 \uc99d\uac00\ub85c \uc774\uc5b4\uc838, \ud45c\uc801 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \ud658\uc790 \uc218\uc694\ub97c \uc99d\ub300\uc2dc\ud0a4\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023\ub144 \ubbf8\uad6d \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \uc7ac\ub2e8 \ud658\uc790 \ub4f1\ub85d \ubcf4\uace0\uc11c\uc5d0 \ub530\ub974\uba74, 2023\ub144 \ubbf8\uad6d \ub0b4 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \ud658\uc790\ub294 \uc57d 33,288\uba85\uc73c\ub85c \uc9d1\uacc4\ub418\uc5c8\uc73c\uba70, \uc774 \uc911 17% \uc774\uc0c1\uc774 \ud788\uc2a4\ud328\ub2c9, \ud751\uc778 \ub610\ub294 \ub2e4\uc778\uc885\uc73c\ub85c \ub098\ud0c0\ub098 \uc778\uad6c \uad6c\uc131\uc758 \ub2e4\uc591\uc131\uc744 \ubcf4\uc5ec\uc8fc\uc5c8\uc2b5\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ud658\uc790 \uc778\uad6c\uc758 \uc99d\uac00\ub294 \uc81c\uc57d \ud68c\uc0ac\ub4e4\uc774 \uce58\ub8cc\uc81c \uac1c\ubc1c\uc5d0 \ub300\ud55c \ud22c\uc790\ub97c \uac15\ud654\ud558\ub3c4\ub85d \uc720\ub3c4\ud558\uc5ec \uc2dc\uc7a5 \ud655\ub300\ub97c \ucd09\uc9c4\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd \uc81c\uace0: \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd\uc774 \ub192\uc544\uc9c0\uba74\uc11c \uc870\uae30 \uc9c4\ub2e8\uc774 \uc6a9\uc774\ud574\uc9c0\uace0 \ud658\uc790 \uc639\ud638 \ud65c\ub3d9\uc774 \ud65c\ubc1c\ud574\uc838 \ucca8\ub2e8 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc218\uc694\uac00 \uc99d\ud3ed\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub300\uc911\uc758 \uc815\ubcf4 \ubc0f \uce58\ub8cc \uc635\uc158\uc5d0 \ub300\ud55c \uad00\uc2ec\uc774 \uc99d\uac00\ud568\uc5d0 \ub530\ub77c, \uc758\ub8cc \uc2dc\uc2a4\ud15c\uc740 \uc720\uc804 \uac80\uc0ac \ubc0f \uc0c1\ub2f4\uc744 \ud45c\uc900 \uc9c4\ub8cc\uc5d0 \ud1b5\ud569\ud558\ub294 \ucd94\uc138\uc774\uba70, \uc774\ub294 \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc744 \ub354\uc6b1 \ud48d\uc694\ub86d\uac8c \ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc77c\ub840\ub85c, 2024\ub144 9\uc6d4\uc5d0\ub294 \uacb8\uc0c1 \uc801\ud608\uad6c \uc778\uc2dd\uc758 \ub2ec\uc774 \uc9c0\uc815\ub418\uc5b4 \uc9c8\ubcd1 \uad50\uc721 \ubc0f \ud5cc\ud608\uc758 \uc911\uc694\uc131\uc744 \uac15\uc870\ud558\ub294 \ucea0\ud398\uc778\uc774 \uc9c4\ud589\ub418\uc5c8\uc73c\uba70, 2024\ub144 5\uc6d4 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \uc7ac\ub2e8\uc740 CF \uc778\uc2dd\uc758 \ub2ec\uc744 \ub9de\uc544 \uc18c\uc15c \ubbf8\ub514\uc5b4\ub97c \ud1b5\ud574 \ud68c\ubcf5\ub825\uacfc \ucee4\ubba4\ub2c8\ud2f0 \uc2a4\ud1a0\ub9ac\ub97c \uc870\uba85\ud558\uba70 \uce58\ub8cc \uc811\uadfc\uc131 \ubc0f \uc5f0\uad6c \uc790\uae08 \uc9c0\uc6d0 \ud655\ub300\ub97c \ucd09\uad6c\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ud65c\ubc1c\ud55c \uc5f0\uad6c \uac1c\ubc1c(R&#038;D) \ud65c\ub3d9: \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc744 \uc704\ud55c \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95 \uac1c\ubc1c\uc5d0 \uc788\uc5b4 \ud65c\ubc1c\ud55c R&#038;D \ub178\ub825\uc740 \ud575\uc2ec\uc801\uc778 \uc5ed\ud560\uc744 \ud569\ub2c8\ub2e4. \uc774\ud574\uad00\uacc4\uc790\ub4e4 \uac04\uc758 \ud22c\uc790 \ubc0f \ud611\ub825 \uc99d\uac00\ub294 \ud68d\uae30\uc801\uc778 \ud601\uc2e0\uc744 \uc704\ud55c \uae38\uc744 \uc5f4\uace0 \uc788\uc73c\uba70, \ud2b9\ud788 \uc720\uc804\uc790 \uce58\ub8cc\ub294 \uc2dc\uc7a5 \ud655\uc7a5\uc5d0 \ud06c\uac8c \uae30\uc5ec\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2024\ub144 9\uc6d4 \uc18c\uc544 \uc720\uc804 \uc9c8\ud658\uc744 \uc704\ud55c \uae30\uc131 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc5d0 \uc8fc\ub825\ud558\ub294 \ubc14\uc774\uc624 \uae30\uc5c5 Genespire\ub294 4,660\ub9cc \uc720\ub85c(5,200\ub9cc \ub2ec\ub7ec) \uaddc\ubaa8\uc758 \uc2dc\ub9ac\uc988 B \ud22c\uc790\ub97c \uc720\uce58\ud588\uc2b5\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ud65c\ubc1c\ud55c R&#038;D \ud658\uacbd\uc740 \uc0c8\ub85c\uc6b4 \uce58\ub8cc\uc81c\uc758 \uc9c0\uc18d\uc801\uc778 \uacf5\uae09\uc744 \ubcf4\uc7a5\ud560 \ubfd0\ub9cc \uc544\ub2c8\ub77c \uacbd\uc7c1\uc744 \ucd09\uc9c4\ud558\uc5ec \ud658\uc790 \ube44\uc6a9\uc744 \uc7a0\uc7ac\uc801\uc73c\ub85c \uc808\uac10\ud558\uace0 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \ub4b7\ubc1b\uce68\ud569\ub2c8\ub2e4.<\/p>\n<p># 4. \uc2dc\uc7a5 \uc131\uc7a5 \uc800\ud574 \uc694\uc778<\/p>\n<p>\uc774\ub7ec\ud55c \uae0d\uc815\uc801\uc778 \uc804\ub9dd\uc5d0\ub3c4 \ubd88\uad6c\ud558\uace0, \ub192\uc740 \uce58\ub8cc \ube44\uc6a9, \uc81c\ud55c\uc801\uc778 \uc131\uacf5\ub960, \uadf8\ub9ac\uace0 \uaddc\uc81c \uc7a5\ubcbd\uacfc \uac19\uc740 \uacfc\uc81c\ub4e4\uc774 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud560 \uc218 \uc788\ub294 \uc694\uc778\uc73c\ub85c \uc791\uc6a9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 5. \uae00\ub85c\ubc8c \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30\ub825<\/p>\n<p> 5.1. \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc \ubd80\ubb38, \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc0c1\ub2f9\ud55c \uc810\uc720\uc728 \uc720\uc9c0 \uc608\uc0c1<\/p>\n<p>\ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc744 \uc704\ud55c \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc\ub294 \ud2b9\uc815 \uc720\uc804\uc801 \ub3cc\uc5f0\ubcc0\uc774 \ub610\ub294 \uc601\ud5a5\uc744 \ubc1b\ub294 \uc0dd\ud654\ud559\uc801 \uacbd\ub85c\ub97c \ud45c\uc801\uc73c\ub85c \ud558\ub294 \uc758\uc57d\ud488\uc744 \ud65c\uc6a9\ud569\ub2c8\ub2e4. \uc774 \ubd80\ubb38\uc758 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \ub3d9\uc778\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \uc138\ud3ec \ubc0f \uc720\uc804\uc790 \uce58\ub8cc\uc758 \ubc1c\uc804: \uc774\ub7ec\ud55c \ud601\uc2e0\uc740 \uc720\uc804\uc801 \ub3cc\uc5f0\ubcc0\uc774\ub97c \uc9c1\uc811 \ud574\uacb0\ud558\ub294 \uce58\ub8cc\ubc95\uc744 \uac00\ub2a5\ud558\uac8c \ud558\uc5ec \ud6a8\ub2a5\uc744 \ub192\uc774\uace0 \ud658\uc790 \uacb0\uacfc\ub97c \uac1c\uc120\ud569\ub2c8\ub2e4.<br \/>\n*   R&#038;D \ud22c\uc790 \uc99d\ub300: \uacf5\uacf5 \ubc0f \ubbfc\uac04 \uc790\uae08 \uc9c0\uc6d0\uc5d0 \ud798\uc785\uc5b4 \uc5f0\uad6c \uac1c\ubc1c \ud22c\uc790\uac00 \uc99d\uac00\ud558\uba74\uc11c \uc2e0\uc57d \ud6c4\ubcf4 \ubc0f \uc720\uc804\uc790 \uce58\ub8cc\uc81c \ubc1c\uacac\uc774 \uac00\uc18d\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023\ub144 10\uc6d4 Triveni Bio\ub294 9,200\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\uc758 \uc2dc\ub9ac\uc988 A \ud22c\uc790\ub97c \uc720\uce58\ud558\uc5ec \uba74\uc5ed \ubc0f \uc5fc\uc99d \uc9c8\ud658\uc744 \ud3ec\ud568\ud55c \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc744 \uc704\ud55c \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uac1c\ubc1c\uc744 \ubaa9\ud45c\ub85c \ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uc790\uae08 \uc720\uc785\uc740 \uc0c8\ub85c\uc6b4 \uc57d\ubb3c \ud6c4\ubcf4\uc758 \ubc1c\uacac \ubc0f \uac1c\ubc1c\uc744 \uac00\uc18d\ud654\ud558\uc5ec \ubd80\ubb38 \uc131\uc7a5\uc744 \ucd09\uc9c4\ud560 \uac83\uc785\ub2c8\ub2e4.<br \/>\n*   \uaddc\uc81c \uae30\uad00\uc758 \ud601\uc2e0 \ucd09\uc9c4: \uaddc\uc81c \uae30\uad00\ub4e4\uc740 \ud68d\uae30\uc801\uc778 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc2b9\uc778 \uc808\ucc28\ub97c \uc2e0\uc18d\ud558\uac8c \ucc98\ub9ac\ud558\uc5ec \ud601\uc2e0\uc744 \uc7a5\ub824\ud558\uace0 \ud22c\uc790\ub97c \uc720\uce58\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023\ub144 12\uc6d4 \ubbf8\uad6d \uc2dd\ud488\uc758\uc57d\uad6d(FDA)\uc740 12\uc138 \uc774\uc0c1 \uacb8\uc0c1 \uc801\ud608\uad6c \uc9c8\ud658(SCD) \ud658\uc790 \uce58\ub8cc\ub97c \uc704\ud55c \ucd5c\ucd08\uc758 \uc138\ud3ec \uae30\ubc18 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc778 Casgevy\uc640 Lyfgenia \ub450 \uac00\uc9c0 \ud68d\uae30\uc801\uc778 \uce58\ub8cc\uc81c\ub97c \uc2b9\uc778\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc778\uc2dd \uc99d\uac00: \uc778\uc2dd\uc774 \ub192\uc544\uc9d0\uc5d0 \ub530\ub77c \ub354 \ub9ce\uc740 \ud658\uc790\ub4e4\uc774 \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc73c\ub85c \uc9c4\ub2e8\ubc1b\uace0 \uc788\uc73c\uba70, \uc774\ub294 \ud6a8\uacfc\uc801\uc778 \uce58\ub8cc\ubc95\uc744 \ucc3e\ub294 \uac1c\uc778\uc758 \ud480\uc744 \ud655\ub300\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2024\ub144 7\uc6d4 \uc778\ub3c4 \ubaa8\ub514 \ucd1d\ub9ac\ub294 2047\ub144\uae4c\uc9c0 \uacb8\uc0c1 \uc801\ud608\uad6c \uc9c8\ud658\uc744 \uacf5\uc911 \ubcf4\uac74 \ubb38\uc81c\uc5d0\uc11c \uc81c\uac70\ud558\ub294 \uac83\uc744 \ubaa9\ud45c\ub85c \ud558\ub294 \uad6d\uac00 \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d \ud1f4\uce58 \ubbf8\uc158\uc744 \ucd9c\ubc94\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uacb0\ub860\uc801\uc73c\ub85c, R&#038;D \ud22c\uc790 \uc99d\ub300, \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd \uc81c\uace0, \uadf8\ub9ac\uace0 \uc9c0\uc6d0\uc801\uc778 \uaddc\uc81c \ud658\uacbd\uc758 \uc0c1\ud638 \uc791\uc6a9\uc740 \ud5a5\ud6c4 \uba87 \ub144\uac04 \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658\uc744 \uc704\ud55c \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc \ubd80\ubb38\uc758 \uc131\uc7a5\uc744 \ucd09\uc9c4\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p> 5.2. \ubd81\ubbf8 \uc9c0\uc5ed, \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc0c1\ub2f9\ud55c \uc2dc\uc7a5 \uc810\uc720\uc728 \uc720\uc9c0 \uc608\uc0c1<\/p>\n<p>\ubd81\ubbf8 \uc9c0\uc5ed\uc740 \uc8fc\uc694 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc8fc\uc694 \ub3d9\uc778\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \uc815\ubd80 \ud22c\uc790 \uc99d\uac00: \uc815\ubd80\uc758 \ud22c\uc790\uac00 \uc99d\uac00\ud558\uba74\uc11c \uc5f0\uad6c \ubc0f \uac1c\ubc1c \ud65c\ub3d9\uc774 \ud65c\ubc1c\ud574\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc720\uc804\uc790 \uce58\ub8cc R&#038;D \ubc1c\uc804: \uc720\uc804\uc790 \uce58\ub8cc \uc5f0\uad6c \ubc0f \uac1c\ubc1c\uc758 \ubc1c\uc804\uc774 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uacac\uc778\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ud45c\uc801 \uc9c8\ud658 \uc720\ubcd1\ub960 \uc99d\uac00: \ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uc9c4\ub2e8\uc774 \uc99d\uac00\ud568\uc5d0 \ub530\ub77c \ud6a8\uacfc\uc801\uc778 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc218\uc694\uac00 \uc99d\uac00\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2024\ub144 1\uc6d4 Taylor and Francis \uae30\uc0ac\uc5d0 \ub530\ub974\uba74, 2023\ub144 \uce90\ub098\ub2e4\uc5d0\ub294 \uc57d 6,500\uba85\uc758 \uacb8\uc0c1 \uc801\ud608\uad6c \uc9c8\ud658(SCD) \ud658\uc790\uac00 \uc788\uc5c8\uc73c\uba70, \uc628\ud0c0\ub9ac\uc624\uc8fc, \ud2b9\ud788 \ud1a0\ub860\ud1a0 \ubc0f \uc778\uadfc \uc9c0\uc5ed\uc774 \uc774 \uc911 3,500\uac74 \uc774\uc0c1\uc744 \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ub300\uc911 \uc778\uc2dd \ubc0f \uc639\ud638 \ud65c\ub3d9 \uc99d\ub300: \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \ub300\uc911\uc758 \uc778\uc2dd\uacfc \uc639\ud638 \ud65c\ub3d9\uc774 \ub192\uc544\uc9c0\uba74\uc11c \uc5f0\uad6c \ubc0f \uce58\ub8cc \ubc1c\uc804\uc758 \uc720\ub9ac\ud55c \ud658\uacbd\uc774 \uc870\uc131\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023\ub144 9\uc6d4 \uc720\uc804 \uc9c8\ud658 \uac80\uc0ac\ub97c \uc639\ud638\ud558\ub294 JScreen\uc740 Tay-Sachs \uc9c8\ud658\uc73c\ub85c \uc601\ud5a5\uc744 \ubc1b\uc740 \uac00\uc871\ub4e4\uc744 \uc870\uba85\ud558\ub294 \ucea0\ud398\uc778\uc744 \uc2dc\uc791\ud588\uc73c\uba70, \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \ubc0f \uace0\uc154\ubcd1\uacfc \uac19\uc740 \ub2e4\ub978 \uc720\uc804 \uc9c8\ud658 \uc644\ud654\ub97c \uc704\ud574\uc11c\ub3c4 \uc801\uadf9\uc801\uc73c\ub85c \ub178\ub825\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uaddc\uc81c \uae30\uad00\uc758 \uc2e0\uc18d\ud55c \uc2b9\uc778: FDA\ub97c \ud3ec\ud568\ud55c \uaddc\uc81c \uae30\uad00\ub4e4\uc740 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc2b9\uc778 \uc808\ucc28\ub97c \uc2e0\uc18d\ud558\uac8c \ucc98\ub9ac\ud558\uc5ec \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95\uc758 \uc2e0\uc18d\ud55c \uac1c\ubc1c \ubc0f \ub3c4\uc785\uc744 \uc704\ud55c \uae38\uc744 \uc5f4\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc608\ub97c \ub4e4\uc5b4, 2023\ub144 4\uc6d4 Vertex Pharmaceuticals Incorporated\ub294 \ubbf8\uad6d FDA\uac00 TRIKAFTA(elexacaftor\/tezacaftor\/ivacaftor \ubc0f ivacaftor)\uc758 \ud655\uc7a5 \uc0ac\uc6a9\uc744 \uc2b9\uc778\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. \uc774 \uc2b9\uc778\uc740 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \ub9c9\ud6a1\ub2e8 \uc804\ub3c4 \uc870\uc808\uae30(CFTR) \uc720\uc804\uc790\uc5d0 \ucd5c\uc18c \ud558\ub098\uc758 F508del \ub3cc\uc5f0\ubcc0\uc774\ub97c \ubcf4\uc720\ud55c 2\uc138\uc5d0\uc11c 5\uc138 \uc0ac\uc774\uc758 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d(CF) \uc544\ub3d9\uc744 \ud3ec\ud568\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc694\uc57d\ud558\uc790\uba74, R&#038;D \ud22c\uc790 \uc99d\ub300, \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd \uc81c\uace0, \uadf8\ub9ac\uace0 \uc6b0\ud638\uc801\uc778 \uaddc\uc81c \ud658\uacbd\uc774 \ud5a5\ud6c4 \uba87 \ub144\uac04 \ubd81\ubbf8 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uacac\uc778\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p># 6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<p>\ub2e8\uc77c \uc720\uc804 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 \ud1b5\ud569\ub41c(consolidated) \ud615\ud0dc\ub97c \ub760\uace0 \uc788\uc73c\uba70, \ub9ce\uc740 \uc2dc\uc7a5 \ucc38\uc5ec\uc790\ub4e4\uc774 \uc2dc\uc7a5 \uc131\uc7a5 \uae30\ud68c\ub97c \ud65c\uc6a9\ud558\uae30 \uc704\ud574 \ubcf4\ub2e4 \ud6a8\uc728\uc801\uc778 \uce58\ub8cc\ubc95\uc744 \uc81c\uacf5\ud558\ub294 \uc2e0\uc57d \uac1c\ubc1c\uc5d0 \uc8fc\ub825\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc8fc\uc694 \uae30\uc5c5\ub4e4\uc740 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uc2dc\uc7a5 \uc9c0\uc704\ub97c \uac15\ud654\ud558\uae30 \uc704\ud574 \ud611\ub825, \ud569\ubcd1, \uc778\uc218\ub97c \ud65c\ubc1c\ud788 \uc9c4\ud589\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc8fc\uc694 \uae30\uc5c5\uc73c\ub85c\ub294 Bayer AG, UniQure, Abbott Laboratories, Novartis, Vertex Pharmaceuticals, Sanofi AG, Pfizer Inc., Bluebird Bio \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 7. \ucd5c\uadfc \uc0b0\uc5c5 \ub3d9\ud5a5<\/p>\n<p>*   2024\ub144 9\uc6d4: Vertex Pharmaceuticals Incorporated\ub294 Health Canada\ub85c\ubd80\ud130 PrCASGEVY(exagamglogene autotemcel)\uc5d0 \ub300\ud55c \ub9c8\ucf00\ud305 \uc2b9\uc778\uc744 \ud68d\ub4dd\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\uc2b5\ub2c8\ub2e4. \uc774 \uce58\ub8cc\ubc95\uc740 \uc790\uac00 \uc720\uc804\uccb4 \ud3b8\uc9d1 \uc870\ud608\ubaa8\uc138\ud3ec \uae30\ubc18\uc73c\ub85c, \ubc18\ubcf5\uc801\uc778 \ud608\uad00 \ud3d0\uc1c4 \uc704\uae30(VOCs)\ub97c \uacaa\ub294 \uacb8\uc0c1 \uc801\ud608\uad6c \uc9c8\ud658(SCD) \ud658\uc790 \ub610\ub294 \uc218\ud608 \uc758\uc874\uc131 \ubca0\ud0c0-\uc9c0\uc911\ud574\ube48\ud608(TDT) \ud658\uc790 \uc911 12\uc138 \uc774\uc0c1\uc744 \ub300\uc0c1\uc73c\ub85c \ud569\ub2c8\ub2e4.<br \/>\n*   2024\ub144 9\uc6d4: ReCode Therapeutics\ub294 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d(CF) \uce58\ub8cc\ub97c \ubaa9\ud45c\ub85c \ud558\ub294 \uc2e4\ud5d8\uc801\uc778 \ud761\uc785\ud615 mRNA \uce58\ub8cc\uc81c RCT2100\uc758 Phase 1b \uc5f0\uad6c\uc5d0\uc11c \uccab \ud658\uc790\uc5d0\uac8c \ud22c\uc5ec\ub97c \uc2dc\uc791\ud588\uc2b5\ub2c8\ub2e4. RCT2100\uc740 CFTR mRNA\ub97c \ud3d0\uc758 \ud45c\uc801 \uc138\ud3ec\uc5d0 \uc9c1\uc811 \uc804\ub2ec\ud558\uc5ec, CF\ub97c \uc553\ub294 \ud2b9\uc815 \uac1c\uc778\uc5d0\uac8c \uacb0\ud54d\ub41c \uae30\ub2a5\uc131 CFTR \ub2e8\ubc31\uc9c8\uc744 \uc0dd\uc131\ud558\ub3c4\ub85d \uc138\ud3ec\uc5d0 \uc9c0\uc2dc\ud558\ub294 \ub370 \uc911\uc810\uc744 \ub461\ub2c8\ub2e4.<\/p>\n<p>\uc774 \ubcf4\uace0\uc11c\ub294 \ub2e8\uc77c \uc720\uc804\uc790 \ub3cc\uc5f0\ubcc0\uc774\ub85c \uc778\ud574 \ubc1c\uc0dd\ud558\ub294 \uc9c8\ud658\uc778 \ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658(Monogenetic Disease) \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \ub300\ud55c \ud3ec\uad04\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658\uc740 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d, \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d, \ud5cc\ud305\ud134\ubcd1 \ub4f1\uc774 \uc788\uc73c\uba70, \uc774 \uce58\ub8cc\ubc95\uc740 \uacb0\ud568 \uc788\ub294 \uc720\uc804\uc790\ub97c \uad50\uc815\ud558\uac70\ub098 \ub300\uccb4\ud558\ub294 \uc720\uc804\uc790 \uce58\ub8cc\ub97c \ud3ec\ud568\ud569\ub2c8\ub2e4. \ubcf8 \ubcf4\uace0\uc11c\ub294 \uc2dc\uc7a5\uc758 \uc8fc\uc694 \ub3d9\uc778, \uc81c\uc57d \uc694\uc778, \uc138\ubd84\ud654 \ubc0f \uacbd\uc7c1 \ud658\uacbd\uc744 \ub2e4\ub8e8\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658 \uce58\ub8cc \uc2dc\uc7a5\uc740 2024\ub144 323.6\uc5b5 \ub2ec\ub7ec, 2025\ub144 362.8\uc5b5 \ub2ec\ub7ec \uaddc\ubaa8\ub85c \ucd94\uc815\ub418\uba70, 2025\ub144\ubd80\ud130 2030\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 10.80%\ub85c \uc131\uc7a5\ud558\uc5ec 2030\ub144\uc5d0\ub294 605.8\uc5b5 \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \ub3d9\uc778\uc73c\ub85c\ub294 \ub2e8\uc77c \uc720\uc804\uc790 \uc9c8\ud658\uc758 \ubc1c\ubcd1\ub960 \uc99d\uac00, \uc720\uc804 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc778\uc2dd \uc81c\uace0, \ud65c\ubc1c\ud55c \uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9\uc774 \uc8fc\uc694 \uc694\uc778\uc73c\ub85c \uaf3d\ud799\ub2c8\ub2e4. \ubc18\uba74, \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uacfc \uc81c\ud55c\uc801\uc778 \uc131\uacf5\ub960, \uadf8\ub9ac\uace0 \uaddc\uc81c \ubb38\uc81c\ub294 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c \uc791\uc6a9\ud569\ub2c8\ub2e4. \ubcf4\uace0\uc11c\ub294 \ub610\ud55c \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d(\uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611, \uad6c\ub9e4\uc790\uc758 \uad50\uc12d\ub825, \uacf5\uae09\uc790\uc758 \uad50\uc12d\ub825, \ub300\uccb4\uc7ac\uc758 \uc704\ud611, \uacbd\uc7c1 \uac15\ub3c4)\uc744 \ud1b5\ud574 \uc2dc\uc7a5\uc758 \uacbd\uc7c1 \ud658\uacbd\uc744 \uc2ec\uce35\uc801\uc73c\ub85c \ud3c9\uac00\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc740 \uc720\uc804 \ud328\ud134, \uce58\ub8cc \uc720\ud615, \uc9c8\ubcd1 \uc720\ud615, \uc9c0\uc5ed\ubcc4\ub85c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4. \uc720\uc804 \ud328\ud134\ubcc4\ub85c\ub294 \uc0c1\uc5fc\uc0c9\uccb4(Autosomal) \ubc0f \uc5fc\uc0c9\uccb4(Chromosomal) \ud328\ud134\uc73c\ub85c \ub098\ub269\ub2c8\ub2e4. \uce58\ub8cc \uc720\ud615\ubcc4\ub85c\ub294 \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc, \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT), RNA \uae30\ubc18 \uce58\ub8cc, \uc904\uae30\uc138\ud3ec \uce58\ub8cc, CRISPR \uae30\ubc18 \uc720\uc804\uc790 \ud3b8\uc9d1 \ubc0f \uae30\ud0c0 \uce58\ub8cc\ubc95\uc73c\ub85c \uad6c\uc131\ub429\ub2c8\ub2e4. \uc9c8\ubcd1 \uc720\ud615\ubcc4\ub85c\ub294 \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d, \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d, \ud5cc\ud305\ud134\ubcd1 \ubc0f \uae30\ud0c0 \uc9c8\ud658\uc73c\ub85c \ubd84\ub958\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\uc5ed\ubcc4\ub85c\ub294 \ubd81\ubbf8, \uc720\ub7fd, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8\ub85c \uad6c\ubd84\ub429\ub2c8\ub2e4. \ud2b9\ud788 \ubd81\ubbf8\ub294 2025\ub144 \uae30\uc900 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \uc608\uce21 \uae30\uac04(2025-2030\ub144) \ub3d9\uc548 \uac00\uc7a5 \ub192\uc740 CAGR\uc744 \ubcf4\uc774\uba70 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uac01 \uc9c0\uc5ed \ub0b4 \ubbf8\uad6d, \uce90\ub098\ub2e4, \uba55\uc2dc\ucf54, \ub3c5\uc77c, \uc601\uad6d, \ud504\ub791\uc2a4, \uc774\ud0c8\ub9ac\uc544, \uc2a4\ud398\uc778, \uc911\uad6d, \uc77c\ubcf8, \uc778\ub3c4, \ud638\uc8fc, \ud55c\uad6d, GCC, \ub0a8\uc544\ud504\ub9ac\uce74, \ube0c\ub77c\uc9c8, \uc544\ub974\ud5e8\ud2f0\ub098 \ub4f1 17\uac1c \uc8fc\uc694 \uad6d\uac00\uc758 \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \ub3d9\ud5a5\uc744 \ud3ec\ud568\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc2dc\uc7a5 \ucc38\uc5ec\uc790\ub85c\ub294 Bayer AG, UniQure, Bristol-Myers Squibb, Abbott Laboratories, Novartis, Vertex Pharmaceuticals, Pfizer Inc., Sarepta Therapeutics, Bluebird Bio, Grifols S.A., Sanofi S.A. \ub4f1\uc774 \uc788\uc73c\uba70, \uc774\ub4e4 \uae30\uc5c5\uc758 \uc0ac\uc5c5 \uac1c\uc694, \uc7ac\ubb34, \uc81c\ud488 \ubc0f \uc804\ub7b5, \ucd5c\uadfc \uac1c\ubc1c \ub3d9\ud5a5 \ub4f1\uc774 \ubcf4\uace0\uc11c\uc5d0 \ud3ec\ud568\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf4\uace0\uc11c\ub294 \ub610\ud55c \uc2dc\uc7a5 \uae30\ud68c\uc640 \ubbf8\ub798 \ub3d9\ud5a5\uc5d0 \ub300\ud55c \ubd84\uc11d\uc744 \uc81c\uacf5\ud558\uc5ec \uc2dc\uc7a5 \ucc38\uc5ec\uc790\ub4e4\uc774 \uc804\ub7b5\uc744 \uc218\ub9bd\ud558\ub294 \ub370 \ud544\uc694\ud55c \ud1b5\ucc30\ub825\uc744 \uc81c\uc2dc\ud569\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-31070","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/31070"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=31070"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/31070\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=31070"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=31070"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=31070"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}