{"id":42027,"date":"2026-02-13T21:37:05","date_gmt":"2026-02-13T21:37:05","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/nucleic-acid-based-therapeutics-market-mordor\/"},"modified":"2026-10-02T18:18:14","modified_gmt":"2026-10-02T09:18:14","slug":"nucleic-acid-based-therapeutics-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/nucleic-acid-based-therapeutics-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2025-2030\ub144)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/nucleic-acid-based-therapeutics-market_1679986377708_Nucleic_Acid_Based_Therapeutics_Market_-_major_players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/nucleic-acid-based-therapeutics-market-size-image-1735468982778.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \uc5ed\ud559<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 \uc720\uc804 \uc9c8\ud658\uc758 \uae09\uc99d\ud558\ub294 \uc720\ubcd1\ub960<\/li>\n<li class=\"toc-level-3\">4.2.2 \uc758\ub8cc \ubd80\ubb38 \ud22c\uc790 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.3 \uc81c\uc57d \uc0b0\uc5c5\uc758 \ud601\uc2e0\uc801\uc778 \uc0dd\ubb3c\ud559\uc801 \uc81c\uc81c\ub85c\uc758 \ube60\ub978 \uc804\ud658<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ud575\uc0b0 \uc5f0\uad6c\uc758 \ub192\uc740 \ube44\uc6a9<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.4.1 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.2 \uad6c\ub9e4\uc790\/\uc18c\ube44\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.3 \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.4 \ub300\uccb4 \uc81c\ud488\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uc138\ubd84\ud654 (\uac00\uce58 \uae30\uc900 \uc2dc\uc7a5 \uaddc\ubaa8, \ubc31\ub9cc USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uc81c\ud488 \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 RNA \uac04\uc12d [RNAi] \ubc0f \uc9e7\uc740 \uac04\uc12d RNA [siRNA]<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc (ASO)<\/li>\n<li class=\"toc-level-3\">5.1.3 \uae30\ud0c0 \uc81c\ud488 \uc720\ud615<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \uc801\uc6a9 \ubd84\uc57c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc790\uac00\uba74\uc5ed \uc9c8\ud658<\/li>\n<li class=\"toc-level-3\">5.2.2 \uac10\uc5fc\uc131 \uc9c8\ud658<\/li>\n<li class=\"toc-level-3\">5.2.3 \uc720\uc804 \uc9c8\ud658<\/li>\n<li class=\"toc-level-3\">5.2.4 \uc554<\/li>\n<li class=\"toc-level-3\">5.2.5 \uae30\ud0c0 \uc801\uc6a9 \ubd84\uc57c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ubcd1\uc6d0 \ubc0f \ud074\ub9ac\ub2c9<\/li>\n<li class=\"toc-level-3\">5.3.2 \ud559\uc220 \ubc0f \uc5f0\uad6c \uae30\uad00<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.4.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.4.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.4.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.4.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.4.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.4.2.6 \uae30\ud0c0 \uc720\ub7fd<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.4.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.4.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.4.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.4.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.6 \uae30\ud0c0 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-3\">5.4.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.4.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.3 \uae30\ud0c0 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-3\">5.4.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.4.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.4.5.3 \uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \ud68c\uc0ac \ud504\ub85c\ud544\n<ul>\n<li class=\"toc-level-3\">6.1.1 \uc0ac\uc77c\ub7f0\uc2a4 \ud14c\ub77c\ud4e8\ud2f1\uc2a4 PLC<\/li>\n<li class=\"toc-level-3\">6.1.2 \uc544\uc774\uc624\ub2c8\uc2a4 \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.3 \ub178\ubc14\ud2f0\uc2a4 \ud30c\ub9c8 AG<\/li>\n<li class=\"toc-level-3\">6.1.4 \uc560\ub85c\uc6b0\ud5e4\ub4dc \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.5 \uc2a4\ud1a0\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.6 \ubaa8\ub354\ub098 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.7 \uc54c\ub2d0\ub78c \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.8 \ubc14\uc774\uc624\uc820 Inc.<\/li>\n<li class=\"toc-level-3\">6.1.9 \uc6e8\uc774\ube0c \ub77c\uc774\ud504 \uc0ac\uc774\uc5b8\uc2a4<\/li>\n<li class=\"toc-level-3\">6.1.10 \uc0ac\ub819\ud0c0 \ud14c\ub77c\ud4e8\ud2f1\uc2a4 Inc.<\/li>\n<\/ul>\n<\/li>\n<li><strong>*\ubaa9\ub85d\uc740 \uc804\uccb4\uac00 \uc544\ub2d8<\/strong><\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \ub3d9\ud5a5<\/p>\n<div style=\"font-family:regular_semibold\">\uc774\uc6a9 \uac00\ub2a5 \uc5ec\ubd80\uc5d0 \ub530\ub77c \ub2ec\ub77c\uc9c8 \uc218 \uc788\uc74c<\/div>\n<div style=\"font-family:regular_semibold\">\uacbd\uc7c1 \ud658\uacbd \ud3ec\ud568 &#8211; \uc0ac\uc5c5 \uac1c\uc694, \uc7ac\ubb34, \uc81c\ud488 \ubc0f \uc804\ub7b5, \ucd5c\uadfc \uac1c\ubc1c<\/div><\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uac1c\uc694<\/p>\n<p>\ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 2025\ub144 63\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2030\ub144 124\uc5b5 6\ucc9c\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc608\uce21 \uae30\uac04(2025-2030) \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 14.29%\ub97c \uae30\ub85d\ud560 \uc804\ub9dd\uc785\ub2c8\ub2e4. \uc774 \uc2dc\uc7a5\uc740 RNA \uac04\uc12d(RNAi) \ubc0f \ub2e8\uc77c \uac00\ub2e5 RNA(siRNA), \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO) \ub4f1 \ub2e4\uc591\ud55c \uc81c\ud488 \uc720\ud615\uacfc \uc790\uac00\uba74\uc5ed \uc9c8\ud658, \uac10\uc5fc\uc131 \uc9c8\ud658, \uc720\uc804 \uc9c8\ud658 \ub4f1\uc758 \uc751\uc6a9 \ubd84\uc57c, \uadf8\ub9ac\uace0 \ubcd1\uc6d0 \ubc0f \ud074\ub9ac\ub2c9, \ud559\uc220 \ubc0f \uc5f0\uad6c \uae30\uad00 \ub4f1\uc758 \ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4\ub85c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4. \ubd81\ubbf8\uac00 \uac00\uc7a5 \ud070 \uc2dc\uc7a5\uc774\uba70, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4. \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\ub294 \ub0ae\uc740 \ud3b8\uc785\ub2c8\ub2e4.<\/p>\n<p># \uc2dc\uc7a5 \ubd84\uc11d \ubc0f \uc8fc\uc694 \ub3d9\uc778<\/p>\n<p>\ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc0b0\uc5c5\uc740 \uc18c\ud615 \uac04\uc12d RNA(siRNA), \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO), \ub9c8\uc774\ud06c\ub85c RNA(miRNA) \ub4f1 \ub2e4\uc591\ud55c \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc758 \ubc1c\uc804\uacfc \ud568\uaed8 \uae09\uaca9\ud55c \uae30\uc220 \uc9c4\ud654\ub97c \uacaa\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud604\uc7ac \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uc57d 400\uac1c\uc758 RNA \uce58\ub8cc\uc81c \ud504\ub85c\uc81d\ud2b8\uac00 \ub2e4\uc591\ud55c \ub2e8\uacc4\uc5d0 \uc788\uc73c\uba70, \ud2b9\ud788 \uc804\ub2ec \uba54\ucee4\ub2c8\uc998 \uac1c\uc120\uacfc \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c\uc758 \uc548\uc815\uc131 \ud5a5\uc0c1\uc5d0 \uc911\uc810\uc744 \ub450\uc5b4 \ud6a8\ub2a5\uc744 \ub192\uc774\uace0 \ubd80\uc791\uc6a9\uc744 \uc904\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uae30\uc220 \ubc1c\uc804\uc740 \uc9c8\ubcd1 \uc720\ubc1c \uc720\uc804\uc790\uc758 \ubcf4\ub2e4 \uc815\ubc00\ud55c \ud45c\uc801\ud654\ub97c \uac00\ub2a5\ud558\uac8c \ud558\uba70 \uc720\uc804 \uc758\ud559\uc758 \uc7a0\uc7ac\uc801 \uc751\uc6a9 \ubd84\uc57c\ub97c \ud655\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc740 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc5d0 \ub300\ud55c \uc2e0\ub8b0 \uc99d\uac00\ub97c \ubc18\uc601\ud558\uc5ec \uc0c1\ub2f9\ud55c \ud22c\uc790 \ud65c\ub3d9\uacfc \uc804\ub7b5\uc801 \ud30c\ud2b8\ub108\uc2ed\uc744 \ubaa9\uaca9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc77c\ub840\ub85c Agilent Technologies\ub294 2023\ub144 1\uc6d4 \uce58\ub8cc\uc6a9 \ud575\uc0b0 \uc81c\uc870 \uc5ed\ub7c9\uc744 \ub450 \ubc30\ub85c \ub298\ub9ac\uae30 \uc704\ud574 7\uc5b5 2,500\ub9cc \ub2ec\ub7ec\ub97c \ud22c\uc790\ud588\uc73c\uba70, 2023\ub144 2\uc6d4\uc5d0\ub294 CMT Research Foundation\uacfc Nanite Inc.\uac00 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc \uce58\ub8cc\uc81c\uc758 \uce58\ub8cc \ud6a8\ub2a5 \uac15\ud654\ub97c \uc704\ud55c \ud30c\ud2b8\ub108\uc2ed\uc744 \uccb4\uacb0\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9 \ub610\ud55c \ud65c\ubc1c\ud558\uba70, \uce58\ub8cc \uc751\uc6a9 \ubd84\uc57c \ud655\uc7a5 \ubc0f \uc804\ub2ec \uba54\ucee4\ub2c8\uc998 \uac1c\uc120\uc5d0 \ucd08\uc810\uc744 \ub9de\ucd94\uace0 \uc788\uc2b5\ub2c8\ub2e4. Switch Therapeutics\uac00 2023\ub144 3\uc6d4 \uc2dc\ub9ac\uc988 A \uc790\uae08\uc73c\ub85c 5,200\ub9cc \ub2ec\ub7ec\ub97c \uc131\uacf5\uc801\uc73c\ub85c \uc720\uce58\ud55c \uac83\uc740 \ud601\uc2e0\uc801\uc778 RNAi \uce58\ub8cc \uae30\uc220 \uac1c\ubc1c\uc5d0 \ub300\ud55c \ud22c\uc790\uc790\ub4e4\uc758 \ub192\uc740 \uad00\uc2ec\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<\/p>\n<p>\uc81c\uc870 \uc5ed\ub7c9 \ubc0f \uc0dd\uc0b0 \uc778\ud504\ub77c\ub3c4 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc99d\uac00\ud558\ub294 \uc218\uc694\ub97c \ucda9\uc871\uc2dc\ud0a4\uae30 \uc704\ud574 \ubc1c\uc804\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uae30\uc5c5\ub4e4\uc740 \uc81c\uc870 \uc2dc\uc124 \ud655\uc7a5\uc5d0 \ub9c9\ub300\ud55c \ud22c\uc790\ub97c \ud558\uace0 \uc788\uc73c\uba70, \uc77c\uad00\ub41c \ud488\uc9c8\uacfc \uaddc\ubaa8 \ud655\uc7a5 \uc5ed\ub7c9\uc744 \ubcf4\uc7a5\ud558\uae30 \uc704\ud574 \ucca8\ub2e8 \uc0dd\uc0b0 \uae30\uc220\uc744 \ub3c4\uc785\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud6a8\uc728\uc801\uc774\uace0 \ube44\uc6a9 \ud6a8\uc728\uc801\uc778 \uc0dd\uc0b0 \ubc29\uc2dd\uc73c\ub85c\uc758 \uc804\ud658\uc774 \uc774\ub8e8\uc5b4\uc9c0\uace0 \uc788\uc73c\uba70, \uc790\ub3d9\ud654\ub41c \uc81c\uc870 \uacf5\uc815 \uac1c\ubc1c \ubc0f \ud488\uc9c8 \uad00\ub9ac \uc870\uce58 \uad6c\ud604\uc5d0 \ub300\ud55c \uad00\uc2ec\uc774 \ub192\uc544\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># \uc8fc\uc694 \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30\ub825<\/p>\n<p>1.  \uc720\uc804 \uc9c8\ud658 \uc720\ubcd1\ub960 \uc99d\uac00: \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uc720\uc804 \uc9c8\ud658\uc758 \ubd80\ub2f4\uc774 \uc99d\uac00\ud558\uba74\uc11c \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c\uc5d0 \ub300\ud55c \uc0c1\ub2f9\ud55c \uc218\uc694\uac00 \ubc1c\uc0dd\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. 2022\ub144 8\uc6d4 \ub370\uc774\ud130\uc5d0 \ub530\ub974\uba74 \uc0ac\ud558\ub77c \uc774\ub0a8 \uc544\ud504\ub9ac\uce74\uc5d0\uc11c\ub294 \ub9e4\ub144 \uc57d 23\ub9cc 6\ucc9c \uba85\uc758 \uc544\uae30\uac00 \uacb8\uc0c1 \uc801\ud608\uad6c \ube48\ud608\uc99d(SCD)\uc744 \uac00\uc9c0\uace0 \ud0dc\uc5b4\ub098\uba70, \uc774\ub294 \ubbf8\uad6d\ubcf4\ub2e4 80\ubc30 \uc774\uc0c1 \ub9ce\uc740 \uc218\uce58\uc785\ub2c8\ub2e4. \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d(CF) \ub610\ud55c 2022\ub144 \uae30\uc900 \ubbf8\uad6d\uc5d0\uc11c\ub9cc \uc57d 4\ub9cc \uba85, \uc804 \uc138\uacc4 94\uac1c\uad6d\uc5d0\uc11c \uc57d 10\ub9cc 5\ucc9c \uba85\uc774 \uc9c4\ub2e8\ubc1b\uc740 \uac00\uc7a5 \ud754\ud55c \uc720\uc804 \uc9c8\ud658 \uc911 \ud558\ub098\uc785\ub2c8\ub2e4. \ub2e4\uc6b4 \uc99d\ud6c4\uad70(DS) \ubc0f \uc120\ucc9c\uc131 \uc2ec\uc7a5 \uacb0\ud568(CHD)\uacfc \uac19\uc740 \ub2e4\ub978 \uc720\uc804 \uc9c8\ud658\uc758 \uc720\ubcd1\ub960 \uc99d\uac00\ub3c4 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc758 \ud544\uc694\uc131\uc744 \uac15\uc870\ud569\ub2c8\ub2e4.<\/p>\n<p>2.  \ud5ec\uc2a4\ucf00\uc5b4 \ubd80\ubb38 \ud22c\uc790 \uc99d\uac00: \ud5ec\uc2a4\ucf00\uc5b4 \ubd80\ubb38\uc740 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc5f0\uad6c \uac1c\ubc1c\uc5d0 \uc0c1\ub2f9\ud55c \ud22c\uc790\ub97c \uc720\uce58\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. 2023\ub144 3\uc6d4 Myeloid Therapeutics\ub294 \ub274\uc0ac\uc6b0\uc2a4\uc6e8\uc77c\uc2a4(NSW) \uc8fc \uc815\ubd80\uc758 9,600\ub9cc \ud638\uc8fc \ub2ec\ub7ec(\uc57d 6,570\ub9cc \ub2ec\ub7ec) \uc9c0\uc6d0\uc744 \ubc1b\uc544 RNA \uce58\ub8cc\uc81c \uc0c1\uc6a9\ud654\ub97c \uac00\uc18d\ud654\ud558\uae30 \uc704\ud55c \uc0c8\ub85c\uc6b4 \uc81c\uc870 \uc2dc\uc124\uc744 \uc124\ub9bd\ud588\uc2b5\ub2c8\ub2e4. \ub610\ud55c 2023\ub144 1\uc6d4\uc5d0\ub294 Matthew Wood \uad50\uc218\uac00 \uc774\ub044\ub294 \ucee8\uc18c\uc2dc\uc5c4\uc774 UKRI, LifeArc, NATA\ub85c\ubd80\ud130 \ud575\uc0b0 \uce58\ub8cc \uc5f0\uad6c \ubc1c\uc804\uc744 \uc704\ud574 800\ub9cc \ud30c\uc6b4\ub4dc(\uc57d 981\ub9cc \ub2ec\ub7ec)\uc758 \uc790\uae08\uc744 \uc9c0\uc6d0\ubc1b\uc558\uc2b5\ub2c8\ub2e4. Generation Bio\uc640 Moderna\uc758 \ud30c\ud2b8\ub108\uc2ed, Agilent Technologies\uc758 7\uc5b5 2,500\ub9cc \ub2ec\ub7ec \ud22c\uc790, \ub0ad\ud3ec\uc131 \uc12c\uc720\uc99d \uc7ac\ub2e8\uc758 ReCode Therapeutics\uc5d0 \ub300\ud55c 1,500\ub9cc \ub2ec\ub7ec \ud22c\uc790 \ub4f1 \ubbfc\uac04 \ubd80\ubb38 \ud22c\uc790 \ubc0f \uc804\ub7b5\uc801 \ud611\ub825\ub3c4 \ud65c\ubc1c\ud569\ub2c8\ub2e4.<\/p>\n<p>3.  \uc81c\uc57d \uc0b0\uc5c5\uc758 \ud601\uc2e0\uc801\uc778 \ubc14\uc774\uc624 \uc758\uc57d\ud488\uc73c\ub85c\uc758 \ube60\ub978 \uc804\ud658: \uc81c\uc57d \uc0b0\uc5c5\uc740 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c\ub97c \ud3ec\ud568\ud55c \uc0dd\ubb3c\ud559\uc801 \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \uc9d1\uc911\uc774 \uc99d\uac00\ud558\uba74\uc11c \uc0c1\ub2f9\ud55c \ubcc0\ud654\ub97c \uacaa\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ubbf8\uad6d \ud654\ud559 \ud559\ud68c(American Chemical Society)\uc758 2021\ub144 4\uc6d4 \ubcf4\uace0\uc11c\uc5d0 \ub530\ub974\uba74, FDA \uc2b9\uc778\uc744 \ubc1b\uc740 \uce58\ub8cc\uc81c\ub294 7\uac1c\uc5d0 \ubd88\uacfc\ud558\uc9c0\ub9cc, \uc2e0\uc81c\ud488 \ud30c\uc774\ud504\ub77c\uc778\uc5d0\ub294 \uc57d 1,200\uac1c\uc758 \uc2e4\ud5d8\uc801 \uce58\ub8cc\ubc95\uc774 \uc788\uc73c\uba70, \uc808\ubc18 \uc774\uc0c1\uc774 2\uc0c1 \uc784\uc0c1 \uc2dc\ud5d8 \uc911\uc785\ub2c8\ub2e4. \uc774\ub294 \uae30\uc874 \uc57d\ubb3c\ubcf4\ub2e4 \ub354 \uc9c0\uc18d\uc801\uc778 \ud6a8\uacfc\ub97c \uc81c\uacf5\ud558\uace0 \ud604\uc7ac \uce58\ub8cc\ubc95\uc774 \uc5c6\ub294 \ud76c\uadc0 \uc9c8\ud658\uc744 \ud574\uacb0\ud560 \uc218 \uc788\ub294 \ubd84\uc790 \uce58\ub8cc\uc81c \ubc0f \uc720\uc804 \uc758\ud559\uacfc \uac19\uc740 \ud601\uc2e0\uc801\uc778 \uc0dd\ubb3c\ud559\uc801 \uc194\ub8e8\uc158 \uac1c\ubc1c\ub85c\uc758 \uc804\ub7b5\uc801 \uc804\ud658\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. Ausper Biopharma\uc758 \ub9cc\uc131 B\ud615 \uac04\uc5fc \uce58\ub8cc\uc81c \uc784\uc0c1 1\uc0c1 \uc9c4\ud589 \ubc0f Switch Therapeutics\uc758 RNAi \uacfc\ud559 \ubc1c\uc804\uc744 \uc704\ud55c 5,200\ub9cc \ub2ec\ub7ec \uc790\uae08 \uc720\uce58 \ub4f1\uc774 \uc774\ub7ec\ud55c \ucd94\uc138\ub97c \ub4b7\ubc1b\uce68\ud569\ub2c8\ub2e4.<\/p>\n<p># \uc138\uadf8\uba3c\ud2b8 \ubd84\uc11d<\/p>\n<p>1. \uc81c\ud488 \uc720\ud615\ubcc4:<br \/>\n*   \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO): 2024\ub144 \uc2dc\uc7a5 \uc810\uc720\uc728 \uc57d 71%\ub85c \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc744 \uc9c0\ubc30\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \ucc99\uc218\uc131 \uadfc\uc704\ucd95\uc99d, \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d \ub4f1 \ub2e4\uc591\ud55c \uc720\uc804 \uc9c8\ud658 \ubc0f \ud76c\uadc0 \uc9c8\ud658 \uce58\ub8cc\uc5d0 \ub300\ud55c \uc785\uc99d\ub41c \ud6a8\uacfc\uc640 \uc9c0\uc18d\uc801\uc778 \uae30\uc220 \ubc1c\uc804 \ub355\ubd84\uc785\ub2c8\ub2e4.<br \/>\n*   RNA \uac04\uc12d(RNAi) \ubc0f siRNA: 2024\ub144\ubd80\ud130 2029\ub144\uae4c\uc9c0 \uc57d 16%\uc758 \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. RNAi \uce58\ub8cc\uc81c \uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9 \uc99d\uac00, \ub2e4\uc591\ud55c \uc9c8\ubcd1 \uce58\ub8cc\uc5d0 \ub300\ud55c \uc0c8\ub85c\uc6b4 \uc751\uc6a9, \uc804\ub2ec \uc2dc\uc2a4\ud15c\uc758 \uae30\uc220 \ubc1c\uc804\uc774 \uc131\uc7a5\uc744 \uacac\uc778\ud569\ub2c8\ub2e4.<br \/>\n*   \uae30\ud0c0 \uc81c\ud488 \uc720\ud615: \ud63c\ud569 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc \ubc0f \uae30\ud0c0 \uc0c8\ub85c\uc6b4 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc \uc591\uc2dd\uc744 \ud3ec\ud568\ud558\uba70, \ud2b9\uc815 \uce58\ub8cc \uacfc\uc81c\ub97c \ud574\uacb0\ud558\uace0 \uae30\uc874 \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \ubcf4\uc644 \uc194\ub8e8\uc158\uc744 \uc81c\uacf5\ud560 \uc7a0\uc7ac\ub825\uc73c\ub85c \uc8fc\ubaa9\ubc1b\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>2. \uc751\uc6a9 \ubd84\uc57c\ubcc4:<br \/>\n*   \uc720\uc804 \uc9c8\ud658: 2024\ub144 \uc804\uccb4 \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 \uc57d 89%\ub97c \ucc28\uc9c0\ud558\uba70 \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc744 \uacc4\uc18d \uc9c0\ubc30\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ucc99\uc218\uc131 \uadfc\uc704\ucd95\uc99d, \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d, \uc9c0\uc911\ud574\ube48\ud608, \ud5cc\ud305\ud134\ubcd1 \ub4f1 \ub2e4\uc591\ud55c \uc720\uc804 \uc9c8\ud658\uc758 \uc720\ubcd1\ub960 \uc99d\uac00\uc640 \uc720\uc804\uc790 \uc5b5\uc81c, \ucd94\uac00, \ub300\uccb4 \ub610\ub294 \ud3b8\uc9d1 \uba54\ucee4\ub2c8\uc998\uc744 \ud1b5\ud55c \uce58\ub8cc \ud6a8\uacfc\uac00 \uc8fc\uc694 \ub3d9\uc778\uc785\ub2c8\ub2e4.<br \/>\n*   \uac10\uc5fc\uc131 \uc9c8\ud658: 2024\ub144\ubd80\ud130 2029\ub144\uae4c\uc9c0 \uc57d 94%\uc758 \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. B\ud615 \uac04\uc5fc \ubc0f \uc2e0\uc885 \ubc14\uc774\ub7ec\uc2a4 \uc704\ud611\uc5d0 \ub300\ud55c RNA \uae30\ubc18 \uce58\ub8cc\uc81c \uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9 \uc99d\uac00\uc640 RNA \uae30\uc220\uc758 \uc131\uacf5\uc801\uc778 \uc801\uc6a9\uc774 \uc131\uc7a5\uc744 \uac00\uc18d\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uae30\ud0c0 \uc751\uc6a9 \ubd84\uc57c: \uc790\uac00\uba74\uc5ed \uc9c8\ud658, \uc554, \uc2ec\ud608\uad00 \uc9c8\ud658 \ubc0f \ub300\uc0ac \uc7a5\uc560 \ub4f1\uc744 \ud3ec\ud568\ud558\uba70, RNA \uac04\uc12d \uba54\ucee4\ub2c8\uc998 \ubc0f \ud45c\uc801 \uc720\uc804\uc790 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc5d0 \ub300\ud55c \uc5f0\uad6c\uac00 \ud65c\ubc1c\ud788 \uc9c4\ud589\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>3. \ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4:<br \/>\n*   \ubcd1\uc6d0 \ubc0f \ud074\ub9ac\ub2c9: 2024\ub144 \uc2dc\uc7a5 \uc810\uc720\uc728 \uc57d 55%\ub85c \ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc744 \uc9c0\ubc30\ud558\uba70, 2024\ub144\ubd80\ud130 2029\ub144\uae4c\uc9c0 \uc57d 15%\uc758 \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc720\uc804\ud559\uc790, \uc885\uc591\ud559\uc790, \uac10\uc5fc\ubcd1 \uc804\ubb38\uac00 \ub4f1 \uc804\ubb38 \uc758\ub8cc\ud300\uc758 \uc874\uc7ac, \uc815\uad50\ud55c \uc778\ud504\ub77c \ubc0f \uc7a5\ube44, \uc784\uc0c1 \uc2dc\ud5d8 \uc218\ud589 \uc5ed\ud560\uc774 \uc8fc\uc694 \uc694\uc778\uc785\ub2c8\ub2e4.<br \/>\n*   \ud559\uc220 \ubc0f \uc5f0\uad6c \uae30\uad00: \ud68d\uae30\uc801\uc778 \uc5f0\uad6c \uac1c\ubc1c \ud65c\ub3d9\uc744 \ud1b5\ud574 \ud575\uc0b0 \uce58\ub8cc\uc81c \ubd84\uc57c \ubc1c\uc804\uc5d0 \uc911\uc694\ud55c \uc5ed\ud560\uc744 \ud569\ub2c8\ub2e4. \uc0c8\ub85c\uc6b4 \uc751\uc6a9 \ubd84\uc57c \uc870\uc0ac, \uc548\uc804\ud558\uace0 \ud6a8\uacfc\uc801\uc778 \uc804\ub2ec \uc2dc\uc2a4\ud15c \uac1c\ubc1c, \uc0b0\uc5c5 \ud30c\ud2b8\ub108\uc640\uc758 \ud611\ub825, \ucc28\uc138\ub300 \uacfc\ud559\uc790 \ubc0f \uc784\uc0c1\uc758 \uc591\uc131\uc5d0 \uae30\uc5ec\ud569\ub2c8\ub2e4.<\/p>\n<p># \uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \ubd84\uc11d<\/p>\n<p>*   \ubd81\ubbf8: \uc120\uc9c4 \uc758\ub8cc \uc778\ud504\ub77c\uc640 \ud65c\ubc1c\ud55c \uc5f0\uad6c \ud65c\ub3d9\uc5d0 \ud798\uc785\uc5b4 \uac15\ub825\ud55c \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \ubcf4\uc785\ub2c8\ub2e4. \ubbf8\uad6d\uc774 \uc9c0\uc5ed \uc2dc\uc7a5\uc758 \uc57d 86%\ub97c \ucc28\uc9c0\ud558\uba70 \uc9c0\ubc30\uc801\uc778 \uc704\uce58\uc5d0 \uc788\uc73c\uba70, 2024\ub144\ubd80\ud130 2029\ub144\uae4c\uc9c0 \uc57d 15%\uc758 CAGR\ub85c \uc131\uc7a5\uc744 \uc720\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774\ub294 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc\ubc95 \uac1c\ubc1c, \uad11\ubc94\uc704\ud55c \uc5f0\uad6c \ud65c\ub3d9, \uc720\uc804 \uc9c8\ud658 \uc720\ubcd1\ub960 \uc99d\uac00, \uc815\ubc00 \uc758\ud559 \ucc44\ud0dd \uc99d\uac00\uc5d0 \uae30\uc778\ud569\ub2c8\ub2e4.<br \/>\n*   \uc720\ub7fd: \ub3c5\uc77c, \uc601\uad6d, \ud504\ub791\uc2a4, \uc774\ud0c8\ub9ac\uc544, \uc2a4\ud398\uc778\uc774 \uc8fc\uc694 \uae30\uc5ec\uad6d\uc774\uba70, \uac15\ub825\ud55c \uc5f0\uad6c \uc778\ud504\ub77c, \uc0dd\uba85\uacf5\ud559 \ud22c\uc790 \uc99d\uac00, \uc9c0\uc6d0\uc801\uc778 \uc758\ub8cc \uc815\ucc45\uc73c\ub85c \uc0c1\ub2f9\ud55c \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ub3c5\uc77c\uc740 \uc720\ub7fd \uc2dc\uc7a5\uc758 \uc57d 22%\ub97c \ucc28\uc9c0\ud558\ub294 \uac00\uc7a5 \ud070 \uc2dc\uc7a5\uc774\uba70, 2024\ub144\ubd80\ud130 2029\ub144\uae4c\uc9c0 \uc57d 16%\uc758 CAGR\ub85c \uc131\uc7a5\uc744 \uc9c0\uc18d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<br \/>\n*   \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591: \uc911\uad6d, \uc77c\ubcf8, \uc778\ub3c4, \ud638\uc8fc, \ud55c\uad6d\uc744 \ud3ec\ud568\ud558\uba70, \ud5ec\uc2a4\ucf00\uc5b4 \ud22c\uc790 \uc99d\uac00, \uc5f0\uad6c \uc5ed\ub7c9 \uac15\ud654, \ud601\uc2e0\uc801\uc778 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc5d0 \ub300\ud55c \uad00\uc2ec \uc99d\ub300\ub85c \uc0c1\ub2f9\ud55c \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \uc911\uad6d\uc774 \uc9c0\uc5ed \uc2dc\uc7a5\uc744 \uc120\ub3c4\ud558\uba70, \uc778\ub3c4\ub294 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc73c\ub85c \ubd80\uc0c1\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74: GCC \uad6d\uac00\uc640 \ub0a8\uc544\ud504\ub9ac\uce74\uac00 \uc8fc\uc694 \uc2dc\uc7a5\uc774\uba70, \ud5ec\uc2a4\ucf00\uc5b4 \uc778\ud504\ub77c \ud22c\uc790 \uc99d\uac00\uc640 \ucca8\ub2e8 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc5d0 \ub300\ud55c \uad00\uc2ec \uc99d\ub300\ub85c \uc720\ub9dd\ud55c \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \ubcf4\uc785\ub2c8\ub2e4. GCC\ub294 \uc774 \uc9c0\uc5ed\uc5d0\uc11c \uac00\uc7a5 \ud06c\uace0 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc785\ub2c8\ub2e4.<br \/>\n*   \ub0a8\ubbf8: \ube0c\ub77c\uc9c8\uacfc \uc544\ub974\ud5e8\ud2f0\ub098\uac00 \uc8fc\uc694 \uae30\uc5ec\uad6d\uc774\uba70, \ud5ec\uc2a4\ucf00\uc5b4 \uc778\ud504\ub77c \ud22c\uc790 \uc99d\uac00\uc640 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\uc5d0 \ub300\ud55c \uad00\uc2ec \uc99d\ub300\ub85c \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ube0c\ub77c\uc9c8\uc740 \uc774 \uc9c0\uc5ed\uc5d0\uc11c \uac00\uc7a5 \ud06c\uace0 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc785\ub2c8\ub2e4.<\/p>\n<p># \uacbd\uc7c1 \ud658\uacbd<\/p>\n<p>\ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 Ionis Pharmaceuticals, Biogen, Moderna, Novartis, Alnylam Pharmaceuticals, Sarepta Therapeutics\uc640 \uac19\uc740 \ud655\uace0\ud55c \uae30\uc5c5\ub4e4\uc774 \uc874\uc7ac\ud558\uba70 \ube44\uad50\uc801 \ud1b5\ud569\ub41c \uad6c\uc870\ub97c \ubcf4\uc785\ub2c8\ub2e4. \uc774\ub4e4 \uae30\uc5c5\uc740 \uc81c\ud488 \ud3ec\ud2b8\ud3f4\ub9ac\uc624 \ud655\uc7a5\uc744 \uc704\ud574 R&#038;D\uc5d0 \ub9c9\ub300\ud55c \ud22c\uc790\ub97c \ud558\uace0 \uc788\uc73c\uba70, \ud2b9\ud788 \ud601\uc2e0\uc801\uc778 \ubc14\uc774\uc624 \uc758\uc57d\ud488 \ubc0f RNA \uce58\ub8cc \uae30\uc220\uc5d0 \uc911\uc810\uc744 \ub461\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc740 \uc0c1\ub2f9\ud55c \uc790\ubcf8 \uc694\uad6c \uc0ac\ud56d, \ubcf5\uc7a1\ud55c \uaddc\uc81c \ud504\ub808\uc784\uc6cc\ud06c, \uc804\ubb38 \uae30\uc220 \ud544\uc694\uc131\uc73c\ub85c \uc778\ud574 \uc9c4\uc785 \uc7a5\ubcbd\uc774 \ub192\uc2b5\ub2c8\ub2e4. \uc778\uc218\ud569\ubcd1 \ud65c\ub3d9\uc774 \ud65c\ubc1c\ud558\uba70, \ub300\uae30\uc5c5\ub4e4\uc740 \uc720\ub9dd\ud55c \uc18c\uaddc\ubaa8 \uc0dd\uba85\uacf5\ud559 \uae30\uc5c5\uc744 \uc778\uc218\ud558\uc5ec \uae30\uc220 \uc5ed\ub7c9\uc744 \uac15\ud654\ud558\uace0 \uc81c\ud488 \ud30c\uc774\ud504\ub77c\uc778\uc744 \ud655\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774 \uc2dc\uc7a5\uc5d0\uc11c\uc758 \uc131\uacf5\uc740 \ud601\uc2e0\uc801\uc778 \uc804\ub2ec \uc2dc\uc2a4\ud15c \uac1c\ubc1c, \uac15\ub825\ud55c \uc5f0\uad6c \ud30c\uc774\ud504\ub77c\uc778 \uc720\uc9c0, \uc804\ub7b5\uc801 \ud30c\ud2b8\ub108\uc2ed \uad6c\ucd95 \ub2a5\ub825\uc5d0 \ub2ec\ub824 \uc788\uc2b5\ub2c8\ub2e4. \uae30\uc874 \uae30\uc5c5\ub4e4\uc740 \ub0b4\ubd80 \uac1c\ubc1c \ub610\ub294 \uc804\ub7b5\uc801 \uc778\uc218\ub97c \ud1b5\ud574 \uae30\uc220 \uc5ed\ub7c9\uc744 \ud655\uc7a5\ud558\uace0, \ud5ec\uc2a4\ucf00\uc5b4 \uc81c\uacf5\uc5c5\uccb4 \ubc0f \uc5f0\uad6c \uae30\uad00\uacfc\uc758 \uac15\ub825\ud55c \uad00\uacc4\ub97c \uad6c\ucd95\ud574\uc57c \ud569\ub2c8\ub2e4. \uc2e0\uaddc \uc9c4\uc785\uc790 \ubc0f \uc18c\uaddc\ubaa8 \uae30\uc5c5\uc758 \uacbd\uc6b0, \ud2b9\uc815 \uce58\ub8cc \ubd84\uc57c \ub610\ub294 \uc804\ub2ec \uae30\uc220\uc5d0 \ub300\ud55c \uc804\ubb38 \uc9c0\uc2dd \uac1c\ubc1c, \uac15\ub825\ud55c \uc9c0\uc801 \uc7ac\uc0b0\uad8c \ud3ec\ud2b8\ud3f4\ub9ac\uc624 \uad6c\ucd95, \ub300\ud615 \uc81c\uc57d \ud68c\uc0ac\uc640\uc758 \uc804\ub7b5\uc801 \uc81c\ud734\uac00 \uc911\uc694\ud569\ub2c8\ub2e4. CRISPR \uce58\ub8cc\uc81c \ubc0f \uc720\uc804 \uc758\ud559\uc758 \ud1b5\ud569\uc740 \uc0c1\ub2f9\ud55c \uacbd\uc7c1 \uc6b0\uc704\ub97c \uc81c\uacf5\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc0b0\uc5c5 \ub9ac\ub354\ub85c\ub294 Silence Therapeutics plc, Ionis Pharmaceuticals, Inc., Novartis Pharma AG, Sarepta Therapeutics, Inc., Alnylam Pharmaceuticals, Inc. \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># \ucd5c\uadfc \uc0b0\uc5c5 \ub3d9\ud5a5<\/p>\n<p>*   2023\ub144 3\uc6d4, Ionis Pharmaceutical\uc740 SOD1-ALS \uce58\ub8cc\uc81c \ud1a0\ud37c\uc13c(Tofersen)\uc758 \uac00\uc18d \uc2b9\uc778 \uac00\ub2a5\uc131\uc5d0 \ub300\ud574 \ubbf8\uad6d \uc2dd\ud488\uc758\uc57d\uad6d(FDA) \uc790\ubb38\uc704\uc6d0\ud68c\ub85c\ubd80\ud130 \ub9cc\uc7a5\uc77c\uce58 \ucc2c\uc131\ud45c\ub97c \ubc1b\uc558\uc2b5\ub2c8\ub2e4. \ud1a0\ud37c\uc13c\uc740 SOD1 \uba54\uc2e0\uc800 RNA \ubd84\ud574\ub97c \ub9e4\uac1c\ud558\uc5ec SOD1 \ub2e8\ubc31\uc9c8 \ud569\uc131\uc744 \uac10\uc18c\uc2dc\ud0a4\ub294 \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc\uc785\ub2c8\ub2e4.<br \/>\n*   2023\ub144 2\uc6d4, Myeloid Therapeutics Inc.\ub294 \ud638\uc8fc \ub274\uc0ac\uc6b0\uc2a4\uc6e8\uc77c\uc2a4(NSW) \uc8fc \uc815\ubd80\uc640 \ud611\ub825\ud558\uc5ec RNA \uba74\uc5ed \uce58\ub8cc\uc81c\uc5d0 \uc911\uc810\uc744 \ub454 \ucd5c\ucca8\ub2e8 GMP \uc81c\uc870 \uc2dc\uc124\uc744 \uac1c\ubc1c\ud558\uae30\ub85c \ud588\uc2b5\ub2c8\ub2e4. \uc774 \uc2dc\uc124\uc740 Myeloid\uc758 RNA \uce58\ub8cc\uc81c \uc0c1\uc6a9\ud654\ub97c \uac00\uc18d\ud654\ud558\uace0 NSW\uc5d0 RNA \uc0dd\ud0dc\uacc4\ub97c \uad6c\ucd95\ud558\ub294 \ub370 \uae30\uc5ec\ud560 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\ud575\uc0b0 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \ubcf4\uace0\uc11c\ub294 \ub2e4\uc591\ud55c \uc9c8\ubcd1 \uce58\ub8cc\ub97c \uc704\ud574 \ud575\uc0b0 \ub610\ub294 \uad00\ub828 \ud654\ud559 \ud654\ud569\ubb3c\uc744 \uae30\ubc18\uc73c\ub85c \ud558\ub294 \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \uc2ec\uce35 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \uc774 \uce58\ub8cc\uc81c\ub294 \ud2b9\uc815 \uc720\uc804\uc790\uc758 \uae30\ub2a5\uc744 \uc815\ubc00\ud558\uac8c \uc5b5\uc81c\ud558\uc5ec \uc9c8\ubcd1\uc744 \uce58\ub8cc\ud558\ub294 \ub370 \uc0ac\uc6a9\ub418\uba70, \uc544\ud504\ud0c0\uba38, \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO), \uc9e7\uc740 \uac04\uc12d RNA(siRNA) \ub4f1\uc744 \ud3ec\ud568\ud569\ub2c8\ub2e4. ASO\uc640 siRNA\ub294 mRNA\uc758 \ub2e8\ubc31\uc9c8 \ubc88\uc5ed \ubc0f \ud575 DNA\uc758 mRNA \uc804\uc0ac\ub97c \ubc29\ud574\ud558\uc5ec \uc720\uc804\uc790\ub97c \ud6a8\uacfc\uc801\uc73c\ub85c \uce68\ubb35\uc2dc\ud0a4\uc9c0\ub9cc, \uc720\uc804\uc790\ub97c \ubcc0\ud615\uc2dc\ud0a4\uc9c0\ub294 \uc54a\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \uc2dc\uc7a5\uc740 2024\ub144 54.8\uc5b5 \ub2ec\ub7ec \uaddc\ubaa8\ub85c \ucd94\uc815\ub418\uba70, 2025\ub144\uc5d0\ub294 63.9\uc5b5 \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774\ud6c4 2030\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 14.29%\ub97c \uae30\ub85d\ud558\uba70 124.6\uc5b5 \ub2ec\ub7ec \uaddc\ubaa8\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \ub3d9\uc778\uc73c\ub85c\ub294 \uc720\uc804 \uc9c8\ud658\uc758 \uc720\ubcd1\ub960 \uc99d\uac00, \ud5ec\uc2a4\ucf00\uc5b4 \ubd80\ubb38\uc5d0 \ub300\ud55c \ud22c\uc790 \ud655\ub300, \uc81c\uc57d \uc0b0\uc5c5\uc758 \ud601\uc2e0\uc801\uc778 \ubc14\uc774\uc624 \uc758\uc57d\ud488\uc73c\ub85c\uc758 \ube60\ub978 \uc804\ud658\uc774 \uc788\uc2b5\ub2c8\ub2e4. \ubc18\uba74, \ud575\uc0b0 \uc5f0\uad6c\uc758 \ub192\uc740 \ube44\uc6a9\uc740 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc8fc\uc694 \uc694\uc778\uc73c\ub85c \uc791\uc6a9\ud569\ub2c8\ub2e4. \ubcf4\uace0\uc11c\ub294 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d(\uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611, \uad6c\ub9e4\uc790\/\uc18c\ube44\uc790\uc758 \uad50\uc12d\ub825, \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825, \ub300\uccb4 \uc81c\ud488\uc758 \uc704\ud611, \uacbd\uc7c1 \uac15\ub3c4)\uc744 \ud1b5\ud574 \uc2dc\uc7a5\uc758 \uacbd\uc7c1 \ud658\uacbd\uc744 \uc2ec\uce35\uc801\uc73c\ub85c \ud3c9\uac00\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc740 \uc81c\ud488 \uc720\ud615, \uc801\uc6a9 \ubd84\uc57c, \ucd5c\uc885 \uc0ac\uc6a9\uc790 \ubc0f \uc9c0\uc5ed\ubcc4\ub85c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4.<br \/>\n\uc81c\ud488 \uc720\ud615\ubcc4\ub85c\ub294 RNA \uac04\uc12d(RNAi) \ubc0f \uc9e7\uc740 \uac04\uc12d RNA(siRNA), \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO), \uae30\ud0c0 \uc81c\ud488 \uc720\ud615\uc73c\ub85c \ub098\ub269\ub2c8\ub2e4.<br \/>\n\uc801\uc6a9 \ubd84\uc57c\ubcc4\ub85c\ub294 \uc790\uac00\uba74\uc5ed \uc9c8\ud658, \uac10\uc5fc\uc131 \uc9c8\ud658, \uc720\uc804 \uc9c8\ud658, \uc554, \uae30\ud0c0 \uc801\uc6a9 \ubd84\uc57c\ub97c \ud3ec\ud568\ud569\ub2c8\ub2e4.<br \/>\n\ucd5c\uc885 \uc0ac\uc6a9\uc790\ubcc4\ub85c\ub294 \ubcd1\uc6d0 \ubc0f \ud074\ub9ac\ub2c9, \ud559\uc220 \ubc0f \uc5f0\uad6c \uae30\uad00\uc73c\ub85c \uad6c\ubd84\ub429\ub2c8\ub2e4.<br \/>\n\uc9c0\uc5ed\ubcc4\ub85c\ub294 \ubd81\ubbf8, \uc720\ub7fd, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8\ub85c \uad11\ubc94\uc704\ud558\uac8c \ubd84\ub958\ub418\uba70, \uc8fc\uc694 \uae00\ub85c\ubc8c \uc9c0\uc5ed \ub0b4 17\uac1c\uad6d\uc5d0 \ub300\ud55c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \ub3d9\ud5a5\uc744 \ub2e4\ub8f9\ub2c8\ub2e4. \ud2b9\ud788, \ubd81\ubbf8\ub294 2025\ub144 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \uc608\uce21 \uae30\uac04(2025-2030\ub144) \ub3d9\uc548 \uac00\uc7a5 \ub192\uc740 CAGR\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc2dc\uc7a5 \ucc38\uc5ec\uc790\ub85c\ub294 Silence Therapeutics plc, Ionis Pharmaceuticals, Inc., Novartis Pharma AG, Sarepta Therapeutics, Inc., Alnylam Pharmaceuticals, Inc. \ub4f1\uc774 \uc788\uc73c\uba70, \uc774\ub4e4 \uae30\uc5c5\uc758 \ube44\uc988\ub2c8\uc2a4 \uac1c\uc694, \uc7ac\ubb34, \uc81c\ud488 \ubc0f \uc804\ub7b5, \ucd5c\uadfc \uac1c\ubc1c \ub3d9\ud5a5 \ub4f1\uc774 \ubcf4\uace0\uc11c\uc5d0 \ud3ec\ud568\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \ub610\ud55c \uc2dc\uc7a5 \uae30\ud68c\uc640 \ubbf8\ub798 \ub3d9\ud5a5\uc5d0 \ub300\ud55c \ubd84\uc11d\uc744 \uc81c\uacf5\ud558\uc5ec, \uc2dc\uc7a5 \ucc38\uc5ec\uc790\ub4e4\uc774 \uc804\ub7b5\uc801 \uc758\uc0ac\uacb0\uc815\uc744 \ub0b4\ub9b4 \uc218 \uc788\ub3c4\ub85d \uc9c0\uc6d0\ud569\ub2c8\ub2e4. \ubcf4\uace0\uc11c\ub294 2019\ub144\ubd80\ud130 2024\ub144\uae4c\uc9c0\uc758 \uacfc\uac70 \uc2dc\uc7a5 \uaddc\ubaa8\uc640 2025\ub144\ubd80\ud130 2030\ub144\uae4c\uc9c0\uc758 \uc608\uce21 \uc2dc\uc7a5 \uaddc\ubaa8\ub97c \ud3ec\ud568\ud558\uc5ec \ud3ec\uad04\uc801\uc778 \uc2dc\uc7a5 \uc815\ubcf4\ub97c \uc81c\uacf5\ud569\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-42027","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/42027"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=42027"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/42027\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=42027"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=42027"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=42027"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}