{"id":43881,"date":"2026-02-14T20:37:41","date_gmt":"2026-02-14T20:37:41","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/huntingtons-disease-treatment-mordor\/"},"modified":"2026-03-27T02:02:52","modified_gmt":"2026-03-26T17:02:52","slug":"huntingtons-disease-treatment-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/huntingtons-disease-treatment-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2026-2031\ub144)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/huntingtons-disease-therapy_1646747014936_Market_Players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/huntingtons-disease-treatment-size-image-1767809148329.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 &amp; \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 \uace0\ub839\uce35 \uc778\uad6c \ub0b4 \ubc1c\ubcd1\ub960 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 HTT \uc800\ud558 \uc784\uc0c1 \ud30c\uc774\ud504\ub77c\uc778 \ud601\uc2e0 \uac00\uc18d\ud654<\/li>\n<li class=\"toc-level-3\">4.2.3 \uc544\uc2dc\uc544 \uc9c0\uc5ed\uc5d0\uc11c 1\uc77c 1\ud68c VMAT2 \uc5b5\uc81c\uc81c \uc0c1\uc5c5\uc801 \ucd9c\uc2dc<\/li>\n<li class=\"toc-level-3\">4.2.4 \ubbf8\uad6d\/EU \ub0b4 \uc2e0\uc18d \uc2ec\uc0ac &amp; \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815<\/li>\n<li class=\"toc-level-3\">4.2.5 AI \uae30\ubc18 \ubc14\uc774\uc624\ub9c8\ucee4 \ubc1c\uacac\uc744 \ud1b5\ud55c \uc784\uc0c1 \uc131\uacf5\ub960 \ud5a5\uc0c1<\/li>\n<li class=\"toc-level-3\">4.2.6 \ubca0\ud0c0 \ucc28\ub2e8\uc81c \uc6a9\ub3c4 \ubcc0\uacbd\uc744 \ud1b5\ud55c \uc9c8\ubcd1 \uc870\uc808 \uc2e0\ud638 \ud655\uc778<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778\n<ul>\n<li class=\"toc-level-3\">4.3.1 \uc720\uc804\uc790 &amp; \uc138\ud3ec \uce58\ub8cc\uc81c\uc758 \ucd08\uace0\uac00 \ube44\uc6a9<\/li>\n<li class=\"toc-level-3\">4.3.2 \ubd81\ubbf8 &amp; EU \uc678 \uc9c0\uc5ed\uc758 \uc81c\ud55c\uc801\uc778 \uc804\ubb38 \uc13c\ud130<\/li>\n<li class=\"toc-level-3\">4.3.3 \uc99d\uc0c1 \uc644\ud654 \ub2e4\uc911 \uc57d\ubb3c \uc694\ubc95\uc5d0 \ub300\ud55c \ubd88\ucda9\ubd84\ud55c \uc21c\uc751\ub3c4<\/li>\n<li class=\"toc-level-3\">4.3.4 \uc2e0\uacbd \uc870\uc9c1 \ub0b4 CRISPR\uc5d0 \ub300\ud55c \ub370\uc774\ud130 \uc548\uc804\uc131 \uc6b0\ub824<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778\n<ul>\n<li class=\"toc-level-3\">4.4.1 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.2 \uad6c\ub9e4\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.3 \uacf5\uae09\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.4.4 \ub300\uccb4\uc7ac\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.4.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 &amp; \uc131\uc7a5 \uc608\uce21 (\uac00\uce58, USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uce58\ub8cc \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \uc99d\uc0c1 \uce58\ub8cc<\/li>\n<li class=\"toc-level-4\">5.1.1.1 VMAT2 \uc5b5\uc81c\uc81c<\/li>\n<li class=\"toc-level-4\">5.1.1.2 \ud56d\ub3c4\ud30c\ubbfc\uc131 \uc57d\ubb3c (\ud56d\uc815\uc2e0\ubcd1 \uc57d\ubb3c)<\/li>\n<li class=\"toc-level-4\">5.1.1.3 \ud56d\uc6b0\uc6b8\uc81c &amp; \ud56d\ubd88\uc548\uc81c<\/li>\n<li class=\"toc-level-4\">5.1.1.4 \ud56d\uacbd\ub828\uc81c \/ \uae30\ud0c0<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc<\/li>\n<li class=\"toc-level-4\">5.1.2.1 \uc720\uc804\uc790 \uce68\ubb35 \/ ASO<\/li>\n<li class=\"toc-level-4\">5.1.2.2 \uc720\uc804\uc790 \uce58\ub8cc (AAV, LNP \ub4f1)<\/li>\n<li class=\"toc-level-4\">5.1.2.3 \uc904\uae30\uc138\ud3ec \uce58\ub8cc<\/li>\n<li class=\"toc-level-4\">5.1.2.4 \uc800\ubd84\uc790 HTT \uc870\uc808\uc81c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \ud22c\uc5ec \uacbd\ub85c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uacbd\uad6c<\/li>\n<li class=\"toc-level-3\">5.2.2 \uc815\ub9e5\ub0b4<\/li>\n<li class=\"toc-level-3\">5.2.3 \uc218\ub9c9\uac15\ub0b4<\/li>\n<li class=\"toc-level-3\">5.2.4 \ud53c\ud558<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc720\ud1b5 \ucc44\ub110\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ubcd1\uc6d0 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.2 \uc18c\ub9e4 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.3 \uc804\ubb38 &amp; \uc628\ub77c\uc778 \uc57d\uad6d<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc9c8\ubcd1 \ub2e8\uacc4\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \uc804\uc99d\uc0c1 \/ \uc804\uad6c\uae30<\/li>\n<li class=\"toc-level-3\">5.4.2 \ucd08\uae30 \ub2e8\uacc4<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc911\uae30 \ub2e8\uacc4<\/li>\n<li class=\"toc-level-3\">5.4.4 \ub9d0\uae30 \ub2e8\uacc4<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.5 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.5.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.5.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.5.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.5.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.5.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.5.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.5.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.5.2.6 \uae30\ud0c0 \uc720\ub7fd<\/li>\n<li class=\"toc-level-3\">5.5.3 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.5.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.5.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.5.3.4 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.5 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.5.3.6 \uae30\ud0c0 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-3\">5.5.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.5.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.3 \uae30\ud0c0 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-3\">5.5.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.5.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.5.5.3 \uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uac1c\uc694, \uc2dc\uc7a5 \uac1c\uc694, \ud575\uc2ec \ubd80\ubb38, \uc7ac\ubb34 \uc815\ubcf4(\uc0ac\uc6a9 \uac00\ub2a5\ud55c \uacbd\uc6b0), \uc804\ub7b5 \uc815\ubcf4, \uc8fc\uc694 \uae30\uc5c5\uc758 \uc2dc\uc7a5 \uc21c\uc704\/\uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 \ud654\uc774\uc790 Inc<\/li>\n<li class=\"toc-level-3\">6.3.2 \ud14c\ubc14 \uc81c\uc57d \uc0b0\uc5c5<\/li>\n<li class=\"toc-level-3\">6.3.3 \ub274\ub85c\ud06c\ub9b0 \ubc14\uc774\uc624\uc0ac\uc774\uc5b8\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.4 \uc54c\ub2d0\ub78c \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">6.3.5 \uc544\uc774\uc624\ub2c8\uc2a4 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">6.3.6 \ub85c\uc288 \/ \uc81c\ub128\ud14d<\/li>\n<li class=\"toc-level-3\">6.3.7 \ub178\ubc14\ud2f0\uc2a4 AG<\/li>\n<li class=\"toc-level-3\">6.3.8 \uc720\ub2c8\ud050\uc5b4<\/li>\n<li class=\"toc-level-3\">6.3.9 \uc0c1\uac00\ubaa8 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.10 PTC \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.11 \ud504\ub9ac\ub808\ub2c8\uc544 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.12 \uc6e8\uc774\ube0c \ub77c\uc774\ud504 \uc0ac\uc774\uc5b8\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.13 \uc138\uc774\uc9c0 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.14 \ubc14\uc774\uc624\uc820 Inc.<\/li>\n<li class=\"toc-level-3\">6.3.15 \ub8ec\ub4dc\ubca1<\/li>\n<li class=\"toc-level-3\">6.3.16 \uc544\uc81c\ubc18 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">6.3.17 \ubcf4\uc774\uc800 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.18 \uc778\ud2b8\ub77c\ubc14\uc774\uc624<\/li>\n<li class=\"toc-level-3\">6.3.19 \ucfc4\uc640 \uae30\ub9b0<\/li>\n<li class=\"toc-level-3\">6.3.20 \ubc31\uc2dc\ub2c8\ud2f0<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c &amp; \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc608\uce21 (2026-2031)<\/p>\n<p># 1. \uc2dc\uc7a5 \uac1c\uc694 \ubc0f \uc8fc\uc694 \uc218\uce58<\/p>\n<p>\ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 2025\ub144 8\uc5b5 2\ucc9c\ub9cc \ub2ec\ub7ec\ub97c \uae30\ub85d\ud588\uc73c\uba70, 2026\ub144 8\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2031\ub144\uae4c\uc9c0 13\uc5b5 1\ucc9c\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\uce21 \uae30\uac04(2026-2031\ub144) \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR)\uc740 8.12%\uc5d0 \ub2ec\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uc131\uc7a5\uc740 \uc99d\uc0c1 \uc644\ud654\uc5d0\uc11c \uc9c8\ubcd1 \uc870\uc808 \uc194\ub8e8\uc158\uc73c\ub85c\uc758 \uad6c\uc870\uc801 \uc804\ud658\uc744 \uc758\ubbf8\ud558\uba70, \ud68d\uae30\uc801\uc778 \uc720\uc804\uc790 \uce58\ub8cc\ubc95\uc758 \ubc1c\uc804, \uaddc\uc81c \uacbd\ub85c \uac00\uc18d\ud654, \ud22c\uc790\uc790 \uc2e0\ub8b0 \uc99d\uc9c4\uc5d0 \ud798\uc785\uc5b4 \uac00\uc18d\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub178\ubc14\ud2f0\uc2a4\uc758 PTC 518 29\uc5b5 \ub2ec\ub7ec \uc778\uc218\ub294 \ud5cc\ud305\ud2f4 \uc800\ud574 \uce58\ub8cc\ubc95\uc774 \uc2e4\ud5d8\uc801 \uac00\ub2a5\uc131\uc5d0\uc11c \uc0c1\uc5c5\uc801 \ud604\uc2e4\ub85c \uc804\ud658\ub418\uace0 \uc788\uc74c\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ub3d9\uc2dc\uc5d0 VMAT2 \uc5b5\uc81c\uc81c \ub9e4\ucd9c\uc740 \uc9c0\uc18d\uc801\uc73c\ub85c \uc99d\uac00\ud558\uace0 \uc788\uc73c\uba70, \ub514\uc9c0\ud138 \ubc14\uc774\uc624\ub9c8\ucee4\ub294 \uc784\uc0c1\uc2dc\ud5d8 \uc124\uacc4\ub97c \uac1c\uc120\ud558\uace0, \uc720\uc804\uc790 \uce58\ub8cc \ube44\uc6a9\uc744 \uc644\ud654\ud558\uae30 \uc704\ud55c \ud601\uc2e0\uc801\uc778 \uc790\uae08 \uc870\ub2ec \ubaa8\ub378\uc774 \ub4f1\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub300\ub9ac \ud3c9\uac00\ubcc0\uc218(surrogate endpoint) \uac80\uc99d, \uc804\ubb38 \uc13c\ud130 \ud655\uc0b0, \uc99d\uc0c1 \uc644\ud654 \ubc0f \uc9c8\ubcd1 \uc870\uc808 \uc774\uc810\uc744 \uacb0\ud569\ud55c \ubcf5\ud569 \uc694\ubc95\uc758 \ub4f1\uc7a5\uc73c\ub85c \uc2dc\uc7a5\uc758 \uc131\uc7a5 \ubaa8\uba58\ud140\uc740 \uacc4\uc18d \uac15\ud558\uac8c \uc720\uc9c0\ub420 \uac83\uc73c\ub85c \ubcf4\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc2dc\uc7a5 \uc2a4\ub0c5\uc0f7 (2026-2031\ub144 \uc608\uce21):<br \/>\n*   \uc5f0\uad6c \uae30\uac04: 2020\ub144 &#8211; 2031\ub144<br \/>\n*   2026\ub144 \uc2dc\uc7a5 \uaddc\ubaa8: 8\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec<br \/>\n*   2031\ub144 \uc2dc\uc7a5 \uaddc\ubaa8: 13\uc5b5 1\ucc9c\ub9cc \ub2ec\ub7ec<br \/>\n*   \uc131\uc7a5\ub960 (2026-2031\ub144): 8.12% CAGR<br \/>\n*   \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5: \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591<br \/>\n*   \uac00\uc7a5 \ud070 \uc2dc\uc7a5: \ubd81\ubbf8<br \/>\n*   \uc2dc\uc7a5 \uc9d1\uc911\ub3c4: \uc911\uac04<\/p>\n<p># 2. \uc8fc\uc694 \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30<\/p>\n<p>2.1. \uc131\uc7a5 \ub3d9\ub825 (Drivers)<\/p>\n<p>\ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \uc694\uc778\ub4e4\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   HTT \uc800\ud574 \uc784\uc0c1 \ud30c\uc774\ud504\ub77c\uc778\uc758 \ud68d\uae30\uc801\uc778 \ubc1c\uc804 (CAGR \uc601\ud5a5 +2.8%): \uc5ec\ub7ec \ud50c\ub7ab\ud3fc\uc5d0\uc11c \ub3cc\uc5f0\ubcc0\uc774 \ud5cc\ud305\ud2f4 \ub2e8\ubc31\uc9c8\uc758 \uc720\uc758\ubbf8\ud55c \uac10\uc18c\ub97c \ubcf4\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4. Wave Life Sciences\uc758 WVE-003\uc740 \uc57c\uc0dd\ud615 \ub2e8\ubc31\uc9c8\uc744 \ubcf4\uc874\ud558\uba74\uc11c \ub1cc\ucc99\uc218\uc561 \ub0b4 \ud5cc\ud305\ud2f4\uc744 46% \uac10\uc18c\uc2dc\ucf30\uc73c\uba70, \uacbd\uad6c\uc6a9 PTC 518\uc740 \ud608\uc561 \ub0b4 \ud5cc\ud305\ud2f4\uc744 \ucd5c\ub300 43% \uac10\uc18c\uc2dc\ud0a4\uace0 12\uac1c\uc6d4 \ub3d9\uc548 \ucd1d \uc6b4\ub3d9 \uc810\uc218 \uc9c4\ud589\uc744 70% \uc774\uc0c1 \ub2a6\ucdc4\uc2b5\ub2c8\ub2e4. \ub178\ubc14\ud2f0\uc2a4\uc758 PTC 518 29\uc5b5 \ub2ec\ub7ec \uc778\uc218\ub294 \uc774 \uce58\ub8cc\ubc95\uc758 \uc0c1\uc5c5\uc801 \uc7a0\uc7ac\ub825\uc744 \ud655\uace0\ud788 \ud558\uba70 \ud22c\uc790\uc790 \uc2e0\ub8b0\ub97c \ub192\uc600\uc2b5\ub2c8\ub2e4. \ubbf8\uad6d FDA\uac00 \ud5cc\ud305\ud2f4 \uc800\ud574\ub97c \ub300\ub9ac \ud3c9\uac00\ubcc0\uc218\ub85c \uc218\uc6a9\ud560 \uc758\ud5a5\uc744 \ubcf4\uc774\uba74\uc11c \uac1c\ubc1c \uae30\uac04\uc774 \ub2e8\ucd95\ub418\uace0 \uc2dc\uc7a5 \uc131\uc7a5\uc774 \uac00\uc18d\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc544\uc2dc\uc544 \uc9c0\uc5ed\uc758 1\uc77c 1\ud68c VMAT2 \uc5b5\uc81c\uc81c \uc0c1\uc5c5\uc801 \ucd9c\uc2dc (CAGR \uc601\ud5a5 +1.5%): Teva\uc640 Jiangsu Nhwa\uc758 \uc81c\ud734\ub85c \uc911\uad6d\uc5d0\uc11c AUSTEDO\uac00 \ucd5c\ucd08\uc758 \uc911\uc218\uc18c\ud654 \uc57d\ubb3c \uc2b9\uc778\uc744 \ubc1b\uc544 \ubb34\ub3c4\ubcd1 \uad00\ub9ac \uc811\uadfc\uc131\uc744 \ud655\ub300\ud558\uace0 \ubbf8\ub798 \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc\uc81c \uc9c4\uc785\uc758 \ubc1c\ud310\uc744 \ub9c8\ub828\ud588\uc2b5\ub2c8\ub2e4. INGREZZA\ub294 2024\ub144\uc5d0 23\uc5b5 \ub2ec\ub7ec\uc758 \ub9e4\ucd9c\uc744 \uae30\ub85d\ud588\uc73c\uba70, \uc5f0\ud558\uace4\ub780 \ud658\uc790\ub97c \uc704\ud55c \uc2a4\ud504\ub9c1\ud074 \uc81c\ud615\uc740 \ud22c\uc5ec \ud3b8\uc758\uc131\uc744 \ub192\uc600\uc2b5\ub2c8\ub2e4. \uc544\uc2dc\uc544 \uc9c0\uc5ed\uc758 \ub0ae\uc740 \uc720\ubcd1\ub960(\uc720\ub7fd 10\ub9cc \uba85\ub2f9 5.70\uba85 \ub300\ube44 0.40\uba85)\uc740 \ub300\uaddc\ubaa8 \uc2dc\uc7a5 \ucea0\ud398\uc778\ubcf4\ub2e4\ub294 \uc758\uc0ac \uad50\uc721 \uc911\uc2ec \ubaa8\ub378\uc758 \ud544\uc694\uc131\uc744 \uac15\uc870\ud558\uba70, \uc804\ub7b5\uc801\uc778 \uc544\uc2dc\uc544 \uc2dc\uc7a5 \ucd9c\uc2dc\ub294 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \ubc1c\uc790\ucde8\ub97c \uc11c\uad6c \uac15\uad6d\uc744 \ub118\uc5b4 \ud655\uc7a5\uc2dc\ud0a4\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ubbf8\uad6d\/\uc720\ub7fd\uc758 \uc2e0\uc18d \uc2ec\uc0ac \ubc0f \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815 (CAGR \uc601\ud5a5 +1.8%): AMT-130\uc740 2025\ub144 \ud601\uc2e0 \uce58\ub8cc\uc81c(Breakthrough Therapy) \uc9c0\uc704\ub97c \ud68d\ub4dd\ud588\uc73c\uba70, PTC 518\uc740 \uc2e0\uc18d \uc2ec\uc0ac(Fast Track) \uc9c0\uc815\uc744 \ubc1b\uc558\uace0, \ud504\ub9ac\ub3c4\ud53c\ub518(pridopidine)\uc740 \uc720\ub7fd \ub9c8\ucf00\ud305 \uc2ec\uc0ac\uc5d0 \ub4e4\uc5b4\uac14\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uaddc\uc81c \uae30\uad00\uc774 \ubc14\uc774\uc624\ub9c8\ucee4 \uae30\ubc18 \uc11c\ub958\ub97c \uc218\uc6a9\ud558\ub824\ub294 \uc758\uc9c0\ub97c \ubc18\uc601\ud569\ub2c8\ub2e4. ENROLL-HD \uc678\ubd80 \ub300\uc870\uad70 \ub370\uc774\ud130 \uc0ac\uc6a9\uc5d0 \ub300\ud55c \ud569\uc758\ub294 \uac15\ub825\ud55c \uc2e4\uc81c \uc99d\uac70 \ud504\ub808\uc784\uc6cc\ud06c\ub97c \uc0ac\uc6a9\ud558\ub294 \uae30\uc5c5\uc5d0 \uc720\ub9ac\ud55c \uaddc\uc81c \ud328\ub7ec\ub2e4\uc784\uc758 \ubcc0\ud654\ub97c \uc758\ubbf8\ud569\ub2c8\ub2e4.<br \/>\n*   \uace0\ub839\ud654 \uc778\uad6c \ucf54\ud638\ud2b8\uc758 \ubc1c\ubcd1\ub960 \uc99d\uac00 (CAGR \uc601\ud5a5 +1.2%): \uc9c4\ub2e8 \ubc94\uc704 \uac1c\uc120\uc740 \ub354 \ub9ce\uc740 \ud6c4\uae30 \ubc1c\ubcd1 \uc0ac\ub840\ub97c \ubc1c\uacac\ud558\uace0, \uc804 \uc138\uacc4 \uae30\ub300 \uc218\uba85 \uc99d\uac00\ub294 \ud658\uc790 \ud480\uc744 \ud655\ub300\ud569\ub2c8\ub2e4. \ubd81\ubbf8\uc640 \uc720\ub7fd\uc758 \ucf54\ud638\ud2b8 \uc5f0\uad6c\ub294 2030\ub144\uae4c\uc9c0 \uc720\ubcd1\ub960\uc774 \uafb8\uc900\ud788 \uc99d\uac00\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ud558\uba70, \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \uc9c0\uc18d\uc801\uc778 \ubb3c\ub7c9 \ubaa8\uba58\ud140\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4.<br \/>\n*   AI \uae30\ubc18 \ubc14\uc774\uc624\ub9c8\ucee4 \ubc1c\uacac\uc744 \ud1b5\ud55c \uc784\uc0c1\uc2dc\ud5d8 \uc131\uacf5\ub960 \ud5a5\uc0c1 (CAGR \uc601\ud5a5 +0.9%):<br \/>\n*   \ubca0\ud0c0 \ucc28\ub2e8\uc81c \uc7ac\ud65c\uc6a9\uc744 \ud1b5\ud55c \uc9c8\ubcd1 \uc870\uc808 \uc2e0\ud638 \ubc1c\ud604 (CAGR \uc601\ud5a5 +0.6%):<\/p>\n<p>2.2. \uc81c\uc57d \uc694\uc778 (Restraints)<\/p>\n<p>\uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc8fc\uc694 \uc694\uc778\ub4e4\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc\uc81c\uc758 \ucd08\uace0\uac00 (CAGR \uc601\ud5a5 -1.8%): \ud658\uc790\ub2f9 100\ub9cc \ub2ec\ub7ec\ub97c \ucd08\uacfc\ud558\ub294 \uac00\uaca9\uc740 \uacf5\ud3c9\ud55c \uc811\uadfc\uc744 \uc704\ud611\ud569\ub2c8\ub2e4. 1\ub9cc \uac1c \ud76c\uadc0 \uc9c8\ud658 \uc911 FDA \uc2b9\uc778 \uce58\ub8cc\uc81c\uac00 5% \ubbf8\ub9cc\uc774\ub77c\ub294 \uc810\uc740 \uc0c1\ud658 \uc7a5\ubcbd\uc744 \ubd80\uac01\uc2dc\ud0a4\uba70, \uac00\uce58 \uae30\ubc18 \ubaa8\ub378 \ubc0f \uc7ac\ubcf4\ud5d8 \ub3c4\uc785\uc5d0\ub3c4 \ubd88\uad6c\ud558\uace0 \ub9ce\uc740 \uc2dc\uc7a5\uc5d0\uc11c \uc811\uadfc\uc131\uc744 \uc81c\ud55c\ud558\uace0 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \ucd08\uae30 \ucc44\ud0dd\uc744 \ub2a6\ucd94\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ubd81\ubbf8 \ubc0f \uc720\ub7fd \uc678 \uc9c0\uc5ed\uc758 \uc81c\ud55c\ub41c \uc804\ubb38 \uc13c\ud130 (CAGR \uc601\ud5a5 -1.2%): \ubd81\ubbf8\uc758 \ud751\uc778 \ud658\uc790\ub4e4\uc740 \uc9c4\ub2e8 \uc9c0\uc5f0\uc774 12\uac1c\uc6d4\uc5d0 \ub2ec\ud558\ub294 \ub4f1 \uc120\uc9c4 \uc2dc\uc2a4\ud15c\uc5d0\uc11c\ub3c4 \uc2dc\uc2a4\ud15c\uc801 \ubd88\ud3c9\ub4f1\uc774 \uc874\uc7ac\ud569\ub2c8\ub2e4. \uc2e0\ud765 \uc9c0\uc5ed\uc740 \ucc99\uc218\uac15 \ub0b4 \ub610\ub294 \uc720\uc804\uc790 \uce58\ub8cc \uc2dc\uc124\uc774 \ubd80\uc871\ud558\uc5ec \uc6d0\uaca9 \uc758\ub8cc\uac00 \uc784\uc2dc\ubc29\ud3b8\uc5d0 \ubd88\uacfc\ud569\ub2c8\ub2e4. \ub530\ub77c\uc11c \uc778\ud504\ub77c \ud22c\uc790\uc640 \uc784\uc0c1\uc758 \uad50\uc721\uc740 \uae00\ub85c\ubc8c \uc2dc\uc7a5 \uc131\uc219\uc744 \uc704\ud55c \ud544\uc218 \uc804\uc81c \uc870\uac74\uc73c\ub85c \ub0a8\uc544 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc99d\uc0c1 \uc644\ud654 \ub2e4\uc81c \uc694\ubc95\uc5d0 \ub300\ud55c \ub0ae\uc740 \uc21c\uc751\ub3c4 (CAGR \uc601\ud5a5 -0.7%):<br \/>\n*   \uc2e0\uacbd \uc870\uc9c1 \ub0b4 CRISPR\uc5d0 \ub300\ud55c \ub370\uc774\ud130 \uc548\uc804\uc131 \uc6b0\ub824 (CAGR \uc601\ud5a5 -0.9%):<\/p>\n<p># 3. \uc138\uadf8\uba3c\ud2b8 \ubd84\uc11d<\/p>\n<p>3.1. \uce58\ub8cc \uc720\ud615\ubcc4: \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc\ubc95\uc774 \ud601\uc2e0 \uc8fc\ub3c4<\/p>\n<p>2025\ub144\uc5d0\ub294 \uc99d\uc0c1 \uc644\ud654 \uc57d\ubb3c\uc774 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 61.92%\ub97c \ucc28\uc9c0\ud588\uc9c0\ub9cc, \uc9c8\ubcd1 \uc870\uc808\uc81c\ub294 2031\ub144\uae4c\uc9c0 15.84%\uc758 CAGR\ub85c \ub354 \ube60\ub974\uac8c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uacbd\uad6c\uc6a9 \uc18c\ubd84\uc790, \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc, RNA \uac04\uc12d \uad6c\uc870, AAV \uc720\uc804\uc790 \uce58\ub8cc\ubc95\uc774 \uc735\ud569\ub418\uba74\uc11c \uc2dc\uc7a5\uc744 \ud655\ub300\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. INGREZZA\uc758 2024\ub144 23\uc5b5 \ub2ec\ub7ec \ub9e4\ucd9c\uc740 \ubb34\ub3c4\ubcd1 \uc870\uc808\uc5d0 \ub300\ud55c \uac15\ub825\ud55c \uc218\uc694\ub97c \ubcf4\uc5ec\uc8fc\uba70, AMT-130\uc774 \uc678\ubd80 \ub300\uc870\uad70 \ub300\ube44 \uc9c8\ubcd1 \uc9c4\ud589\uc744 80% \ub2a6\ucd98 \uac83\uc740 \uc720\uc804\uc790 \uce58\ub8cc\uc758 \ud601\uc2e0\uc801\uc778 \uac00\ub2a5\uc131\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ubca0\ud0c0 \ucc28\ub2e8\uc81c \uc7ac\ud65c\uc6a9\uc740 \uc804\uc99d\uc0c1 \ubcf4\uade0\uc790\uc5d0\uc11c \uc6b4\ub3d9 \uc99d\uc0c1 \uc704\ud5d8\uc744 34% \uac10\uc18c\uc2dc\ucf1c \uc99d\uc0c1 \uc644\ud654\uc640 \uc9c8\ubcd1 \uc870\uc808 \ud328\ub7ec\ub2e4\uc784\uc744 \uc5f0\uacb0\ud569\ub2c8\ub2e4. \ubcf5\ud569 \uc694\ubc95\uc774 \ud1b5\ud569\ub428\uc5d0 \ub530\ub77c \uac1c\ubc1c\uc790\ub4e4\uc740 \uc21c\uc11c, \uc548\uc804\uc131 \ubaa8\ub2c8\ud130\ub9c1, \uc9c0\ubd88\uc790 \uc99d\uac70 \ud328\ud0a4\uc9c0\ub97c \ucd5c\uc801\ud654\ud574\uc57c \ud560 \uac83\uc785\ub2c8\ub2e4. \uc9c8\ubcd1 \uc870\uc808 \uc81c\ud488\uc758 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2031\ub144\uae4c\uc9c0 5\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0 \ub2ec\ud558\uc5ec \uc99d\ubd84 \ub9e4\ucd9c \uc131\uc7a5\uc758 \uac70\uc758 45.00%\ub97c \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>3.2. \ud22c\uc5ec \uacbd\ub85c\ubcc4: \uc815\ub9e5 \ud22c\uc5ec\uac00 \ubaa8\uba58\ud140 \ud655\ubcf4<\/p>\n<p>2025\ub144\uc5d0\ub294 \uacbd\uad6c \uc81c\ud615\uc774 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8\uc758 54.05%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, \uc774\ub294 \ub192\uc740 \uc21c\uc751\ub3c4\uc640 1\ucc28 \uc9c4\ub8cc \ucc98\ubc29 \ud328\ud134\uacfc \uc77c\uce58\ud569\ub2c8\ub2e4. \uc815\ub9e5 \ud22c\uc5ec(Intravenous) \ubd80\ubb38\uc740 11.73%\uc758 CAGR\ub85c \uc131\uc7a5\ud558\uace0 \uc788\uc73c\uba70, \uc774\ub294 1\ud68c\uc131 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc640 \ubc18\ubcf5\uc801\uc778 \uc548\ud2f0\uc13c\uc2a4 \uc8fc\uc785\uc774 \uc911\ucd94\uc2e0\uacbd\uacc4\uc5d0 \uc815\ud655\ud55c \ubd84\ud3ec\ub97c \uc694\uad6c\ud558\uae30 \ub54c\ubb38\uc785\ub2c8\ub2e4. \ucc99\uc218\uac15 \ub0b4 \ud22c\uc5ec\ub294 \uc804\uc2e0 \ub178\ucd9c \uc5c6\uc774 \ub1cc\ucc99\uc218\uc561 \uc811\uadfc\uc774 \ud544\uc694\ud55c \ub300\ub9bd\uc720\uc804\uc790 \uc120\ud0dd\uc801 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc\uc5d0 \ud544\uc218\uc801\uc774\uc9c0\ub9cc \uc5ec\uc804\ud788 \ud2c8\uc0c8\uc2dc\uc7a5\uc785\ub2c8\ub2e4. \ubcd1\uc6d0\uc740 \uc2e4\uc2dc\uac04 \uc2e0\uacbd \ubaa8\ub2c8\ud130\ub9c1\uc774 \uac00\ub2a5\ud55c \uc8fc\uc785\uc2e4\uc5d0 \ud22c\uc790\ud558\uace0 \uc788\uc73c\uba70, \uc804\ubb38 \uc57d\uad6d\uc740 \ucf5c\ub4dc \uccb4\uc778 \ubc0f \uc7a5\uae30 \ucd94\uc801 \uad00\ub9ac\ub97c \ub2f4\ub2f9\ud569\ub2c8\ub2e4. \uc2dc\ud310 \ud6c4 \ub370\uc774\ud130\uac00 \ub0b4\uad6c\uc131\uacfc \uc548\uc804\uc131\uc744 \ud655\uc778\ud558\uba74\uc11c \uc815\ub9e5 \ud22c\uc5ec \uc810\uc720\uc728\uc740 2031\ub144\uae4c\uc9c0 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 29.40%\uc5d0 \uc721\ubc15\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>3.3. \uc720\ud1b5 \ucc44\ub110\ubcc4: \uc804\ubb38 \uc57d\uad6d\uc774 \uc131\uc7a5 \uc8fc\ub3c4<\/p>\n<p>2025\ub144\uc5d0\ub294 \ubcd1\uc6d0 \uc57d\uad6d\uc774 \ub9e4\ucd9c\uc758 54.60%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, \uc774\ub294 \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc2dc\uc791 \ubc0f \uae09\uc131 \uc2e0\uacbd\uc815\uc2e0\uacfc\uc801 \uc0ac\uac74 \uad00\ub9ac\ub97c \ubc18\uc601\ud569\ub2c8\ub2e4. \uc804\ubb38 \uc57d\uad6d \ubc0f \uc628\ub77c\uc778 \ucc44\ub110\uc740 \ud658\uc790 \uc9c1\uc811 \ubc30\uc1a1 \ubb3c\ub958, \uc21c\uc751\ub3c4 \ubd84\uc11d, \uc131\uacfc \uae30\ubc18 \uc0c1\ud658 \uad00\ub9ac \ub4f1\uc744 \ud1b5\ud574 14.92%\uc758 \uac00\uc7a5 \uac15\ub825\ud55c CAGR\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc18c\ub9e4 \uc57d\uad6d\uc740 \uacbd\uad6c\uc6a9 \uc99d\uc0c1 \uc644\ud654 \ucc98\ubc29\uc744 \uacc4\uc18d \uc81c\uacf5\ud558\uc9c0\ub9cc, \ube44\uc21c\uc751\ub3c4 \ubc0f \ubd80\uc791\uc6a9 \ud328\ud134\uc744 \uac10\uc9c0\ud558\uae30 \uc704\ud55c \ub514\uc9c0\ud138 \ub3c4\uad6c\ub97c \ud1b5\ud569\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc81c\uc57d \ud68c\uc0ac\ub4e4\uc740 \uc804\ubb38 \ub124\ud2b8\uc6cc\ud06c \ub0b4\uc5d0 \uac04\ud638\uc0ac \uad50\uc721\uc790\ub97c \ubc30\uce58\ud558\uc5ec \uc720\uc804 \uc0c1\ub2f4, \uc6d0\uaca9 \ubaa8\ub2c8\ud130\ub9c1, \ud3c9\uc0dd 1\ud68c \uc8fc\uc785\uc744 \uc704\ud55c \ubb3c\ub958 \uc870\uc815\uc744 \uac04\uc18c\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uacb0\uacfc\uc801\uc73c\ub85c \uc804\ubb38 \ucc44\ub110\uc740 2031\ub144\uae4c\uc9c0 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \ucc98\ubc29\uc758 \uac70\uc758 \uc808\ubc18\uc744 \uad00\ub9ac\ud560 \uc218 \uc788\uc744 \uac83\uc73c\ub85c \ubcf4\uc785\ub2c8\ub2e4.<\/p>\n<p>3.4. \uc9c8\ubcd1 \ub2e8\uacc4\ubcc4: \uc804\uc99d\uc0c1(Pre-symptomatic) \ub2e8\uacc4\uac00 \ud601\uc2e0 \uc8fc\ub3c4<\/p>\n<p>2025\ub144\uc5d0\ub294 \ucd08\uae30 \ub2e8\uacc4 \ud658\uc790\uac00 \ub9e4\ucd9c\uc758 40.25%\ub97c \ucc28\uc9c0\ud588\uc9c0\ub9cc, \ubc14\uc774\uc624\ub9c8\ucee4 \uae30\ubc18 \uc2a4\ud06c\ub9ac\ub2dd\uc744 \ud1b5\ud574 \ubc1c\ubcd1 \ud6e8\uc52c \uc774\uc804\uc5d0 \ubcf4\uade0\uc790\ub97c \uc2dd\ubcc4\ud558\uba74\uc11c \uc804\uc99d\uc0c1(pre-symptomatic) \ub2e8\uacc4\uac00 2031\ub144\uae4c\uc9c0 16.25%\uc758 CAGR\ub85c \uae09\uc99d\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc608\ubc29\uc801 \uac1c\uc785\uc744 \uc704\ud55c \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2031\ub144\uae4c\uc9c0 2\uc5b5 8\ucc9c\ub9cc \ub2ec\ub7ec\ub97c \ub118\uc5b4\uc124 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc911\uae30 \ubc0f \ud6c4\uae30 \ub2e8\uacc4 \uce58\ub8cc\ub294 \uc5ec\uc804\ud788 \uc0c1\ub2f9\ud55c \uc790\uc6d0 \uc9d1\uc57d\ub3c4\ub97c \uc694\uad6c\ud558\uba70, \ud3c9\uade0 4.1\ub144\uc758 \uc694\uc591\uc6d0 \uccb4\ub958\uc640 \ub2e4\uac01\uc801\uc778 \uc644\ud654 \uc694\uad6c \uc0ac\ud56d\uc774 \uc788\uc2b5\ub2c8\ub2e4. \ub530\ub77c\uc11c \ubbf8\ub798 \ud30c\uc774\ud504\ub77c\uc778\uc740 \uc801\uc751\uc99d\uc744 \uacc4\uce35\ud654\ud558\uc5ec, \uc9c8\ubcd1 \uc870\uc808 \uc81c\ud488\uc740 \uc804\uad6c \uc99d\uc0c1 \ub2e8\uacc4\ub97c, \ub2e4\uc81c \ubb34\ub3c4\ubcd1 \uce75\ud14c\uc77c \ubc0f \ud1b5\uc99d \uc870\uc808 \uc694\ubc95\uc740 \uc9c4\ud589\ub41c \ub2e8\uacc4\ub97c \ubaa9\ud45c\ub85c \ud569\ub2c8\ub2e4.<\/p>\n<p># 4. \uc9c0\uc5ed \ubd84\uc11d<\/p>\n<p>*   \ubd81\ubbf8: 2025\ub144 \uc804 \uc138\uacc4 \ub9e4\ucd9c\uc758 38.20%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, FDA\uc758 \uc2e0\uc18d \uc2b9\uc778 \uacbd\ub85c \uc8fc\ub3c4, \uc804\ubb38 \ud074\ub9ac\ub2c9 \uc9d1\uc911, VMAT2 \uc5b5\uc81c\uc81c\uc5d0 \ub300\ud55c \uac15\ub825\ud55c \uc9c0\ubd88\uc790 \uc218\uc6a9\uc5d0 \ud798\uc785\uc5c8\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ud751\uc778 \uc778\uad6c\uc758 \uc9c4\ub2e8 \uc9c0\uc5f0\uc740 \uc808\ub300 \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \uc57d\ud654\uc2dc\ud0a4\ub294 \uc2dc\uc2a4\ud15c\uc801 \ubd88\ud3c9\ub4f1\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \uce90\ub098\ub2e4\uc640 \uba55\uc2dc\ucf54\ub294 \ubbf8\uad6d \uc13c\ud130\uc640 \ud611\ub825\ud558\uc5ec \uc720\uc804\uc790 \uce58\ub8cc \uc784\uc0c1\uc2dc\ud5d8 \uc811\uadfc\uc131\uc744 \ud655\ub300\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc720\ub7fd: \uaddc\uc81c \uc870\ud654\ub97c \ud65c\uc6a9\ud558\uc5ec \uc9c8\ubcd1 \uc870\uc808 \uc11c\ub958\ub97c \uc2e0\uc18d\ud558\uac8c \ucc98\ub9ac\ud558\uace0 \uc788\uc73c\uba70, EMA\ub294 2025\ub144 \ud558\ubc18\uae30 \ucd9c\uc2dc \uac00\ub2a5\uc131\uc774 \uc788\ub294 \ud504\ub9ac\ub3c4\ud53c\ub518\uc744 \uac80\ud1a0 \uc911\uc785\ub2c8\ub2e4. \ub2e4\uad6d\uc801 \ucee8\uc18c\uc2dc\uc5c4\uc740 \ud5cc\ud305\ud134 \uc9c0\uc6d0 \uc571\uc744 \uac1c\ubc1c\ud558\uc5ec \uace0\ub974\uc9c0 \ubabb\ud55c \ud074\ub9ac\ub2c9 \ubc00\ub3c4\ub97c \uc0c1\uc1c4\ud558\ub294 \ube44\uc6a9 \ud6a8\uc728\uc801\uc778 \ub514\uc9c0\ud138 \uc811\uadfc \ubc29\uc2dd\uc744 \ubcf4\uc5ec\uc8fc\uc5c8\uc2b5\ub2c8\ub2e4. \ub3c5\uc77c, \uc601\uad6d, \ud504\ub791\uc2a4\uac00 \uc784\uc0c1\uc2dc\ud5d8 \ud6c4\uc6d0\uc744 \uc8fc\ub3c4\ud558\uace0 \uc788\uc73c\uba70, \ub3d9\uc720\ub7fd\uc758 \ud604\ub300\ud654\ub418\ub294 \uc2e0\uacbd\ud559 \uc778\ud504\ub77c\ub294 \ub450 \uc790\ub9bf\uc218 \uc131\uc7a5\uc744 \uc57d\uc18d\ud569\ub2c8\ub2e4.<br \/>\n*   \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591: 2031\ub144\uae4c\uc9c0 14.55%\uc758 CAGR\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc9c0\uc5ed\uc73c\ub85c, \uc911\uad6d\uc758 \uccab \uc911\uc218\uc18c\ud654 \uc57d\ubb3c \uc2b9\uc778(AUSTEDO)\uacfc \uc77c\ubcf8\uc758 \uc815\uad50\ud55c \ud76c\uadc0 \uc9c8\ud658 \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uc774 \uc131\uc7a5\uc744 \uc8fc\ub3c4\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud55c\uad6d\uc758 \uc804\ub2f4 \ud559\ud68c\ub294 \ud604\uc9c0 \uc784\uc0c1\uc758 \uad50\uc721\uc744 \ubc1c\uc804\uc2dc\ud0a4\uace0 \uc788\uc73c\uba70, \ud638\uc8fc\uc758 \uaddc\uc81c \ubcd1\ub82c \ucc98\ub9ac(parallel-processing)\ub294 \uad6d\uc81c \uc5f0\uad6c\ub97c \uac00\uc18d\ud654\ud569\ub2c8\ub2e4. \ub0ae\uc740 \uc720\ubcd1\ub960\uc740 \uc758\uc0ac \uc8fc\ub3c4 \ud658\uc790 \ub9e4\ud551, \uc6b0\uc218 \uc13c\ud130 \uc778\uc99d, \uc6d0\uaca9 \ubaa8\ub2c8\ud130\ub9c1\uacfc \uac19\uc740 \uace0\ubc00\ub3c4 \ucc38\uc5ec\ub97c \uc694\uad6c\ud569\ub2c8\ub2e4.<br \/>\n*   \ub77c\ud2f4 \uc544\uba54\ub9ac\uce74, \uc911\ub3d9, \uc544\ud504\ub9ac\uce74: \uc544\uc9c1 \ucd08\uae30 \ub2e8\uacc4\uc774\uc9c0\ub9cc, \uc9c4\ub2e8\uc728 \uac1c\uc120\uacfc \uc639\ud638 \ub2e8\uccb4 \uc8fc\ub3c4\uc758 \uc815\ucc45 \ub17c\uc758\uac00 \ube44\uc6a9 \uc7a5\ubcbd\uc774 \ud574\uc18c\ub418\uba74 \uc810\uc9c4\uc801\uc778 \ucc44\ud0dd\uc744 \uc608\uace0\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 5. \uacbd\uc7c1 \ud658\uacbd \ubc0f \uc8fc\uc694 \uae30\uc5c5<\/p>\n<p>5.1. \uacbd\uc7c1 \uad6c\ub3c4<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd\uc740 \ub300\ud615 \uc81c\uc57d\uc0ac\uc758 \uaddc\ubaa8\uc640 \ubc14\uc774\uc624\ud14d\uc758 \uc804\ubb38\uc131\uc774 \uacb0\ud569\ub41c \ud615\ud0dc\uc785\ub2c8\ub2e4. Teva\ub294 \ud655\uace0\ud55c VMAT2 \ud504\ub79c\ucc28\uc774\uc988\ub97c \ud65c\uc6a9\ud558\uace0, Neurocrine\uc740 \uc0bc\ud0a4\uae30 \uc5b4\ub824\uc6b4 \ud658\uc790\ub97c \uc704\ud55c \uc2a4\ud504\ub9c1\ud074 \uc81c\ud615\uc73c\ub85c \uc9c0\ubc30\ub825\uc744 \uac15\ud654\ud558\uba70, uniQure\ub294 \uc5f0\uc18d\uc801\uc778 FDA \uc9c0\uc815\uc744 \ud1b5\ud574 \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uac80\uc99d\uc744 \uc120\ub3c4\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. PTC 518\uc758 \ub178\ubc14\ud2f0\uc2a4 29\uc5b5 \ub2ec\ub7ec \uc778\uc218\ub294 1\ucc28 \uc5f0\uad6c\ubcf4\ub2e4\ub294 \uc704\ud5d8\uc774 \uc644\ud654\ub41c 2\uc0c1 \uc790\uc0b0\uc5d0 \ub300\ud55c \ub300\ud615 \uae30\uc5c5\uc758 \uad00\uc2ec\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \ub300\ub9bd\uc720\uc804\uc790 \uc120\ud0dd\uc801 \uc800\ud574, \uc18c\ubd84\uc790 \uce68\ud22c, \ub0b4\uad6c\uc131 \uc788\ub294 AAV \ud398\uc774\ub85c\ub4dc\uac00 \uc8fc\uc694 \uae30\uc220 \uacbd\uc7c1 \ubd84\uc57c\ub97c \ud615\uc131\ud569\ub2c8\ub2e4. \uc804\ub2ec \ubc29\uc2dd\uc740 \ud3ec\ud2b8\ud3f4\ub9ac\uc624\ub97c \ucc28\ubcc4\ud654\ud558\uba70, \ucc99\uc218\uac15 \ub0b4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc\ub294 1\ud68c\uc131 \uc815\ub9e5 \ud22c\uc5ec \ubca1\ud130 \ubc0f \ub9e4\uc77c \uacbd\uad6c \ud22c\uc5ec \uc870\uc808\uc81c\uc640 \ub300\uc870\ub429\ub2c8\ub2e4. \uacbd\uc7c1 \uc6b0\uc704\ub294 \ubc14\uc774\uc624\ub9c8\ucee4 \uc815\uad50\ud654, \uc2e4\uc81c \uc99d\uac70 \uc804\ub7b5, \ud658\uc790 \uc911\uc2ec \uc11c\ube44\uc2a4 \ubaa8\ub378\uc5d0\uc11c \uc810\uc810 \ub354 \ub9ce\uc774 \ubc1c\uc0dd\ud569\ub2c8\ub2e4. \ud1b5\uc99d \uad00\ub9ac \ubcf5\ud569 \uc694\ubc95, \ubca0\ud0c0 \ucc28\ub2e8\uc81c \uc7ac\ud65c\uc6a9, \ub514\uc9c0\ud138 \uce58\ub8cc \ubcf4\uc870\uc81c \ub4f1\uc774 \ubbf8\uac1c\ucc99 \uae30\ud68c\ub85c \ub0a8\uc544 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>5.2. \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc0b0\uc5c5 \ub9ac\ub354<\/p>\n<p>*   Pfizer, Inc.<br \/>\n*   Alnylam Pharmaceuticals Inc.<br \/>\n*   Teva Pharmaceutical Industries Ltd.<br \/>\n*   Neurocrine Biosciences, Inc.<br \/>\n*   Ionis Pharmaceuticals<\/p>\n<p>5.3. \ucd5c\uadfc \uc0b0\uc5c5 \ub3d9\ud5a5<\/p>\n<p>*   2025\ub144 5\uc6d4: PTC \ud14c\ub77c\ud4e8\ud2f1\uc2a4\ub294 PIVOT-HD 2\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc5d0\uc11c \ud5cc\ud305\ud2f4 \ub2e8\ubc31\uc9c8\uc758 \uc720\uc758\ubbf8\ud55c \uac10\uc18c\uc640 \uc591\ud638\ud55c \uc548\uc804\uc131 \ud504\ub85c\ud30c\uc77c\uc744 \ub2ec\uc131\ud588\ub2e4\uace0 \ubcf4\uace0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2025\ub144 4\uc6d4: uniQure\ub294 AMT-130\uc774 \uc678\ubd80 \ub300\uc870\uad70 \ub300\ube44 \uc9c8\ubcd1 \uc9c4\ud589\uc744 80% \ub2a6\ucd98 \ud6c4 FDA \ud601\uc2e0 \uce58\ub8cc\uc81c \uc9c0\uc815\uc744 \ubc1b\uc558\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 6. \uacb0\ub860<\/p>\n<p>\ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 \uc99d\uc0c1 \uc644\ud654\uc5d0\uc11c \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc\ub85c\uc758 \uc804\ud658, \ud601\uc2e0\uc801\uc778 \ud30c\uc774\ud504\ub77c\uc778\uc758 \ubc1c\uc804, \uadf8\ub9ac\uace0 \uc9c0\uc5ed\ubcc4 \ud2b9\ud654\ub41c \uc131\uc7a5 \uc804\ub7b5\uc744 \ud1b5\ud574 \uc9c0\uc18d\uc801\uc778 \uc131\uc7a5\uc744 \uc774\ub8f0 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc\uc81c\uc758 \ub192\uc740 \ube44\uc6a9\uacfc \uc804\ubb38 \uc13c\ud130 \ubd80\uc871\uc774\ub77c\ub294 \uc81c\uc57d \uc694\uc778\uc774 \uc874\uc7ac\ud558\uc9c0\ub9cc, \uaddc\uc81c \uae30\uad00\uc758 \uc720\uc5f0\uc131, \ubc14\uc774\uc624\ub9c8\ucee4 \uae30\uc220\uc758 \ubc1c\uc804, \uadf8\ub9ac\uace0 \uace0\ub839\ud654 \uc778\uad6c\uc758 \uc99d\uac00\uac00 \uc2dc\uc7a5 \ud655\ub300\ub97c \uacac\uc778\ud560 \uac83\uc785\ub2c8\ub2e4. \ud2b9\ud788 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\uc138\ub97c \ubcf4\uc774\uba70 \uae00\ub85c\ubc8c \uc2dc\uc7a5\uc758 \uc911\uc694\ud55c \ucd95\uc73c\ub85c \ubd80\uc0c1\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \ub300\ud55c \ud3ec\uad04\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ud5cc\ud305\ud134\ubcd1\uc740 \uc8fc\ub85c 30\uc138\uc5d0\uc11c 50\uc138 \uc0ac\uc774\uc5d0 \ubc1c\ubcd1\ud558\uba70 \ub1cc \uc2e0\uacbd\uc138\ud3ec \ud1f4\ud589\uc744 \uc720\ubc1c\ud558\ub294 \uc720\uc804 \uc9c8\ud658\uc73c\ub85c, \ubcf4\uace0\uc11c\ub294 \uc0c1\uc5c5\uc801\uc73c\ub85c \uc774\uc6a9 \uac00\ub2a5\ud55c \ub2e4\uc591\ud55c \uce58\ub8cc \uc591\uc2dd\uc744 \ub2e4\ub8e8\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc804\ub9dd\uc5d0 \ub530\ub974\uba74, \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 2026\ub144 8\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2031\ub144\uae4c\uc9c0 13\uc5b5 1\ucc9c\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uce58\ub8cc \uc720\ud615\ubcc4\ub85c\ub294 \uc99d\uc0c1 \uc644\ud654 \uce58\ub8cc\uc640 \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc\ub85c \uad6c\ubd84\ub429\ub2c8\ub2e4. \ud2b9\ud788 \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc \ubd80\ubb38\uc740 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 15.84%\uc758 \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc99d\uc0c1 \uc644\ud654 \uce58\ub8cc\uc5d0\ub294 VMAT2 \uc5b5\uc81c\uc81c, \ud56d\ub3c4\ud30c\ubbfc\uc81c(\ud56d\uc815\uc2e0\ubcd1 \uc57d\ubb3c), \ud56d\uc6b0\uc6b8\uc81c \ubc0f \ud56d\ubd88\uc548\uc81c, \ud56d\uacbd\ub828\uc81c \ub4f1\uc774 \ud3ec\ud568\ub418\uba70, \uc9c8\ubcd1 \uc870\uc808 \uce58\ub8cc\uc5d0\ub294 \uc720\uc804\uc790 \uce68\ubb35\/ASO(\uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc), \uc720\uc804\uc790 \uce58\ub8cc(AAV, LNP \ub4f1), \uc904\uae30\uc138\ud3ec \uce58\ub8cc, \uc18c\ubd84\uc790 HTT(Huntingtin) \uc870\uc808\uc81c \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ud22c\uc5ec \uacbd\ub85c\ubcc4\ub85c\ub294 \uacbd\uad6c, \uc815\ub9e5 \uc8fc\uc0ac, \ucc99\uc218\uac15 \ub0b4 \uc8fc\uc0ac, \ud53c\ud558 \uc8fc\uc0ac\ub85c \ub098\ub269\ub2c8\ub2e4. \uc720\uc804\uc790 \uce58\ub8cc \ubc0f \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO)\uc758 \ud1b5\uc81c\ub41c \uc804\uc2e0 \ub610\ub294 \ub1cc\ucc99\uc218\uc561 \uc804\ub2ec \ud544\uc694\uc131\uc73c\ub85c \uc778\ud574 \uc815\ub9e5 \uc8fc\uc0ac \ubd80\ubb38\uc740 \uc5f0\ud3c9\uade0 11.73%\uc758 \uc131\uc7a5\uc744 \ubcf4\uc774\uba70 \uc8fc\ubaa9\ubc1b\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc720\ud1b5 \ucc44\ub110\uc740 \ubcd1\uc6d0 \uc57d\uad6d, \uc18c\ub9e4 \uc57d\uad6d, \uc804\ubb38 \ubc0f \uc628\ub77c\uc778 \uc57d\uad6d\uc73c\ub85c \ubd84\ub958\ub418\uba70, \uc9c8\ubcd1 \ub2e8\uacc4\ubcc4\ub85c\ub294 \uc804\uad6c \uc99d\uc0c1\/\uc804\uc870\uae30, \ucd08\uae30, \uc911\uae30, \ub9d0\uae30 \ub2e8\uacc4\ub85c \ubd84\uc11d\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\uc5ed\ubcc4\ub85c\ub294 \ubd81\ubbf8, \uc720\ub7fd, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8\ub85c \uc138\ubd84\ud654\ub429\ub2c8\ub2e4. \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \uc804\ub7b5\uc801 \ud30c\ud2b8\ub108\uc2ed\uacfc \uaddc\uc81c \uc870\ud654\uc5d0 \ud798\uc785\uc5b4 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 14.55%\uc758 \uac00\uc7a5 \ub192\uc740 \uc131\uc7a5 \uc7a0\uc7ac\ub825\uc744 \uac00\uc9c8 \uac83\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc131\uc7a5\uc758 \uc8fc\uc694 \ub3d9\uc778\uc73c\ub85c\ub294 \uace0\ub839\uce35 \uc778\uad6c\uc758 \ubc1c\ubcd1\ub960 \uc99d\uac00, HTT \ub2e8\ubc31\uc9c8 \uac10\uc18c \uc784\uc0c1 \ud30c\uc774\ud504\ub77c\uc778\uc758 \ud68d\uae30\uc801\uc778 \ubc1c\uc804, \uc544\uc2dc\uc544 \uc2dc\uc7a5\uc5d0\uc11c\uc758 1\uc77c 1\ud68c VMAT2 \uc5b5\uc81c\uc81c \uc0c1\uc5c5\uc801 \ucd9c\uc2dc, \ubbf8\uad6d\/EU\uc758 \uc2e0\uc18d \uc2ec\uc0ac \ubc0f \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815, AI \uae30\ubc18 \ubc14\uc774\uc624\ub9c8\ucee4 \ubc1c\uad74\uc744 \ud1b5\ud55c \uc784\uc0c1 \uc131\uacf5\ub960 \ud5a5\uc0c1, \ubca0\ud0c0 \ucc28\ub2e8\uc81c \uc7ac\ud65c\uc6a9\uc744 \ud1b5\ud55c \uc9c8\ubcd1 \uc870\uc808 \uc2e0\ud638 \ubc1c\uacac \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubc18\uba74, \uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778\uc73c\ub85c\ub294 \uc720\uc804\uc790 \ubc0f \uc138\ud3ec \uce58\ub8cc\uc81c\uc758 \ucd08\uace0\uac00 \ube44\uc6a9, \ubd81\ubbf8 \ubc0f EU \uc678 \uc9c0\uc5ed\uc758 \uc81c\ud55c\uc801\uc778 \uc804\ubb38 \uce58\ub8cc \uc13c\ud130, \uc99d\uc0c1 \uc644\ud654 \ub2e4\uc81c \ubcd1\uc6a9 \uc694\ubc95\uc5d0 \ub300\ud55c \ub0ae\uc740 \ud658\uc790 \uc21c\uc751\ub3c4, \uc2e0\uacbd \uc870\uc9c1 \ub0b4 CRISPR \uc720\uc804\uc790 \uac00\uc704 \uae30\uc220\uc758 \ub370\uc774\ud130 \uc548\uc804\uc131 \uc6b0\ub824 \ub4f1\uc774 \uc9c0\uc801\ub429\ub2c8\ub2e4. \uace0\uac00\uc758 \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uac00\uaca9 \ubb38\uc81c \ud574\uacb0\uc744 \uc704\ud574 \uac00\uce58 \uae30\ubc18 \uc9c0\ubd88 \ubaa8\ub378, \uc7ac\ubcf4\ud5d8, \ud560\ubd80 \uacc4\ud68d \ub4f1\uc774 \ubaa8\uc0c9\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd \ubd84\uc11d\uc740 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4, \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d, \uadf8\ub9ac\uace0 Pfizer Inc., Teva Pharmaceutical Industries, Neurocrine Biosciences, Alnylam Pharmaceuticals, Ionis Pharmaceuticals, Roche\/Genentech, Novartis AG \ub4f1 \uc8fc\uc694 20\uac1c \uae30\uc5c5\uc758 \ud504\ub85c\ud544\uc744 \ud1b5\ud574 \uc81c\uacf5\ub429\ub2c8\ub2e4. \ubcf4\uace0\uc11c\ub294 \ub610\ud55c \uc2dc\uc7a5 \uae30\ud68c\uc640 \ubbf8\ub798 \uc804\ub9dd, \ubbf8\ucda9\uc871 \uc218\uc694 \ud3c9\uac00\ub97c \ud3ec\ud568\ud569\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-43881","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/43881"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=43881"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/43881\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=43881"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=43881"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=43881"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}