{"id":44858,"date":"2026-02-15T06:07:21","date_gmt":"2026-02-15T06:07:21","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/mitochondrial-disease-therapies-market-mordor\/"},"modified":"2026-09-25T13:05:46","modified_gmt":"2026-09-25T04:05:46","slug":"mitochondrial-disease-therapies-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/mitochondrial-disease-therapies-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2025-2030\ub144)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/mitochondrial-disease-therapies-market-1754053080239-major-players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/mitochondrial-disease-therapies-market-size-image-1755588151826.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud604\ud669<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 LHON \ubc0f FA\uc5d0 \ub300\ud55c \uc720\uc804\uc790 \uce58\ub8cc \uc2b9\uc778<\/li>\n<li class=\"toc-level-3\">4.2.2 \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \ubca4\ucc98 \uc790\uae08 \uc720\uc785<\/li>\n<li class=\"toc-level-3\">4.2.3 \ubc1c\uc804\ud558\ub294 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 DNA \ud3b8\uc9d1 \ud50c\ub7ab\ud3fc (TALENs, DdCBE)<\/li>\n<li class=\"toc-level-3\">4.2.4 AI \uae30\ubc18 \ub300\uc0ac \uc870\uc808\uc81c \uc6a9\ub3c4 \ubcc0\uacbd<\/li>\n<li class=\"toc-level-3\">4.2.5 \uae09\uc131 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc190\uc0c1 \ub300\uc751\ucc45\uc5d0 \ub300\ud55c \uad70\uc0ac \uc790\uae08 \uc9c0\uc6d0<\/li>\n<li class=\"toc-level-3\">4.2.6 \uc2e4\uc81c \uc99d\uac70 \ub4f1\ub85d\uc758 \ud65c\uc6a9 \uc99d\uac00<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ub3cc\uc5f0\ubcc0\uc774\ub2f9 \uadf9\ud788 \uc801\uc740 \ub300\uc0c1 \ud658\uc790 \ud480<\/li>\n<li class=\"toc-level-3\">4.3.2 \uc784\uc0c1 \uc2dc\ud5d8 \ubaa8\uc9d1\uc758 \uc5b4\ub824\uc6c0 \ubc0f \uc774\uc9c8\uc801\uc778 \ud3c9\uac00 \ubcc0\uc218<\/li>\n<li class=\"toc-level-3\">4.3.3 AAV \ubca1\ud130 \ubc0f \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ubd84\ub9ac\ub97c \uc704\ud55c \ub192\uc740 \ub9e4\ucd9c\uc6d0\uac00<\/li>\n<li class=\"toc-level-3\">4.3.4 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \uac00\uce58 \/ \uacf5\uae09\ub9dd \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">4.5 \uaddc\uc81c \ud658\uacbd<\/li>\n<li class=\"toc-level-2\">4.6 \uae30\uc220 \uc804\ub9dd<\/li>\n<li class=\"toc-level-2\">4.7 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.7.1 \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.7.2 \uad6c\ub9e4\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.7.3 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.7.4 \ub300\uccb4\uc7ac\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.7.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc608\uce21 (\uac00\uce58-USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uce58\ub8cc \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \uc720\uc804\uc790 \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc57d\ub9ac\ud559\uc801 \uc81c\uc81c<\/li>\n<li class=\"toc-level-3\">5.1.3 \ub274\ud2b8\ub77c\uc288\ud2f0\uceec &amp; \ubcf4\ucda9\uc81c<\/li>\n<li class=\"toc-level-3\">5.1.4 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.1.5 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ud45c\uc801 \ud56d\uc0b0\ud654\uc81c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \uc9c8\ubcd1 \uc801\uc751\uc99d\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \ub808\ubc84 \uc720\uc804\uc131 \uc2dc\uc2e0\uacbd\ubcd1\uc99d (LHON)<\/li>\n<li class=\"toc-level-3\">5.2.2 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uadfc\ubcd1\uc99d<\/li>\n<li class=\"toc-level-3\">5.2.3 \ub9ac \uc99d\ud6c4\uad70<\/li>\n<li class=\"toc-level-3\">5.2.4 \uba5c\ub77c\uc2a4<\/li>\n<li class=\"toc-level-3\">5.2.5 \uae30\ud0c0 \uc8fc\uc694 MD<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc791\uc6a9 \uae30\uc804\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \uc0b0\ud654\uc801 \uc778\uc0b0\ud654 \uc870\uc808\uc81c<\/li>\n<li class=\"toc-level-3\">5.3.2 \uc720\uc804\uc790 \ub300\uccb4 \/ \ud3b8\uc9d1<\/li>\n<li class=\"toc-level-3\">5.3.3 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc0dd\ud569\uc131 \ucd09\uc9c4\uc81c<\/li>\n<li class=\"toc-level-3\">5.3.4 mtDNA \ubd84\ud574 \ub3c4\uad6c<\/li>\n<li class=\"toc-level-3\">5.3.5 \ud6a8\uc18c \/ \ubcf4\uc870\uc778\uc790 \ub300\uccb4<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \ud22c\uc5ec \uacbd\ub85c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \uacbd\uad6c<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc815\ub9e5 \uc8fc\uc0ac<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc720\ub9ac\uccb4\ub0b4<\/li>\n<li class=\"toc-level-3\">5.4.4 \ud53c\ud558<\/li>\n<li class=\"toc-level-3\">5.4.5 \uae30\ud0c0<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.5 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.5.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.5.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.5.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.5.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.5.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.5.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.5.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.5.2.6 \uc720\ub7fd \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.5.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.5.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.5.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.5.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.5.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.6 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.5.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.5.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.3 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.5.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.5.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.5.5.3 \ub0a8\ubbf8 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uc218\uc900 \uac1c\uc694, \uc2dc\uc7a5 \uc218\uc900 \uac1c\uc694, \ud575\uc2ec \ubd80\ubb38, \uc0ac\uc6a9 \uac00\ub2a5\ud55c \uc7ac\ubb34 \uc815\ubcf4, \uc804\ub7b5 \uc815\ubcf4, \uc8fc\uc694 \uae30\uc5c5\uc758 \uc2dc\uc7a5 \uc21c\uc704\/\uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 \uc2a4\ud154\uc2a4 \ubc14\uc774\uc624\ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.2 \uc820\uc0ac\uc774\ud2b8 \ubc14\uc774\uc624\ub85c\uc9c1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.3 \uc0b0\ud14c\ub77c \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.4 \ub808\uc544\ud0c0 \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.5 \uc544\uc2a4\ud154\ub77c\uc2a4 (\ubbf8\ud1a0\ube0c\ub9bf\uc9c0)<\/li>\n<li class=\"toc-level-3\">6.3.6 \ubbf8\ub178\ube44\uc544 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.7 \ucf58\ub4dc\ub9ac\uc628<\/li>\n<li class=\"toc-level-3\">6.3.8 PTC \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.9 \uc544\ube14\ub9ac\ubc14 (\ub274\ub85c\ubc14\uc774\ube0c)<\/li>\n<li class=\"toc-level-3\">6.3.10 \ub808\ub124\uc624 \ud30c\ub9c8<\/li>\n<li class=\"toc-level-3\">6.3.11 \uc2a4\ud2f0\uc5b4Tx<\/li>\n<li class=\"toc-level-3\">6.3.12 \ubbf8\ud1a0\ucf58 \ud30c\ub9c8\uc288\ud2f0\uceec\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.13 \ucf54\ubc14<\/li>\n<li class=\"toc-level-3\">6.3.14 \ubca0\ub9c1\uac70 \uc778\uac94\ud558\uc784<\/li>\n<li class=\"toc-level-3\">6.3.15 \ud0a4\uc5d0\uc2dc \ud30c\ub9c8\uc288\ud2f0\uce58<\/li>\n<li class=\"toc-level-3\">6.3.16 \uc2dc\uc624\ub178\uae30<\/li>\n<li class=\"toc-level-3\">6.3.17 \uc5d8\ub808\ubc14 \ubc14\uc774\uc624\ub85c\uc9c1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.18 \ubbf8\ud2b8\ub9ad\uc2a4 \ubc14\uc774\uc624<\/li>\n<li class=\"toc-level-3\">6.3.19 \uc0ac\ub819\ud0c0 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c &amp; \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uac1c\uc694: \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc608\uce21 (2025-2030)<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc758 \uaddc\ubaa8, \uc810\uc720\uc728, \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f 2030\ub144\uae4c\uc9c0\uc758 \uc608\uce21\uc744 \uc0c1\uc138\ud788 \ubd84\uc11d\ud569\ub2c8\ub2e4. \uce58\ub8cc \uc720\ud615(\uc720\uc804\uc790 \uce58\ub8cc, \uc57d\ub9ac\ud559\uc801 \uc81c\uc81c, \uc601\uc591 \ubcf4\uc870\uc81c \ub4f1), \uc9c8\ubcd1 \uc801\uc751\uc99d(\ub808\ubc84 \uc720\uc804\uc131 \uc2dc\uc2e0\uacbd\ubcd1\uc99d(LHON) \ub4f1), \uc791\uc6a9 \uae30\uc804(\uc0b0\ud654\uc801 \uc778\uc0b0\ud654 \uc870\uc808\uc81c \ub4f1), \ud22c\uc5ec \uacbd\ub85c(\uacbd\uad6c, \uc815\ub9e5 \uc8fc\uc0ac \ub4f1) \ubc0f \uc9c0\uc5ed\ubcc4\ub85c \uc2dc\uc7a5\uc744 \uc138\ubd84\ud654\ud558\uc5ec \uac00\uce58(USD) \uae30\uc900\uc73c\ub85c \uc608\uce21\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4.<\/p>\n<p># 1. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc804\ub9dd<\/p>\n<p>\ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 2025\ub144 4\uc5b5 6,816\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\uc5d0\uc11c 2030\ub144\uc5d0\ub294 6\uc5b5 5,865\ub9cc \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub418\uba70, \uc608\uce21 \uae30\uac04(2025-2030) \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 7.07%\ub97c \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uc131\uc7a5\uc740 \uc138 \uac00\uc9c0 \uc8fc\uc694 \uc694\uc778\uc5d0 \uc758\ud574 \uacac\uc778\ub429\ub2c8\ub2e4. \uccab\uc9f8, LUMEVOQ \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uac00 \uc720\ub7fd \uaddc\uc81c \uc2b9\uc778\uc744 \ud68d\ub4dd\ud558\ub294 \ub4f1 \uaddc\uc81c \ud658\uacbd\uc774 \uc131\uc219\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub458\uc9f8, TALEN \ubc0f \uc774\uc911 \uac00\ub2e5 \uc808\ub2e8 \uc5c6\ub294 \uc5fc\uae30 \ud3b8\uc9d1\uae30\uc640 \uac19\uc740 \uc815\ubc00 \uc720\uc804\uc790 \ud3b8\uc9d1 \ub3c4\uad6c\uc5d0 \ub300\ud55c \uc2e0\ub8b0\uac00 \uc99d\uac00\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc14b\uc9f8, \ucd08\ud76c\uadc0 \ud658\uc790 \uc9d1\ub2e8\uc744 \ub300\uc0c1\uc73c\ub85c \ud558\ub294 \uc784\uc0c1 \uc2dc\ud5d8\uc758 \ub192\uc740 \ube44\uc6a9\uc744 \uc0c1\uc1c4\ud560 \uc218 \uc788\ub294 \ubca4\ucc98 \ubc0f \uc790\uc120 \uc790\ubcf8\uc758 \uc804\ub840 \uc5c6\ub294 \uc720\uc785\uc774 \uc774\ub8e8\uc5b4\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ub610\ud55c, \ub9ac \uc99d\ud6c4\uad70 \ubc0f \uae09\uc131 \uc2ec\uc7a5 \uc190\uc0c1\uc5d0 \ub300\ud55c \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd\uc758 \uc784\uc0c1\uc801 \uc9c4\uc804\uc740 \uce58\ub8cc \uc9c0\ud3c9\uc744 \ub113\ud788\uace0 \uc788\uc73c\uba70, \uad6d\ubc29\ubd80 \uc790\uae08 \uc9c0\uc6d0 \uc5f0\uad6c\ub294 \uc804\uc7a5 \ud1b5\ucc30\ub825\uc744 \ubbfc\uac04 \uc758\ub8cc \uacbd\ub85c\ub85c \uc804\ud658\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub3d9\uc2dc\uc5d0 \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130(Real-World Evidence) \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uc740 \uc784\uc0c1 \uc2dc\ud5d8 \uc124\uacc4\ub97c \uac15\ud654\ud558\uace0 \ubaa8\uc9d1 \uc8fc\uae30\ub97c \ub2e8\ucd95\ud558\uc5ec, \ube44\uc6a9 \ubc0f \uc81c\uc870 \uc81c\uc57d\uc5d0\ub3c4 \ubd88\uad6c\ud558\uace0 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc5d0 \uad6c\uc870\uc801\uc73c\ub85c \ub354 \ub192\uc740 \uc131\uc7a5 \uae30\ubc18\uc744 \uc81c\uacf5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 2. \uc8fc\uc694 \uc2dc\uc7a5 \uc694\uc57d (2024\ub144 \uae30\uc900)<\/p>\n<p>*   \uce58\ub8cc \uc720\ud615\ubcc4: \uc720\uc804\uc790 \uce58\ub8cc\uac00 39.54%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud588\uc73c\uba70, \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc\ub294 2030\ub144\uae4c\uc9c0 11.11%\uc758 \uac00\uc7a5 \ub192\uc740 CAGR\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n*   \uc9c8\ubcd1 \uc801\uc751\uc99d\ubcc4: \ub808\ubc84 \uc720\uc804\uc131 \uc2dc\uc2e0\uacbd\ubcd1\uc99d(LHON)\uc774 34.81%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud588\uc73c\uba70, \ub9ac \uc99d\ud6c4\uad70\uc740 2030\ub144\uae4c\uc9c0 10.36%\uc758 CAGR\ub85c \ube60\ub974\uac8c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc791\uc6a9 \uae30\uc804\ubcc4: \uc720\uc804\uc790 \ub300\uccb4\/\ud3b8\uc9d1\uc774 36.78%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \uae30\ub85d\ud588\uc73c\uba70, mtDNA \ubd84\ud574 \ub3c4\uad6c\ub294 \uac19\uc740 \uae30\uac04 \ub3d9\uc548 10.66%\uc758 CAGR\ub85c \uc131\uc7a5\ud560 \uc900\ube44\uac00 \ub418\uc5b4 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ud22c\uc5ec \uacbd\ub85c\ubcc4: \uc720\ub9ac\uccb4\ub0b4 \uc8fc\uc0ac\uac00 41.28%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\ub85c \uc120\ub450\ub97c \ub2ec\ub838\uc73c\uba70, \uc815\ub9e5 \uc8fc\uc0ac\ub294 2030\ub144\uae4c\uc9c0 9.48%\uc758 \uac00\uc7a5 \ub192\uc740 \uc608\uc0c1 CAGR\uc744 \ubcf4\uc785\ub2c8\ub2e4.<br \/>\n*   \uc9c0\uc5ed\ubcc4: \ubd81\ubbf8\uac00 44.36%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\ub85c \uac00\uc7a5 \ud070 \uc2dc\uc7a5\uc744 \ud615\uc131\ud588\uc73c\uba70, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591\uc740 2030\ub144\uae4c\uc9c0 9.83%\uc758 CAGR\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p># 3. \uae00\ub85c\ubc8c \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30\ub825 (\uc131\uc7a5 \ub3d9\uc778)<\/p>\n<p>*   LHON \ubc0f \ud504\ub9ac\ub4dc\ub9ac\ud788 \uc6b4\ub3d9\uc2e4\uc870\uc99d(FA)\uc5d0 \ub300\ud55c \uc720\uc804\uc790 \uce58\ub8cc \uc2b9\uc778: \ucd5c\uadfc \uc548\uacfc \ubc0f \uc804\uc2e0 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\uc758 \uc2b9\uc778 \ubc0f \ud6c4\uae30 \ub2e8\uacc4 \uac80\ud1a0\ub294 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uc804\ubc18\uc758 \uac1c\ubc1c \uc704\ud5d8\uc744 \uac10\uc18c\uc2dc\ucf30\uc2b5\ub2c8\ub2e4. GenSight\uc758 LUMEVOQ\ub294 LHON \uc7a5\uae30 \ucd94\uc801 \ub370\uc774\ud130\uc5d0\uc11c \ud6a8\ub2a5 \uae30\uc900\uc744 \uc9c0\uc18d\uc801\uc73c\ub85c \ucda9\uc871\ud558\uba70 AAV \ub9e4\uac1c \uc804\ub2ec\uc5d0 \ub300\ud55c \uc2e0\ub8b0\ub97c \uac15\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. Lexeo Therapeutics\uc758 \ud504\ub9ac\ub4dc\ub9ac\ud788 \uc6b4\ub3d9\uc2e4\uc870\uc99d \uc2ec\uadfc\ubcd1\uc99d \uc784\uc0c1 \uc2dc\ud5d8\uc758 \ubcd1\ud589 \uc9c4\uc804\uc740 \uc804\uc2e0 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc720\uc804\uc790 \uad50\uc815\uc758 \uac00\ub2a5\uc131\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ud504\ub85c\uadf8\ub7a8\uc5d0\uc11c \uc0dd\uc131\ub41c \uaddc\uc81c \uba85\ud655\uc131\uc740 \ub2e4\ub978 \uc8fc\uc694 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658\uc73c\ub85c\uc758 \ud3ec\ud2b8\ud3f4\ub9ac\uc624 \ud655\uc7a5\uc744 \ucd09\uc9c4\ud558\uace0 \uc788\uc73c\uba70, \uc774\ud615\uc131 \ubcc0\ud654 \ubc0f ATP \uc0dd\uc0b0\uacfc \uac19\uc740 \ub300\uccb4 \ud3c9\uac00 \ubcc0\uc218\ub97c \ud45c\uc900\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \ucd08\uae30 \ub2e8\uacc4 \uc790\uc0b0\uc758 \uac00\uce58 \ubc30\uc218\ub97c \ub192\uc774\uace0 \uc2dc\uc7a5 \ub0b4 \uac70\ub798 \ud750\ub984\uc744 \uc99d\ud3ed\uc2dc\ud0a4\ub294 \ud6a8\uacfc\ub97c \uac00\uc838\uc635\ub2c8\ub2e4.<br \/>\n*   \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \ubca4\ucc98 \uc790\uae08 \uc720\uc785: 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \ud504\ub85c\uadf8\ub7a8\uc5d0 \ub300\ud55c \uae00\ub85c\ubc8c \ubca4\ucc98 \ud22c\uc790\ub294 5\uc5b5 \ub2ec\ub7ec\ub97c \ucd08\uacfc\ud588\uc73c\uba70, \uc774\ub294 \ud76c\uadc0\uc758\uc57d\ud488 \uc138\uae08 \uacf5\uc81c, 7~10\ub144\uc758 \ub3c5\uc810 \uae30\uac04, \uadf8\ub9ac\uace0 \uc9c8\ubcd1 \uc870\uc808 \ubc29\uc2dd\uc5d0 \ub300\ud55c \uc9c0\ubd88\uc790\uc758 \uc218\uc6a9\uc774 \ubcf5\ud569\uc801\uc73c\ub85c \uc791\uc6a9\ud55c \uacb0\uacfc\uc785\ub2c8\ub2e4. Abliva\uc758 2\uc5b5 SEK \uc870\ub2ec \ubc0f Mission Therapeutics\uc758 2,520\ub9cc \ud30c\uc6b4\ub4dc \uc870\ub2ec\uc740 \uc804 \uc138\uacc4\uc801\uc73c\ub85c 10,000\uba85 \ubbf8\ub9cc\uc758 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud558\ub294 \ud504\ub85c\uadf8\ub7a8\uc758 \uc790\ubcf8 \uaca9\ucc28\ub97c \ud574\uc18c\ud558\ub294 \ub370 \uc804\uc6a9 \uc790\uae08\uc774 \uc5b4\ub5bb\uac8c \ud65c\uc6a9\ub420 \uc218 \uc788\ub294\uc9c0\ub97c \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. Khondrion\uc758 500\ub9cc \uc720\ub85c \ud601\uc2e0 \uc2e0\uc6a9\uacfc \uac19\uc740 \uacf5\uacf5 \ubd80\ubb38\uc758 \ucc38\uc5ec\ub294 \uc8fc\uc694 \uc784\uc0c1 \uc2dc\ud5d8\uc758 \uc790\uae08 \uc870\ub2ec \uae30\uac04\uc744 \ub354\uc6b1 \uc5f0\uc7a5\ud569\ub2c8\ub2e4.<br \/>\n*   mtDNA \ud3b8\uc9d1 \ud50c\ub7ab\ud3fc \ubc1c\uc804 (TALENs, DdCBEs): \uc774\uc911 \uac00\ub2e5 \uc808\ub2e8 \uc5c6\ub294 \ud3b8\uc9d1\uae30\uac00 \ube44\ud45c\uc801 \ud575 \ud3b8\uc9d1 \uc5c6\uc774 \ud1b5\uc81c\ub41c \uc774\ud615\uc131 \ubcc0\ud654\ub97c \ub2ec\uc131\ud558\uba74\uc11c \uc815\ubc00 \ud3b8\uc9d1 \uae30\uc220\uc774 \uc5f0\uad6c\uc2e4\uc5d0\uc11c \uc784\uc0c1\uc73c\ub85c \uc804\ud658\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \ud6c4\uc9c0\ud0c0 \ubcf4\uac74\ub300\ud559\uad50\ub294 \ubc31\uae08 TALEN\uc744 \uc0ac\uc6a9\ud558\uc5ec MELAS \uc99d\ud6c4\uad70 \uc138\ud3ec\uc5d0\uc11c \ub3cc\uc5f0\ubcc0\uc774 \ubd80\ud558 \uac10\uc18c\ub97c \uc785\uc99d\ud588\uc73c\uba70, \uc774 \uc5f0\uad6c\ub294 \ud604\uc7ac \uc778\uac04 \ub300\uc0c1 \uc5f0\uad6c\ub85c \uc804\ud658\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. MITO-Porter\uc640 \uac19\uc740 \ubcf4\uc644\uc801\uc778 \uc9c0\uc9c8 \ub098\ub178\uc785\uc790 \uc6b4\ubc18\uccb4\ub294 20%\uc758 \uc138\ud3ec \ub0b4 \ud3b8\uc9d1 \ud6a8\uc728\uc5d0 \ub3c4\ub2ec\ud558\uc5ec \ud575\uc2ec \uc804\ub2ec \ub09c\uad00\uc744 \ud574\uacb0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   AI \uae30\ubc18 \ub300\uc0ac \uc870\uc808\uc81c \uc7ac\ud65c\uc6a9: \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc0c1\ud638\uc791\uc6a9\uccb4\uc5d0 \ub300\ud574 \ud6c8\ub828\ub41c \uba38\uc2e0\ub7ec\ub2dd \uc54c\uace0\ub9ac\uc998\uc740 \uc0b0\ud654\uc801 \uc778\uc0b0\ud654\ub97c \ud5a5\uc0c1\uc2dc\ud0a4\uac70\ub098 POLG \ud6a8\uc18c \uae30\ub2a5\uc744 \uc548\uc815\ud654\ud560 \uc218 \uc788\ub294 \uc800\ubd84\uc790 \ud654\ud569\ubb3c\uc744 \ubc1c\uad74\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. Pretzel Therapeutics\uc758 PZL-A \ud6c4\ubcf4 \ubb3c\uc9c8\uc740 \uadf8\ub798\ud504 \uae30\ubc18 \uc2a4\ud06c\ub9ac\ub2dd\uc744 \ud1b5\ud574 18\uac1c\uc6d4 \uc774\ub0b4\uc5d0 \uc804\uc784\uc0c1 \uc5f0\uad6c \ub2e8\uacc4\ub85c \uc9c4\uc785\ud588\uc2b5\ub2c8\ub2e4. \uc54c\uace0\ub9ac\uc998 \uae30\ubc18\uc758 \uc7ac\ud65c\uc6a9\uc740 \uc54c\ub824\uc9c4 \uc548\uc804\uc131 \ub370\uc774\ud130\ub97c \ud65c\uc6a9\ud558\uc5ec \ucd08\uae30 \ub2e8\uacc4\uc758 \uc2e4\ud328\uc728\uc744 \uc904\uc774\uba70, \ub77c\ubca8 \ud655\uc7a5\uc744 \uc9c0\uc6d0\ud558\uae30 \uc704\ud55c \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130\uc5d0 \ub300\ud55c \uaddc\uc81c \ub2f9\uad6d\uc758 \uc694\uad6c\uc640\ub3c4 \uc798 \ubd80\ud569\ud569\ub2c8\ub2e4.<br \/>\n*   \uae09\uc131 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc190\uc0c1 \ub300\uc751\ucc45\uc5d0 \ub300\ud55c \uad70\uc0ac \uc790\uae08 \uc9c0\uc6d0: \ubbf8\uad6d \uad6d\ubc29\ubd80\uc758 \uc790\uae08 \uc9c0\uc6d0 \uc5f0\uad6c\ub294 \uc804\uc7a5\uc5d0\uc11c \uc5bb\uc740 \ud1b5\ucc30\ub825\uc744 \ubbfc\uac04 \uc758\ub8cc \uacbd\ub85c\ub85c \uc804\ud658\ud558\ub294 \ub370 \uae30\uc5ec\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130 \ub4f1\ub85d \uc2dc\uc2a4\ud15c \ud65c\uc6a9 \uc99d\uac00: \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130 \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uc758 \ud65c\uc6a9 \uc99d\uac00\ub294 \uc784\uc0c1 \uc2dc\ud5d8 \uc124\uacc4\ub97c \uac15\ud654\ud558\uace0 \ud658\uc790 \ubaa8\uc9d1 \uc8fc\uae30\ub97c \ub2e8\ucd95\ud558\uc5ec \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \uae0d\uc815\uc801\uc778 \uc601\ud5a5\uc744 \ubbf8\uce58\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 4. \uc131\uc7a5 \uc81c\uc57d \uc694\uc778<\/p>\n<p>*   \ub3cc\uc5f0\ubcc0\uc774\ub2f9 \uadf9\uc18c\uc218\uc758 \ud658\uc790 \ud480: \uac1c\ubcc4 mtDNA \ub3cc\uc5f0\ubcc0\uc774\ub294 \uc804 \uc138\uacc4\uc801\uc73c\ub85c 1,000\uba85 \ubbf8\ub9cc\uc758 \ud658\uc790\uc5d0\uac8c \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 \uacbd\uc6b0\uac00 \ub9ce\uc544, \uc0dd\ubb3c\ud559\uc801 \uc99d\uac70\uac00 \ud655\uc2e4\ud558\ub354\ub77c\ub3c4 \uc0c1\uc5c5\uc801 \uaddc\ubaa8 \ud655\uc7a5\uc744 \uc5b4\ub835\uac8c \ud569\ub2c8\ub2e4. \ud30c\ud3b8\ud654\ub41c \uc720\ubcd1\ub960\uc740 \uc2a4\ud3f0\uc11c\uac00 \ud1b5\uacc4\uc801 \uac80\uc815\ub825 \ubc0f \uaddc\uc81c \ucc38\uc5ec\ub97c \ubcf5\uc7a1\ud558\uac8c \ub9cc\ub4dc\ub294 \ubc14\uc2a4\ucf13 \ub610\ub294 \ub3cc\uc5f0\ubcc0\uc774 \ube44\ud2b9\uc774\uc801 \uc124\uacc4\ub97c \ucd94\uad6c\ud558\ub3c4\ub85d \uac15\uc694\ud569\ub2c8\ub2e4.<br \/>\n*   \uc784\uc0c1 \uc2dc\ud5d8 \ubaa8\uc9d1 \ub09c\uad00 \ubc0f \uc774\uc9c8\uc801\uc778 \ud3c9\uac00 \ubcc0\uc218: \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \ub0b4\uc678\uc758 \ud45c\ud604\ud615 \ub2e4\uc591\uc131\uc740 \ud3c9\uac00 \ubcc0\uc218 \uc120\ud0dd\uc744 \ubaa8\ud638\ud558\uac8c \ud558\uace0 \ucd94\uc801 \uad00\ucc30 \uae30\uac04\uc744 \uc5f0\uc7a5\uc2dc\ud0b5\ub2c8\ub2e4. \uc2e0\uacbd\uadfc \uc9c8\ud658\uc5d0\uc11c \uac80\uc99d\ub41c \uae30\ub2a5 \ucc99\ub3c4\ub294 \uc548\uacfc\uc801 \uac1c\uc120\uc744 \ub193\uce60 \uc218 \uc788\uc73c\uba70, \uc0dd\ud654\ud559\uc801 \ub9c8\ucee4\ub294 \ubcf4\ud3b8\uc801\uc778 \uae30\uc900\uc810\uc774 \ubd80\uc871\ud569\ub2c8\ub2e4.<br \/>\n*   AAV \ubca1\ud130 \ubc0f \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ubd84\ub9ac \ube44\uc6a9(COGS) \ub192\uc74c: AAV \ubca1\ud130 \ubc0f \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ubd84\ub9ac \uacfc\uc815\uc758 \ub192\uc740 \uc81c\uc870 \uc6d0\uac00\ub294 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc81c\uc57d\ud558\ub294 \uc694\uc778 \uc911 \ud558\ub098\uc785\ub2c8\ub2e4.<br \/>\n*   \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uad00\ub828 \uaddc\uc81c \ubd88\ud655\uc2e4\uc131: \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131\uc740 \uad00\ud560\uad8c\uc5d0 \ub530\ub77c \ub2e4\ub974\uba70, \uc774\ub294 \uce58\ub8cc\ubc95 \uac1c\ubc1c \ubc0f \uc0c1\uc6a9\ud654\uc5d0 \uc601\ud5a5\uc744 \ubbf8\uce69\ub2c8\ub2e4.<\/p>\n<p># 5. \uc138\uadf8\uba3c\ud2b8 \ubd84\uc11d<\/p>\n<p>*   \uce58\ub8cc \uc720\ud615\ubcc4: \uc720\uc804\uc790 \uce58\ub8cc\uc758 \uc9c0\ubc30\uc640 \uc138\ud3ec \ud601\uc2e0 \uc18d \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd\uc758 \uc131\uc7a5<br \/>\n    \uc720\uc804\uc790 \uce58\ub8cc\ub294 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 39.54%\ub97c \ucc28\uc9c0\ud558\uba70 \uc9c0\ubc30\uc801\uc778 \uc704\uce58\ub97c \uc720\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uc798 \ud655\ub9bd\ub41c \uc81c\uc870 \ubc0f \uaddc\uc81c \uc7a5\ubcbd\uc744 \uc81c\uacf5\ud558\ub294 AAV \ud50c\ub7ab\ud3fc\uc5d0 \ud798\uc785\uc740 \ubc14 \ud07d\ub2c8\ub2e4. \ucd08\uae30 \uc548\uacfc\uc801 \uc131\uacf5\uc740 \uc804\uc2e0 \uc801\uc6a9\uc758 \uc704\ud5d8\uc744 \uc904\uc600\uc73c\uba70, \uc5ec\ub7ec \uc2a4\ud3f0\uc11c\ub4e4\uc740 \ub354 \ub9ce\uc740 \ud658\uc790 \ud480\uc744 \ud655\ubcf4\ud558\uae30 \uc704\ud574 \ub2e4\uae30\uad00 \uc804\ub2ec \ud504\ub85c\ud1a0\ucf5c\uc744 \ucd94\uad6c\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc57d\ub9ac\ud559\uc801 \uc81c\uc81c\uc640 \uc601\uc591 \ubcf4\uc870\uc81c\ub294 \uc99d\uc0c1 \uc644\ud654\uc5d0 \uae30\uc5ec\ud558\uc9c0\ub9cc, \ubca1\ud130\ud654\ub41c \ud398\uc774\ub85c\ub4dc\ub85c \ub2ec\uc131\ud560 \uc218 \uc788\ub294 \ub3cc\uc5f0\ubcc0\uc774 \uc218\uc900\uc758 \uad50\uc815\uc5d0\ub294 \ubbf8\uce58\uc9c0 \ubabb\ud569\ub2c8\ub2e4. \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc\ub294 \ud604\uc7ac \uac00\uc7a5 \uc791\uc740 \ub9e4\ucd9c\uc744 \uae30\ub85d\ud558\uace0 \uc788\uc9c0\ub9cc, 11.11%\uc758 CAGR\uc744 \uae30\ub85d\ud558\uba70 \uae09\uc131 \uc0c1\ud669\uc5d0\uc11c \uc989\uac01\uc801\uc778 ATP \uc0dd\uc131 \ub2a5\ub825\uc744 \uc81c\uacf5\ud568\uc73c\ub85c\uc368 \uc784\uc0c1\uc801 \uae30\ub300\ub97c \uc7ac\uc124\uc815\ud560 \uc704\uce58\uc5d0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc9c8\ubcd1 \uc801\uc751\uc99d\ubcc4: LHON\uc758 \uc120\ub450 \uc720\uc9c0\uc640 \ub9ac \uc99d\ud6c4\uad70\uc758 \ub3c4\uc804<br \/>\n    \ub808\ubc84 \uc720\uc804\uc131 \uc2dc\uc2e0\uacbd\ubcd1\uc99d(LHON)\uc740 \uad11\ubc94\uc704\ud55c \uc790\uc5f0\uc0ac \uc9c0\uc2dd, \uac80\uc99d\ub41c \uc2dc\ub825 \ud3c9\uac00 \ubcc0\uc218, \ube44\uad50\uc801 \uac04\ub2e8\ud55c \uc720\ub9ac\uccb4\ub0b4 \uc804\ub2ec \ub355\ubd84\uc5d0 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc758 34.81%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 LHON\uc758 \uce58\ub8cc \ud3ec\ud654\ub294 \ud3ec\ud2b8\ud3f4\ub9ac\uc624 \ub2e4\uac01\ud654\ub97c \uc704\ud55c \ubc1c\ud310\uc744 \ub9c8\ub828\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub9ac \uc99d\ud6c4\uad70\uc740 \uac15\ub825\ud55c \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \ub370\uc774\ud130\uc640 POLG \uad00\ub828 \uc0dd\ud654\ud559\uc801 \uacb0\ud568\uc744 \uc644\ud654\ud558\ub294 \ub274\ud074\ub808\uc624\uc0ac\uc774\ub4dc \ubcf5\ud569 \uc694\ubc95\uc5d0 \ud798\uc785\uc5b4 10.36%\uc758 CAGR\ub85c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc2a4\ud3f0\uc11c\ub4e4\uc740 \ubbf8\ucda9\uc871 \uc218\uc694\uac00 \ub192\uace0 \uacbd\uc7c1 \ubc00\ub3c4\uac00 \ub0ae\uc740 \uc911\ucd94\uc2e0\uacbd\uacc4 \ubc0f \uc2ec\ud608\uad00 \ub300\uc0ac \ud45c\ud604\ud615\uc73c\ub85c R&#038;D \uc6b0\uc120\uc21c\uc704\ub97c \uc7ac\uc870\uc815\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc791\uc6a9 \uae30\uc804\ubcc4: \uc720\uc804\uc790 \ub300\uccb4\/\ud3b8\uc9d1\uc758 \uc120\ub450\uc640 \ud3b8\uc9d1 \ub3c4\uad6c\uc758 \uac00\uc18d\ud654<br \/>\n    \uc720\uc804\uc790 \ub300\uccb4 \ubc0f \ud3b8\uc9d1\uc740 AAV \ub9e4\uac1c \ud398\uc774\ub85c\ub4dc\uc758 \uc785\uc99d\ub41c \uc2e4\uc801\uc5d0 \ud798\uc785\uc5b4 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 36.78%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uc5fc\uae30 \ud3b8\uc9d1 \ubc0f mtDNA \ubd84\ud574 \ub3c4\uad6c\ub294 \uc808\ub300 \ub9e4\ucd9c\uc5d0\uc11c\ub294 \ub4a4\ucc98\uc9c0\uc9c0\ub9cc, \uae30\uc874 \ub300\uccb4 \uc811\uadfc \ubc29\uc2dd\uc73c\ub85c\ub294 \ub2ec\uc131\ud560 \uc218 \uc5c6\ub294 \ub3cc\uc5f0\ubcc0\uc774 \uc720\uc804\uccb4\ub97c \uc120\ud0dd\uc801\uc73c\ub85c \uc81c\uac70\ud558\ub294 \ub2a5\ub825\uc73c\ub85c 10.66%\uc758 CAGR\uc744 \uae30\ub85d\ud558\uba70 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \ud558\uc704 \uc138\uadf8\uba3c\ud2b8\ub97c \ub300\ud45c\ud569\ub2c8\ub2e4. \uc0b0\ud654\uc801 \uc778\uc0b0\ud654 \uc870\uc808\uc81c\uc640 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc0dd\ud569\uc131 \ucd09\uc9c4\uc81c\ub294 \uc720\uc804\uc790 \uad50\uc815 \ud6c4 \uc138\ud3ec \uc5d0\ub108\uc9c0 \uade0\ud615\uc744 \ucd5c\uc801\ud654\ud568\uc73c\ub85c\uc368 \uc2dc\ub108\uc9c0 \ud6a8\uacfc\ub97c \uc81c\uacf5\ud569\ub2c8\ub2e4.<br \/>\n*   \ud22c\uc5ec \uacbd\ub85c\ubcc4: \uc720\ub9ac\uccb4\ub0b4 \uc8fc\uc0ac\uc758 \uc9c0\ubc30\uc640 \uc804\uc2e0 \ud22c\uc5ec\uc758 \ub3c4\uc804<br \/>\n    \uc720\ub9ac\uccb4\ub0b4 \uc8fc\uc0ac\ub294 LHON \uc911\uc2ec\uc758 \ud3ec\ud2b8\ud3f4\ub9ac\uc624\uc640 \ub9dd\ub9c9 \uc804\ubb38\uc758\ub4e4 \uc0ac\uc774\uc5d0\uc11c \ud655\ub9bd\ub41c \uc804\ub2ec \ud3b8\uc758\uc131 \ub355\ubd84\uc5d0 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc758 41.28%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uc548\uad6c \ud22c\uc5ec\uc758 \uc548\uc804\uc131 \uacbd\ud5d8\uc740 \ucd08\uae30 \uc2b9\uc778\uc758 \uc704\ud5d8\uc744 \uc904\uc774\uace0 \uc784\uc0c1\uc758\uc758 \uce5c\uc219\ub3c4\ub97c \ub192\uc600\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ub9ce\uc740 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658\uc758 \uc804\uc2e0\uc801 \ubd80\ub2f4\uc740 9.48%\uc758 CAGR\uc744 \uae30\ub85d\ud558\ub294 \uc815\ub9e5 \uc8fc\uc0ac \ud50c\ub7ab\ud3fc\uc5d0 \ub300\ud55c \uad00\uc2ec\uc744 \ubd88\ub7ec\uc77c\uc73c\ud0a4\uace0 \uc788\uc73c\uba70, \uc774\ub294 \uac04 \uaca9\ub9ac \ubc0f \ube44\ud45c\uc801 \ud761\uc218\ub97c \ud574\uacb0\ud558\ub294 \ucea1\uc2dc\ub4dc \uacf5\ud559\uc5d0 \ub300\ud55c \uc2e0\ub8b0 \uc99d\uac00\uc5d0 \ud798\uc785\uc740 \ubc14 \ud07d\ub2c8\ub2e4.<\/p>\n<p># 6. \uc9c0\uc5ed \ubd84\uc11d<\/p>\n<p>*   \ubd81\ubbf8: 2024\ub144 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 44.36%\ub97c \ucc28\uc9c0\ud558\uba70 \uc120\ub450\ub97c \ub2ec\ub838\uc2b5\ub2c8\ub2e4. \uc774\ub294 FDA\uc758 \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c, \ud76c\uadc0 \uc9c8\ud658 \uc13c\ud130\uc758 \uc9d1\uc911\ub41c \uc804\ubb38\uc131, \uace0\uc218\uc775 \ud2c8\uc0c8 \ubc14\uc774\uc624 \uc81c\uc57d\uc5d0 \ub300\ud55c \ud22c\uc790\uc790\ub4e4\uc758 \uad00\uc2ec\uc5d0 \ud798\uc785\uc740 \ubc14 \ud07d\ub2c8\ub2e4. \uad6d\ubc29\ubd80 \ubc0f \uc7ac\ud5a5\uad70\uc778\ud68c\uc640 \uac19\uc740 \uc5f0\ubc29 \uae30\uad00\uc740 \uae09\uc131 \uc190\uc0c1 \ubc0f \uc774\uc2dd \uc5f0\uad6c\uc5d0 \ube44\ud76c\uc11d\uc131 \uc790\uae08\uc744 \ud22c\uc785\ud558\uc5ec \uad6d\ub0b4 \ud30c\uc774\ud504\ub77c\uc778 \ubc00\ub3c4\ub97c \uac15\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591: \uc77c\ubcf8\uc758 \uc7ac\uc0dd\uc758\ub8cc \uc2e0\uc18d \ud2b8\ub799, \ud638\uc8fc\uc758 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uae30\uc99d \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uac00\ub2a5\ud558\uac8c \ud558\ub294 Maeve&#8217;s Law, \uadf8\ub9ac\uace0 \uc911\uad6d\uc758 \uacf5\uc778 \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc81c\uc870 \uc2dc\uc124\uc758 \uc131\uc7a5\uc138\uc5d0 \ud798\uc785\uc5b4 2030\ub144\uae4c\uc9c0 9.83%\uc758 CAGR\ub85c \ud655\uc7a5\ub420 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc5ed\ub0b4 \uc815\ubd80\ub294 \uad6d\ub0b4 \ud601\uc2e0 \uae30\uc5c5\uc758 \uc9c4\uc785 \uc7a5\ubcbd\uc744 \ub0ae\ucd94\uae30 \uc704\ud574 \ubcf4\uc870\uae08 \ubc0f \uc138\uae08 \uc778\uc13c\ud2f0\ube0c\ub97c \uc81c\uacf5\ud558\uace0 \uc788\uc73c\uba70, \ub2e4\uad6d\uc801 \uae30\uc5c5\ub4e4\uc740 \uc5ed\ub7c9 \ud655\ubcf4 \ubc0f \ud604\uc9c0 \uaddc\uc81c \uc900\uc218\ub97c \uc704\ud574 \ud569\uc791 \ud22c\uc790\ub97c \ud615\uc131\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc720\ub7fd: \uad6d\uacbd \uac04 \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uacfc Horizon Europe \uc790\uae08 \uc9c0\uc6d0\uc744 \ud65c\uc6a9\ud558\uc5ec \ud611\ub825 \uc5f0\uad6c \ud5c8\ube0c\ub97c \uc720\uc9c0\ud558\uba70 \uafb8\uc900\ud55c \uc131\uacfc\ub97c \ubcf4\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># 7. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<p>\uc624\ub298\ub0a0 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc740 \ud30c\ud3b8\ud654\ub418\uc5b4 \uc788\uc2b5\ub2c8\ub2e4. \ub2e8\uc77c \uae30\uc804\uc774 \uc784\uc0c1 \uc9c4\ub8cc\ub97c \uc9c0\ubc30\ud558\uc9c0 \uc54a\uc73c\uba70, \uc0c1\uc704 5\uac1c \uae30\uc5c5\uc774 \uc804\uccb4 \ub9e4\ucd9c\uc758 30% \ubbf8\ub9cc\uc744 \ucc28\uc9c0\ud558\uc5ec \ud601\uc2e0\uc744 \uc704\ud55c \uc5ec\uc9c0\uac00 \ub9ce\uc2b5\ub2c8\ub2e4. \uae30\uc5c5\ub4e4\uc740 \ud50c\ub7ab\ud3fc\uc758 \ud3ed\uc744 \ud1b5\ud574 \ucc28\ubcc4\ud654\ud558\uace0 \uc788\uc73c\uba70, Stealth BioTherapeutics\ub294 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ud45c\uc801 \ud3a9\ud0c0\uc774\ub4dc\uc5d0, GenSight\ub294 \uc548\uacfc AAV \ubca1\ud130\uc5d0, Minovia\ub294 \uc790\uac00 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd\uc5d0 \uc9d1\uc911\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uae30\uc874 \uac15\uc790\uc758 \ubd80\uc7ac\ub294 \ud30c\ud2b8\ub108\ub9c1 \ub9c8\ucc30\uc744 \uc904\uc5ec\uc8fc\ubbc0\ub85c, \ud30c\uc774\ud504\ub77c\uc778\uc774 \ud48d\ubd80\ud55c \uc2a4\ud0c0\ud2b8\uc5c5\ub4e4\uc740 \ud658\uc790\uc640 \uae30\uc804 \uc804\ubb38 \uc9c0\uc2dd\uc744 \ubaa8\ub450 \uc81c\uacf5\ud558\ub294 \ud559\uc220 \ucee8\uc18c\uc2dc\uc5c4\uacfc \uc790\uc8fc \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uacf5\ub3d9 \uc9c4\ud589\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc81c\uc870 \uc5ed\ub7c9\uc740 \ubcd1\ubaa9 \ud604\uc0c1\uc774\uc790 \uc804\ub7b5\uc801 \uc790\uc0b0\uc73c\ub85c \uc791\uc6a9\ud569\ub2c8\ub2e4. Lonza\uc640 \uac19\uc740 CDMO(Contract Development and Manufacturing Organization)\ub294 GMP \ub4f1\uae09 AAV\uc5d0 \ub300\ud55c \ub2e4\ub144\uac04\uc758 \uacf5\uae09 \uacc4\uc57d\uc744 \uccb4\uacb0\ud558\uc5ec \ud30c\uc774\ud504\ub77c\uc778 \uc77c\uc815\uc744 \ub4b7\ubc1b\uce68\ud558\uace0 \uc790\uae08 \uc81c\uc57d\uc774 \uc788\ub294 \ubc14\uc774\uc624\ud14d\uc758 \ud575\uc2ec \uc5ed\ud560\uc744 \ud569\ub2c8\ub2e4. \ud55c\ud3b8, \uc601\uad6d MHRA\uc640 \uac19\uc740 \uaddc\uc81c \uae30\uad00\uc774 \ucd08\uc548\uc744 \uc791\uc131\ud55c \ubaa8\ub4c8\ud615 \ud604\uc7a5 \uc9c4\ub8cc \uc9c0\uce68\uc740 \uc804\ud1b5\uc801\uc778 \uacf5\uae09\ub9dd\uc744 \ub4a4\uc5ce\uc744 \uc218 \uc788\ub294 \ubd84\uc0b0\ud615 \uc81c\uc870 \ubaa8\ub378\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4. \uc9c0\uc801 \uc7ac\uc0b0\uad8c \uc804\ub7b5\uc740 \ubca1\ud130 \ucea1\uc2dc\ub4dc \uccad\uad6c\uc640 \uc9c8\ubcd1 \ud2b9\uc774\uc801 \ubc14\uc774\uc624\ub9c8\ucee4 \ud328\ub110\uc744 \ubb36\uc5b4 \ub2e4\uce35\uc801\uc778 \ud574\uc790\ub97c \ub9cc\ub4dc\ub294 \ubc29\ud5a5\uc73c\ub85c \uc9c4\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774\uc2dd \ubc0f \ud3b8\uc9d1 \ubc29\uc2dd \uc804\ubc18\uc5d0 \uac78\uccd0 \uac1c\ub150 \uc99d\uba85 \ub370\uc774\ud130\uac00 \ucd95\uc801\ub428\uc5d0 \ub530\ub77c \uacbd\uc7c1\uc740 \ub354\uc6b1 \uc2ec\ud654\ub420 \uac83\uc785\ub2c8\ub2e4. \ubca1\ud130 \ud50c\ub7ab\ud3fc\uacfc \uc138\ud3ec \ucc98\ub9ac \ub178\ud558\uc6b0\ub97c \uacb0\ud569\ud558\uae30 \uc704\ud55c \uc804\ub7b5\uc801 \ud569\ubcd1\uc774 \uc608\uc0c1\ub418\uba70, \ub300\ud615 \uc81c\uc57d\uc0ac\uc758 \uad00\uc2ec\uc740 \uc81c\uc870 \ud655\uc7a5\uc131\uacfc \uc9c0\ubd88\uc790 \uc218\uc6a9\uc758 \uc608\uce21 \uac00\ub2a5\uc131\uc5d0 \ub2ec\ub824 \uc788\uc744 \uac83\uc785\ub2c8\ub2e4. \uadf8\ub54c\uae4c\uc9c0\ub294 \ubbfc\ucca9\ud55c \ubc14\uc774\uc624\ud14d \uc804\ubb38 \uae30\uc5c5\ub4e4\uc774 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc0b0\uc5c5\uc758 \uc8fc\uc694 \uac00\uce58 \ucc3d\ucd9c\uc790\ub85c \ub0a8\uc744 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc0b0\uc5c5 \ub9ac\ub354: Stealth BioTherapeutics, GenSight Biologics, Santhera Pharmaceuticals, Reata Pharmaceuticals, Astellas (\uc21c\uc11c\ub294 \ubb34\uc791\uc704)<\/p>\n<p># 8. \ucd5c\uadfc \uc0b0\uc5c5 \ub3d9\ud5a5<\/p>\n<p>*   2025\ub144 6\uc6d4: Minovia Therapeutics\ub294 \ud53c\uc5b4\uc2a8 \uc99d\ud6c4\uad70(Pearson syndrome) \uce58\ub8cc\uc81c MNV-201\uc5d0 \ub300\ud574 FDA \uc2e0\uc18d \uc2ec\uc0ac \ubc0f \ud76c\uadc0 \uc18c\uc544 \uc9c8\ud658 \uc9c0\uc815\uc744 \ubc1b\uc558\uc2b5\ub2c8\ub2e4.<br \/>\n*   2025\ub144 5\uc6d4: Khondrion\uc740 sonlicromanol\uc758 3\uc0c1 \uc784\uc0c1 \uc2dc\ud5d8 \uc790\uae08 \uc870\ub2ec\uc744 \uc704\ud574 \ub124\ub35c\ub780\ub4dc \uae30\uc5c5\uccad(Netherlands Enterprise Agency)\uc73c\ub85c\ubd80\ud130 \ucd5c\ub300 500\ub9cc \uc720\ub85c\uc758 \ud601\uc2e0 \uc2e0\uc6a9\uc744 \ud655\ubcf4\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2025\ub144 5\uc6d4: Stealth BioTherapeutics\ub294 \ubc14\ub974\ud2b8 \uc99d\ud6c4\uad70(Barth syndrome) \uce58\ub8cc\uc81c elamipretide\uc5d0 \ub300\ud55c FDA \uc2b9\uc778 \uacbd\ub85c\ub97c \ubcf4\uace0\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2024\ub144 11\uc6d4: Mito Fund\ub294 sonlicromanol\uc758 3\uc0c1 \uac1c\ubc1c\uc744 \uac00\uc18d\ud654\ud558\uae30 \uc704\ud574 Khondrion\uc5d0 \ud22c\uc790\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5\uc5d0 \ub300\ud55c \ud3ec\uad04\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud558\uba70, \uc2dc\uc7a5\uc758 \ud604\uc7ac \uc0c1\ud669, \uc131\uc7a5 \uc804\ub9dd, \uc8fc\uc694 \ub3d9\uc778 \ubc0f \uc81c\uc57d \uc694\uc778, \uacbd\uc7c1 \ud658\uacbd \ub4f1\uc744 \ub2e4\ub8e8\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>2025\ub144 \uae30\uc900 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8\ub294 4\uc5b5 6,816\ub9cc \ub2ec\ub7ec\ub85c \ud3c9\uac00\ub418\uc5c8\uc73c\uba70, 2030\ub144\uc5d0\ub294 7.07%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR)\uc744 \uae30\ub85d\ud558\uba70 6\uc5b5 5,865\ub9cc \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc758 \uc8fc\uc694 \uc131\uc7a5 \ub3d9\ub825\uc73c\ub85c\ub294 \ub808\ubc84 \uc720\uc804\uc131 \uc2dc\uc2e0\uacbd\ubcd1\uc99d(LHON) \ubc0f \ud504\ub9ac\ub4dc\ub9ac\ud788 \uc6b4\ub3d9\uc2e4\uc870\uc99d(FA)\uc5d0 \ub300\ud55c \uc720\uc804\uc790 \uce58\ub8cc\uc81c \uc2b9\uc778, \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \ubca4\ucc98 \uc790\uae08 \uc720\uc785, TALENs, DdCBE \ub4f1 mtDNA \ud3b8\uc9d1 \ud50c\ub7ab\ud3fc\uc758 \ubc1c\uc804, AI \uae30\ubc18 \ub300\uc0ac \uc870\uc808\uc81c \uc7ac\ud65c\uc6a9, \uae09\uc131 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc190\uc0c1 \ub300\uc751\ucc45\uc5d0 \ub300\ud55c \uad70\uc0ac \uc790\uae08 \uc9c0\uc6d0, \uadf8\ub9ac\uace0 \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130(RWE) \ub4f1\ub85d \ud65c\uc6a9 \uc99d\uac00 \ub4f1\uc774 \uaf3d\ud799\ub2c8\ub2e4.<\/p>\n<p>\ubc18\uba74, \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c\ub294 \ub3cc\uc5f0\ubcc0\uc774\ubcc4\ub85c \ub9e4\uc6b0 \uc801\uc740 \ud658\uc790 \ud480, \uc784\uc0c1 \uc2dc\ud5d8 \ud658\uc790 \ubaa8\uc9d1\uc758 \uc5b4\ub824\uc6c0 \ubc0f \uc774\uc9c8\uc801\uc778 \ud3c9\uac00 \ubcc0\uc218, AAV \ubca1\ud130 \ubc0f \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ubd84\ub9ac \ube44\uc6a9\uc758 \ub192\uc740 \uc6d0\uac00, \uadf8\ub9ac\uace0 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131 \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4. \ud2b9\ud788, \uac1c\ubcc4 \ub3cc\uc5f0\ubcc0\uc774\uc5d0 \ub300\ud55c \ud658\uc790 \ud480\uc774 \ub9e4\uc6b0 \uc791\uc544 \uc784\uc0c1 \uc124\uacc4, \uaddc\ubaa8 \ud655\uc7a5 \ubc0f \ubcf4\ud5d8 \uc0c1\ud658\uc5d0 \uc5b4\ub824\uc6c0\uc744 \uacaa\ub294 \uc810\uc774 \uac00\uc7a5 \ud070 \uacfc\uc81c\ub85c \uc9c0\ubaa9\ub429\ub2c8\ub2e4.<\/p>\n<p>\uce58\ub8cc \uc720\ud615\ubcc4 \ubd84\uc11d\uc5d0\uc11c\ub294 \uc720\uc804\uc790 \uce58\ub8cc\uac00 39.54%\uc758 \uc2dc\uc7a5 \uc810\uc720\uc728\ub85c \uc120\ub450\ub97c \ub2ec\ub9ac\uace0 \uc788\uc73c\uba70, \uc774\ub294 \uaddc\uc81c \uc2b9\uc778 \ubc0f \uc784\uc0c1\uc801 \ud6a8\ub2a5\uc5d0 \uae30\uc778\ud569\ub2c8\ub2e4. \uc774 \uc678\uc5d0\ub3c4 \uc57d\ubb3c \uce58\ub8cc\uc81c, \uac74\uac15 \ubcf4\uc870 \uc2dd\ud488, \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc, \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \ud45c\uc801 \ud56d\uc0b0\ud654\uc81c \ub4f1\uc774 \uc8fc\uc694 \uce58\ub8cc \uc720\ud615\uc73c\ub85c \ubd84\uc11d\ub429\ub2c8\ub2e4. \uc9c8\ubcd1 \uc801\uc751\uc99d\ubcc4\ub85c\ub294 LHON, \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uadfc\ubcd1\uc99d, \ub9ac \uc99d\ud6c4\uad70, MELAS \ubc0f \uae30\ud0c0 \uc6d0\ubc1c\uc131 \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc9c8\ud658\uc774 \ub2e4\ub8e8\uc5b4\uc9d1\ub2c8\ub2e4. \uc791\uc6a9 \uae30\uc804\ubcc4\ub85c\ub294 \uc0b0\ud654\uc801 \uc778\uc0b0\ud654 \uc870\uc808\uc81c, \uc720\uc804\uc790 \ub300\uccb4\/\ud3b8\uc9d1, \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc0dd\ud569\uc131 \ucd09\uc9c4\uc81c, mtDNA \ubd84\ud574 \ub3c4\uad6c, \ud6a8\uc18c\/\ubcf4\uc870\uc778\uc790 \ub300\uccb4 \ub4f1\uc774 \ubd84\uc11d \ub300\uc0c1\uc5d0 \ud3ec\ud568\ub429\ub2c8\ub2e4. \ud22c\uc5ec \uacbd\ub85c\ubcc4\ub85c\ub294 \uacbd\uad6c, \uc815\ub9e5 \uc8fc\uc0ac, \uc548\ub0b4 \uc8fc\uc0ac, \ud53c\ud558 \uc8fc\uc0ac \ub4f1\uc774 \uc870\uc0ac\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\uc5ed\ubcc4 \ubd84\uc11d\uc5d0\uc11c\ub294 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 2025\ub144\ubd80\ud130 2030\ub144\uae4c\uc9c0 9.83%\uc758 \uac00\uc7a5 \ube60\ub978 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ubd81\ubbf8, \uc720\ub7fd, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8 \uc9c0\uc5ed \ub610\ud55c \uc0c1\uc138\ud788 \ubd84\uc11d\ub429\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd \uc139\uc158\uc5d0\uc11c\ub294 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4, \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d \ubc0f Stealth BioTherapeutics, GenSight Biologics, Santhera Pharmaceuticals \ub4f1 \uc8fc\uc694 \uae30\uc5c5\ub4e4\uc758 \ud504\ub85c\ud544\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ubbf8\ud1a0\ucf58\ub4dc\ub9ac\uc544 \uc774\uc2dd \uce58\ub8cc\ub294 2025\ub144 \ud604\uc7ac \uc644\uc804\ud55c \uaddc\uc81c \uc2b9\uc778\uc744 \ubc1b\uc740 \uc0ac\ub840\ub294 \uc5c6\uc9c0\ub9cc, \uc2e0\uc18d \uc2ec\uc0ac(Fast Track) \uc9c0\uc815 \ub4f1\uc744 \ud1b5\ud574 \uac1c\ubc1c\uc774 \uac00\uc18d\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ubcf4\uace0\uc11c\ub294 \ub610\ud55c \uc2dc\uc7a5 \uae30\ud68c\uc640 \ubbf8\ub798 \uc804\ub9dd, \ucda9\uc871\ub418\uc9c0 \uc54a\uc740 \uc758\ub8cc \uc218\uc694\uc5d0 \ub300\ud55c \ud3c9\uac00\ub97c \ud3ec\ud568\ud558\uc5ec \uc2dc\uc7a5\uc758 \uc7a0\uc7ac\ub825\uc744 \uc870\uba85\ud569\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-44858","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/44858"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=44858"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/44858\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=44858"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=44858"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=44858"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}