{"id":48473,"date":"2026-02-20T05:34:47","date_gmt":"2026-02-20T05:34:47","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/fabry-disease-treatment-market-mordor\/"},"modified":"2026-10-30T03:16:52","modified_gmt":"2026-10-29T18:16:52","slug":"fabry-disease-treatment-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/fabry-disease-treatment-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2026-2031\ub144)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/fabry-disease-treatment-market_1689164214301_fabry.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/fabry-disease-treatment-market-size-image-1770995574763.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud604\ud669<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 \ud30c\ube0c\ub9ac\ubcd1 \uc720\ubcd1\ub960 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 \uc720\uc804\uc790 \ubc0f mRNA \uae30\ubc18 \uce58\ub8cc\ubc95\uc758 \ubc1c\uc804<\/li>\n<li class=\"toc-level-3\">4.2.3 \uc720\ub9ac\ud55c \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc2e0\uc18d \uc2ec\uc0ac \uc9c0\uc815<\/li>\n<li class=\"toc-level-3\">4.2.4 \ud76c\uadc0 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc804 \uc138\uacc4 \uc758\ub8cc \uc9c0\ucd9c \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.5 \uc804\ub7b5\uc801 \ud611\ub825 \ubc0f \ub77c\uc774\uc120\uc2a4 \uacc4\uc57d<\/li>\n<li class=\"toc-level-3\">4.2.6 \uc6d0\uaca9 \uc758\ub8cc \ubc0f \uac00\uc815 \ub0b4 \uc8fc\uc785 \uc11c\ube44\uc2a4 \ud655\ub300<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \uc9c0\ubd88\uc790\uc758 \uc608\uc0b0 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">4.3.2 \uc2e0\ud765 \uc2dc\uc7a5\uc758 \uc81c\ud55c\ub41c \uc9c4\ub2e8 \uc778\ud504\ub77c<\/li>\n<li class=\"toc-level-3\">4.3.3 \ucca8\ub2e8 \uce58\ub8cc\ubc95\uc758 \uc81c\uc870 \uc5ed\ub7c9 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">4.3.4 \uc5c4\uaca9\ud55c \uc0c1\ud658 \uae30\uc900 \ubc0f \uc811\uadfc \uc7a5\ubcbd<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \uaddc\uc81c \ud658\uacbd<\/li>\n<li class=\"toc-level-2\">4.5 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.5.1 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.2 \uad6c\ub9e4\uc790\/\uc18c\ube44\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.5.3 \uacf5\uae09\uc5c5\uccb4\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.5.4 \ub300\uccb4 \uc81c\ud488\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc608\uce21 (\uac00\uce58, USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uce58\ub8cc\ubc95\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95<\/li>\n<li class=\"toc-level-3\">5.1.2 \uacbd\uad6c \uc0e4\ud398\ub860 \uc694\ubc95<\/li>\n<li class=\"toc-level-3\">5.1.3 \uc720\uc804\uc790 \uce58\ub8cc<\/li>\n<li class=\"toc-level-3\">5.1.4 \uae30\uc9c8 \uac10\uc18c \uc694\ubc95<\/li>\n<li class=\"toc-level-3\">5.1.5 \uae30\ud0c0 \uce58\ub8cc\ubc95<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \ud22c\uc5ec \uacbd\ub85c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc815\ub9e5<\/li>\n<li class=\"toc-level-3\">5.2.2 \uacbd\uad6c<\/li>\n<li class=\"toc-level-3\">5.2.3 \ud53c\ud558<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc720\ud1b5 \ucc44\ub110\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ubcd1\uc6d0 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.2 \uc18c\ub9e4 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.3 \uc804\ubb38 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.4 \uc628\ub77c\uc778 \uc57d\uad6d<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.4.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.4.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.4.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.4.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.4.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.4.2.6 \uae30\ud0c0 \uc720\ub7fd<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.4.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.4.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.4.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.4.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.6 \uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-3\">5.4.4 \uc911\ub3d9 &amp; \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.4.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.3 \uae30\ud0c0 \uc911\ub3d9 &amp; \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-5\">5.4.4.3.1 GCC<\/li>\n<li class=\"toc-level-3\">5.4.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.4.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.4.5.3 \uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uac1c\uc694, \uc2dc\uc7a5 \uac1c\uc694, \ud575\uc2ec \uc0ac\uc5c5 \ubd80\ubb38, \uc7ac\ubb34, \uc778\ub825, \uc8fc\uc694 \uc815\ubcf4, \uc2dc\uc7a5 \uc21c\uc704, \uc2dc\uc7a5 \uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ubd84\uc11d \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 \uc0ac\ub178\ud53c (\uc820\uc790\uc784)<\/li>\n<li class=\"toc-level-3\">6.3.2 \ub2e4\ucf00\ub2e4 \uc81c\uc57d<\/li>\n<li class=\"toc-level-3\">6.3.3 \uc544\ubbf8\ucfe0\uc2a4 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.4 \ud0a4\uc5d0\uc2dc \ud30c\ub9c8\uc288\ud2f0\uce58<\/li>\n<li class=\"toc-level-3\">6.3.5 \ud504\ub85c\ud0c8\ub9ad\uc2a4 \ubc14\uc774\uc624\ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.6 JCR \ud30c\ub9c8\uc288\ud2f0\uceec\uc988 \uc8fc\uc2dd\ud68c\uc0ac<\/li>\n<li class=\"toc-level-3\">6.3.7 \uc774\uc218\uc571\uc9c0\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.8 \ud504\ub9ac\ub77c\uc778 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.9 \uc720\ud55c\uc591\ud589<\/li>\n<li class=\"toc-level-3\">6.3.10 M6P \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.11 \uc544\ube0c\ub85c\ubc14\uc774\uc624<\/li>\n<li class=\"toc-level-3\">6.3.12 \uc0c1\uac00\ubaa8 \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.13 4D \ubd84\uc790 \uce58\ub8cc\uc81c<\/li>\n<li class=\"toc-level-3\">6.3.14 \uc774\ub3c4\ub974\uc2dc\uc544<\/li>\n<li class=\"toc-level-3\">6.3.15 \ubc14\uc774\uc624\ub9c8\ub9b0 \ud30c\ub9c8\uc288\ud2f0\uceec<\/li>\n<li class=\"toc-level-3\">6.3.16 \uc624\ucc28\ub4dc \ud14c\ub77c\ud4e8\ud2f1\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.17 \ubaa8\ub354\ub098 Tx<\/li>\n<li class=\"toc-level-3\">6.3.18 \uc6b8\ud2b8\ub77c\uc81c\ub2c9\uc2a4<\/li>\n<li class=\"toc-level-3\">6.3.19 \ub85c\ucf13 \ud30c\ub9c8\uc288\ud2f0\uceec\uc988<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c &amp; \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uac1c\uc694: \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f 2031\ub144 \uc804\ub9dd<\/p>\n<p>\ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 \ud76c\uadc0 \uc720\uc804 \uc9c8\ud658\uc778 \ud30c\ube0c\ub9ac\ubcd1\uc758 \uc9c4\ub2e8 \ubc0f \uce58\ub8cc\uc5d0 \uc0ac\uc6a9\ub418\ub294 \uc758\uc57d\ud488 \ubc0f \uc694\ubc95\uc744 \ud3ec\uad04\ud558\uba70, 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uacac\uace0\ud55c \uc131\uc7a5\uc774 \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774 \uc2dc\uc7a5\uc740 \uae30\uc874\uc758 \uaca9\uc8fc \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT) \uc8fc\uc785 \ubc29\uc2dd\uc5d0\uc11c \ub2e8\uc77c \ud22c\uc5ec \uc720\uc804\uc790 \uce58\ub8cc \ubc0f \uacbd\uad6c \uae30\uc9c8 \uac10\uc18c \uc694\ubc95\uc73c\ub85c \uc9c4\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub2a6\uc740 \ubc1c\ubcd1 \ubcc0\uc774\ud615\uc5d0 \ub300\ud55c \uc784\uc0c1\uc801 \uc778\uc2dd \uc99d\uac00, \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac \ud655\ub300, \uadf8\ub9ac\uace0 \ud76c\uadc0\uc758\uc57d\ud488\uc5d0 \ub300\ud55c \uc6b0\ud638\uc801\uc778 \uaddc\uc81c \ud658\uacbd\uc774 \uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \uac00\uc18d\ud654\ud558\ub294 \uc8fc\uc694 \uc694\uc778\uc73c\ub85c \uc791\uc6a9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>1. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc804\ub9dd<\/p>\n<p>Mordor Intelligence\uc758 \ubd84\uc11d\uc5d0 \ub530\ub974\uba74, \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 2025\ub144 26\uc5b5 3\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2026\ub144 28\uc5b5 3\ucc9c\ub9cc \ub2ec\ub7ec\ub85c \uc131\uc7a5\ud588\uc73c\uba70, 2031\ub144\uc5d0\ub294 40\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0 \ub3c4\ub2ec\ud558\uc5ec 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 7.63%\ub97c \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \ubd81\ubbf8 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud558\uace0 \uc788\uc73c\uba70, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\ub294 \uc911\uac04 \uc218\uc900\uc73c\ub85c \ud3c9\uac00\ub429\ub2c8\ub2e4.<\/p>\n<p>2. \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \uc131\uc7a5 \ub3d9\ub825<\/p>\n<p>\ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \ub3d9\ub825\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \ud30c\ube0c\ub9ac\ubcd1 \uc720\ubcd1\ub960 \uc99d\uac00: \uc120\ubcc4 \ud504\ub85c\uadf8\ub7a8\uc758 \uc7ac\ud3c9\uac00 \uacb0\uacfc, \ud30c\ube0c\ub9ac\ubcd1\uc740 \uc57d 1\ub9cc \uba85\ub2f9 1\uba85\uc5d0\uac8c \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 \uac83\uc73c\ub85c \ub098\ud0c0\ub0ac\uc73c\uba70, \uc774\ub294 \uc774\uc804 \ucd94\uc815\uce58\ubcf4\ub2e4 4\ubc30 \uc99d\uac00\ud55c \uc218\uce58\uc785\ub2c8\ub2e4. \ud2b9\ud788 \ub2a6\uc740 \ubc1c\ubcd1 \ud615\ud0dc\uac00 \ub300\ubd80\ubd84\uc758 \uc99d\uc0c1\uc131 \uc0ac\ub840\ub97c \ucc28\uc9c0\ud558\uba70, \uc7a5\uae30 \uc190\uc0c1\uc774 \uc9c4\ud589\ub420 \ub54c\uae4c\uc9c0 \uc9c4\ub2e8\ub418\uc9c0 \uc54a\ub294 \uacbd\uc6b0\uac00 \ub9ce\uc544 \uce58\ub8cc\ubc1b\uc9c0 \uc54a\uc740 \uc131\uc778 \ud658\uc790\uce35\uc774 \uc0c1\ub2f9\ud569\ub2c8\ub2e4. \uc2e0\uc7a5 \ubc0f \uc2ec\uc7a5\ud559 \uc120\ubcc4 \uac80\uc0ac \ud655\ub300\uc640 \uc5ec\ub7ec \uad6d\uac00\uc5d0\uc11c\uc758 \uc2e0\uc0dd\uc544 \uac80\uc0ac \ub3c4\uc785\uc740 \uc7a0\uc7ac \ud658\uc790\uad70\uc744 \uc804\ubb38 \ud074\ub9ac\ub2c9\uc73c\ub85c \uc720\uc785\uc2dc\ucf1c \uc2dc\uc7a5 \uc218\uc694\ub97c \uc9c0\uc18d\uc801\uc73c\ub85c \ub4b7\ubc1b\uce68\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc720\uc804\uc790 \ubc0f mRNA \uae30\ubc18 \uce58\ub8cc\ubc95 \ubc1c\uc804: \uc5ec\ub7ec AAV(Adeno-Associated Virus) \uae30\ubc18 \ubca1\ud130\uac00 \ucd5c\uc18c 2\ub144 \ub3d9\uc548 \uc9c0\uc18d\uc801\uc778 \u03b1-\uac08\ub77d\ud1a0\uc2dc\ub2e4\uc544\uc81c A \ubc1c\ud604\uc744 \ubcf4\uc5ec \uba74\uc5ed\uc6d0\uc131 \ubc0f \uc8fc\uc785 \ubd80\ub2f4\uc744 \ucd5c\uc18c\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. Sangamo\uc758 ST-920\uc5d0 \ub300\ud55c FDA\uc758 \uac00\uc18d \uc2b9\uc778 \uacbd\ub85c \ud569\uc758\ub294 \ubc14\uc774\uc624\ub9c8\ucee4 \uae30\ubc18 \ud3c9\uac00 \uc9c0\ud45c\uc5d0 \ub300\ud55c \uaddc\uc81c \ub2f9\uad6d\uc758 \uc2e0\ub8b0 \uc99d\uac00\ub97c \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. uniQure\uc758 AMT-191\uacfc Exegenesis Bio\uc758 EXG110\uc740 \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815\uc744 \ubc1b\uc558\uc73c\uba70, \ucd08\uae30 \uc548\uc804\uc131 \ub370\uc774\ud130\ub294 \ub2e8\uc77c \ud22c\uc5ec\ub85c \uce58\ub8cc \uac00\ub2a5\uc131\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ubc1c\uc804\uc740 \ud22c\uc790\uc790\ub4e4\uc758 \uad00\uc2ec\uc744 \ub192\uc774\uace0 \uc2dc\uc7a5\uc744 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc \ubc29\uc2dd\uc73c\ub85c \uc774\ub04c\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc6b0\ud638\uc801\uc778 \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc2e0\uc18d \uc2ec\uc0ac \uc9c0\uc815: 7\ub144\uac04\uc758 \uc2dc\uc7a5 \ub3c5\uc810\uad8c, \uc138\uae08 \uacf5\uc81c, \uc6b0\uc120 \uc2ec\uc0ac \ubc14\uc6b0\ucc98\ub294 \uc2dc\uc7a5 \ucd9c\uc2dc \uae30\uac04\uc744 \ub2e8\ucd95\ud558\uace0 \uac00\uaca9 \uc720\uc5f0\uc131\uc744 \ubcf4\ud638\ud569\ub2c8\ub2e4. \uc778\ud50c\ub808\uc774\uc158 \uac10\ucd95\ubc95(IRA)\uc758 \ud76c\uadc0\uc758\uc57d\ud488 \uba74\uc81c \uc870\ud56d\uc740 \ud76c\uadc0 \uc9c8\ud658 \uce58\ub8cc\uc81c\ub97c \uc758\ubb34\uc801\uc778 \uba54\ub514\ucf00\uc5b4 \ud611\uc0c1\uc5d0\uc11c \ubcf4\ud638\ud558\uc5ec \uc218\uc775 \uc7a0\uc7ac\ub825\uc744 \uc720\uc9c0\ud569\ub2c8\ub2e4. \uc774\ub7ec\ud55c \uc815\ucc45\uc801 \uc9c0\uc6d0\uc740 \ud30c\uc774\ud504\ub77c\uc778 \ud22c\uc790 \uc704\ud5d8\uc744 \uc904\uc774\uace0 \uc0c8\ub85c\uc6b4 \uce58\ub8cc\uc81c\uc758 \uac00\uc6a9\uc131\uc744 \uac00\uc18d\ud654\ud569\ub2c8\ub2e4.<br \/>\n*   \ud76c\uadc0 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc804 \uc138\uacc4 \uc758\ub8cc \uc9c0\ucd9c \uc99d\uac00: \ud76c\uadc0\uc758\uc57d\ud488\uc740 2026\ub144\uae4c\uc9c0 \uc804\uccb4 \ucc98\ubc29 \uc9c0\ucd9c\uc758 20%\ub97c \ucc28\uc9c0\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ud76c\uadc0 \uc9c8\ud658 \ud658\uc790 1\uc778\ub2f9 \ud3c9\uade0 \uc5f0\uac04 \uce58\ub8cc \ube44\uc6a9\uc740 14\ub9cc 7\ucc9c \ub2ec\ub7ec\ub85c \uc99d\uac00\ud588\uc73c\uba70, \uc77c\ubd80 \uc2dc\uc7a5\uc5d0\uc11c\ub294 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc\uc81c\uac00 \uc5f0\uac04 40\ub9cc \ub2ec\ub7ec\ub97c \ucd08\uacfc\ud569\ub2c8\ub2e4. \uc911\uad6d \ud558\uc774\ub09c\uc131\uc758 \ud76c\uadc0 \uc9c8\ud658 \uc9c0\ucd9c\uc774 2019\ub144\ubd80\ud130 2023\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 88.99% \uc131\uc7a5\ud55c \uac83\uc740 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc744 \ub4b7\ubc1b\uce68\ud558\ub294 \uc790\uc6d0 \ud22c\uc785\uc758 \uc99d\uac00\ub97c \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<br \/>\n*   \uc804\ub7b5\uc801 \ud611\ub825 \ubc0f \ub77c\uc774\uc120\uc2a4 \uacc4\uc57d, \uc6d0\uaca9 \uc758\ub8cc \ubc0f \uc7ac\ud0dd \uc8fc\uc785 \uc11c\ube44\uc2a4 \ud655\ub300 \ub610\ud55c \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \uae0d\uc815\uc801\uc778 \uc601\ud5a5\uc744 \ubbf8\uce58\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>3. \uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778<\/p>\n<p>\uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc8fc\uc694 \uc81c\uc57d \uc694\uc778\uc740 \ub2e4\uc74c\uacfc \uac19\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \uc9c0\ubd88\uc790 \uc608\uc0b0 \uc81c\uc57d: Elfabrio\uc758 \uc5f0\uac04 \uac00\uaca9\uc774 43\ub9cc \ub2ec\ub7ec\ub97c \ucd08\uacfc\ud558\ub294 \ub4f1 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc\ub294 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uac00\uc7a5 \ube44\uc2fc \ucc98\ubc29 \uc911 \ud558\ub098\uc785\ub2c8\ub2e4. \ubcf4\ud5d8\uc0ac\ub4e4\uc740 \uc885\uc885 \uc7a5\uae30 \ubcd1\ub9ac\uac00 \ud655\uc778\ub420 \ub54c\uae4c\uc9c0 \uc0c1\ud658\uc744 \uc81c\ud55c\ud558\uc5ec \uce58\ub8cc \uc2dc\uc791\uc744 \uc9c0\uc5f0\uc2dc\ud0a4\uace0 \uc608\ud6c4\ub97c \uc545\ud654\uc2dc\ud0ac \uc218 \uc788\uc2b5\ub2c8\ub2e4. \uc2e0\ud765 \uc2dc\uc7a5\uc5d0\uc11c\ub294 \uac00\ubcc0\uc801\uc778 \uacf5\uacf5 \uc7ac\uc815 \uc9c0\uc6d0\uc73c\ub85c \uc778\ud574 \ud658\uc790\ub4e4\uc774 \ub9c9\ub300\ud55c \ubcf8\uc778 \ubd80\ub2f4\uae08\uc744 \uc9c0\ubd88\ud574\uc57c \ud558\uba70, \uc774\ub294 \uc784\uc0c1\uc801 \ud544\uc694\uc131 \uc99d\uac00\uc5d0\ub3c4 \ubd88\uad6c\ud558\uace0 \uc2dc\uc7a5 \uce68\ud22c\uc728\uc744 \ub0ae\ucd94\ub294 \uc694\uc778\uc774 \ub429\ub2c8\ub2e4.<br \/>\n*   \uc2e0\ud765 \uc2dc\uc7a5\uc758 \uc81c\ud55c\ub41c \uc9c4\ub2e8 \uc778\ud504\ub77c: \uc815\uad50\ud55c \ud6a8\uc18c \ubd84\uc11d \ubc0f \uc720\uc804\uc790 \uc2dc\ud000\uc2f1\uc740 \uc8fc\uc694 \ub3c4\uc2dc \uc678 \uc9c0\uc5ed\uc5d0\uc11c\ub294 \uc5ec\uc804\ud788 \ubd80\uc871\ud569\ub2c8\ub2e4. \uc2e0\uacbd\ubcd1\uc131 \ud1b5\uc99d, \ub2e8\ubc31\ub1e8, \ube44\ub300\uc131 \uc2ec\uadfc\ubcd1\uc99d\uc774 \ub354 \ud754\ud55c \uc9c8\ud658\uacfc \uc720\uc0ac\ud558\uc5ec \uc624\uc9c4\uc774 \ud754\ud569\ub2c8\ub2e4. \ub9ce\uc740 \uc800\uc18c\ub4dd \ubc0f \uc911\uac04 \uc18c\ub4dd \uad6d\uac00\uc5d0\uc11c \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac\uac00 \ubd80\uc7ac\ud558\uc5ec \uc9c4\ub2e8\uc774 \uc218\ub144 \uc9c0\uc5f0\ub418\uace0, \uc774\ub294 \uce58\ub8cc\ubc1b\ub294 \ud658\uc790\uad70\uc744 \ucd95\uc18c\uc2dc\ucf1c \uc2dc\uc7a5 \ud655\uc7a5\uc744 \uc800\ud574\ud569\ub2c8\ub2e4.<br \/>\n*   \ucca8\ub2e8 \uce58\ub8cc\ubc95\uc758 \uc81c\uc870 \uc5ed\ub7c9 \uc81c\uc57d \ubc0f \uc5c4\uaca9\ud55c \uc0c1\ud658 \uae30\uc900 \ubc0f \uc811\uadfc\uc131 \uc7a5\ubcbd \ub610\ud55c \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \ubd80\uc815\uc801\uc778 \uc601\ud5a5\uc744 \ubbf8\uce69\ub2c8\ub2e4.<\/p>\n<p>4. \uc138\uadf8\uba3c\ud2b8 \ubd84\uc11d<\/p>\n<p>*   \uce58\ub8cc\ubc95\ubcc4: \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(ERT)\uc740 2025\ub144 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \ub9e4\ucd9c\uc758 67.85%\ub97c \ucc28\uc9c0\ud558\uba70 \uc784\uc0c1 \uc9c4\ub8cc\uc758 \ud575\uc2ec\uc73c\ub85c \uc790\ub9ac \uc7a1\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \uc720\uc804\uc790 \uce58\ub8cc\ub294 \ub2e8\uc77c \ud22c\uc5ec\ub85c \uc7a0\uc7ac\uc801\uc73c\ub85c \uc644\uce58 \uac00\ub2a5\ud55c \uc194\ub8e8\uc158\uc5d0 \ub300\ud55c \ud658\uc790 \uc218\uc694\ub97c \ubc18\uc601\ud558\uc5ec 9.18%\uc758 CAGR\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uacbd\uad6c\uc6a9 \uc0e4\ud398\ub860 \ubbf8\uac08\ub77c\uc2a4\ud0c0\ud2b8\ub294 \ud2b9\uc815 \ub3cc\uc5f0\ubcc0\uc774 \ud658\uc790\uc5d0\uac8c \uc801\uc6a9\ub418\uba70, \uae30\uc9c8 \uac10\uc18c\uc81c \ubcb5\uae00\ub8e8\uc2a4\ud0c0\ud2b8\ub294 \uc2e0\uacbd\ubcd1\uc131 \ud1b5\uc99d \uad00\ub9ac\ub97c \uc704\ud574 3\uc0c1 \uc784\uc0c1 \uc2dc\ud5d8 \uc911\uc785\ub2c8\ub2e4. \uc774\ub7ec\ud55c \ub2e4\uc591\ud55c \ud30c\uc774\ud504\ub77c\uc778\uc740 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc774 \ub2e8\uc77c \uce58\ub8cc\ubc95 \uc9c0\ubc30\uac00 \uc544\ub2cc \ub2e4\uc6d0\uc801\uc778 \uce58\ub8cc \ubc29\uc2dd\uc73c\ub85c \uc804\ud658\ub420 \uac83\uc784\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4.<br \/>\n*   \ud22c\uc5ec \uacbd\ub85c\ubcc4: \uc815\ub9e5 \uc8fc\uc0ac(Intravenous)\ub294 \ubaa8\ub4e0 \uc2b9\uc778\ub41c ERT\uac00 \uc815\ub9e5 \uc811\uadfc\uc744 \ud544\uc694\ub85c \ud558\ubbc0\ub85c 2025\ub144 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8\uc758 72.60%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ud658\uc790\ub4e4\uc774 \uc790\uac00 \ud22c\uc5ec\uac00 \uac00\ub2a5\ud55c \ud53c\ud558 \uc8fc\uc0ac(Subcutaneous) \uc81c\ud615\uc744 \uc120\ud638\ud568\uc5d0 \ub530\ub77c \uc774 \uacbd\ub85c\ub294 9.21%\uc758 CAGR\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uacbd\uad6c\uc6a9 \ubbf8\uac08\ub77c\uc2a4\ud0c0\ud2b8\ub294 \ud2b9\uc815 \ub3cc\uc5f0\ubcc0\uc774 \ud658\uc790\uc5d0\uac8c \ud0c1\uc6d4\ud55c \ud3b8\uc758\uc131\uc744 \uc81c\uacf5\ud558\uc9c0\ub9cc, \uc81c\ud55c\ub41c \ud2c8\uc0c8\uc2dc\uc7a5\uc744 \uacf5\ub7b5\ud569\ub2c8\ub2e4.<br \/>\n*   \uc720\ud1b5 \ucc44\ub110\ubcc4: \ubcd1\uc6d0 \uc57d\uad6d\uc740 \ubcd1\uc6d0 \ub0b4 \uc8fc\uc785 \uce58\ub8cc\uc758 \uc9c0\ubc30\ub825\uc5d0 \ud798\uc785\uc5b4 2025\ub144 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 55.70%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \ud2b9\uc218 \uc57d\uad6d(Specialty Pharmacies)\uc740 \ubcf5\uc7a1\ud55c \uc870\uc81c, \uac04\ud638 \uc870\uc815, \ubcf4\ud5d8 \uc548\ub0b4 \ub4f1 \uace0\ub3c4\uc758 \uad00\ub9ac\uac00 \ud544\uc694\ud55c \ud76c\uadc0 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc11c\ube44\uc2a4\ub97c \uc81c\uacf5\ud558\uba70 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 10.05%\uc758 \uac00\uc7a5 \ub192\uc740 CAGR\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>5. \uc9c0\uc5ed \ubd84\uc11d<\/p>\n<p>*   \ubd81\ubbf8: 2025\ub144 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5 \ub9e4\ucd9c\uc758 42.85%\ub97c \ucc28\uc9c0\ud558\uba70 \uc120\ub450\ub97c \ub2ec\ub838\uc2b5\ub2c8\ub2e4. \uad11\ubc94\uc704\ud55c \uc2e0\uc0dd\uc544 \uc120\ubcc4 \uac80\uc0ac, \uc804\ubb38 \uc13c\ud130, \ud3ec\uad04\uc801\uc778 \uc0c1\ud658 \uc2dc\uc2a4\ud15c\uc774 \uc131\uc7a5\uc744 \ub4b7\ubc1b\uce68\ud569\ub2c8\ub2e4. FDA\uc758 \uc6b0\uc120 \ubc0f \ud601\uc2e0 \uce58\ub8cc\uc81c \uc9c0\uc815\uc740 \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95\uc758 \uc2e0\uc18d\ud55c \ucc44\ud0dd\uc744 \uac00\ub2a5\ud558\uac8c \ud569\ub2c8\ub2e4.<br \/>\n*   \uc720\ub7fd: \ub450 \ubc88\uc9f8\ub85c \ud070 \uc2dc\uc7a5\uc73c\ub85c, EMA\ub97c \ud1b5\ud55c \uad6d\uacbd \uac04 \uaddc\uc81c \uc870\ud654\uc640 \uc7a5\uae30 \uacb0\uacfc\ub97c \ucd94\uc801\ud558\ub294 \uac15\ub825\ud55c \ud559\uc220 \ub4f1\ub85d \uc2dc\uc2a4\ud15c\uc758 \ud61c\ud0dd\uc744 \ubc1b\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ucd5c\uadfc \uc2a4\ucf54\ud2c0\ub79c\ub4dc\uc5d0\uc11c pegunigalsidase alfa\uac00 \uc2b9\uc778\ub41c \uac83\uc740 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \uc9c0\uc18d\uc801\uc778 \uc9c0\uc5ed \ud655\uc7a5\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<br \/>\n*   \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591: 8.28%\uc758 CAGR\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc9c0\uc5ed\uc785\ub2c8\ub2e4. \uc77c\ubcf8\uc758 \uc870\uac74\ubd80 \uc870\uae30 \uc811\uadfc \ud504\ub808\uc784\uc6cc\ud06c\uc640 \ud55c\uad6d\uc758 ERT \uad6d\uac00 \ubcf4\ud5d8 \uc801\uc6a9\uc740 \uc131\uc219\ud55c \uc2dc\uc2a4\ud15c \uc5ed\ub7c9\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \uc911\uad6d\uc758 \ud76c\uadc0 \uc9c8\ud658 \ubaa9\ub85d \ud655\ub300, \uc0c1\ud658 \uac1c\uc120, \uad6d\ub0b4 \ubc14\uc774\uc624 \uae30\uc220 \ud22c\uc790\ub294 \uc2dc\uc7a5 \uce68\ud22c\ub97c \uac00\uc18d\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc778\ub3c4\uc640 \ub3d9\ub0a8\uc544\uc2dc\uc544\uc758 \uc784\uc0c1 \uc2dc\ud5d8 \ud65c\ub3d9 \ubc0f \uc778\ud504\ub77c \uc5c5\uadf8\ub808\uc774\ub4dc\ub294 \ud5a5\ud6c4 \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc758 \ucd94\uac00\uc801\uc778 \uc131\uc7a5\uc744 \uc2dc\uc0ac\ud569\ub2c8\ub2e4.<\/p>\n<p>6. \uacbd\uc7c1 \ud658\uacbd \ubc0f \uc8fc\uc694 \uae30\uc5c5<\/p>\n<p>\ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 \uc911\uac04 \uc815\ub3c4\uc758 \uc9d1\uc911\ub3c4\ub97c \ubcf4\uc774\uc9c0\ub9cc \uacbd\uc7c1\uc774 \uc2ec\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. Sanofi, Takeda, Chiesi\ub294 \uae30\uc874 ERT \ud504\ub79c\ucc28\uc774\uc988\ub97c \ubc29\uc5b4\ud558\uba70 \ubc14\uc774\uc624\uc2dc\ubc00\ub7ec \uc704\ud611\uc5d0 \ub300\uc751\ud558\uae30 \uc704\ud574 \uc81c\uc870 \uaddc\ubaa8\ub97c \ud655\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. Amicus Therapeutics\ub294 \uacbd\uad6c\uc6a9 \ubbf8\uac08\ub77c\uc2a4\ud0c0\ud2b8\uc758 \ucc28\ubcc4\ud654\ub97c \ud1b5\ud574 2024\ub144 5\uc5b5 2,830\ub9cc \ub2ec\ub7ec\uc758 \ub9e4\ucd9c\uc744 \uae30\ub85d\ud558\uba70 33%\uc758 \uc5f0\uac04 \uc131\uc7a5\uc744 \ub2ec\uc131, \uac15\ub825\ud55c \uc758\uc0ac \ucc44\ud0dd\uc744 \ud655\uc778\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc720\uc804\uc790 \uce58\ub8cc \ubd84\uc57c\uc758 \uacbd\uc7c1\uc790\ub4e4\uc740 \uc644\uce58 \uac00\ub2a5\uc131\uc744 \ubaa9\ud45c\ub85c \ud569\ub2c8\ub2e4. Sangamo\uc758 ST-920\uc740 eGFR \uae30\uc6b8\uae30\ub97c \uae30\ubc18\uc73c\ub85c \ud55c \uac00\uc18d \uc2b9\uc778\uc5d0 \ub300\ud574 FDA\uc640 \ud569\uc758\ud588\uc73c\uba70, 2027\ub144\uae4c\uc9c0 \ucd9c\uc2dc\ub97c \ubaa9\ud45c\ub85c \ud569\ub2c8\ub2e4. uniQure\uc758 AMT-191\uacfc Exegenesis\uc758 EXG110\uc740 \uacbd\uc7c1 \ub2e4\uc591\uc131\uc744 \ub354\ud558\uc5ec \ud658\uc790 \uc120\ud0dd\uad8c\uacfc \uac00\uaca9 \uaddc\uc728\uc744 \uac15\ud654\ud569\ub2c8\ub2e4. Protalix\uc640 Chiesi\uc758 Pegylated PRX-102\ub294 ERT \ud074\ub798\uc2a4 \ub0b4\uc5d0\uc11c \uc8fc\uc785 \uac04\uaca9\uc744 4\uc8fc\ub85c \uc5f0\uc7a5\ud558\uace0 \uc57d\ub3d9\ud559\uc744 \uac1c\uc120\ud558\ub294 \uc810\uc9c4\uc801\uc778 \ud601\uc2e0\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4.<\/p>\n<p>\uacf5\uae09\ub9dd \uc2e0\ub8b0\uc131\uacfc \ud658\uc790 \uc9c0\uc6d0 \ud504\ub85c\uadf8\ub7a8\uc740 \uacb0\uc815\uc801\uc778 \ucc28\ubcc4\ud654 \uc694\uc18c\ub85c \ubd80\uc0c1\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud2b9\uc218 \uc57d\uad6d\uacfc \uc7ac\ud0dd \uc8fc\uc785 \uc11c\ube44\uc2a4 \uc81c\uacf5\uc5c5\uccb4\ub294 \ub514\uc9c0\ud138 \uc21c\uc751\ub3c4 \ub3c4\uad6c\uc640 \uac04\ud638\uc0ac \ucf54\uce6d\uc744 \ud1b5\ud569\ud558\uc5ec \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc774 \uc9c4\ud654\ud568\uc5d0 \ub530\ub77c \uacbd\uc7c1\uc790\ub4e4\uc774 \ub530\ub77c\uc7a1\uc544\uc57c \ud560 \uc11c\ube44\uc2a4 \uacc4\uce35\uc744 \uad6c\ucd95\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uae30\uc5c5\uc73c\ub85c\ub294 Sanofi (Genzyme Corporation), Takeda Pharmaceutical Company Limited, Amicus Therapeutics, Inc., ISU ABXIS, JCR Pharmaceuticals Co., Ltd. \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>7. \ucd5c\uadfc \uc0b0\uc5c5 \ub3d9\ud5a5<\/p>\n<p>*   2025\ub144 2\uc6d4: Amicus Therapeutics\ub294 2024\ub144 5\uc5b5 2,830\ub9cc \ub2ec\ub7ec\uc758 \uae30\ub85d\uc801\uc778 \ub9e4\ucd9c\uc744 \ub2ec\uc131\ud558\uba70 \uc804\ub144 \ub300\ube44 33% \uc99d\uac00\ud588\uace0, 2028\ub144 \ub9e4\ucd9c \uac00\uc774\ub358\uc2a4\ub97c 10\uc5b5 \ub2ec\ub7ec \uc774\uc0c1\uc73c\ub85c \uc0c1\ud5a5 \uc870\uc815\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2025\ub144 1\uc6d4: Sangamo Therapeutics\ub294 ST-920\uc758 \uac00\uc18d \uc2b9\uc778\uc744 \uc704\ud574 1\ub144 eGFR \uae30\uc6b8\uae30\uac00 \uc9c0\uc9c0\ub420 \uac83\uc774\ub77c\ub294 FDA \ud569\uc758\ub97c \ud655\ubcf4\ud588\uc73c\uba70, 2026\ub144 \ud558\ubc18\uae30 BLA(\uc0dd\ubb3c\ud559\uc801 \uc81c\uc81c \ud5c8\uac00 \uc2e0\uccad) \uc81c\ucd9c\uc744 \uc608\uc0c1\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   2024\ub144 12\uc6d4: Exegenesis Bio\ub294 EXG110\uc5d0 \ub300\ud574 FDA \ud76c\uadc0\uc758\uc57d\ud488 \uc9c0\uc815\uc744 \ud68d\ub4dd\ud558\uace0 \uc911\uad6d\uc5d0\uc11c 1\uc0c1 \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uc2dc\uc791\ud588\uc73c\uba70, \ubbf8\uad6d \ud658\uc790 \ub4f1\ub85d\ub3c4 \uacc4\ud68d\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   2024\ub144 9\uc6d4: Chiesi\ub294 \ud30c\ube0c\ub9ac\ubcd1 \ud504\ub85c\uc81d\ud2b8\ub97c \ud3ec\ud568\ud55c \ub9ac\uc18c\uc880 \ucd95\uc801 \uc9c8\ud658 \uc5f0\uad6c \uc790\uae08 \uc9c0\uc6d0\uc744 \uc704\ud55c \ubcf4\uc870\uae08 \uc774\ub2c8\uc154\ud2f0\ube0c\ub97c \uc2dc\uc791\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2024\ub144 7\uc6d4: Scottish Medicines Consortium\uc740 Chiesi\uc758 pegunigalsidase alfa\ub97c \uc2b9\uc778\ud558\uc5ec \uc601\uad6d \ub0b4 \uc811\uadfc\uc131\uc744 \ud655\ub300\ud588\uc2b5\ub2c8\ub2e4.<br \/>\n*   2024\ub144 12\uc6d4: AdventHealth\ub294 \ud30c\ube0c\ub9ac\ubcd1 \uc2e0\uacbd\ubcd1\uc131 \ud1b5\uc99d \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud55c \ubcb5\uae00\ub8e8\uc2a4\ud0c0\ud2b8 \uc815\uc81c\uc758 3\uc0c1 PERIDOT \uc5f0\uad6c \ucc38\uac00\uc790 \ubaa8\uc9d1\uc744 \uc2dc\uc791\ud588\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774 \ubcf4\uace0\uc11c\ub294 \ud76c\uadc0 \uc720\uc804 \uc9c8\ud658\uc778 \ud30c\ube0c\ub9ac\ubcd1(Fabry Disease) \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \ub300\ud55c \ud3ec\uad04\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ud30c\ube0c\ub9ac\ubcd1\uc740 \uc54c\ud30c-\uac08\ub77d\ud1a0\uc2dc\ub2e4\uc544\uc81c A \ud6a8\uc18c \uacb0\ud54d\uc73c\ub85c \uc778\ud574 \uc911\ucd94\uc2e0\uacbd\uacc4, \uc2ec\uc7a5, \uc2e0\uc7a5, \ud53c\ubd80 \ub4f1 \uc2e0\uccb4 \uc870\uc9c1\uc5d0 \uae00\ub85c\ubcf4\ud2b8\ub9ac\uc544\uc624\uc2e4\uc138\ub77c\ub9c8\uc774\ub4dc(GL-3)\uac00 \ucd95\uc801\ub418\ub294 \uc9c8\ud658\uc73c\ub85c \uc815\uc758\ub429\ub2c8\ub2e4. \ubcf8 \ubcf4\uace0\uc11c\ub294 \uce58\ub8cc\ubc95, \ud22c\uc5ec \uacbd\ub85c, \uc720\ud1b5 \ucc44\ub110 \ubc0f \uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \uc138\ubd84\ud654\ub97c \ud1b5\ud574 \uc2dc\uc7a5 \uac00\uce58(USD)\ub97c \uc81c\uc2dc\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc804\ub9dd\uc5d0 \ub530\ub974\uba74, \ud30c\ube0c\ub9ac\ubcd1 \uce58\ub8cc \uc2dc\uc7a5\uc740 2026\ub144 28\uc5b5 3\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2031\ub144\uae4c\uc9c0 40\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\ub85c \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 7.63%\ub97c \uae30\ub85d\ud558\uba70 \uafb8\uc900\ud788 \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc758 \uc8fc\uc694 \uc131\uc7a5 \ub3d9\ub825\uc73c\ub85c\ub294 \ud30c\ube0c\ub9ac\ubcd1 \uc720\ubcd1\ub960 \uc99d\uac00, \uc720\uc804\uc790 \ubc0f mRNA \uae30\ubc18 \uce58\ub8cc\ubc95\uc758 \ubc1c\uc804, \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc2e0\uc18d \uc2ec\uc0ac \uc9c0\uc815, \ud76c\uadc0 \uc9c8\ud658\uc5d0 \ub300\ud55c \uc804 \uc138\uacc4 \uc758\ub8cc\ube44 \uc9c0\ucd9c \uc99d\uac00, \uc804\ub7b5\uc801 \ud611\ub825 \ubc0f \ub77c\uc774\uc120\uc2a4 \uacc4\uc57d, \uadf8\ub9ac\uace0 \uc6d0\uaca9 \uc758\ub8cc \ubc0f \uc7ac\ud0dd \uc8fc\uc785 \uc11c\ube44\uc2a4\uc758 \ud655\uc7a5\uc774 \uaf3d\ud799\ub2c8\ub2e4. \ubc18\uba74, \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uacfc \uc9c0\ubd88\uc790 \uc608\uc0b0 \uc81c\uc57d, \uc2e0\ud765 \uc2dc\uc7a5\uc758 \uc81c\ud55c\uc801\uc778 \uc9c4\ub2e8 \uc778\ud504\ub77c, \ucca8\ub2e8 \uce58\ub8cc\ubc95\uc758 \uc81c\uc870 \uc5ed\ub7c9 \uc81c\uc57d, \uc5c4\uaca9\ud55c \ubcf4\ud5d8 \uc0c1\ud658 \uae30\uc900 \ubc0f \uc811\uadfc \uc7a5\ubcbd\uc740 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c \uc791\uc6a9\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uce58\ub8cc\ubc95\ubcc4 \ubd84\uc11d\uc5d0\uc11c\ub294 \ud6a8\uc18c \ub300\uccb4 \uc694\ubc95(Enzyme Replacement Therapy)\uc774 2025\ub144 \uae30\uc900 67.85%\uc758 \ub9e4\ucd9c \uc810\uc720\uc728\ub85c \uc2dc\uc7a5\uc744 \uc9c0\ubc30\ud558\uace0 \uc788\uc73c\ub098, \uc720\uc804\uc790 \uce58\ub8cc(Gene Therapy)\ub294 \uc5f0\ud3c9\uade0 9.18%\ub85c \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\ub960\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc774 \uc678\uc5d0\ub3c4 \uacbd\uad6c \uc0e4\ud398\ub860 \uc694\ubc95(Oral Chaperone Therapy), \uae30\uc9c8 \uac10\uc18c \uc694\ubc95(Substrate Reduction Therapy) \ubc0f \uae30\ud0c0 \uce58\ub8cc\ubc95\uc774 \ud3ec\ud568\ub429\ub2c8\ub2e4. \ud22c\uc5ec \uacbd\ub85c\ubcc4\ub85c\ub294 \uc815\ub9e5 \uc8fc\uc0ac, \uacbd\uad6c, \ud53c\ud558 \uc8fc\uc0ac \ubc29\uc2dd\uc774 \ubd84\uc11d\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc720\ud1b5 \ucc44\ub110 \uce21\uba74\uc5d0\uc11c\ub294 \ubcd1\uc6d0 \uc57d\uad6d, \uc18c\ub9e4 \uc57d\uad6d, \uc804\ubb38 \uc57d\uad6d, \uc628\ub77c\uc778 \uc57d\uad6d\uc774 \uc788\uc73c\uba70, \ud2b9\ud788 \uc804\ubb38 \uc57d\uad6d\uc740 \ub9de\ucda4\ud615 \ud658\uc790 \uc9c0\uc6d0 \ubc0f \ubcf5\uc7a1\ud55c \ubcf4\ud5d8 \uc0c1\ud658 \uc11c\ube44\uc2a4 \uc81c\uacf5\uc744 \ud1b5\ud574 \uc5f0\ud3c9\uade0 10.05%\uc758 \ub192\uc740 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud558\uba70 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ud655\ub300\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\uc5ed\ubcc4\ub85c\ub294 \ubd81\ubbf8(\ubbf8\uad6d, \uce90\ub098\ub2e4, \uba55\uc2dc\ucf54), \uc720\ub7fd(\ub3c5\uc77c, \uc601\uad6d, \ud504\ub791\uc2a4, \uc774\ud0c8\ub9ac\uc544, \uc2a4\ud398\uc778 \ub4f1), \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591(\uc911\uad6d, \uc77c\ubcf8, \uc778\ub3c4, \ud638\uc8fc, \ud55c\uad6d \ub4f1), \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8\uac00 \ud3ec\ud568\ub429\ub2c8\ub2e4. \uc774 \uc911 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \uc9c4\ub2e8\uc728 \uc99d\uac00, \ubcf4\ud5d8 \uc0c1\ud658 \ud655\ub300, \ud65c\ubc1c\ud55c \ud604\uc9c0 \uc784\uc0c1 \uc2dc\ud5d8 \ud65c\ub3d9\uc5d0 \ud798\uc785\uc5b4 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 8.28%\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd \ubd84\uc11d\uc5d0\uc11c\ub294 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\uc640 \uc2dc\uc7a5 \uc810\uc720\uc728\uc774 \ub2e4\ub8e8\uc5b4\uc9c0\uba70, Sanofi (Genzyme), Takeda Pharmaceutical, Amicus Therapeutics, Chiesi Farmaceutici, Protalix BioTherapeutics, JCR Pharmaceuticals Co., Ltd., ISU ABXIS, Freeline Therapeutics, Yuhan Corporation, Moderna Tx, Ultragenyx \ub4f1 \uc8fc\uc694 \uae00\ub85c\ubc8c \ubc0f \uc9c0\uc5ed \uae30\uc5c5\ub4e4\uc758 \ud504\ub85c\ud544\uacfc \ucd5c\uadfc \uac1c\ubc1c \ub3d9\ud5a5\uc774 \uc0c1\uc138\ud788 \uc81c\uc2dc\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf4\uace0\uc11c\ub294 \ub610\ud55c \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd, \ud2b9\ud788 \ubbf8\uac1c\ucc99 \uc601\uc5ed(White-space) \ubc0f \ubbf8\ucda9\uc871 \uc218\uc694(Unmet-Need) \ud3c9\uac00\ub97c \ud1b5\ud574 \uc2dc\uc7a5\uc758 \uc7a0\uc7ac\ub825\uc744 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