{"id":53660,"date":"2026-02-23T16:10:32","date_gmt":"2026-02-23T16:10:32","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/vyndaqel-market-mordor\/"},"modified":"2026-04-03T15:25:10","modified_gmt":"2026-04-03T06:25:10","slug":"vyndaqel-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/vyndaqel-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ube48\ub2e4\ucf08 \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2026-2031\ub144)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/vyndaqel-market-1753865881886-major-players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/vyndaqel-market-size-image-1771005619149.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 \uc9c8\ubcd1 \uc778\uc2dd \ubc0f \uc9c4\ub2e8\uc728 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 \uaddc\uc81c \uc2b9\uc778 \ubc0f \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c<\/li>\n<li class=\"toc-level-3\">4.2.3 \uc720\ub9ac\ud55c \uc0c1\ud658 \ubc0f \ube44\uc6a9 \ubd84\ub2f4 \uc815\ucc45<\/li>\n<li class=\"toc-level-3\">4.2.4 \uc804\ubb38 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uce58\ub8cc \uc13c\ud130 \ud655\uc7a5<\/li>\n<li class=\"toc-level-3\">4.2.5 \uc0c8\ub85c\uc6b4 \ube44\uce68\uc2b5 \uc9c4\ub2e8 \uae30\uc220<\/li>\n<li class=\"toc-level-3\">4.2.6 \uace0\ub839\ud654 \uc778\uad6c \uc99d\uac00 \ubc0f \uc2ec\uc7a5 \uc9c8\ud658 \ubd80\ub2f4<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ube44\uc6a9 \ud6a8\uc728\uc131 \ubb38\uc81c<\/li>\n<li class=\"toc-level-3\">4.3.2 \ub300\uccb4 \uc694\ubc95\uc758 \uacbd\uc7c1\uc801 \ud30c\uc774\ud504\ub77c\uc778<\/li>\n<li class=\"toc-level-3\">4.3.3 \uac1c\ubc1c\ub3c4\uc0c1\uad6d\uc758 \uc81c\ud55c\ub41c \uc9c4\ub2e8 \uc778\ud504\ub77c<\/li>\n<li class=\"toc-level-3\">4.3.4 \uc7a0\uc7ac\uc801\uc778 \uc57d\uac00 \ud611\uc0c1 \ubc0f \uc815\ucc45 \uc555\ub825<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \uaddc\uc81c \ud658\uacbd<\/li>\n<li class=\"toc-level-2\">4.5 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.5.1 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.2 \uad6c\ub9e4\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.5.3 \uacf5\uae09\uc790\uc758 \uad50\uc12d\ub825<\/li>\n<li class=\"toc-level-3\">4.5.4 \ub300\uccb4\uc7ac\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc608\uce21 (\uac00\uce58, USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uc9c8\ubcd1 \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \ub9e4\uac1c \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uc2ec\uadfc\ubcd1\uc99d (ATTR-CM)<\/li>\n<li class=\"toc-level-3\">5.1.2 \ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \ub9e4\uac1c \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \ub2e4\ubc1c\uc131 \uc2e0\uacbd\ubcd1\uc99d (ATTR-PN\/FAP)<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \ud658\uc790 \ud658\uacbd\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc785\uc6d0 \ud658\uc790 \uc0ac\uc6a9<\/li>\n<li class=\"toc-level-3\">5.2.2 \uc678\ub798 \ud658\uc790 \uc0ac\uc6a9<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc9c0\ubd88\uc790 \uc720\ud615\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \uacf5\uacf5 \/ \uc815\ubd80 \ubcf4\ud5d8<\/li>\n<li class=\"toc-level-3\">5.3.2 \ubbfc\uac04 \/ \uc0c1\uc5c5 \ubcf4\ud5d8<\/li>\n<li class=\"toc-level-3\">5.3.3 \uc790\uac00 \ubd80\ub2f4 \/ \ubcf8\uc778 \ubd80\ub2f4<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc720\ud1b5 \ucc44\ub110\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \ubcd1\uc6d0 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc18c\ub9e4 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc628\ub77c\uc778 \/ \uc804\ubb38 \uc57d\uad6d<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.5 \uc9c0\uc5ed\n<ul>\n<li class=\"toc-level-3\">5.5.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.5.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.5.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.5.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.5.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.5.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.5.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.5.2.6 \uae30\ud0c0 \uc720\ub7fd<\/li>\n<li class=\"toc-level-3\">5.5.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.5.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.5.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.5.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.5.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.5.3.6 \uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-3\">5.5.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.5.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.5.4.3 \uae30\ud0c0 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-3\">5.5.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.5.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.5.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.5.5.3 \uae30\ud0c0 \ub0a8\ubbf8<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uc218\uc900 \uac1c\uc694, \uc2dc\uc7a5 \uc218\uc900 \uac1c\uc694, \ud575\uc2ec \ubd80\ubb38, \uc7ac\ubb34 \uc815\ubcf4 (\uac00\ub2a5\ud55c \uacbd\uc6b0), \uc804\ub7b5 \uc815\ubcf4, \uc2dc\uc7a5 \uc21c\uc704\/\uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 Pfizer Inc.<\/li>\n<li class=\"toc-level-3\">6.3.2 Alnylam Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.3 Ionis Pharmaceuticals \/ AstraZeneca<\/li>\n<li class=\"toc-level-3\">6.3.4 Bridgebio Pharma (Eidos)<\/li>\n<li class=\"toc-level-3\">6.3.5 Intellia Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.6 Regeneron Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.7 Novo Nordisk Rare Disease<\/li>\n<li class=\"toc-level-3\">6.3.8 CSL Behring<\/li>\n<li class=\"toc-level-3\">6.3.9 Dr. Reddy&#8217;s Laboratories<\/li>\n<li class=\"toc-level-3\">6.3.10 Aurobindo Pharma<\/li>\n<li class=\"toc-level-3\">6.3.11 Viatris<\/li>\n<li class=\"toc-level-3\">6.3.12 Lupin Ltd.<\/li>\n<li class=\"toc-level-3\">6.3.13 Sun Pharma<\/li>\n<li class=\"toc-level-3\">6.3.14 Teva Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.15 Sandoz<\/li>\n<li class=\"toc-level-3\">6.3.16 Sangamo Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.17 Arrowhead Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.18 Silence Therapeutics<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Vyndaqel \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc608\uce21 (2026-2031)<\/p>\n<p>Vyndaqel \uc2dc\uc7a5\uc740 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 13.02%\uc758 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud558\uba70 2031\ub144\uc5d0\ub294 175\uc5b5 6\ucc9c\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc774\ub294 \uc9c4\ub2e8\uc728 \uc99d\uac00, \ubcf4\ud5d8 \uc801\uc6a9 \ud655\ub300, \uadf8\ub9ac\uace0 \uc644\ud654 \uce58\ub8cc\uc5d0\uc11c \uc9c8\ubcd1 \ubcc0\ud615 \uce58\ub8cc\ub85c\uc758 \uc804\ud658\uc5d0 \ud798\uc785\uc740 \uacb0\uacfc\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uac1c\uc694 \ubc0f \uc8fc\uc694 \uc218\uce58<\/p>\n<p>Mordor Intelligence \ubcf4\uace0\uc11c\uc5d0 \ub530\ub974\uba74, Vyndaqel \uc2dc\uc7a5\uc740 2020\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0\ub97c \uc5f0\uad6c \uae30\uac04\uc73c\ub85c \ud558\uba70, 2026\ub144 95\uc5b5 1\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0\uc11c 2031\ub144 175\uc5b5 6\ucc9c\ub9cc \ub2ec\ub7ec\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774 \uae30\uac04 \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR)\uc740 13.02%\uc5d0 \ub2ec\ud560 \uac83\uc774\uba70, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\uace0 \ubd81\ubbf8 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ud070 \uc2dc\uc7a5\uc744 \ud615\uc131\ud560 \uac83\uc73c\ub85c \ubd84\uc11d\ub429\ub2c8\ub2e4. \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\ub294 &#8216;\uc911\uac04&#8217; \uc218\uc900\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \ubd84\uc11d \ubc0f \uc131\uc7a5 \ub3d9\uc778<\/p>\n<p>Vyndaqel \uc2dc\uc7a5\uc740 \uc9c4\ub2e8\uc728 \ud5a5\uc0c1, \uad11\ubc94\uc704\ud55c \ubcf4\ud5d8 \uc801\uc6a9, \uadf8\ub9ac\uace0 \uc644\ud654 \uce58\ub8cc\uc5d0\uc11c \uc9c8\ubcd1 \ubcc0\ud615 \uce58\ub8cc\ub85c\uc758 \uc9c0\uc18d\uc801\uc778 \uc804\ud658\uc73c\ub85c \uc778\ud574 \uce58\ub8cc \ub300\uc0c1 \uc778\uad6c\uac00 \ud655\ub300\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ud2b9\ud788 \ud654\uc774\uc790(Pfizer)\uc758 \ud0c0\ud30c\ubbf8\ub514\uc2a4(tafamidis)\ub294 \uc2ec\ud608\uad00 \uc0ac\ub9dd \ubc0f \uc785\uc6d0\uc728\uc744 \uc9c0\uc18d\uc801\uc73c\ub85c \uac10\uc18c\uc2dc\ud0a4\ub294 \ud6a8\uacfc\ub97c \ubcf4\uc5ec 1\ucc28 \uce58\ub8cc\uc81c\ub85c\uc11c\uc758 \uc785\uc9c0\ub97c \uad73\ud788\uace0 \uc788\uc73c\uba70, \uc870\uae30 \uc9c4\ub2e8\uc744 \uc704\ud55c \uc804\ubb38 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uc13c\ud130\ub85c\uc758 \uc758\ub8b0\ub97c \uc7a5\ub824\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ucc28\uc138\ub300 \uacbd\uc7c1 \uc57d\ubb3c\ub4e4\uc758 \ud601\uc2e0 \uce58\ub8cc\uc81c \uc9c0\uc815, \uc778\uacf5\uc9c0\ub2a5(AI) \uae30\ubc18\uc758 \uc9c4\ub2e8 \uc2a4\ud06c\ub9ac\ub2dd\uc744 \ud1b5\ud55c \uc9c4\ub2e8 \uc2dc\uac04 \ub2e8\ucd95, \uadf8\ub9ac\uace0 \uc804\ubb38 \uc13c\ud130\uc758 \uc2e0\uc18d\ud55c \ud655\uc7a5\uc740 \uc2dc\uc7a5 \uc218\uc694\ub97c \uac00\uc18d\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>RNA \uac04\uc12d(RNA-interference), \uc720\uc804\uc790 \uce68\ubb35(gene-silencing), \ub2e8\uc77c \uc6a9\ub7c9 CRISPR \uae30\ubc18 \uce58\ub8cc\uc81c \ub4f1 \uacbd\uc7c1 \uc57d\ubb3c\ub4e4\uc774 \ud6c4\uae30 \uc784\uc0c1 \ub2e8\uacc4\uc5d0 \uc9c4\uc785\ud558\uba74\uc11c \uacbd\uc7c1 \uc555\ub825\uc774 \uc99d\uac00\ud558\uace0 \uc788\uc9c0\ub9cc, \uc774\ub7ec\ud55c \uc2e0\uaddc \uc9c4\uc785\uc790\ub4e4\uc740 \uc2dc\uc7a5 \uc778\uc2dd\uc744 \ub192\uc774\uace0 \uce58\ub8cc \uc120\ud0dd\uc758 \ud3ed\uc744 \ub113\ud788\ub294 \uae0d\uc815\uc801\uc778 \ud6a8\uacfc\ub3c4 \uac00\uc838\uc635\ub2c8\ub2e4. \ubcf4\ud5d8\uc0ac\uc758 \uc218\uc6a9\ub3c4 \ub610\ud55c \uc810\uc9c4\uc801\uc73c\ub85c \uac1c\uc120\ub418\uace0 \uc788\uc73c\uba70, \uba54\ub514\ucf00\uc5b4(Medicare) \uc9c0\ucd9c\uc740 2019\ub144\uc5d0\uc11c 2021\ub144 \uc0ac\uc774\uc5d0 4\ubc30 \uc99d\uac00\ud588\uace0, \ubbfc\uac04 \ubcf4\ud5d8\uc0ac\ub4e4\uc740 \ub192\uc740 \uc57d\uac00\uc640 \uce21\uc815 \uac00\ub2a5\ud55c \uce58\ub8cc \uacb0\uacfc \uac1c\uc120\uc758 \uade0\ud615\uc744 \ub9de\ucd94\ub294 \uac00\uce58 \uae30\ubc18 \ud504\ub808\uc784\uc6cc\ud06c\ub97c \ucc44\ud0dd\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \ubcf4\uace0\uc11c \uc694\uc57d<\/p>\n<p>*   \uc9c8\ubcd1 \uc720\ud615\ubcc4: 2025\ub144 Vyndaqel \uc2dc\uc7a5 \uc810\uc720\uc728\uc758 81.78%\ub97c ATTR-CM(\ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uc2ec\uadfc\ubcd1\uc99d)\uc774 \ucc28\uc9c0\ud588\uc73c\uba70, ATTR-PN\/FAP(\ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \ub2e4\ubc1c\uc2e0\uacbd\ubcd1\uc99d\/\uac00\uc871\uc131 \uc544\ubc00\ub85c\uc774\ub4dc\uc131 \ub2e4\ubc1c\uc2e0\uacbd\ubcd1\uc99d)\ub294 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 15.12%\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n*   \ud658\uc790 \uce58\ub8cc \ud658\uacbd\ubcc4: 2025\ub144 Vyndaqel \uc2dc\uc7a5 \uaddc\ubaa8\uc758 67.95%\ub294 \uc785\uc6d0 \uce58\ub8cc\uac00 \ucc28\uc9c0\ud588\uc73c\ub098, \uc678\ub798 \uce58\ub8cc\ub294 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 15.05%\ub85c \ube60\ub974\uac8c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ubcf4\ud5d8 \uc720\ud615\ubcc4: 2025\ub144 \ub9e4\ucd9c\uc758 57.74%\ub294 \uacf5\uacf5\/\uc815\ubd80 \ubcf4\ud5d8 \ud504\ub85c\uadf8\ub7a8\uc5d0\uc11c \ubc1c\uc0dd\ud588\uc73c\uba70, \ubbfc\uac04 \ubcf4\ud5d8\uc740 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 15.33%\ub85c \uac00\uc7a5 \ube60\ub978 \uc131\uc7a5\uc744 \ubcf4\uc785\ub2c8\ub2e4.<br \/>\n*   \uc720\ud1b5 \ucc44\ub110\ubcc4: 2025\ub144 \ubcd1\uc6d0 \uc57d\uad6d\uc774 60.82%\uc758 \uc810\uc720\uc728\ub85c \uc120\ub450\ub97c \ub2ec\ub838\uc73c\uba70, \uc628\ub77c\uc778 \ubc0f \uc804\ubb38 \uc57d\uad6d\uc740 \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc5f0\ud3c9\uade0 16.02%\ub85c \uc131\uc7a5\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc9c0\uc5ed\ubcc4: 2025\ub144 \ubd81\ubbf8 \uc9c0\uc5ed\uc774 41.95%\uc758 \ub9e4\ucd9c \uc810\uc720\uc728\ub85c \uac00\uc7a5 \ud070 \uc2dc\uc7a5\uc744 \ud615\uc131\ud588\uc73c\uba70, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 14.32%\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc9c0\uc5ed\uc785\ub2c8\ub2e4.<\/p>\n<p>\uae00\ub85c\ubc8c Vyndaqel \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30 (\uc131\uc7a5 \ub3d9\uc778)<\/p>\n<p>*   \uc9c8\ubcd1 \uc778\uc2dd \ubc0f \uc9c4\ub2e8\uc728 \uc99d\uac00: \uba38\uc2e0\ub7ec\ub2dd \uc54c\uace0\ub9ac\uc998\uc774 \uc804\uc790 \uac74\uac15 \uae30\ub85d \uc2dc\uc2a4\ud15c\uc5d0 \ud1b5\ud569\ub418\uc5b4 \uace0\uc704\ud5d8 \ud658\uc790\ub97c 12\uc2dc\uac04 \uc774\ub0b4\uc5d0 \uc2dd\ubcc4\ud560 \uc218 \uc788\uac8c \ub418\uba74\uc11c, \uacfc\uac70 8.6\ub144\uc5d0 \ub2ec\ud588\ub358 \uc9c4\ub2e8 \uc9c0\uc5f0\uc774 \ud06c\uac8c \ub2e8\ucd95\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \ud654\uc774\uc790\uc640 \ud559\uc220 \ud611\ub825\uc790\ub4e4\uc740 \uc2ec\ubd80\uc804 \uae30\ub85d \uc2a4\ud06c\ub9ac\ub2dd\uc5d0\uc11c 93%\uc758 \ubbfc\uac10\ub3c4\ub97c \ubcf4\uace0\ud588\uc73c\uba70, \uba54\uc774\uc694 \ud074\ub9ac\ub2c9\uc758 ATTR-CM \uc810\uc218\ub3c4 \ube44\uc804\ubb38\uac00\uc5d0\uac8c \uc2e4\uc6a9\uc801\uc778 \ubd84\ub958 \ub3c4\uad6c\ub97c \uc81c\uacf5\ud569\ub2c8\ub2e4. \uc720\uc804\uc790 \uac80\uc0ac \ucea0\ud398\uc778\uc740 \uc720\uc804\uc801 \ubcc0\uc774\ub97c \ubc1d\ud600\ub0b4 \uce58\ub8cc \uac00\ub2a5\ud55c \ud658\uc790\uad70\uc744 \ud655\ub300\ud558\uace0 \uc788\uc73c\uba70, \uc2ec\uc7a5 \uc804\ubb38\uc758 \ubc0f \uc2e0\uacbd\uacfc \uc804\ubb38\uc758\ub97c \uc704\ud55c \uc9c0\uc18d\uc801\uc778 \uc758\ud559 \uad50\uc721\uc740 \uc624\uc9c4\uc728\uc744 \ub0ae\ucd94\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uaddc\uc81c \uc2b9\uc778 \ubc0f \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c: \ubbf8\uad6d\uc5d0\uc11c\uc758 7\ub144, \uc720\ub7fd\uc5d0\uc11c\uc758 10\ub144 \uc2dc\uc7a5 \ub3c5\uc810\uad8c\uc740 \ud601\uc2e0\uc744 \uc704\ud55c \uac15\ub825\ud55c \ucd09\ub9e4\uc81c\uc785\ub2c8\ub2e4. \uc778\ud154\ub9ac\uc544(Intellia)\uc758 CRISPR \uae30\ubc18 \ud6c4\ubcf4 \ubb3c\uc9c8\uc778 \ub125\uc2dc\uad6c\ub780 \uc9c0\ud074\ub8e8\uba54\ub780(nexiguran ziclumeran)\uc740 2025\ub144 \uc7ac\uc0dd\uc758\ud559 \ucca8\ub2e8 \uce58\ub8cc\uc81c(RMAT) \uc9c0\uc815\uc744 \ubc1b\uc544 \uc2ec\uc0ac \uae30\uac04\uc774 \ub2e8\ucd95\ub418\uc5c8\uc2b5\ub2c8\ub2e4. \ub3d9\uc2dc\uc5d0 \uc720\ub7fd\uc5d0\uc11c\ub294 \ube0c\ub9bf\uc9c0\ubc14\uc774\uc624(BridgeBio)\uc758 \uc544\ucf54\ub77c\ubbf8\ub514\uc2a4(acoramidis)\uac00 \uc2b9\uc778\ub418\uc5b4 \uc0c8\ub85c\uc6b4 \ud6a8\ub2a5 \uae30\uc900\uc744 \uc81c\uc2dc\ud588\uc2b5\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ud0c0\ud30c\ubbf8\ub514\uc2a4\uc758 \ud2b9\ud5c8 \ub9cc\ub8cc(2025-2026\ub144)\ub294 \uc81c\ub124\ub9ad \uc57d\ubb3c\uc758 \uc9c4\uc785\uc744 \uc608\uace0\ud558\uba70, \uace0\uac00 \uc2dc\uc7a5\uc5d0 \uac00\uaca9 \uacbd\uc7c1\uc744 \ubd88\ub7ec\uc62c \uac83\uc785\ub2c8\ub2e4.<br \/>\n*   \uc6b0\ud638\uc801\uc778 \ubcf4\ud5d8 \uc0c1\ud658 \ubc0f \ube44\uc6a9 \ubd84\ub2f4 \uc815\ucc45: \ud658\uc790 \uc9c0\uc6d0 \ud504\ub85c\uadf8\ub7a8\uc740 \uacbd\uc81c\uc801 \ubd80\ub2f4\uc744 \uc644\ud654\ud558\ub294 \ub370 \uae30\uc5ec\ud569\ub2c8\ub2e4. \uba54\ub514\ucf00\uc5b4 \ud0c0\ud30c\ubbf8\ub514\uc2a4 \uc0ac\uc6a9\uc790 \uc911 35%\uac00 \uc774\ub7ec\ud55c \ud504\ub85c\uadf8\ub7a8\uc5d0 \uc804\uc801\uc73c\ub85c \uc758\uc874\ud558\uba70, 14%\ub294 \uacf5\uacf5 \ubcf4\ud5d8\uacfc \ubcd1\ud589\ud569\ub2c8\ub2e4. \ud638\uc8fc\uc758 \uc758\uc57d\ud488 \ud61c\ud0dd \uc81c\ub3c4(PBS)\ub294 \ucd5c\uadfc \uc720\uc804\uc131 \ub2e4\ubc1c\uc2e0\uacbd\ubcd1\uc99d \uce58\ub8cc\uc81c\ub97c \ub4f1\uc7ac\ud558\uc5ec \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc758 \uc120\ub840\ub97c \uac15\ud654\ud588\uc2b5\ub2c8\ub2e4. \uba54\ub514\ucf00\uc5b4 \ud658\uc790 1\uc778\ub2f9 \ubcf8\uc778 \ubd80\ub2f4\uae08\uc740 \uac10\uc18c\ud588\uc9c0\ub9cc, \uc5ec\uc804\ud788 \uc218\ud61c\uc790 \uc18c\ub4dd \ub300\ube44 \ub192\uc740 \uc218\uc900\uc785\ub2c8\ub2e4. \ubbfc\uac04 \ubcf4\ud5d8\uc0ac\uc758 \ucc44\ud0dd\uc740 \uacb0\uacfc \uae30\ubc18 \uacc4\uc57d\uacfc \ud568\uaed8 \uc99d\uac00\ud558\uace0 \uc788\uc73c\uba70, \ubbf8\uad6d \uacf5\uacf5 \uc9c0\ucd9c\uc774 \uc5f0\uac04 10\uc5b5 \ub2ec\ub7ec\uc5d0 \uc721\ubc15\ud558\uba74\uc11c \uac00\uce58 \uae30\ubc18 \ud611\uc0c1\uc774 \uc2ec\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc804\ubb38 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uce58\ub8cc \uc13c\ud130 \ud655\uc7a5: \uba54\uc774\uc694 \ud074\ub9ac\ub2c9\uc740 \uc5f0\uac04 2,500\uac74 \uc774\uc0c1, \ud558\uc774\ub378\ubca0\ub974\ud06c \ub300\ud559\ubcd1\uc6d0\uc740 1,500\uac74\uc758 \uc0ac\ub840\ub97c \uad00\ub9ac\ud558\uba70 \uc804\ubb38 \ud5c8\ube0c\uc758 \uae00\ub85c\ubc8c \ud655\uc7a5\uc744 \ubcf4\uc5ec\uc90d\ub2c8\ub2e4. \uad6d\uc81c \uc2ec\uc7a5\uc885\uc591\ud559\ud68c(International Cardio-Oncology Society) \ud45c\uc900\uc740 \ub2e4\ud559\uc81c \ud300\uacfc \uacf5\uc720 \ud504\ub85c\ud1a0\ucf5c\uc744 \uc7a5\ub824\ud558\uc5ec \uc9c0\uc5ed\ubcc4 \uce58\ub8cc \uacb0\uacfc \ud3b8\ucc28\ub97c \uc904\uc785\ub2c8\ub2e4. \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc758 \uc2e0\uc18d\ud55c \uc13c\ud130 \ud655\uc7a5\uc740 \uc9c4\ub2e8 \uc99d\uac00\ub97c \ubc18\uc601\ud558\uba70, \uc77c\ubcf8, \ud55c\uad6d, \ud638\uc8fc\uc758 \uc0c8\ub85c \uc778\uc99d\ub41c \uae30\uad00\ub4e4\uc740 \uacfc\uac70\uc758 \uc811\uadfc\uc131 \uaca9\ucc28\ub97c \ud574\uc18c\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc2e0\ud765 \ube44\uce68\uc2b5 \uc9c4\ub2e8 \uae30\uc220: AI \uae30\ubc18 \uc2a4\ud06c\ub9ac\ub2dd, \uc2ec\uc7a5 \uc2e0\ud2f0\uadf8\ub798\ud53c, \uc720\uc804\uc790 \uac80\uc0ac \ub4f1\uc758 \ubc1c\uc804\uc740 \uc9c4\ub2e8 \uacfc\uc815\uc744 \ud601\uc2e0\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uace0\ub839\ud654 \uc778\uad6c \ubc0f \uc2ec\uc7a5 \uc9c8\ud658 \ubd80\ub2f4 \uc99d\uac00: \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uace0\ub839\ud654\uac00 \uc9c4\ud589\ub418\uace0 \uc2ec\uc7a5 \uc9c8\ud658 \uc720\ubcd1\ub960\uc774 \ub192\uc544\uc9c0\uba74\uc11c Vyndaqel \uc2dc\uc7a5\uc758 \uc7a5\uae30\uc801\uc778 \uc131\uc7a5\uc744 \uacac\uc778\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778<\/p>\n<p>*   \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ube44\uc6a9 \ud6a8\uc728\uc131 \uc6b0\ub824: ICER(\uc784\uc0c1\uacbd\uc81c\uc131\ud3c9\uac00\uc5f0\uad6c\uc18c) \uacc4\uc0b0\uc5d0 \ub530\ub974\uba74 \ud0c0\ud30c\ubbf8\ub514\uc2a4\ub294 \uc804\ud1b5\uc801\uc778 \ube44\uc6a9 \ud6a8\uc728\uc131 \uae30\uc900\uc744 \ucda9\uc871\ud558\uae30 \uc704\ud574 \uc815\uac00\uc778 268,000\ub2ec\ub7ec\uc5d0\uc11c 96%\uc758 \uac00\uaca9 \uc778\ud558\uac00 \ud544\uc694\ud569\ub2c8\ub2e4. \uba54\ub514\ucf00\uc5b4(Medicare)\uc640 \uac19\uc740 \uacf5\uacf5 \ubc0f \ubbfc\uac04 \ubcf4\ud5d8\uc0ac\uc758 \uc81c\ud55c\uc801\uc778 \ubcf4\uc7a5 \ubc94\uc704\ub294 \ud658\uc790\uc758 \uc811\uadfc\uc131\uc744 \uc800\ud574\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>*   \uc9c4\ub2e8 \uc9c0\uc5f0 \ubc0f \uc624\uc9c4: ATTR-CM\uc758 \ubcf5\uc7a1\ud55c \ud2b9\uc131\uc73c\ub85c \uc778\ud574 \uc9c4\ub2e8\uc774 \uc9c0\uc5f0\ub418\uac70\ub098 \uc624\uc9c4\ub418\ub294 \uacbd\uc6b0\uac00 \ub9ce\uc544 \uc801\uc2dc\uc5d0 \uce58\ub8cc\ub97c \uc2dc\uc791\ud558\uae30 \uc5b4\ub835\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uae30\ud68c<\/p>\n<p>*   \ubbf8\uc9c4\ub2e8 \ud658\uc790 \uc778\uad6c \uc99d\uac00: ATTR-CM\uc740 \uc5ec\uc804\ud788 \uacfc\uc18c \uc9c4\ub2e8\ub418\ub294 \uacbd\ud5a5\uc774 \uc788\uc5b4, \uc9c4\ub2e8\uc728\uc774 \uac1c\uc120\ub420 \uacbd\uc6b0 Vyndaqel \uc2dc\uc7a5\uc758 \uc0c1\ub2f9\ud55c \uc131\uc7a5\uc744 \uc774\ub04c \uc218 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc2e0\ud765 \uc2dc\uc7a5\uc758 \uc131\uc7a5 \uc7a0\uc7ac\ub825: \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \ubc0f \ub77c\ud2f4 \uc544\uba54\ub9ac\uce74\uc640 \uac19\uc740 \uc2e0\ud765 \uc2dc\uc7a5\uc740 \uc758\ub8cc \uc778\ud504\ub77c \uac1c\uc120\uacfc \uc9c8\ubcd1 \uc778\uc2dd \uc99d\uac00\ub85c \uc778\ud574 Vyndaqel \uc2dc\uc7a5\uc5d0 \ud070 \uc131\uc7a5 \uae30\ud68c\ub97c \uc81c\uacf5\ud569\ub2c8\ub2e4.<br \/>\n*   \uce58\ub8cc\ubc95 \uac1c\ubc1c \ubc0f \uc784\uc0c1 \uc2dc\ud5d8: ATTR-CM\uc5d0 \ub300\ud55c \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95\uacfc \ubcd1\uc6a9 \uc694\ubc95\uc5d0 \ub300\ud55c \uc9c0\uc18d\uc801\uc778 \uc5f0\uad6c \ubc0f \uc784\uc0c1 \uc2dc\ud5d8\uc740 Vyndaqel \uc2dc\uc7a5\uc758 \ud655\uc7a5\uc744 \ucd09\uc9c4\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \ub3d9\ud5a5<\/p>\n<p>*   \ud658\uc790 \uc911\uc2ec \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd: \ud658\uc790\uc758 \uc0b6\uc758 \uc9c8 \ud5a5\uc0c1\uacfc \uac1c\ubcc4\ud654\ub41c \uce58\ub8cc \uacc4\ud68d\uc5d0 \uc911\uc810\uc744 \ub450\ub294 \uacbd\ud5a5\uc774 \uac15\ud574\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ub514\uc9c0\ud138 \ud5ec\uc2a4 \ubc0f \uc6d0\uaca9 \ubaa8\ub2c8\ud130\ub9c1: \uc6d0\uaca9 \ubaa8\ub2c8\ud130\ub9c1 \ubc0f \ub514\uc9c0\ud138 \ud5ec\uc2a4 \uc194\ub8e8\uc158\uc758 \ub3c4\uc785\uc740 \ud658\uc790 \uad00\ub9ac \ubc0f \uce58\ub8cc \uc21c\uc751\ub3c4\ub97c \uac1c\uc120\ud558\ub294 \ub370 \uae30\uc5ec\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uc804\ub7b5\uc801 \ud30c\ud2b8\ub108\uc2ed \ubc0f \ud611\ub825: \uc81c\uc57d \ud68c\uc0ac, \uc5f0\uad6c \uae30\uad00 \ubc0f \uc758\ub8cc \uc11c\ube44\uc2a4 \uc81c\uacf5\uc790 \uac04\uc758 \ud611\ub825\uc740 ATTR-CM \uce58\ub8cc\ubc95 \uac1c\ubc1c \ubc0f \uc2dc\uc7a5 \ud655\uc7a5\uc744 \uac00\uc18d\ud654\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc2dc\uc7a5 \uc138\ubd84\ud654<\/p>\n<p>Vyndaqel \uc2dc\uc7a5\uc740 \uc5ec\ub7ec \uae30\uc900\uc5d0 \ub530\ub77c \uc138\ubd84\ud654\ub420 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc720\ud615\ubcc4:<\/p>\n<p>*   Vyndaqel (\ud0c0\ud30c\ubbf8\ub514\uc2a4 \uba54\uae00\ub8e8\ubbfc)<br \/>\n*   Vyndaqel (\ud0c0\ud30c\ubbf8\ub514\uc2a4)<\/p>\n<p>\uc801\uc6a9 \ubd84\uc57c\ubcc4:<\/p>\n<p>*   ATTR-CM (\ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uc2ec\uadfc\ubcd1\uc99d)<br \/>\n*   ATTR-PN (\ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \ub2e4\ubc1c\uc2e0\uacbd\ubcd1\uc99d)<\/p>\n<p>\uc720\ud1b5 \ucc44\ub110\ubcc4:<\/p>\n<p>*   \ubcd1\uc6d0 \uc57d\uad6d<br \/>\n*   \uc18c\ub9e4 \uc57d\uad6d<br \/>\n*   \uc628\ub77c\uc778 \uc57d\uad6d<\/p>\n<p>\uc9c0\uc5ed\ubcc4:<\/p>\n<p>*   \ubd81\ubbf8 (\ubbf8\uad6d, \uce90\ub098\ub2e4)<br \/>\n*   \uc720\ub7fd (\ub3c5\uc77c, \uc601\uad6d, \ud504\ub791\uc2a4, \uc774\ud0c8\ub9ac\uc544, \uc2a4\ud398\uc778, \uae30\ud0c0 \uc720\ub7fd)<br \/>\n*   \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 (\uc77c\ubcf8, \uc911\uad6d, \uc778\ub3c4, \ud55c\uad6d, \ud638\uc8fc, \uae30\ud0c0 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591)<br \/>\n*   \ub77c\ud2f4 \uc544\uba54\ub9ac\uce74 (\ube0c\ub77c\uc9c8, \uba55\uc2dc\ucf54, \uae30\ud0c0 \ub77c\ud2f4 \uc544\uba54\ub9ac\uce74)<br \/>\n*   \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74 (GCC \uad6d\uac00, \ub0a8\uc544\ud504\ub9ac\uce74, \uae30\ud0c0 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74)<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd<\/p>\n<p>Vyndaqel \uc2dc\uc7a5\uc740 \ud654\uc774\uc790(Pfizer)\uac00 \uc9c0\ubc30\ud558\uace0 \uc788\uc73c\uba70, \uc8fc\uc694 \uacbd\uc7c1\uc0ac\ub85c\ub294 Alnylam Pharmaceuticals (\uc628\ud30c\ud2b8\ub85c, \uc554\ubd80\ud2b8\ub77c), Ionis Pharmaceuticals (\ud14c\uadf8\uc138\ub514, \uc6e8\uc774\ube44\uc988), BridgeBio Pharma (\uc544\ucf54\ub77c\ubbf8\ub514\uc2a4) \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub4e4 \uae30\uc5c5\uc740 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ud655\ubcf4\ud558\uae30 \uc704\ud574 \uc5f0\uad6c \uac1c\ubc1c, \uc804\ub7b5\uc801 \uc81c\ud734, \uc81c\ud488 \ud601\uc2e0\uc5d0 \uc801\uadf9\uc801\uc73c\ub85c \ud22c\uc790\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uae30\uc5c5 \ubaa9\ub85d:<\/p>\n<p>*   \ud654\uc774\uc790(Pfizer)<br \/>\n*   Alnylam Pharmaceuticals<br \/>\n*   Ionis Pharmaceuticals<br \/>\n*   BridgeBio Pharma<br \/>\n*   Eidos Therapeutics (BridgeBio Pharma\uc758 \uc790\ud68c\uc0ac)<br \/>\n*   Intellia Therapeutics<br \/>\n*   CRISPR Therapeutics<br \/>\n*   Moderna<br \/>\n*   AstraZeneca<br \/>\n*   Novartis<\/p>\n<p>\uc774 \ubcf4\uace0\uc11c\ub294 Vyndaqel \uc2dc\uc7a5\uc758 \ud604\uc7ac \ubc0f \ubbf8\ub798 \ub3d9\ud5a5, \uc131\uc7a5 \ub3d9\ub825, \uc81c\uc57d \uc694\uc778, \uae30\ud68c \ubc0f \uacbd\uc7c1 \ud658\uacbd\uc5d0 \ub300\ud55c \uc2ec\uce35\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. \ub610\ud55c, \uc2dc\uc7a5 \uc138\ubd84\ud654, \uc9c0\uc5ed\ubcc4 \ubd84\uc11d \ubc0f \uc8fc\uc694 \uae30\uc5c5 \ud504\ub85c\ud544\uc744 \ud3ec\ud568\ud558\uc5ec \uc774\ud574 \uad00\uacc4\uc790\ub4e4\uc774 \uc815\ubcf4\uc5d0 \uc785\uac01\ud55c \uc758\uc0ac \uacb0\uc815\uc744 \ub0b4\ub9b4 \uc218 \uc788\ub3c4\ub85d \ub3d5\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc774 \ubcf4\uace0\uc11c\ub294 \ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uc2ec\uadfc\ubcd1\uc99d(ATTR-CM) \uce58\ub8cc\uc81c\uc778 Vyndaqel(\ud0c0\ud30c\ubbf8\ub514\uc2a4 \uba54\uae00\ub8e8\ubbfc) \uc2dc\uc7a5\uc5d0 \ub300\ud55c \ud3ec\uad04\uc801\uc778 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. Vyndaqel\uc740 \ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \ub2e8\ubc31\uc9c8\uc744 \uc548\uc815\ud654\ud558\uc5ec \uc2ec\uc7a5\uc5d0 \uc720\ud574\ud55c \uc544\ubc00\ub85c\uc774\ub4dc \uce68\uc804\ubb3c \ud615\uc131\uc744 \uc5b5\uc81c\ud558\uba70, \uc57c\uc0dd\ud615 \ub610\ub294 \uc720\uc804\uc131 ATTR-CM \uc131\uc778 \ud658\uc790\uc758 \uc0ac\ub9dd \ubc0f \uc785\uc6d0 \uac00\ub2a5\uc131\uc744 \uc720\uc758\ubbf8\ud558\uac8c \ub0ae\ucd94\ub294 \ud6a8\uacfc\ub97c \uac00\uc9d1\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc804\ub9dd\uc5d0 \ub530\ub974\uba74, Vyndaqel \uc2dc\uc7a5\uc740 2026\ub144 95.1\uc5b5 \ub2ec\ub7ec \uaddc\ubaa8\uc5d0\uc11c 2031\ub144\uae4c\uc9c0 175.6\uc5b5 \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc774\ub294 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 13.02%\ub97c \uae30\ub85d\ud560 \uac83\uc785\ub2c8\ub2e4. \uc9c8\ubcd1 \uc720\ud615\ubcc4\ub85c\ub294 ATTR-CM\uc774 2025\ub144 \ub9e4\ucd9c\uc758 81.78%\ub97c \ucc28\uc9c0\ud558\uba70 \uc804\uccb4 \uc218\uc694\uc5d0 \uac00\uc7a5 \ud06c\uac8c \uae30\uc5ec\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc9c0\uc5ed\ubcc4\ub85c\ub294 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uc2e0\uaddc \uc2b9\uc778 \ubc0f \uc804\ubb38 \uce58\ub8cc \uc13c\ud130 \ud655\uc7a5\uc5d0 \ud798\uc785\uc5b4 14.32%\uc758 \uac00\uc7a5 \ube60\ub978 CAGR\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5\uc758 \uc8fc\uc694 \uc131\uc7a5 \ub3d9\ub825\uc73c\ub85c\ub294 \uc9c8\ubcd1 \uc778\uc2dd \ubc0f \uc9c4\ub2e8\uc728 \uc99d\uac00, \uaddc\uc81c \uc2b9\uc778 \ubc0f \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c, \uc6b0\ud638\uc801\uc778 \ubcf4\ud5d8 \uc0c1\ud658 \ubc0f \ube44\uc6a9 \ubd84\ub2f4 \uc815\ucc45, \uc804\ubb38 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \uce58\ub8cc \uc13c\ud130\uc758 \ud655\uc7a5, \ube44\uce68\uc2b5\uc801 \uc9c4\ub2e8 \uae30\uc220\uc758 \ubc1c\uc804, \uadf8\ub9ac\uace0 \uace0\ub839\ud654 \uc778\uad6c \uc99d\uac00 \ubc0f \uc2ec\uc7a5 \uc9c8\ud658 \ubd80\ub2f4 \uc2ec\ud654 \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4. \ubc18\uba74, \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c\ub294 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ube44\uc6a9 \ud6a8\uc728\uc131 \ubb38\uc81c, \ub300\uccb4 \uce58\ub8cc\ubc95\uc758 \uacbd\uc7c1\uc801\uc778 \ud30c\uc774\ud504\ub77c\uc778, \uac1c\ubc1c\ub3c4\uc0c1\uad6d\uc758 \uc81c\ud55c\uc801\uc778 \uc9c4\ub2e8 \uc778\ud504\ub77c, \uc7a0\uc7ac\uc801\uc778 \uc57d\uac00 \ud611\uc0c1 \ubc0f \uc815\ucc45 \uc555\ub825 \ub4f1\uc774 \uc9c0\ubaa9\ub429\ub2c8\ub2e4.<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 Vyndaqel \uc2dc\uc7a5\uc744 \uc9c8\ubcd1 \uc720\ud615(ATTR-CM, \ud2b8\ub79c\uc2a4\ud2f0\ub808\ud2f4 \uc544\ubc00\ub85c\uc774\ub4dc\uc99d \ub2e4\ubc1c\uc2e0\uacbd\ubcd1\uc99d(ATTR-PN\/FAP)), \ud658\uc790 \uce58\ub8cc \ud658\uacbd(\uc785\uc6d0, \uc678\ub798), \uc9c0\ubd88\uc790 \uc720\ud615(\uacf5\uacf5\/\uc815\ubd80 \ubcf4\ud5d8, \ubbfc\uac04\/\uc0c1\uc5c5 \ubcf4\ud5d8, \uc790\uac00 \ubd80\ub2f4), \uc720\ud1b5 \ucc44\ub110(\ubcd1\uc6d0 \uc57d\uad6d, \uc18c\ub9e4 \uc57d\uad6d, \uc628\ub77c\uc778\/\uc804\ubb38 \uc57d\uad6d) \ubc0f \uc9c0\uc5ed(\ubd81\ubbf8, \uc720\ub7fd, \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591, \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74, \ub0a8\ubbf8)\ubcc4\ub85c \uc138\ubd84\ud654\ud558\uc5ec \ubd84\uc11d\ud569\ub2c8\ub2e4. \ud2b9\ud788, \uc804 \uc138\uacc4 \uc8fc\uc694 17\uac1c\uad6d\uc758 \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \ub3d9\ud5a5\uc744 \ub2e4\ub8f9\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd\uc740 RNA \uac04\uc12d \ubc0f CRISPR \uae30\ubc18 \uce58\ub8cc\ubc95\uc744 \ud3ec\ud568\ud55c \uc2e0\uaddc \uacbd\uc7c1\uc790\ub4e4\uc758 \uc2b9\uc778\uc73c\ub85c \uc778\ud574 \uce58\ub8cc \uba54\ucee4\ub2c8\uc998\uc758 \ub2e4\uc591\uc131\uc774 \ud655\ub300\ub418\uace0 \uacbd\uc7c1\uc774 \uc2ec\ud654\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uce58\ub8cc \ube44\uc6a9\uc740 \uc5ec\uc804\ud788 \uad11\ubc94\uc704\ud55c \uce58\ub8cc\ubc95 \ucc44\ud0dd\uc758 \uc8fc\uc694 \uc7a5\ubcbd\uc73c\ub85c \uc791\uc6a9\ud558\uba70, \uae30\uc874\uc758 \ube44\uc6a9 \ud6a8\uc728\uc131 \uc9c0\ud45c\uc5d0 \ub530\ub974\uba74 \ud0c0\ud30c\ubbf8\ub514\uc2a4 \uac00\uaca9\uc740 \uc9c0\ubd88\uc790 \uae30\uc900\uc744 \ucda9\uc871\ud558\uae30 \uc704\ud574 \uc0c1\ub2f9\ud55c \uc778\ud558\uac00 \ud544\uc694\ud569\ub2c8\ub2e4. \ud55c\ud3b8, \uacbd\uad6c \ud22c\uc5ec \ubc0f \uc6d0\uaca9 \uc758\ub8cc\uc758 \ubc1c\uc804\uc73c\ub85c \uc9c0\uc5ed\uc0ac\ud68c \uae30\ubc18 \uad00\ub9ac\uac00 \uac00\ub2a5\ud574\uc9c0\uba74\uc11c \uc678\ub798 \uce58\ub8cc\uac00 \uc5f0\ud3c9\uade0 15.05%\uc758 \uc131\uc7a5\ub960\uc744 \ubcf4\uc774\uba70 \uc785\uc6d0 \uce58\ub8cc\uc5d0\uc11c \uc804\ud658\ub418\ub294 \ucd94\uc138\uc785\ub2c8\ub2e4.<\/p>\n<p>\ubcf4\uace0\uc11c\ub294 Pfizer, Alnylam Pharmaceuticals, Ionis Pharmaceuticals\/AstraZeneca \ub4f1 \uc8fc\uc694 \uae00\ub85c\ubc8c \uae30\uc5c5\ub4e4\uc758 \ud504\ub85c\ud544\uacfc \uc2dc\uc7a5 \uc9d1\uc911\ub3c4, \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d\uc744 \ud3ec\ud568\ud558\uc5ec \uacbd\uc7c1 \uad6c\ub3c4\ub97c \uc0c1\uc138\ud788 \uc81c\uc2dc\ud569\ub2c8\ub2e4. \ub610\ud55c, \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd, \ubbf8\ucda9\uc871 \uc218\uc694 \ud3c9\uac00 \ub4f1\ub3c4 \ub2e4\ub8f9\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-53660","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/53660"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=53660"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/53660\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=53660"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=53660"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=53660"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}