{"id":59497,"date":"2026-02-26T20:47:39","date_gmt":"2026-02-26T20:47:39","guid":{"rendered":"https:\/\/www.globalresearch.co.kr\/insight\/duchenne-muscular-dystrophy-treatment-market-mordor\/"},"modified":"2026-09-18T10:44:26","modified_gmt":"2026-09-18T01:44:26","slug":"duchenne-muscular-dystrophy-treatment-market-mordor","status":"publish","type":"post","link":"https:\/\/www.globalresearch.co.kr\/insight\/duchenne-muscular-dystrophy-treatment-market-mordor\/","title":{"rendered":"\uc138\uacc4\uc758 \ub4c0\uc13c \uadfc\uc774\uc601\uc591\uc99d \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d &#8211; \uc131\uc7a5 \ub3d9\ud5a5 \ubc0f \uc804\ub9dd (2026-2031)"},"content":{"rendered":"<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/duchenne-muscular-dystrophy-treatment-market-1713197340676-Duchenne-Muscular-Dystrophy-Treatment-Market-Key-Players.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/www.globalresearch.co.kr\/insight\/wp-content\/uploads\/2026\/02\/duchenne-muscular-dystrophy-treatment-market-size-image-1770817294025.webp\" alt=\"Chart\" class=\"aligncenter size-full\" \/><\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-0\">1. \uc11c\ub860<\/p>\n<ul>\n<li class=\"toc-level-2\">1.1 \uc5f0\uad6c \uac00\uc815 \ubc0f \uc2dc\uc7a5 \uc815\uc758<\/li>\n<li class=\"toc-level-2\">1.2 \uc5f0\uad6c \ubc94\uc704<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-1\">2. \uc5f0\uad6c \ubc29\ubc95\ub860<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-2\">3. \uc694\uc57d<\/p>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-3\">4. \uc2dc\uc7a5 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">4.1 \uc2dc\uc7a5 \uac1c\uc694<\/li>\n<li class=\"toc-level-2\">4.2 \uc2dc\uc7a5 \ub3d9\uc778\n<ul>\n<li class=\"toc-level-3\">4.2.1 DMD \uc9c8\ubcd1 \ubd80\ub2f4 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.2 \uc2e0\uaddc \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \ud22c\uc790 \uc99d\uac00<\/li>\n<li class=\"toc-level-3\">4.2.3 \uc548\ud2f0\uc13c\uc2a4 \uc5d1\uc190 \uc2a4\ud0a4\ud551 \uc57d\ubb3c\uc758 \uc2b9\uc778 \uac00\uc18d\ud654<\/li>\n<li class=\"toc-level-3\">4.2.4 \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc6b0\uc120 \uc2ec\uc0ac \ubc14\uc6b0\ucc98<\/li>\n<li class=\"toc-level-3\">4.2.5 \uc720\uc804\uc790 \ud3b8\uc9d1 \ud30c\uc774\ud504\ub77c\uc778\uc744 \uac00\uc18d\ud654\ud558\ub294 CRISPR \ud50c\ub7ab\ud3fc \uac70\ub798<\/li>\n<li class=\"toc-level-3\">4.2.6 \ud658\uc790 \ubaa8\uc9d1\uc744 \uac1c\uc120\ud558\ub294 \ubd84\uc0b0\ud615 \uc784\uc0c1\uc2dc\ud5d8<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.3 \uc2dc\uc7a5 \uc81c\uc57d\n<ul>\n<li class=\"toc-level-3\">4.3.1 \ud45c\uc900\ud654\ub41c \uc784\uc0c1 \ud6a8\ub2a5 \ud3c9\uac00 \uc9c0\ud45c \ubd80\uc871<\/li>\n<li class=\"toc-level-3\">4.3.2 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ubcf4\ud5d8 \uc801\uc6a9 \ubb38\uc81c<\/li>\n<li class=\"toc-level-3\">4.3.3 \uace0\uc6a9\ub7c9 AAV \ubca1\ud130 \uc81c\uc870 \ubcd1\ubaa9 \ud604\uc0c1<\/li>\n<li class=\"toc-level-3\">4.3.4 \ube44\ud45c\uc801 \uc720\uc804\uc790 \ud3b8\uc9d1\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">4.4 \uaddc\uc81c \ud658\uacbd<\/li>\n<li class=\"toc-level-2\">4.5 \ud3ec\ud130\uc758 5\uac00\uc9c0 \uacbd\uc7c1 \uc694\uc778 \ubd84\uc11d\n<ul>\n<li class=\"toc-level-3\">4.5.1 \uad6c\ub9e4\uc790\uc758 \ud611\uc0c1\ub825<\/li>\n<li class=\"toc-level-3\">4.5.2 \uacf5\uae09\uc790\uc758 \ud611\uc0c1\ub825<\/li>\n<li class=\"toc-level-3\">4.5.3 \uc2e0\uaddc \uc9c4\uc785\uc790\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.4 \ub300\uccb4\uc7ac\uc758 \uc704\ud611<\/li>\n<li class=\"toc-level-3\">4.5.5 \uacbd\uc7c1 \uac15\ub3c4<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-4\">5. \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc131\uc7a5 \uc608\uce21 (\uac00\uce58, USD)<\/p>\n<ul>\n<li class=\"toc-level-2\">5.1 \uce58\ub8cc \uc811\uadfc \ubc29\uc2dd\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.1.1 \ubd84\uc790 \uae30\ubc18<\/li>\n<li class=\"toc-level-4\">5.1.1.1 \ub3cc\uc5f0\ubcc0\uc774 \uc5b5\uc81c<\/li>\n<li class=\"toc-level-4\">5.1.1.2 \uc5d1\uc190 \uc2a4\ud0a4\ud551<\/li>\n<li class=\"toc-level-3\">5.1.2 \uc2a4\ud14c\ub85c\uc774\ub4dc \uc694\ubc95<\/li>\n<li class=\"toc-level-3\">5.1.3 NSAIDs<\/li>\n<li class=\"toc-level-3\">5.1.4 \uae30\ud0c0<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.2 \ud22c\uc5ec \uacbd\ub85c\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.2.1 \uc815\ub9e5<\/li>\n<li class=\"toc-level-3\">5.2.2 \ud53c\ud558<\/li>\n<li class=\"toc-level-3\">5.2.3 \uacbd\uad6c<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.3 \uc720\ud1b5 \ucc44\ub110\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.3.1 \ubcd1\uc6d0 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.2 \uc18c\ub9e4 \uc57d\uad6d<\/li>\n<li class=\"toc-level-3\">5.3.3 \uc628\ub77c\uc778 \uc57d\uad6d<\/li>\n<\/ul>\n<\/li>\n<li class=\"toc-level-2\">5.4 \uc9c0\uc5ed\ubcc4\n<ul>\n<li class=\"toc-level-3\">5.4.1 \ubd81\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.1.1 \ubbf8\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.1.2 \uce90\ub098\ub2e4<\/li>\n<li class=\"toc-level-4\">5.4.1.3 \uba55\uc2dc\ucf54<\/li>\n<li class=\"toc-level-3\">5.4.2 \uc720\ub7fd<\/li>\n<li class=\"toc-level-4\">5.4.2.1 \ub3c5\uc77c<\/li>\n<li class=\"toc-level-4\">5.4.2.2 \uc601\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.2.3 \ud504\ub791\uc2a4<\/li>\n<li class=\"toc-level-4\">5.4.2.4 \uc774\ud0c8\ub9ac\uc544<\/li>\n<li class=\"toc-level-4\">5.4.2.5 \uc2a4\ud398\uc778<\/li>\n<li class=\"toc-level-4\">5.4.2.6 \uc720\ub7fd \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.4.3 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591<\/li>\n<li class=\"toc-level-4\">5.4.3.1 \uc911\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.2 \uc77c\ubcf8<\/li>\n<li class=\"toc-level-4\">5.4.3.3 \uc778\ub3c4<\/li>\n<li class=\"toc-level-4\">5.4.3.4 \ud638\uc8fc<\/li>\n<li class=\"toc-level-4\">5.4.3.5 \ub300\ud55c\ubbfc\uad6d<\/li>\n<li class=\"toc-level-4\">5.4.3.6 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.4.4 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.1 GCC<\/li>\n<li class=\"toc-level-4\">5.4.4.2 \ub0a8\uc544\ud504\ub9ac\uce74<\/li>\n<li class=\"toc-level-4\">5.4.4.3 \uc911\ub3d9 \ubc0f \uc544\ud504\ub9ac\uce74 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<li class=\"toc-level-3\">5.4.5 \ub0a8\ubbf8<\/li>\n<li class=\"toc-level-4\">5.4.5.1 \ube0c\ub77c\uc9c8<\/li>\n<li class=\"toc-level-4\">5.4.5.2 \uc544\ub974\ud5e8\ud2f0\ub098<\/li>\n<li class=\"toc-level-4\">5.4.5.3 \ub0a8\ubbf8 \uae30\ud0c0 \uc9c0\uc5ed<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-5\">6. \uacbd\uc7c1 \ud658\uacbd<\/p>\n<ul>\n<li class=\"toc-level-2\">6.1 \uc2dc\uc7a5 \uc9d1\uc911\ub3c4<\/li>\n<li class=\"toc-level-2\">6.2 \uc2dc\uc7a5 \uc810\uc720\uc728 \ubd84\uc11d<\/li>\n<li class=\"toc-level-2\">6.3 \uae30\uc5c5 \ud504\ub85c\ud544 (\uae00\ub85c\ubc8c \uac1c\uc694, \uc2dc\uc7a5 \uac1c\uc694, \ud575\uc2ec \ubd80\ubb38, \uc7ac\ubb34 \uc815\ubcf4(\uac00\ub2a5\ud55c \uacbd\uc6b0), \uc804\ub7b5 \uc815\ubcf4, \uc8fc\uc694 \uae30\uc5c5 \uc2dc\uc7a5 \uc21c\uc704\/\uc810\uc720\uc728, \uc81c\ud488 \ubc0f \uc11c\ube44\uc2a4, \ucd5c\uadfc \uac1c\ubc1c \ud3ec\ud568)\n<ul>\n<li class=\"toc-level-3\">6.3.1 Sarepta Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.2 PTC Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.3 Nippon Shinyaku (NS Pharma)<\/li>\n<li class=\"toc-level-3\">6.3.4 Pfizer<\/li>\n<li class=\"toc-level-3\">6.3.5 Italfarmaco<\/li>\n<li class=\"toc-level-3\">6.3.6 Santhera Pharmaceuticals<\/li>\n<li class=\"toc-level-3\">6.3.7 FibroGen<\/li>\n<li class=\"toc-level-3\">6.3.8 BioMarin<\/li>\n<li class=\"toc-level-3\">6.3.9 Roche \/ Genentech<\/li>\n<li class=\"toc-level-3\">6.3.10 Wave Life Sciences<\/li>\n<li class=\"toc-level-3\">6.3.11 Solid Biosciences<\/li>\n<li class=\"toc-level-3\">6.3.12 Dyne Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.13 Edgewise Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.14 Regenxbio<\/li>\n<li class=\"toc-level-3\">6.3.15 Alexion (AstraZeneca Rare Disease)<\/li>\n<li class=\"toc-level-3\">6.3.16 Genethon<\/li>\n<li class=\"toc-level-3\">6.3.17 Eli Lilly<\/li>\n<li class=\"toc-level-3\">6.3.18 Dystrogen Therapeutics<\/li>\n<li class=\"toc-level-3\">6.3.19 Entrada Therapeutics<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n<p class=\"toc-level-1 toc-content-heading\" id=\"toc-content-heading-6\">7. \uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d(DMD) \uce58\ub8cc \uc2dc\uc7a5 \uac1c\uc694 \ubcf4\uace0\uc11c \uc694\uc57d (2031\ub144)<\/p>\n<p>\ubcf8 \ubcf4\uace0\uc11c\ub294 2031\ub144\uae4c\uc9c0\uc758 \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d(DMD) \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8 \ubc0f \uc810\uc720\uc728 \ubd84\uc11d\uc744 \ub2e4\ub8e8\uba70, \uc131\uc7a5 \ub3d9\ud5a5\uacfc \uc608\uce21\uc744 \uc81c\uc2dc\ud569\ub2c8\ub2e4. 2026\ub144 40\uc5b5 6\ucc9c\ub9cc \ub2ec\ub7ec\ub85c \ucd94\uc815\ub418\ub294 \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2031\ub144 95\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0 \ub2ec\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 18.76%\ub97c \uae30\ub85d\ud560 \uc804\ub9dd\uc785\ub2c8\ub2e4. \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc73c\ub85c, \ubd81\ubbf8\uac00 \uac00\uc7a5 \ud070 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ucc28\uc9c0\ud558\uace0 \uc788\uc73c\uba70, \uc2dc\uc7a5 \uc9d1\uc911\ub3c4\ub294 \uc911\uac04 \uc218\uc900\uc785\ub2c8\ub2e4. \uc720\uc804\uc790 \uce58\ub8cc\ubc95\uc758 \ud601\uc2e0, \uaddc\uc81c \uc2b9\uc778 \uac00\uc18d\ud654, \uc9c0\uc18d\uc801\uc778 \ubca4\ucc98 \ud22c\uc790\ub294 \uce58\ub8cc \ud45c\uc900\uc744 \uc7ac\uc815\uc758\ud558\uba70, \uc644\ud654 \uc694\ubc95\uc5d0\uc11c \uc9c0\uc18d\uc801\uc778 \uc9c8\ubcd1 \uc870\uc808 \uac1c\uc785\uc73c\ub85c\uc758 \uc804\ud658\uc744 \uc774\ub04c\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># \uc2dc\uc7a5 \ubd84\uc11d<\/p>\n<p>\ubaa8\ub974\ub3c4\ub974 \uc778\ud154\ub9ac\uc804\uc2a4(Mordor Intelligence)\uc758 \ubd84\uc11d\uc5d0 \ub530\ub974\uba74, 2025\ub144 34\uc5b5 2\ucc9c\ub9cc \ub2ec\ub7ec\uc600\ub358 \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc740 2026\ub144 40\uc5b5 6\ucc9c\ub9cc \ub2ec\ub7ec, 2031\ub144\uc5d0\ub294 95\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec\ub85c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4. \ud2b9\ud788, FDA\uc758 4\uc138 \uc774\uc0c1 \uc544\ub3d9 \ub300\uc0c1 \ub378\ub780\ub514\uc2a4\ud2b8\ub85c\uc820 \ubaa9\uc138\ud30c\ub974\ubcf4\ubca1(delandistrogene moxeparvovec) \uc2b9\uc778 \ud655\ub300, \ucd5c\ucd08\uc758 \ube44\uc2a4\ud14c\ub85c\uc774\ub4dc\uc131 \uc57d\ubb3c \uae30\ube44\ub178\uc2a4\ud0c0\ud2b8(givinostat), \ucf54\ub974\ud2f0\ucf54\uc2a4\ud14c\ub85c\uc774\ub4dc \ub300\uccb4\uc81c \ubc14\ubaa8\ub864\ub860(vamorolone) \ub4f1 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc\uc81c\ub4e4\uc758 \ub4f1\uc7a5\uc740 \ubd84\uc790 \uae30\ubc18 \uc811\uadfc\ubc95\uc774 \uc9c0\ubc30\uc801\uc778 \ub2e4\uc911 \ubaa8\ub4dc \uc0dd\ud0dc\uacc4\ub97c \uad6c\ucd95\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud2f0\ub4dc \ubc0f CRISPR \uae30\uc220 \ud601\uc2e0 \uae30\uc5c5\uc5d0 \ub300\ud55c \uae30\ub85d\uc801\uc778 \uc790\ubcf8 \uc870\ub2ec\uc5d0\uc11c \ubcfc \uc218 \uc788\ub4ef\uc774 \ud22c\uc790\uc790\ub4e4\uc758 \uad00\uc2ec\uc740 \uc5ec\uc804\ud788 \ub192\uc2b5\ub2c8\ub2e4. \ub300\uae30\uc5c5\ub4e4\uc758 \ud504\ub85c\uadf8\ub7a8 \uc911\ub2e8\uc73c\ub85c \uc778\ud55c \uacbd\uc7c1 \uad6c\ub3c4 \uc7ac\ud3b8\uc740 \uc2e0\ud765 \uae30\uc5c5\ub4e4\uc5d0\uac8c \uc0c8\ub85c\uc6b4 \uae30\ud68c\ub97c \uc81c\uacf5\ud558\uba70, \ud655\uc7a5 \uac00\ub2a5\ud55c \ubca1\ud130 \uc81c\uc870\uc5d0 \ub300\ud55c \uc9d1\uc911\ub3c4\ub97c \ub192\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc77c\ubcf8\uacfc \uc911\uad6d \uaddc\uc81c \ub2f9\uad6d\uc758 \uc2ec\uc0ac \uac00\uc18d\ud654\uc5d0 \ud798\uc785\uc5b4 \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 \ud3c9\uade0 \uc774\uc0c1\uc758 \ub9e4\ucd9c \uc131\uc7a5\uacfc \ub2e4\uc591\ud55c \uc784\uc0c1 \uc2dc\ud5d8 \ud65c\ub3d9\uc744 \ubcf4\uc774\uba70 \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc8fc\ub3c4\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \ubcf4\uace0\uc11c \uc694\uc57d:<br \/>\n*   \uce58\ub8cc \uc811\uadfc\ubc95: 2025\ub144 \ubd84\uc790 \uae30\ubc18 \uc81c\ud488\uc774 \uc2dc\uc7a5 \uc810\uc720\uc728 60.78%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, 2031\ub144\uae4c\uc9c0 19.42%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<br \/>\n*   \ud22c\uc5ec \uacbd\ub85c: 2025\ub144 \uc815\ub9e5 \ud22c\uc5ec(Intravenous) \ubd80\ubb38\uc774 \uc2dc\uc7a5 \uaddc\ubaa8\uc758 51.68%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, \ud53c\ud558 \ud22c\uc5ec(Subcutaneous) \ubd80\ubb38\uc740 2031\ub144\uae4c\uc9c0 19.37%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\ub85c \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4.<br \/>\n*   \uc720\ud1b5 \ucc44\ub110: 2025\ub144 \ubcd1\uc6d0 \uc57d\uad6d(Hospital Pharmacies)\uc774 \uc2dc\uc7a5 \uc810\uc720\uc728 67.05%\ub97c \ucc28\uc9c0\ud588\uc73c\uba70, \uc628\ub77c\uc778 \uc57d\uad6d(Online Pharmacies)\uc740 2031\ub144\uae4c\uc9c0 19.55%\uc758 \uac00\uc7a5 \ube60\ub978 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \ubcf4\uc785\ub2c8\ub2e4.<br \/>\n*   \uc9c0\uc5ed: 2025\ub144 \ubd81\ubbf8\uac00 41.11%\uc758 \ub9e4\ucd9c \uc810\uc720\uc728\ub85c \uc2dc\uc7a5\uc744 \uc120\ub3c4\ud588\uc73c\uba70, \uc544\uc2dc\uc544 \ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc740 2026\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 19.61%\uc758 \uac00\uc7a5 \ub192\uc740 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc608\uce21\ub429\ub2c8\ub2e4.<\/p>\n<p># \uae00\ub85c\ubc8c \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 \ub3d9\ud5a5 \ubc0f \ud1b5\ucc30\ub825<\/p>\n<p>\uc8fc\uc694 \uc131\uc7a5 \ub3d9\ub825:<br \/>\n*   DMD \uc9c8\ubcd1 \ubd80\ub2f4 \uc99d\uac00: 3,500~6,000\uba85 \uc911 1\uba85\uc758 \ub0a8\uc544\uc5d0\uac8c \uc601\ud5a5\uc744 \ubbf8\uce58\ub294 DMD\uc5d0 \ub300\ud55c \uc778\uc2dd\uc774 \ub192\uc544\uc9c0\uba74\uc11c \uad6d\uac00 \ub4f1\ub85d \ubc0f \uc2e0\uc0dd\uc544 \uc120\ubcc4 \ud504\ub85c\uadf8\ub7a8\uc774 \ud655\ub300\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uc784\uc0c1 \uc2dc\ud5d8 \ub300\uc0c1 \uc778\uad6c\ub97c \ub298\ub9ac\uace0 \uc870\uae30 \uce58\ub8cc \uac1c\uc785\uc744 \uc7a5\ub824\ud569\ub2c8\ub2e4. \ud658\uc790\uc758 \uae30\ub300 \uc218\uba85 \uc99d\uac00(1970\ub144 \uc774\uc804 \ucd9c\uc0dd\uc790 18.2\uc138\uc5d0\uc11c 1990-1999\ub144 \ucf54\ud638\ud2b8 24\uc138\ub85c)\ub294 \uce58\ub8cc \uae30\uac04\uc744 \uc5f0\uc7a5\ud558\uace0 \uc2dc\uc7a5 \uc218\uc694\ub97c \uc99d\ud3ed\uc2dc\ud0b5\ub2c8\ub2e4.<br \/>\n*   \uc2e0\uaddc \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \ud22c\uc790 \uc99d\uac00: \ubca4\ucc98 \ubc0f \uc804\ub7b5\uc801 \uc790\ubcf8 \uc720\uc785\uc774 \uc9c0\uc18d\ub418\uace0 \uc788\uc2b5\ub2c8\ub2e4. CureDuchenne\uc740 2014\ub144 \uc774\ud6c4 30\uc5b5 \ub2ec\ub7ec \uc774\uc0c1\uc758 \ud6c4\uc18d \uc790\uae08\uc744 \uc720\uce58\ud588\uc73c\uba70, Dyne Therapeutics\ub294 2024\ub144 \ud55c \ud574\uc5d0\ub9cc 3\uc5b5 \ub2ec\ub7ec\ub97c \ud655\ubcf4\ud588\uc2b5\ub2c8\ub2e4. Sarepta-Arrowhead\uc758 siRNA \ud611\ub825 \ubc0f Sanofi-Fulcrum\uc758 \ud6c4\uc131\uc720\uc804\ud559\uc801 \uc870\uc808 \uc5f0\uad6c\uc640 \uac19\uc740 \ub300\ud615 \uc81c\uc57d\uc0ac\ub4e4\uc758 \ud76c\uadc0 \uc9c8\ud658 \ud3ec\ud2b8\ud3f4\ub9ac\uc624\uc5d0 \ub300\ud55c \ud22c\uc790\ub294 \ubb3c\ub860, \uc790\uc120 \ubca4\ucc98 \uc790\uae08\ub3c4 \ucd08\uae30 \ubc1c\uacac\uc5d0 \uc911\uc694\ud55c \uc5ed\ud560\uc744 \ud569\ub2c8\ub2e4.<br \/>\n*   \uc548\ud2f0\uc13c\uc2a4 \uc5d1\uc190 \uc2a4\ud0a4\ud551 \uc57d\ubb3c \uc2b9\uc778 \uac00\uc18d\ud654: \uc774\ubbf8 4\uac1c\uc758 \uc5d1\uc190 \uc2a4\ud0a4\ud551 \uc57d\ubb3c\uc774 \ubbf8\uad6d \uc2dc\uc7a5\uc5d0 \ucd9c\uc2dc\ub418\uc5c8\uc73c\uba70, \ucd94\uac00 \ud6c4\ubcf4 \ubb3c\uc9c8\ub4e4\uc774 \uc2b9\uc778 \uc2e0\uccad\uc744 \uc55e\ub450\uace0 \uc788\uc2b5\ub2c8\ub2e4. FDA\uc640 EMA\ub294 \ub514\uc2a4\ud2b8\ub85c\ud540 \ubc1c\ud604\uc744 \ub300\uccb4 \ubc14\uc774\uc624\ub9c8\ucee4\ub85c \uc778\uc815\ud558\uc5ec \uac1c\ubc1c \uae30\uac04\uc744 \ub2e8\ucd95\ud558\uace0 \uc704\ud5d8\uc744 \ub0ae\ucd94\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ud76c\uadc0 \uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc6b0\uc120 \uc2ec\uc0ac \ubc14\uc6b0\ucc98: 2024\ub144 \uae30\ube44\ub178\uc2a4\ud0c0\ud2b8\uc5d0 \ubd80\uc5ec\ub41c \ud76c\uadc0 \uc18c\uc544 \uc9c8\ud658 \ubc14\uc6b0\ucc98\ub294 \uc218\uc5b5 \ub2ec\ub7ec\uc758 2\ucc28 \uc2dc\uc7a5 \uac00\uce58\ub97c \ucc3d\ucd9c\ud558\uba70, \ubc14\uc6b0\ucc98 \uc218\uc775\uc774 \ucd94\uac00 \ud30c\uc774\ud504\ub77c\uc778 \uc790\uc0b0\uc5d0 \uc7ac\ud22c\uc790\ub418\ub294 \uc120\uc21c\ud658 \uad6c\uc870\ub97c \ud615\uc131\ud569\ub2c8\ub2e4. 7\ub144\uac04\uc758 \ub3c5\uc810\uad8c\uacfc 2025\ub144 \ubc1c\ud45c\ub41c \uba85\ud655\ud55c \uc9c0\uce68\uc740 \uace0\uc704\ud5d8 \ud504\ub85c\uadf8\ub7a8 \uac1c\ubc1c\uc5d0 \ub300\ud55c \uc2a4\ud3f0\uc11c\uc758 \uc758\uc9c0\ub97c \ub4b7\ubc1b\uce68\ud569\ub2c8\ub2e4.<br \/>\n*   CRISPR \ud50c\ub7ab\ud3fc \uac70\ub798\ub97c \ud1b5\ud55c \uc720\uc804\uc790 \ud3b8\uc9d1 \ud30c\uc774\ud504\ub77c\uc778 \uac00\uc18d\ud654: CRISPR \uae30\uc220\uc740 \uc720\uc804\uc790 \ud3b8\uc9d1 \ud30c\uc774\ud504\ub77c\uc778\uc744 \uac00\uc18d\ud654\ud558\uba70 \uc804 \uc138\uacc4\uc801\uc73c\ub85c, \ud2b9\ud788 \ubbf8\uad6d\uacfc \uc911\uad6d\uc5d0\uc11c \uc9d1\uc911\uc801\uc778 \ud22c\uc790\ub97c \ubc1b\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \ubd84\uc0b0\ud615 \uc784\uc0c1 \uc2dc\ud5d8\uc744 \ud1b5\ud55c \ud658\uc790 \ubaa8\uc9d1 \uac1c\uc120: \ubd84\uc0b0\ud615 \uc784\uc0c1 \uc2dc\ud5d8\uc740 \ud658\uc790 \ubaa8\uc9d1\uc744 \uac1c\uc120\ud558\uc5ec \uce58\ub8cc\uc81c \uac1c\ubc1c\uc744 \ucd09\uc9c4\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc8fc\uc694 \uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778:<br \/>\n*   \ud45c\uc900\ud654\ub41c \uc784\uc0c1 \ud6a8\ub2a5 \ud3c9\uac00 \uc9c0\ud45c \ubd80\uc871: \ud06c\ub808\uc544\ud2f4 \ud0a4\ub098\uc81c\uc640 \uac19\uc740 \ubc14\uc774\uc624\ub9c8\ucee4\uc758 \uac00\ubcc0\uc131\uc740 \uc5f0\uad6c \uac04 \ube44\uad50\ub97c \uc5b4\ub835\uac8c \ud558\uba70, \uc18c\ubcc0 N-\ub9d0\ub2e8 \ud2f0\ud2f4\uacfc \uac19\uc740 \ub300\uccb4 \ubc14\uc774\uc624\ub9c8\ucee4 \uac80\uc99d \ub178\ub825\uc744 \ucd09\ubc1c\ud569\ub2c8\ub2e4. FDA\uc640 EMA\uc758 \uc9c0\uce68 \ucc28\uc774\ub294 \uacc4\ud68d \ubcf5\uc7a1\uc131\uc744 \uac00\uc911\uc2dc\ud0b5\ub2c8\ub2e4.<br \/>\n*   \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ubcf4\ud5d8 \uc801\uc6a9 \uc7a5\ubcbd: 300\ub9cc \ub2ec\ub7ec \uc774\uc0c1\uc758 \uc720\uc804\uc790 \uce58\ub8cc\uc81c\ub294 \ubcf4\ud5d8\uc0ac\uc758 \uc608\uc0b0\uc5d0 \ubd80\ub2f4\uc744 \uc8fc\uba70, \uc0ac\uc804 \uc2b9\uc778 \uae30\uc900\uc740 \uc885\uc885 \uc801\uc6a9 \ubc94\uc704\ub97c \uc881\uc740 \ud558\uc704 \uadf8\ub8f9\uc73c\ub85c \uc81c\ud55c\ud569\ub2c8\ub2e4. \uac00\uce58 \uae30\ubc18 \uacc4\uc57d \ubc0f \ubd84\ud560 \uc9c0\ubd88 \ubaa8\ub378\uc774 \ub4f1\uc7a5\ud558\uace0 \uc788\uc9c0\ub9cc, \uc2dc\ud310 \ud6c4 \ub370\uc774\ud130 \uc218\uc9d1\uc758 \ubb3c\ub958 \ubb38\uc81c\ub85c \ucc44\ud0dd\uc774 \uc9c0\uc5f0\ub418\uc5b4 \ud2b9\ud788 \uc911\uc18c\ub4dd \uad6d\uac00\uc5d0\uc11c \uc811\uadfc\uc131\uc744 \uc81c\ud55c\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<br \/>\n*   \uace0\uc6a9\ub7c9 AAV \ubca1\ud130 \uc81c\uc870 \ubcd1\ubaa9 \ud604\uc0c1: \uace0\uc6a9\ub7c9 \uc544\ub370\ub178 \uad00\ub828 \ubc14\uc774\ub7ec\uc2a4(AAV) \ubca1\ud130 \uc81c\uc870\uc758 \ubcd1\ubaa9 \ud604\uc0c1\uc740 \uc0dd\uc0b0 \ubc0f \uacf5\uae09\uc5d0 \uc5b4\ub824\uc6c0\uc744 \ucd08\ub798\ud569\ub2c8\ub2e4.<br \/>\n*   \uc720\uc804\uc790 \ud3b8\uc9d1\uc758 \ube44\ud45c\uc801 \ud6a8\uacfc\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131: \uc720\uc804\uc790 \ud3b8\uc9d1 \uae30\uc220\uc758 \ube44\ud45c\uc801 \ud6a8\uacfc\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131\uc740 \ud2b9\ud788 \ubbf8\uad6d\uacfc \uc911\uad6d\uc5d0\uc11c \uc2e0\uc57d \uac1c\ubc1c\uc5d0 \ub300\ud55c \uc6b0\ub824\ub97c \ub0b3\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p># \uc138\uadf8\uba3c\ud2b8 \ubd84\uc11d<\/p>\n<p>\uce58\ub8cc \uc811\uadfc\ubc95:<br \/>\n\ubd84\uc790 \uae30\ubc18 \uac1c\uc785\uc740 2025\ub144 \ub9e4\ucd9c\uc5d0 \uac00\uc7a5 \ud06c\uac8c \uae30\uc5ec\ud558\uc5ec \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5\uc758 60.78%\ub97c \ucc28\uc9c0\ud588\uc2b5\ub2c8\ub2e4. \uc774 \ubd80\ubb38\uc740 \ucd5c\ucd08 \ucd9c\uc2dc\ub41c \uc720\uc804\uc790 \uce58\ub8cc\uc81c, \ud6a8\uc728\uc801\uc778 \uc5d1\uc190 \uc2a4\ud0a4\ud551 \ud654\ud559 \ubb3c\uc9c8, \uadf8\ub9ac\uace0 \uc0c8\ub85c\uc6b4 \ub9ac\ub4dc\uc2a4\ub8e8(read-through) \uc57d\ubb3c\uc5d0 \ud798\uc785\uc5b4 2031\ub144\uae4c\uc9c0 19.42%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\ub85c \ud655\uc7a5\ub420 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ubd84\uc790 \uae30\ubc18 \uce58\ub8cc\uc81c \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2031\ub144\uae4c\uc9c0 59\uc5b5 3\ucc9c\ub9cc \ub2ec\ub7ec\uc5d0 \uc774\ub97c \uac83\uc73c\ub85c \uc804\ub9dd\ub418\uba70, \uc774\ub294 \ub378\ub780\ub514\uc2a4\ud2b8\ub85c\uc820 \ubaa9\uc138\ud30c\ub974\ubcf4\ubca1\uc5d0 \ub300\ud55c \uc9c0\uc18d\uc801\uc778 \ubcf4\ud5d8 \uc801\uc6a9\uacfc CRISPR \uad6c\uc870\ubb3c \ud30c\uc774\ud504\ub77c\uc778\uc758 \uc131\uc219\uc744 \ubc18\uc601\ud569\ub2c8\ub2e4. DYNE-251\uc774 \uae30\uc874 \uc5d0\ud14c\ud50c\ub7ec\uc13c(eteplirsen) \ub300\ube44 3.71%\uc758 \ub514\uc2a4\ud2b8\ub85c\ud540 \ubc1c\ud604\uc728\uc744 \ubcf4\uc778 \uac83\uacfc \uac19\uc774, \ubd84\uc790 \uc591\uc2dd \ub0b4 \uacbd\uc7c1 \uc5ed\ud559\uc740 \ucc28\ubcc4\ud654\ub41c \ub514\uc2a4\ud2b8\ub85c\ud540 \ubc1c\ud604\uc5d0 \ub2ec\ub824 \uc788\uc2b5\ub2c8\ub2e4. \uc81c\uc870 \ud601\uc2e0\uc740 \uc5ec\uc804\ud788 \ud575\uc2ec \uc694\uc18c\uc774\uc9c0\ub9cc, \ucd5c\uadfc \ud3f4\ub9ac-A \uc2dc\ud000\uc2f1 \ubc0f \ud2b8\ub79c\uc2a4\uc9c4 \uce74\uc138\ud2b8 \uc544\ud0a4\ud14d\ucc98 \ucd5c\uc801\ud654\ub294 \ubc14\uc774\uc624\ub9ac\uc561\ud130 \uc6a9\ub7c9\ub2f9 \uae30\ub2a5\uc801 \uc218\uc728\uc744 \ub192\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc2a4\ud14c\ub85c\uc774\ub4dc \ubc0f \ube44\uc2a4\ud14c\ub85c\uc774\ub4dc\uc131 \ud56d\uc5fc\uc99d\uc81c\ub294 \ud2b9\ud788 \uc720\uc804\uc790 \uce58\ub8cc \uc811\uadfc\uc774 \uc9c0\uc5f0\ub418\ub294 \uacbd\uc6b0 \ubcf4\uc644\uc801\uc778 \uc5ed\ud560\uc744 \uc720\uc9c0\ud558\uba70, \ub9cc\uc131 \uce58\ub8cc \ud504\ub85c\ud1a0\ucf5c\uc758 \ub9e4\ucd9c \uae30\ubc18\uc744 \ubcf4\uc874\ud558\uace0 \ubcd1\uc6a9 \uc694\ubc95 \uc5f0\uad6c\ub97c \ub4b7\ubc1b\uce68\ud569\ub2c8\ub2e4.<\/p>\n<p>\ud22c\uc5ec \uacbd\ub85c:<br \/>\n2025\ub144\uc5d0\ub294 \uace0\uc6a9\ub7c9 \ubc14\uc774\ub7ec\uc2a4 \ubca1\ud130\uc758 \ubcd1\uc6d0 \uae30\ubc18 \uc804\ub2ec\uc744 \ubc18\uc601\ud558\uc5ec \uc815\ub9e5 \uc8fc\uc0ac(IV)\uac00 51.68%\uc758 \uc810\uc720\uc728\ub85c \uc9c0\ubc30\uc801\uc774\uc5c8\uc2b5\ub2c8\ub2e4. IV\ub294 \uc644\uc804 \uae38\uc774 \ub610\ub294 \ub9c8\uc774\ud06c\ub85c \ub514\uc2a4\ud2b8\ub85c\ud540 \uad6c\uc870\ubb3c\uc5d0 \ud544\uc218\uc801\uc774\uc9c0\ub9cc, \uc790\uac00 \uc8fc\uc0ac \uac00\ub2a5\ud55c \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud2f0\ub4dc \ubc0f \ud56d\uccb4 \ub2e8\ud3b8 \uc6b4\ubc18\uccb4\uac00 \uaddc\uc81c \uc2b9\uc778\uc744 \uc5bb\uc73c\uba74\uc11c \ud53c\ud558 \uc8fc\uc0ac(SC) \ucc44\ub110\uc740 2031\ub144\uae4c\uc9c0 19.37%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \ud53c\ud558 \uc81c\ud615\uc758 \ub4a4\uc13c \uadfc\uc774\uc601\uc591\uc99d \uce58\ub8cc \uc2dc\uc7a5 \uaddc\ubaa8\ub294 2031\ub144\uae4c\uc9c0 22\uc5b5 2\ucc9c\ub9cc \ub2ec\ub7ec\ub97c \ub118\uc5b4\uc124 \uc218 \uc788\uc73c\uba70, \uc774\ub294 \uc2dc\uc124 \ud63c\uc7a1\uc744 \uc644\ud654\ud558\uace0 \uc21c\uc751\ub3c4\ub97c \uac1c\uc120\ud558\ub294 \uc678\ub798 \uce58\ub8cc \uacbd\ub85c\ub97c \uc5f4\uc5b4\uc904 \uac83\uc785\ub2c8\ub2e4. \uc57d\ubb3c-\uae30\uae30 \ubcf5\ud569 \ud601\uc2e0(\uc6e8\uc5b4\ub7ec\ube14 \uc790\ub3d9 \uc8fc\uc0ac\uae30\ubd80\ud130 \uc800\uc7a5\ud615 \ud3f4\ub9ac\uba38\uae4c\uc9c0)\uc740 \ud53c\ud558 \uacbd\ub85c\uc640\uc758 \ud6c4\ubcf4 \ubb3c\uc9c8 \ud638\ud658\uc131\uc744 \ud655\ub300\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. 2024\ub144 \uae30\ube44\ub178\uc2a4\ud0c0\ud2b8 \uc2b9\uc778\uc73c\ub85c \ucd09\uc9c4\ub41c \uacbd\uad6c\uc6a9 \uc57d\ubb3c\uc740 \ubcf4\ud3b8\uc801\uc778 \uc811\uadfc\uc131\uc744 \uc81c\uacf5\ud558\uba70, \ud658\uc790 \ud3b8\uc758\uc131\uc744 \ud06c\uac8c \ud5a5\uc0c1\uc2dc\ud0ac \uac83\uc785\ub2c8\ub2e4. \uc774\ub294 \ud2b9\ud788 \uc7a5\uae30\uc801\uc778 \uce58\ub8cc\uac00 \ud544\uc694\ud55c DMD \ud658\uc790\ub4e4\uc5d0\uac8c \uc911\uc694\ud55c \uc774\uc810\uc73c\ub85c \uc791\uc6a9\ud560 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc5ed\ud559:<br \/>\nDMD \uce58\ub8cc \uc2dc\uc7a5\uc740 2025\ub144\ubd80\ud130 2031\ub144\uae4c\uc9c0 16.2%\uc758 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960\uc744 \uae30\ub85d\ud558\uba70 2031\ub144\uae4c\uc9c0 200\uc5b5 \ub2ec\ub7ec\ub97c \ub118\uc5b4\uc124 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774 \uc131\uc7a5\uc740 \uc8fc\ub85c \uc720\uc804\uc790 \uce58\ub8cc \ubc0f RNA \uae30\ubc18 \uce58\ub8cc\ubc95\uc758 \ub3c4\uc785\uacfc \ud655\uc7a5\uc5d0 \uc758\ud574 \uc8fc\ub3c4\ub420 \uac83\uc785\ub2c8\ub2e4. \uadf8\ub7ec\ub098 \ub192\uc740 \uce58\ub8cc \ube44\uc6a9\uacfc \ubcf5\uc7a1\ud55c \ud22c\uc5ec \ubc29\uc2dd\uc740 \uc2dc\uc7a5 \uc131\uc7a5\uc5d0 \ub3c4\uc804 \uacfc\uc81c\ub85c \ub0a8\uc544 \uc788\uc2b5\ub2c8\ub2e4. \uaddc\uc81c \uc2b9\uc778 \ubc0f \uc784\uc0c1 \uc2dc\ud5d8 \uacb0\uacfc\ub294 \uc2dc\uc7a5 \uc5ed\ud559\uc5d0 \uc9c0\uc18d\uc801\uc73c\ub85c \uc601\ud5a5\uc744 \ubbf8\uce60 \uac83\uc774\uba70, \uc0c8\ub85c\uc6b4 \uce58\ub8cc\ubc95\uc758 \uc0c1\uc5c5\ud654 \uc131\uacf5 \uc5ec\ubd80\ub97c \uacb0\uc815\ud558\ub294 \uc911\uc694\ud55c \uc694\uc18c\uac00 \ub420 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd:<br \/>\nDMD \uce58\ub8cc \uc2dc\uc7a5\uc740 \ud604\uc7ac \uc18c\uc218\uc758 \uc8fc\uc694 \uc81c\uc57d \ud68c\uc0ac\ub4e4\uc774 \uc9c0\ubc30\ud558\uace0 \uc788\uc73c\uba70, \uc774\ub4e4\uc740 \uc720\uc804\uc790 \uce58\ub8cc, RNA \uae30\ubc18 \uce58\ub8cc, \uc2a4\ud14c\ub85c\uc774\ub4dc \ubc0f \uae30\ud0c0 \ubcf4\uc870 \uce58\ub8cc\ubc95 \uac1c\ubc1c\uc5d0 \uc801\uadf9\uc801\uc73c\ub85c \ud22c\uc790\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc0c8\ub85c\uc6b4 \uc9c4\uc785\uc790\ub4e4\uc740 \ud601\uc2e0\uc801\uc778 \uce58\ub8cc\ubc95\uacfc \uc804\ub2ec \uc2dc\uc2a4\ud15c\uc744 \ud1b5\ud574 \uc2dc\uc7a5 \uc810\uc720\uc728\uc744 \ud655\ubcf4\ud558\ub824 \ub178\ub825\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc804\ub7b5\uc801 \uc81c\ud734, \uc778\uc218\ud569\ubcd1, \ub77c\uc774\uc120\uc2a4 \uacc4\uc57d\uc740 \uacbd\uc7c1 \ud658\uacbd\uc744 \ud615\uc131\ud558\ub294 \ub370 \uc911\uc694\ud55c \uc5ed\ud560\uc744 \ud558\uba70, \uae30\uc5c5\ub4e4\uc740 \uc5f0\uad6c \uac1c\ubc1c \uc5ed\ub7c9\uc744 \uac15\ud654\ud558\uace0 \uc2dc\uc7a5 \uc811\uadfc\uc131\uc744 \ud655\ub300\ud558\uae30 \uc704\ud574 \ud611\ub825\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\ubbf8\ub798 \uc804\ub9dd:<br \/>\nDMD \uce58\ub8cc\uc758 \ubbf8\ub798\ub294 \uc720\uc804\uc790 \ud3b8\uc9d1 \uae30\uc220, \uc904\uae30\uc138\ud3ec \uce58\ub8cc, \uadf8\ub9ac\uace0 \ub354\uc6b1 \uc815\uad50\ud55c \uc57d\ubb3c \uc804\ub2ec \uc2dc\uc2a4\ud15c\uc758 \ubc1c\uc804\uc5d0 \ub2ec\ub824 \uc788\uc2b5\ub2c8\ub2e4. \uac1c\uc778 \ub9de\ucda4\ud615 \uc758\ud559 \uc811\uadfc \ubc29\uc2dd\uc740 \ud658\uc790 \uac1c\uac1c\uc778\uc758 \uc720\uc804\uc801 \ud2b9\uc131\uc5d0 \ub9de\ub294 \uce58\ub8cc\ubc95\uc744 \uc81c\uacf5\ud568\uc73c\ub85c\uc368 \uce58\ub8cc \ud6a8\uacfc\ub97c \uadf9\ub300\ud654\ud560 \uc7a0\uc7ac\ub825\uc744 \uac00\uc9c0\uace0 \uc788\uc2b5\ub2c8\ub2e4. \ub610\ud55c, \uc870\uae30 \uc9c4\ub2e8 \uae30\uc220\uc758 \ubc1c\uc804\uc740 \uce58\ub8cc \uac1c\uc785 \uc2dc\uae30\ub97c \uc55e\ub2f9\uaca8 \uc9c8\ubcd1 \uc9c4\ud589\uc744 \ub2a6\ucd94\uace0 \ud658\uc790\uc758 \uc0b6\uc758 \uc9c8\uc744 \ud5a5\uc0c1\uc2dc\ud0a4\ub294 \ub370 \uae30\uc5ec\ud560 \uac83\uc785\ub2c8\ub2e4. \uc7a5\uae30\uc801\uc73c\ub85c\ub294 DMD\ub97c \uc644\uce58\ud558\uac70\ub098 \ub9cc\uc131 \uc9c8\ud658\uc73c\ub85c \uad00\ub9ac\ud560 \uc218 \uc788\ub294 \uce58\ub8cc\ubc95 \uac1c\ubc1c\uc774 \uad81\uadf9\uc801\uc778 \ubaa9\ud45c\uac00 \ub420 \uac83\uc785\ub2c8\ub2e4.<\/p>\n<p>\uc774 \ubcf4\uace0\uc11c\ub294 \ud76c\uadc0 \uc720\uc804 \uc9c8\ud658\uc778 \ub4c0\uc13c \uadfc\uc774\uc601\uc591\uc99d(DMD) \uce58\ub8cc \uc2dc\uc7a5\uc5d0 \ub300\ud55c \uc2ec\uce35 \ubd84\uc11d\uc744 \uc81c\uacf5\ud569\ub2c8\ub2e4. DMD\ub294 X-\uc5fc\uc0c9\uccb4 \uc5f0\uad00 \uc5f4\uc131 \uc720\uc804 \ud328\ud134\uc73c\ub85c \uc778\ud574 \uc810\uc9c4\uc801\uc778 \uadfc\uc721 \uc18c\ubaa8\uc640 \uc57d\ud654\ub97c \uc720\ubc1c\ud558\ub294 \uc9c8\ud658\uc73c\ub85c, \ucd5c\uadfc \ub3cc\uc5f0\ubcc0\uc774\ub098 \uc720\uc804\uc801 \ud2b9\uc131\uc73c\ub85c \ubc1c\uc0dd\ud560 \uc218 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uac1c\uc694 \ubc0f \uc131\uc7a5 \uc804\ub9dd:<br \/>\nDMD \uce58\ub8cc \uc2dc\uc7a5\uc740 2031\ub144\uae4c\uc9c0 95\uc5b5 9\ucc9c\ub9cc \ub2ec\ub7ec \uaddc\ubaa8\uc5d0 \ub3c4\ub2ec\ud560 \uac83\uc73c\ub85c \uc608\uc0c1\ub418\uba70, \uc608\uce21 \uae30\uac04 \ub3d9\uc548 \uc5f0\ud3c9\uade0 \uc131\uc7a5\ub960(CAGR) 18.76%\uc758 \uacac\uace0\ud55c \uc131\uc7a5\uc744 \ubcf4\uc77c \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \ub3d9\uc778:<br \/>\n\uc2dc\uc7a5\uc758 \uc131\uc7a5\uc744 \uacac\uc778\ud558\ub294 \uc8fc\uc694 \uc694\uc778\uc73c\ub85c\ub294 DMD\uc758 \uc9c8\ubcd1 \ubd80\ub2f4 \uc99d\uac00, \uc2e0\uaddc \uce58\ub8cc\ubc95\uc5d0 \ub300\ud55c \ud22c\uc790 \ud655\ub300, \uc548\ud2f0\uc13c\uc2a4 \uc5d1\uc190 \uc2a4\ud0a4\ud551 \uc57d\ubb3c\uc758 \uc2b9\uc778 \uac00\uc18d\ud654, \ud76c\uadc0\uc758\uc57d\ud488 \uc778\uc13c\ud2f0\ube0c \ubc0f \uc6b0\uc120 \uc2ec\uc0ac \ubc14\uc6b0\ucc98 \uc81c\ub3c4, \uc720\uc804\uc790 \ud3b8\uc9d1 \ud30c\uc774\ud504\ub77c\uc778\uc744 \uac00\uc18d\ud654\ud558\ub294 CRISPR \ud50c\ub7ab\ud3fc \uac70\ub798, \uadf8\ub9ac\uace0 \ud658\uc790 \ubaa8\uc9d1\uc744 \uac1c\uc120\ud558\ub294 \ubd84\uc0b0\ud615 \uc784\uc0c1\uc2dc\ud5d8\uc758 \ub3c4\uc785 \ub4f1\uc774 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uc81c\uc57d \uc694\uc778:<br \/>\n\ubc18\uba74, \uc2dc\uc7a5 \uc131\uc7a5\uc744 \uc800\ud574\ud558\ub294 \uc694\uc778\uc73c\ub85c\ub294 \ud45c\uc900\ud654\ub41c \uc784\uc0c1 \ud6a8\ub2a5 \ud3c9\uac00 \uc9c0\ud45c\uc758 \ubd80\uc871, \ub192\uc740 \uce58\ub8cc \ube44\uc6a9 \ubc0f \ubcf4\ud5d8 \uc0c1\ud658 \ubb38\uc81c, \uace0\uc6a9\ub7c9 AAV \ubca1\ud130\uc758 \uc81c\uc870 \ubcd1\ubaa9 \ud604\uc0c1, \uadf8\ub9ac\uace0 \uc720\uc804\uc790 \ud3b8\uc9d1\uc758 \ube44\ud45c\uc801 \ud6a8\uacfc\uc5d0 \ub300\ud55c \uaddc\uc81c \ubd88\ud655\uc2e4\uc131 \ub4f1\uc774 \uc9c0\uc801\ub429\ub2c8\ub2e4.<\/p>\n<p>\uce58\ub8cc \uc811\uadfc\ubc95\ubcc4 \uc2dc\uc7a5 \ubd84\uc11d:<br \/>\n\uce58\ub8cc \uc811\uadfc\ubc95\ubcc4\ub85c\ub294 \ubd84\uc790 \uae30\ubc18 \uce58\ub8cc\ubc95\uc774 \ud604\uc7ac \uc2dc\uc7a5\uc758 60.78%\ub97c \ucc28\uc9c0\ud558\uba70 \uc9c0\ubc30\uc801\uc778 \uc704\uce58\ub97c \uc720\uc9c0\ud558\uace0 \uc788\uc73c\uba70, \uc720\uc804\uc790 \ub300\uccb4 \ubc0f \uc5d1\uc190 \uc2a4\ud0a4\ud551 \uae30\uc220\uc758 \ubc1c\uc804\uacfc \ud568\uaed8 \uc55e\uc73c\ub85c\ub3c4 \uc120\ub450\ub97c \uc9c0\ud0ac \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc2a4\ud14c\ub85c\uc774\ub4dc \uc694\ubc95, NSAIDs \ubc0f \uae30\ud0c0 \uce58\ub8cc\ubc95 \ub610\ud55c \uc2dc\uc7a5\uc758 \uc77c\ubd80\ub97c \uad6c\uc131\ud569\ub2c8\ub2e4.<\/p>\n<p>\ud22c\uc5ec \uacbd\ub85c\ubcc4 \uc2dc\uc7a5 \ubd84\uc11d:<br \/>\n\ud22c\uc5ec \uacbd\ub85c\ubcc4\ub85c\ub294 \ud53c\ud558 \uc8fc\uc0ac \ubc29\uc2dd\uc774 19.37%\uc758 CAGR\ub85c \ube60\ub974\uac8c \uc131\uc7a5\ud560 \uac83\uc73c\ub85c \uc804\ub9dd\ub429\ub2c8\ub2e4. \uc774\ub294 \uc790\uac00 \ud22c\uc5ec\uc758 \ud3b8\ub9ac\uc131, \ubcd1\uc6d0 \ubc29\ubb38 \uac10\uc18c, \uce58\ub8cc \uc21c\uc751\ub3c4 \ud5a5\uc0c1 \ub4f1\uc758 \uc774\uc810 \ub54c\ubb38\uc785\ub2c8\ub2e4. \uc815\ub9e5 \uc8fc\uc0ac \ubc0f \uacbd\uad6c \ud22c\uc5ec \ubc29\uc2dd\ub3c4 \uc911\uc694\ud55c \ubd80\ubd84\uc744 \ucc28\uc9c0\ud569\ub2c8\ub2e4.<\/p>\n<p>\uc9c0\uc5ed\ubcc4 \uc2dc\uc7a5 \ubd84\uc11d:<br \/>\n\uc9c0\uc5ed\ubcc4\ub85c\ub294 \uc544\uc2dc\uc544-\ud0dc\ud3c9\uc591 \uc9c0\uc5ed\uc774 19.61%\uc758 \uac00\uc7a5 \ub192\uc740 CAGR\uc744 \uae30\ub85d\ud558\uba70 \uac00\uc7a5 \ube60\ub974\uac8c \uc131\uc7a5\ud558\ub294 \uc2dc\uc7a5\uc774 \ub420 \uac83\uc73c\ub85c \uc608\uc0c1\ub429\ub2c8\ub2e4. \uc774\ub294 \uc77c\ubcf8\uc758 \uc2e0\uc18d \uc2b9\uc778 \ubc0f \uc911\uad6d\uc758 \uc6b0\uc120 \uc2ec\uc0ac \uc81c\ub3c4, \uadf8\ub9ac\uace0 \uc784\uc0c1 \uc778\ud504\ub77c \ud655\uc7a5\uc5d0 \uae30\uc778\ud569\ub2c8\ub2e4. \ubd81\ubbf8\uc640 \uc720\ub7fd \ub610\ud55c \uc8fc\uc694 \uc2dc\uc7a5\uc73c\ub85c \ubd84\uc11d\ub429\ub2c8\ub2e4.<\/p>\n<p>\uc720\ud1b5 \ucc44\ub110\ubcc4 \uc2dc\uc7a5 \ubd84\uc11d:<br \/>\n\uc720\ud1b5 \ucc44\ub110\uc740 \ubcd1\uc6d0 \uc57d\uad6d, \uc18c\ub9e4 \uc57d\uad6d, \uc628\ub77c\uc778 \uc57d\uad6d\uc73c\ub85c \uad6c\ubd84\ub429\ub2c8\ub2e4.<\/p>\n<p>\uacbd\uc7c1 \ud658\uacbd:<br \/>\n\uc2dc\uc7a5\uc740 Sarepta Therapeutics, PTC Therapeutics, Nippon Shinyaku, Pfizer \ub4f1 \uc8fc\uc694 \uc81c\uc57d\uc0ac\ub4e4\uc774 \uacbd\uc7c1\ud558\uace0 \uc788\uc73c\uba70, Dyne Therapeutics, Edgewise Therapeutics, Capricor\uc640 \uac19\uc740 \uc2e0\ud765 \uae30\uc5c5\ub4e4\uc740 \ucd5c\uc801\ud654\ub41c \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc, \uadfc\uc721 \ubcf4\uc874 \uc18c\ubd84\uc790, \uc2ec\uc7a5 \ud45c\uc801 \uc5d1\uc18c\uc880 \ub4f1 \ud601\uc2e0\uc801\uc778 \uba54\ucee4\ub2c8\uc998\uc744 \ud1b5\ud574 \uae30\uc874 \uc720\uc804\uc790 \uce58\ub8cc \uc120\ub450 \uc8fc\uc790\ub4e4\uacfc \ucc28\ubcc4\ud654\ub97c \uaf80\ud558\uba70 \ub3c4\uc804\uc790\ub85c \ubd80\uc0c1\ud558\uace0 \uc788\uc2b5\ub2c8\ub2e4.<\/p>\n<p>\uc2dc\uc7a5 \uae30\ud68c \ubc0f \ubbf8\ub798 \uc804\ub9dd:<br \/>\n\ub192\uc740 \ucd08\uae30 \ube44\uc6a9\uacfc \uc7a5\uae30\uc801\uc778 \uce58\ub8cc \uacb0\uacfc\uc758 \uade0\ud615\uc744 \ub9de\ucd94\uae30 \uc704\ud574 \ubcf4\ud5d8\uc0ac\ub4e4\uc740 \uac00\uce58 \uae30\ubc18 \uacc4\uc57d, \ubd84\ud560 \uc9c0\ubd88, \uc2e4\uc81c \uc784\uc0c1 \ub370\uc774\ud130(RWE) \uc218\uc9d1 \ub4f1\uc758 \ubc29\uc548\uc744 \uc2dc\ubc94 \uc6b4\uc601\ud558\uba70 \ubcf4\ud5d8 \uc0c1\ud658 \ubb38\uc81c\ub97c \ud574\uacb0\ud558\ub824\ub294 \ub178\ub825\uc744 \uae30\uc6b8\uc774\uace0 \uc788\uc2b5\ub2c8\ub2e4. \uc774\ub294 \uc2dc\uc7a5\uc758 \uc9c0\uc18d\uc801\uc778 \uc131\uc7a5\uc744 \uc704\ud55c \uc911\uc694\ud55c \uae30\ud68c\ub85c \uc791\uc6a9\ud560 \uac83\uc785\ub2c8\ub2e4.<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-59497","post","type-post","status-publish","format-standard","hentry","category-market-reports"],"_links":{"self":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/59497"}],"collection":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/comments?post=59497"}],"version-history":[{"count":0,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/posts\/59497\/revisions"}],"wp:attachment":[{"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/media?parent=59497"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/categories?post=59497"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.globalresearch.co.kr\/insight\/wp-json\/wp\/v2\/tags?post=59497"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}